NCT03362190

Brief Summary

To assess the safety of intravitreal Zimura™ (complement factor C5 inhibitor) administered in combination with Lucentis® 0.5 mg in treatment naïve subjects with neovascular age related macular degeneration (NVAMD)

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
64

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Oct 2017

Shorter than P25 for phase_2

Geographic Reach
3 countries

28 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 11, 2017

Completed
19 days until next milestone

First Submitted

Initial submission to the registry

October 30, 2017

Completed
1 month until next milestone

First Posted

Study publicly available on registry

December 5, 2017

Completed
11 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 18, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 18, 2018

Completed
3.3 years until next milestone

Results Posted

Study results publicly available

February 2, 2022

Completed
Last Updated

June 10, 2025

Status Verified

May 1, 2025

Enrollment Period

1 year

First QC Date

October 30, 2017

Results QC Date

October 14, 2021

Last Update Submit

May 25, 2025

Conditions

Keywords

Zimura (previous name)ARC1905LucentisranibizumabWet AMDavacincaptad pegolcomplement factor C5 inhibitor

Outcome Measures

Primary Outcomes (2)

  • Systemic Adverse Events

    Number of Participants with systemic treatment-emergent Adverse Events (with calculated percentage)

    6 months

  • Ophthalmic Adverse Events

    Number of participants with ophthalmic Adverse Events (with calculated percentage)

    6 months

Other Outcomes (3)

  • Change From Baseline - ECG

    6 months

  • Mean Change From Baseline - Study Eye ETDRS Visual Acuity

    6 months

  • Mean Change From Baseline - Vital Signs

    6 months

Study Arms (4)

Cohort 1

EXPERIMENTAL

Avacincaptad Pegol dosage 1 + Lucentis 0.5 mg

Drug: Avacincaptad PegolDrug: Lucentis

Cohort 2

EXPERIMENTAL

Avacincaptad Pegol dosage 2 + Lucentis 0.5 mg

Drug: Avacincaptad PegolDrug: Lucentis

Cohort 3

EXPERIMENTAL

Avacincaptad Pegol dosage 3 + Lucentis 0.5 mg

Drug: Avacincaptad PegolDrug: Lucentis

Cohort 4

EXPERIMENTAL

Avacincaptad Pegol dosage 4 + Lucentis 0.5 mg

Drug: Avacincaptad PegolDrug: Lucentis

Interventions

Avacincaptad Pegol in combination with Lucentis

Also known as: Zimura (previous name), IZERVAY, ARC1905
Cohort 1Cohort 2Cohort 3Cohort 4

Avacincaptad Pegol in combination with Lucentis

Also known as: ranibizumab
Cohort 1Cohort 2Cohort 3Cohort 4

Eligibility Criteria

Age50 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Active subfoveal NVAMD

You may not qualify if:

  • History or evidence of severe cardiac disease
  • Any major surgical procedure within one month of trial entry
  • Subjects with a clinically significant laboratory value
  • Any treatment with an investigational agent in the past 60 days for any condition
  • Women who are pregnant or nursing
  • Known serious allergies to the fluorescein dye used in angiography, povidone iodine, to the components of the ranibizumab formulation, or to the components of the Zimura formulation
  • Any prior treatment for AMD other than oral supplements of vitamins and minerals

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (28)

Retinal Research Institute

Phoenix, Arizona, 85053, United States

Location

Retina Centers PC

Tucson, Arizona, 85704, United States

Location

Retina Associates SW, PC

Tucson, Arizona, 85710, United States

Location

Retina-Vitreous Associates Medical Group

Beverly Hills, California, 90211, United States

Location

Retina Consultants of Orange County

Fullerton, California, 92835, United States

Location

Retina Consultants of Southern California

Redlands, California, 92374, United States

Location

Retinal Consultants Medical Group

Sacramento, California, 95841, United States

Location

Orange County Retina Medical Group

Santa Ana, California, 92705, United States

Location

Colorado Retina Associates

Golden, Colorado, 80214, United States

Location

Florida Eye Clinic

Altamonte Springs, Florida, 32701, United States

Location

Florida Eye Associates

Melbourne, Florida, 32901, United States

Location

Illinois Eye Center

Peoria, Illinois, 61615, United States

Location

Vitreo Retinal Consultants & Surgeons

Wichita, Kansas, 67214, United States

Location

Ophthalmic Consultants of Boston

Boston, Massachusetts, 02114, United States

Location

VitreoRetinal Surgery

Minneapolis, Minnesota, 55435, United States

Location

Retina Consultants of Nevada

Henderson, Nevada, 89052, United States

Location

Sierra Eye Associates

Reno, Nevada, 89502, United States

Location

Retina Vitreous Surgeons of CNY, PC

Syracuse, New York, 13224, United States

Location

Retina Northwest PC

Portland, Oregon, 97221, United States

Location

Mid Atlantic Retina

Philadelphia, Pennsylvania, 19107, United States

Location

Charleston Neuroscience Institute

Ladson, South Carolina, 29456, United States

Location

Retina Research Institute of Texas

Abilene, Texas, 79606, United States

Location

Strategic Clinical Research Group

Willow Park, Texas, 76087, United States

Location

Peterfy Sandor utcai Korhaz-Rendelointezet es Baleseti Kozpont

Budapest, 1076, Hungary

Location

Budapest Retina Associates

Budapest, 1133, Hungary

Location

Szegedi Tudomanyegyetem Szent-Gyorgyi Albert Klinikai Kozpont Szemeszeti Klinika

Szeged, 6702, Hungary

Location

Pauls Stradins Clinical University Hospital, Clinic of Ophthalmology

Riga, LV-1002, Latvia

Location

Dr. Solomatin's eye rehabilitation and vision correction centre

Riga, LV-1050, Latvia

Location

Related Links

MeSH Terms

Interventions

Ranibizumab

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Results Point of Contact

Title
Hersh Patel, OD / Zimura Medical Director
Organization
IVERIC bio, Inc

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 30, 2017

First Posted

December 5, 2017

Study Start

October 11, 2017

Primary Completion

October 18, 2018

Study Completion

October 18, 2018

Last Updated

June 10, 2025

Results First Posted

February 2, 2022

Record last verified: 2025-05

Data Sharing

IPD Sharing
Will not share

Access to anonymized individual participant level data will not be provided for this trial. Further details on Astellas' data sharing policy can be found at https://www.clinicaltrials.astellas.com/transparency/.

Locations