NCT03486899

Brief Summary

This is a study of experimental medication BMS-986036 given to adults with Nonalcoholic Steatohepatitis (NASH; the buildup of fat and inflammation in the liver that is not caused by alcohol) and stage 3 liver fibrosis (severe fibrosis).

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
197

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jun 2018

Typical duration for phase_2

Geographic Reach
2 countries

89 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 30, 2018

Completed
4 days until next milestone

First Posted

Study publicly available on registry

April 3, 2018

Completed
3 months until next milestone

Study Start

First participant enrolled

June 19, 2018

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 14, 2020

Completed
11 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 17, 2021

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

September 9, 2022

Completed
Last Updated

September 9, 2022

Status Verified

August 1, 2022

Enrollment Period

2.2 years

First QC Date

March 30, 2018

Results QC Date

August 16, 2022

Last Update Submit

August 16, 2022

Conditions

Outcome Measures

Primary Outcomes (1)

  • The Percentage of Participants With Improvement in Fibrosis or Nonalcoholic Steatohepatitis (NASH) at Week 24

    The percentage of participants who achieved a ≥1-stage improvement in fibrosis without worsening of NASH or NASH improvement with no worsening of fibrosis at week 24 in liver biopsy. Improvement in fibrosis is defined by the NASH Clinical Research Network (CRN) Fibrosis Score. Improvement in NASH is defined by a ≥2-stage decrease in the nonalcoholic fatty liver disease activity score (NAS). Worsening of NASH is defined as an increase of the nonalcoholic fatty liver disease (NAFLD) Activity Score (NAS) by ≥1 point. Worsening of fibrosis is defined as an increase of fibrosis by ≥1 point as determined by the NASH CRN Fibrosis Score. NASH CRN Fibrosis is staged on a 0-4 scale: 0 (none); 1 (perisinusoidal or periportal fibrosis); 2 (perisinusoidal and portal/periportal fibrosis); 3 (bridging fibrosis); 4 (cirrhosis).

    From first dose to 24 weeks after first dose

Secondary Outcomes (9)

  • The Percentage of Participants Who Achieved an Improvement in Nonalcoholic Steatohepatitis Clinical Research Network (NASH CRN) Fibrosis Score at Week 24

    From first dose to 24 weeks after first dose

  • The Percentage of Participants Who Achieve a ≥ 1-Stage Improvement in Ishak Fibrosis Score at Week 24

    From first dose to 24 weeks after first dose

  • The Percentage of Participants With Any Improvement in Collagen Proportionate Area (CPA) at Week 24

    From first dose to 24 weeks after first dose

  • The Percentage of Participants With Nonalcoholic Steatohepatitis (NASH) Resolution Without Worsening of Fibrosis at Week 24

    From first dose to 24 weeks after first dose

  • The Percentage of Participants With Nonalcoholic Steatohepatitis (NASH) Resolution at Week 24

    From first dose to 24 weeks after first dose

  • +4 more secondary outcomes

Study Arms (4)

BMS-986036 Dose Level 1

EXPERIMENTAL

Administered by subcutaneous injection.

Drug: BMS-986036

BMS-986036 Dose Level 2

EXPERIMENTAL

Administered by subcutaneous injection.

Drug: BMS-986036

BMS-986036 Dose Level 3

EXPERIMENTAL

Administered by subcutaneous injection.

Drug: BMS-986036

Placebo

PLACEBO COMPARATOR

Administered by subcutaneous injection.

Other: Placebo

Interventions

Specified dose on specified days.

Also known as: Pegbelfermin
BMS-986036 Dose Level 1BMS-986036 Dose Level 2BMS-986036 Dose Level 3
PlaceboOTHER

Specified dose on specified days.

Placebo

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Liver biopsy performed within 6 months (26 weeks) prior to the screening period. If historical biopsy is not available, a liver biopsy will be performed during the screening period. Biopsy must be consistent with NASH, with: a) a score of at least 1 for each NAS component (steatosis, lobular inflammation, and ballooning), as assessed by the central reader, and b) stage 3 liver fibrosis according to the NASH CRN classification, as assessed by the central reader
  • Participants taking anti-diabetic, anti-obesity, or anti-dyslipidemic medications must have been on stable regimens for at least 3 months (12 weeks) (6 weeks for statins) prior to and during the screening period
  • Participants taking vitamin E at doses greater than or equal to (\>=) 800 IU/day must have been on stable doses for at least 6 months (26 weeks) prior to and during the Screening Period. Vitamin E treatment (\>=800 IU/day) must not have been initiated after the qualifying liver biopsy was performed.

You may not qualify if:

  • Other causes of liver disease (e.g., alcoholic liver disease, hepatitis B virus infection, chronic hepatitis C virus \[HCV\] infection, autoimmune hepatitis, drug-induced hepatotoxicity, Wilson disease, α-1-antitrypsin deficiency, iron overload, and hemochromatosis); participants with HCV sustained viral response (undetectable HCV RNA) for at least 2 years prior to biopsy confirming study eligibility may be eligible
  • Current or past history of hepatocellular carcinoma (HCC)
  • Past or current evidence of hepatic decompensation (e.g., ascites, variceal bleeding, hepatic encephalopathy and/or spontaneous bacterial peritonitis) or liver transplantation

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (89)

Local Institution - 0087

Madison, Alabama, 35758, United States

Location

Local Institution - 0005

Chandler, Arizona, 85224, United States

Location

Local Institution - 0088

Phoenix, Arizona, 85013, United States

Location

Local Institution - 0001

Phoenix, Arizona, 85054, United States

Location

The Institute for Liver Health - Tucson

Tucson, Arizona, 85712, United States

Location

Kindred Medical Institute for Clinical Trials

Corona, California, 92879, United States

Location

Local Institution - 0092

Coronado, California, 92118, United States

Location

University of California San Diego

La Jolla, California, 92037, United States

Location

Local Institution - 0017

Los Angeles, California, 90036, United States

Location

Cedars-Sinai Medical Center

Los Angeles, California, 90048, United States

Location

GastroIntestinal Biosciences

Los Angeles, California, 90067-2015, United States

Location

Catalina Research Institute

Montclair, California, 91763, United States

Location

Local Institution - 0008

Oakland, California, 94611, United States

Location

Local Institution - 0044

Oxnard, California, 93030, United States

Location

Huntington Medical Research Institutes - HMRI Liver Center

Pasadena, California, 91105, United States

Location

Local Institution - 0019

Pasadena, California, 91105, United States

Location

Local Institution - 0074

Redwood City, California, 94063, United States

Location

Local Institution - 0013

Rialto, California, 92377, United States

Location

Local Institution - 0089

San Clemente, California, 92673, United States

Location

Medical Associates Research Group

San Diego, California, 92123, United States

Location

Local Institution - 0068

San Francisco, California, 94115, United States

Location

Bridgeport Hospital

Bridgeport, Connecticut, 06610, United States

Location

MedStar Georgetown University Hospital

Washington D.C., District of Columbia, 20007, United States

Location

Local Institution - 0079

Coral Gables, Florida, 33134, United States

Location

Top Medical Research

Cutler Bay, Florida, 33189, United States

Location

Local Institution - 0100

Gainesville, Florida, 32610, United States

Location

Clinical Research of Homestead

Homestead, Florida, 33030, United States

Location

Local Institution - 0082

Jacksonville, Florida, 32224, United States

Location

Local Institution - 0003

Lakewood Rch, Florida, 34211, United States

Location

Local Institution - 0002

Miami, Florida, 33136, United States

Location

A+ Research

Miami, Florida, 33144, United States

Location

IMIC Research

Miami, Florida, 33157, United States

Location

Sensible Healthcare

Ocoee, Florida, 34761, United States

Location

Local Institution - 0081

Orlando, Florida, 32806, United States

Location

Tampa General Hospital

Tampa, Florida, 33606, United States

Location

Local Institution - 0105

Marietta, Georgia, 30060, United States

Location

Tandem Clinical Research

Marrero, Louisiana, 70072, United States

Location

Tulane University Health Sciences Center

New Orleans, Louisiana, 70112, United States

Location

Local Institution - 0027

New Orleans, Louisiana, 70121, United States

Location

Local Institution - 0007

Baltimore, Maryland, 21202, United States

Location

Local Institution - 0057

Catonsville, Maryland, 21228, United States

Location

Boston Medical Center

Boston, Massachusetts, 02118, United States

Location

NECCR PrimaCare Research

Fall River, Massachusetts, 02721, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

Local Institution - 0063

Chesterfield, Missouri, 63005, United States

Location

Saint Lukes Hospital of Kansas City

Kansas City, Missouri, 64111, United States

Location

Saint Louis University

St Louis, Missouri, 63110, United States

Location

University at Buffalo

Buffalo, New York, 14203, United States

Location

Local Institution - 0078

Manhasset, New York, 11030, United States

Location

Local Institution - 0083

New York, New York, 10003, United States

Location

Local Institution - 0038

New York, New York, 10016, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

Local Institution - 0067

Butner, North Carolina, 27509-1626, United States

Location

Local Institution - 0064

Charlotte, North Carolina, 28204, United States

Location

Local Institution - 0096

Concord, North Carolina, 28027, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Local Institution - 0009

Philadelphia, Pennsylvania, 19107, United States

Location

Local Institution - 0006

Pittsburgh, Pennsylvania, 15213, United States

Location

Local Institution - 0047

Germantown, Tennessee, 38138, United States

Location

Local Institution - 0041

Hermitage, Tennessee, 37076, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232-5280, United States

Location

Texas Clinical Research Institute

Arlington, Texas, 76012, United States

Location

Local Institution - 0066

Austin, Texas, 78757, United States

Location

Local Institution - 0053

Dallas, Texas, 75203, United States

Location

Local Institution - 0052

Dallas, Texas, 75234, United States

Location

Texas Digestive Disease Consultants - Dallas

Dallas, Texas, 75246, United States

Location

University of Texas Southwestern Medical Center

Dallas, Texas, 75390-88520, United States

Location

Texas Digestive Disease Consultants - Southlake

Fort Worth, Texas, 76104, United States

Location

Local Institution - 0004

Houston, Texas, 77002, United States

Location

Local Institution - 0059

Houston, Texas, 77030, United States

Location

Local Institution - 0062

Houston, Texas, 77030, United States

Location

Local Institution - 0029

San Antonio, Texas, 78215, United States

Location

Local Institution - 0012

San Antonio, Texas, 78229, United States

Location

Local Institution - 0101

San Antonio, Texas, 78229, United States

Location

University of Vermont Medical Center

Burlington, Vermont, 05401, United States

Location

University of Virginia Health System

Charlottesville, Virginia, 22908, United States

Location

Inova Fairfax Hospital

Falls Church, Virginia, 22042, United States

Location

Gastroenterology Associates, PC

Manassas, Virginia, 20110, United States

Location

Local Institution - 0069

Norfolk, Virginia, 23502, United States

Location

The Gastroenterology Group

Reston, Virginia, 20191, United States

Location

Bon Secours Liver Institute of Richmond

Richmond, Virginia, 23226, United States

Location

Local Institution - 0077

Richmond, Virginia, 23249, United States

Location

Local Institution - 0049

Richmond, Virginia, 23298, United States

Location

Kurume University Hospital

Kurume, Fukuoka, 8300011, Japan

Location

Local Institution - 0056

Yokohama, Kanagawa, 236-0004, Japan

Location

Local Institution - 0072

Kashihara, Nara, 6348522, Japan

Location

Toranomon Hospital

Minato, Tokyo, 105-8470, Japan

Location

Keio University Hospital

Shinjuku-ku, Tokyo, 1600016, Japan

Location

Fukushima Medical University Hospital

Fukushima, 960-1295, Japan

Location

Related Publications (3)

  • Loomba R, Sanyal AJ, Nakajima A, Neuschwander-Tetri BA, Goodman ZD, Harrison SA, Lawitz EJ, Gunn N, Imajo K, Ravendhran N, Akahane T, Boone B, Yamaguchi M, Chatterjee A, Tirucherai GS, Shevell DE, Du S, Charles ED, Abdelmalek MF. Pegbelfermin in Patients With Nonalcoholic Steatohepatitis and Stage 3 Fibrosis (FALCON 1): A Randomized Phase 2b Study. Clin Gastroenterol Hepatol. 2024 Jan;22(1):102-112.e9. doi: 10.1016/j.cgh.2023.04.011. Epub 2023 Apr 23.

  • Brown EA, Minnich A, Sanyal AJ, Loomba R, Du S, Schwarz J, Ehman RL, Karsdal M, Leeming DJ, Cizza G, Charles ED. Effect of pegbelfermin on NASH and fibrosis-related biomarkers and correlation with histological response in the FALCON 1 trial. JHEP Rep. 2023 Jan 7;5(4):100661. doi: 10.1016/j.jhepr.2022.100661. eCollection 2023 Apr.

  • Abdelmalek MF, Charles ED, Sanyal AJ, Harrison SA, Neuschwander-Tetri BA, Goodman Z, Ehman RA, Karsdal M, Nakajima A, Du S, Tirucherai GS, Klinger GH, Mora J, Yamaguchi M, Shevell DE, Loomba R. The FALCON program: Two phase 2b randomized, double-blind, placebo-controlled studies to assess the efficacy and safety of pegbelfermin in the treatment of patients with nonalcoholic steatohepatitis and bridging fibrosis or compensated cirrhosis. Contemp Clin Trials. 2021 May;104:106335. doi: 10.1016/j.cct.2021.106335. Epub 2021 Feb 28.

Related Links

MeSH Terms

Conditions

Liver CirrhosisNon-alcoholic Fatty Liver Disease

Interventions

Pegbelfermin

Condition Hierarchy (Ancestors)

Liver DiseasesDigestive System DiseasesFibrosisPathologic ProcessesPathological Conditions, Signs and SymptomsFatty Liver

Results Point of Contact

Title
Bristol-Myers Squibb Study Director
Organization
Bristol-Myers Squibb

Study Officials

  • Bristol-Myers Squibb

    Bristol-Myers Squibb

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 30, 2018

First Posted

April 3, 2018

Study Start

June 19, 2018

Primary Completion

September 14, 2020

Study Completion

August 17, 2021

Last Updated

September 9, 2022

Results First Posted

September 9, 2022

Record last verified: 2022-08

Locations