NCT03385564

Brief Summary

The main objectives of this trial are to evaluate the long term efficacy and safety of different doses of BI 655064 versus placebo as add-on therapy to Standard of Care (SOC) during maintenance therapy for lupus nephritis.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
69

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jan 2018

Typical duration for phase_2

Geographic Reach
16 countries

36 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 21, 2017

Completed
7 days until next milestone

First Posted

Study publicly available on registry

December 28, 2017

Completed
12 days until next milestone

Study Start

First participant enrolled

January 9, 2018

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 25, 2021

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 27, 2021

Completed
12 months until next milestone

Results Posted

Study results publicly available

July 13, 2022

Completed
Last Updated

July 13, 2022

Status Verified

June 1, 2022

Enrollment Period

3.4 years

First QC Date

December 21, 2017

Results QC Date

May 12, 2022

Last Update Submit

June 21, 2022

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percentage of Patients With Complete Renal Response (CRR) and Without Any Renal Flares

    The adjusted (model-based, adjusted for race and proteinuria at screening) percentage of patients with complete renal response (CRR) and without any renal flares is reported. A logistic regression model was used including treatment and the covariates: race (Asian versus (vs.) non-Asian) and proteinuria \<3 gram (g)/day vs. ≥3 g/day (or Urine protein (UP)/ Urine creatinine (UC) \<3 vs. UP/UC ≥3) at screening. Complete renal response (CRR) was defined as urine protein (UP) \< 0.5 g/day and either estimated glomerular filtration rate (eGFR) within normal range or decrease in eGFR \< 20% from baseline if eGFR was below normal range (below lower limit of normal \[LLN\], where LLN = 90 mL/min.

    At Week 52

Secondary Outcomes (10)

  • Percentage of Patients With Confirmed Complete Renal Response (CRR) and Without Any Renal Flares

    At Week 52

  • Percentage of Patients With Proteinuria <0.8 Grams (g)/Day (d) and Without Any Renal Flares at Week 52

    At Week 52

  • Percentage of Patients With Complete Renal Response (CRR) at Week 52 and Sustained Steroid Reduction to ≤5 Milligrams (mg)/Day (d) From Week 26 to Week 52

    At Week 52 (Sustained Steroid Reduction to ≤5 mg/d was evaluated from Week 26 to Week 52).

  • Percentage of Patients Experiencing at Least One Renal Flare During 52 Weeks

    At Week 52

  • Time to First Renal Flare Over the Course of 52 Weeks

    Up to 52 weeks.

  • +5 more secondary outcomes

Study Arms (4)

BI 655064 120 mg

EXPERIMENTAL

120 milligrams (mg) BI 655064 were administered as solution for subcutaneous injection in a prefilled syringe once every 2 weeks plus the administration of matching placebo as subcutaneous injection in a prefilled syringe once every 2 weeks (in the alternative weeks without BI 655064 administration) over a treatment period of 52 weeks, followed by a 12-week follow-up period. The patients received 1 injection per week.

Drug: BI 655064

Placebo

PLACEBO COMPARATOR

Matching placebo were administered as solution for subcutaneous injection in a prefilled syringe once every week over a treatment period of 52 weeks, followed by a 12-week follow-up period. The patients received 1 injection per week.

Drug: Placebo

BI 655064 180 mg

EXPERIMENTAL

180 milligrams (mg) BI 655064 were administered as solution for subcutaneous injection in a prefilled syringe once every 2 weeks plus the administration of matching placebo as subcutaneous injection in a prefilled syringe once every 2 weeks (in the alternative weeks without BI 655064 administration) over a treatment period of 52 weeks, followed by a 12-week follow-up period. The patients received 1 injection per week.

Drug: BI 655064

BI 655064 240 mg

EXPERIMENTAL

120 milligrams (mg) BI 655064 were administered as solution for subcutaneous injection in a prefilled syringe once every week (240 mg every 2 weeks) over a treatment period of 52 weeks, followed by a 12-week follow-up period. The patients received 1 injection per week.

Drug: BI 655064

Interventions

subcutaneous injection

BI 655064 120 mgBI 655064 180 mgBI 655064 240 mg

subcutaneous injection

Placebo

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female patients.
  • Women of childbearing potential and men able to father a child must be ready and able to use two reliable methods of birth control simultaneously, one of which must be highly effective. Highly effective birth control per International Conference on Harmonisation (ICH) M3(R2) is a method that result in a low failure rate of less than 1% per year when used consistently and correctly. The reliable methods of birth control must be used before starting Mycophenolate mofetil/Azathioprine (MMF/AZA) and the trial drug; then continue during the trial period; and for at least 50 days after the last dose of MMF/AZA and trial medication. In case a female patient is treated with AZA the contraception shall continue for 90 days after treatment with AZA.A list of contraception methods meeting these criteria is provided in the patient information.
  • Sexually active men must be ready to use condoms during treatment with MMF/AZA and for at least 90 days after cessation of MMF/AZA.
  • Permanent sterilisation methods include hysterectomy, bilateral oophorectomy and bilateral salpingectomy.
  • Tubal ligation is NOT a method of permanent sterilisation.
  • A postmenopausal state is defined as no menses for 12 months without an alternative medical cause.
  • Signed and dated written informed consent in accordance with ICH-GCP and local legislation prior to admission to the trial.
  • For Group 1 patients only:
  • \- Achieved either a Complete renal Response (CRR) or a Partial Renal Response (PRR) or proteinuria ≤ 1g/d (or UP/UC ≤ 1) at the end of 1293.10.

You may not qualify if:

  • Evidence of current or previous clinically significant diseases or medical conditions other than lupus, or findings of the medical examination (including vital signs and ECG) that, in the opinion of the investigator, would compromise the safety of the patient or the quality of the data. This criterion provides an opportunity for the investigator to exclude patients based on clinical judgment, even if other eligibility criteria are satisfied.
  • Significant central nervous system symptoms related to Systemic Lupus Erythematosus (SLE) based on investigators assessment.
  • Clinically important acute or chronic infections including but not limited to HIV, hepatitis B or C.
  • Impaired hepatic function defined as serum Aspartate Aminotransferase/Alanine Aminotransferase (AST/ALT), bilirubin or alkaline phosphatase \> 2 x Upper Limit of Normal (ULN).
  • Estimated glomerular filtration rate (eGFR) \< 30 ml/min/1.73m2 at screening (using CKD-EPI formula).
  • Known hypersensitivity to any constituents of the trial medication; and/or contraindications to Mycophenolate mofetil (MMF) or Azathioprine (AZA) or glucocorticoids.
  • The use of any restricted medications or any drug considered likely to interfere with the safe conduct of the trial.
  • Unable to comply with the protocol in the investigator's opinion.
  • Chronic alcohol or drug abuse or any condition that, in the investigator's opinion, makes them an unreliable trial patient or unlikely to complete the trial.
  • Women who are pregnant, nursing, or who plan to become pregnant while in the trial.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (36)

Integral Rheumatology and Immunology Specialist

Plantation, Florida, 33324, United States

Location

Northwell Health

Great Neck, New York, 11021, United States

Location

Feinstein Institute for Medical Research

Manhasset, New York, 11030, United States

Location

Columbia University Medical Center-New York Presbyterian Hospital

New York, New York, 10032, United States

Location

Princess Alexandra Hospital

Woolloongabba, 4102, Australia

Location

CHU de Quebec-Universite Laval Research Centre

Québec, G1V 4G2, Canada

Location

General University Hospital

Prague, 12808, Czechia

Location

Institute of Rheumathology Prague

Prague, 12850, Czechia

Location

Universitätsmedizin der Johannes Gutenberg-Universität Mainz

Mainz, 55131, Germany

Location

Robert-Bosch-Krankenhaus GmbH

Stuttgart, 70376, Germany

Location

University General Hospital Attikon

Athens, 124 62, Greece

Location

University General Hospital of Heraklion

Heraklion, Crete, 71500, Greece

Location

Prince of Wales Hospital

Hong Kong, 999077, Hong Kong

Location

Queen Mary Hospital

Hong Kong, 999077, Hong Kong

Location

Hokkaido University Hospital

Hokkaido, Sapporo, 060-8648, Japan

Location

Tohoku University Hospital

Miyagi, Sendai, 980-8574, Japan

Location

Okayama University Hospital

Okayama, Okayama, 700-8558, Japan

Location

Juntendo University Hospital

Tokyo, Bunkyo-ku, 113-8431, Japan

Location

Hospital Tengku Ampuan Rahimah

Klang, 41200, Malaysia

Location

Centenario Hospital Miguel Hidalgo

Aguascalientes, 20259, Mexico

Location

Instituto Nacional de Cardiologia Ignacio Chavez

Mexico City, 14080, Mexico

Location

Instituto Nacional de Cs Médicas y Nutrición S Zubiran

Mexico City, 14080, Mexico

Location

Southern Philippines Medical Center

Davao City, 8000, Philippines

Location

Mary Mediatrix Medical Center

Lipa City, Batangas, 4217, Philippines

Location

University Clinical Hospital in Bialystok I

Bialystok, 15-540, Poland

Location

Norbert Barlicki University Clinical Hospital No.1, Lodz

Lodz, 90-153, Poland

Location

NZOZ Centrum Medyczne AESKULAP,Private Prac, Radom

Radom, 26610, Poland

Location

Hospital Curry Cabral, EPE

Lisbon, 1069-166, Portugal

Location

Centro Hospitalar Universitário de Lisboa Norte, EPE - Hospital Santa Maria

Lisbon, 1649-028, Portugal

Location

Ajou University Hospital

Suwon, 16499, South Korea

Location

Siriraj Hospital

Bangkok, 10170, Thailand

Location

King Chulalongkorn Memorial Hospital

Bangkok, 10330, Thailand

Location

Chiangmai University

Chiang Mai, 50200, Thailand

Location

Pramongkutklao Hospital

Rajathevee, 10400, Thailand

Location

Addenbrooke's Hospital

Cambridge, CB2 0QQ, United Kingdom

Location

Guy's Hospital

London, SE1 9RT, United Kingdom

Location

Related Links

MeSH Terms

Conditions

Lupus Nephritis

Interventions

BI 655064

Condition Hierarchy (Ancestors)

GlomerulonephritisNephritisKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesLupus Erythematosus, SystemicConnective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Boehringer Ingelheim Call Center
Organization
Boehringer Ingelheim

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 21, 2017

First Posted

December 28, 2017

Study Start

January 9, 2018

Primary Completion

May 25, 2021

Study Completion

July 27, 2021

Last Updated

July 13, 2022

Results First Posted

July 13, 2022

Record last verified: 2022-06

Data Sharing

IPD Sharing
Will share

After the study is completed and the primary manuscript is accepted for publishing, researchers can use this following link https://www.mystudywindow.com/msw/datasharing to request access to the clinical study documents regarding this study, and upon a signed "Document Sharing Agreement". Also, Researchers can use the following link https://www.mystudywindow.com/msw/datasharing to find information in order to request access to the clinical study data, for this and other listed studies, after the submission of a research proposal and according to the terms outlined in the website. The data shared are the raw clinical study data sets.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
After all regulatory activities are completed in the US and EU for the product and indication, and after the primary manuscript has been accepted for publication.
Access Criteria
For study documents - upon signing of a 'Document Sharing Agreement'. For study data - 1. after the submission and approval of the research proposal (checks will be performed by both the independent review panel and the sponsor, including checking that the planned analysis does not compete with sponsor's publication plan); 2. and upon signing of a 'Data Sharing Agreement'.
More information

Locations