NCT03439943

Brief Summary

The main objective of the study is to evaluate the effect of lixisenatide (20 μg/d), versus placebo, administered as add-on therapy with the usual antiparkinsonian treatment, on the progression of motor disability in patients with early PD in order to assess its potential "disease-modifying" effect.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
156

participants targeted

Target at P75+ for phase_2 parkinson-disease

Timeline
Completed

Started Jun 2018

Typical duration for phase_2 parkinson-disease

Geographic Reach
1 country

20 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 13, 2018

Completed
7 days until next milestone

First Posted

Study publicly available on registry

February 20, 2018

Completed
4 months until next milestone

Study Start

First participant enrolled

June 13, 2018

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 15, 2021

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 15, 2021

Completed
Last Updated

November 28, 2025

Status Verified

June 1, 2023

Enrollment Period

2.8 years

First QC Date

February 13, 2018

Last Update Submit

November 21, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change from baseline to end-point (M12) in the MDS-UPDRS III motor (Movement Disorder Society-Unified Parkinson's disease rating scale)

    The main objective of the study is to evaluate the effect of lixisenatide (20 μg/d), versus placebo, administered as add-on therapy with the usual antiparkinsonian treatment, on the progression of motor disability in patients with early PD in order to assess its potential "disease-modifying" effect. The primary endpoint of this study is the change from baseline to end-point (M12) in the MDS-UPDRS III motor examination score, evaluated in the best ON condition in patients with early Parkinson's Disease.

    12 month

Study Arms (2)

Lixisenatide

EXPERIMENTAL

Lixisenatide (10μg/d for 14 days and then 20μg/d): once daily subcutaneous

Drug: Lixisenatide

Placebo

PLACEBO COMPARATOR

Placebo: once daily subcutaneous injection

Drug: placebo

Interventions

Patients randomized in the Lixisenatide group will receive 10μg/day for 14 days and then 20μg/day administered by once-daily subcutaneous injections during 12 months. If patients are unable to tolerable the dose of 20μg/day, this dose can be reduced to 10μg/day

Also known as: injection drug
Lixisenatide

Patients randomized in the placebo group will receive the corresponding placebo administered subcutaneously (once daily subcutaneous injection).

Also known as: placebo injection
Placebo

Eligibility Criteria

Age40 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients with PD according to UKPDSBB criteria (male or female).
  • Patient with a Hoehn and Yahr Stage \<3 in the ON condition.
  • Patients aged from 40 to 75 years old.
  • Early-stage PD patients: diagnosis of PD for less than 3 years, without dyskinesia and motor fluctuations.
  • Patients treated with an "optimized" stable dopaminergic medication regimen (dopamine agonist and/or L-dopa and/or MAOB inhibitor) for at least 1 month before baseline.
  • Patients expected to remain on stable doses of antiparkinsonian medications for at least the first 6 months of the study and preferably for the 12 months of follow-up.
  • Patients (or caregiver) able to self-administer lixisenatide injection.
  • Patients with health insurance.
  • Patients who signed the written informed consent form.

You may not qualify if:

  • Patients suffering from other parkinsonian syndromes other than PD.
  • Patients expected not to be able to remain on stable doses of symptomatic antiparkinsonian medications for at least 6-month.
  • Patients with a Body Mass Index \< 18.5
  • Patients suffering from type 1 or type 2 diabetes.
  • Malnutrition as assessed clinically by the investigator or any sub-investigator and by Mini Nutritional Assessment Short Form (MNA-SF) score \<12 (the judgement of the investigator prevails over questionnaire scores).
  • Weight change of more than 5 kg in body weight during the last 3 months prior to screening.
  • Known history of drug or alcohol abuse within 6 months prior to the time of screening.
  • Patients with hyperthyroidism or uncontrolled hypothyroidism. Note: Patients diagnosed with hypothyroidism need to be on a stable thyroid replacement therapy for at least 6 weeks.
  • Patients with severe depression according to DSM criteria.
  • Patients with cognitive impairment (MoCA score \<26).
  • Severe gastrointestinal disease (e.g. gastroparesis).
  • Patients previously exposed to a GLP-1 agonist.
  • Patients with severely impaired renal function (estimated creatinine clearance \<30ml/min).
  • Patients with a medical history of active liver disease (other than non-alcoholic hepatic steatosis), including chronic active hepatitis B or C (assessed by medical history), primary biliary cirrhosis, or ongoing symptomatic gallbladder disease.
  • Patients with any clinically significant ECG abnormality.
  • +14 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (20)

University Hospital of Amiens

Amiens, France

Location

University Hospital of Besancon

Besançon, France

Location

University Hospital of Bordeaux

Bordeaux, France

Location

University Hospital of Caen

Caen, France

Location

University Hospital of Clermont-Ferrand

Clermont-Ferrand, France

Location

Creteil- Henri Mondor Hospital

Créteil, France

Location

University Hospital of Lille

Lille, France

Location

University Hospital of Limoges

Limoges, France

Location

University Hospital of Lyon

Lyon, France

Location

University Hospital of Marseille

Marseille, France

Location

University Hospital of Montpellier

Montpellier, France

Location

University Hospital of Nancy

Nancy, France

Location

University Hospital of Nantes

Nantes, France

Location

University Hospital of Nice

Nice, France

Location

Pitié Salpêtrière Hospital

Paris, France

Location

University Hospital of Poitiers

Poitiers, France

Location

University Hospital of Rennes

Rennes, France

Location

University Hospital of Rouen

Rouen, France

Location

University Hospital of Strasbourg

Strasbourg, France

Location

CHU Toulouse

Toulouse, 31000, France

Location

Related Publications (1)

  • Meissner WG, Remy P, Giordana C, Maltete D, Derkinderen P, Houeto JL, Anheim M, Benatru I, Boraud T, Brefel-Courbon C, Carriere N, Catala H, Colin O, Corvol JC, Damier P, Dellapina E, Devos D, Drapier S, Fabbri M, Ferrier V, Foubert-Samier A, Frismand-Kryloff S, Georget A, Germain C, Grimaldi S, Hardy C, Hopes L, Krystkowiak P, Laurens B, Lefaucheur R, Mariani LL, Marques A, Marse C, Ory-Magne F, Rigalleau V, Salhi H, Saubion A, Stott SRW, Thalamas C, Thiriez C, Tir M, Wyse RK, Benard A, Rascol O; LIXIPARK Study Group. Trial of Lixisenatide in Early Parkinson's Disease. N Engl J Med. 2024 Apr 4;390(13):1176-1185. doi: 10.1056/NEJMoa2312323.

MeSH Terms

Conditions

Parkinson Disease

Interventions

lixisenatideAdministration, Intravesical

Condition Hierarchy (Ancestors)

Parkinsonian DisordersBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative Diseases

Intervention Hierarchy (Ancestors)

Administration, TopicalDrug Administration RoutesDrug TherapyTherapeutics

Study Officials

  • Olivier. RASCOL, MD, PHD

    University Hospital, Toulouse

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 13, 2018

First Posted

February 20, 2018

Study Start

June 13, 2018

Primary Completion

April 15, 2021

Study Completion

April 15, 2021

Last Updated

November 28, 2025

Record last verified: 2023-06

Locations