NCT03340727

Brief Summary

The objective of this study is to evaluate the effect of continuing treatment with caffeine citrate in the hospital and at home in moderately preterm infants with resolved apnea of prematurity on days of hospitalization after randomization.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
827

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Feb 2019

Typical duration for phase_3

Geographic Reach
1 country

16 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 3, 2017

Completed
10 days until next milestone

First Posted

Study publicly available on registry

November 13, 2017

Completed
1.3 years until next milestone

Study Start

First participant enrolled

February 27, 2019

Completed
3.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 23, 2023

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 20, 2023

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

June 28, 2024

Completed
Last Updated

July 31, 2024

Status Verified

July 1, 2024

Enrollment Period

3.9 years

First QC Date

November 3, 2017

Results QC Date

May 7, 2024

Last Update Submit

July 30, 2024

Conditions

Keywords

Moderate preterm infantCaffeine citrate

Outcome Measures

Primary Outcomes (2)

  • Number of Days Between Randomization and Hospital Discharge

    The number of days between randomization and hospital discharge. This outcome is censored at 48 weeks PMA and at time of transfer or death.

    Randomization through hospital discharge, censored at time of transfer, death, or 48 wks PMA

  • Number of Sick Visits Related to Apneic or Apparent Life-threatening Events Within First 4 Weeks Post-discharge

    Number of sick visits related to apneic or apparent life-threatening events within first 4 weeks post-discharge MEASTYPE=SEC

    Discharge through 4 weeks post-discharge

Secondary Outcomes (20)

  • The Number of Days to Physiologic Maturity After Randomization

    Randomization through hospital discharge, censored at time of transfer, death, or 48 wks PMA

  • The Number of Days to When Out of Incubator for 48 Hours: When Maintained Stable Temp for 48 Hrs

    Randomization through hospital discharge, censored at time of transfer, death, or 48 wks PMA

  • The Number of Days to Apnea/ Bradycardia Free for 5 Consecutive Days

    Randomization through hospital discharge, censored at time of transfer, death, or 48 wks PMA

  • The Number of Days to Oral Feeds >140 ml/kg/Day or Growing on Less Than 140 ml/kg/Day for at Least 48 Hours

    Randomization through hospital discharge, censored at time of transfer, death, or 48 wks PMA

  • Post-menstrual Age at Discharge

    Randomization through hospital discharge, censored at time of transfer, death, or 48 wks PMA

  • +15 more secondary outcomes

Study Arms (2)

Caffeine Citrate

EXPERIMENTAL

Caffeine citrate at 10 mg/kg/dose (5 mg/kg caffeine base) daily, in hospital. Infants will continue at home on the same dose of caffeine citrate for the first 28 days after hospital discharge.

Drug: Caffeine Citrate

Placebo

PLACEBO COMPARATOR

Placebo contains all of the excipients except for the active ingredient, caffeine citrate, (a volume equivalent to 10 mg/kg of caffeine citrate) and given daily. Infants will be continued at home on the same dose of placebo for the first 28 days after hospital discharge.

Drug: Placebo

Interventions

The study intervention is caffeine citrate given once daily at 10 mg/kg/day. It is given orally, before hospital discharge and 28 days after discharge.

Caffeine Citrate

The study intervention is placebo given once daily at a volume equivalent to 10 mg/kg of caffeine citrate. It is given orally, before hospital discharge and 28 days after discharge.

Placebo

Eligibility Criteria

Age29 Weeks - 33 Weeks
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Inborn and outborn infants of 29 0/7 to 33 6/7 weeks gestational age at birth
  • admitted to hospitals of the NICHD NRN who, are at time of enrollment:
  • ≤35 6/7 weeks post-menstrual age at the time of randomization
  • Receiving caffeine with plan to discontinue treatment or just discontinued caffeine treatment
  • Receiving feeds at a volume of ≥120 ml/kg/day by oral and/or tube feeding
  • Ability to start study medication within 72 hours after stopping caffeine

You may not qualify if:

  • On respiratory therapy (oxygen more than room air equivalent for high altitude sites, nasal cannula, continuous positive pressure ventilation, and/or mechanical ventilation)
  • Infants who would otherwise be discharged home on apnea monitor due to underlying disease or family history, including history of a sibling with sudden infant death syndrome
  • Parental request for apnea monitor
  • Congenital heart disease other than atrial septal defect, ventricular septal defect, or patent ductus arteriosus
  • Neuromuscular conditions affecting respiration
  • Major congenital malformation and/or genetic disorder
  • Plans to transfer to a non-NRN site before discharge
  • Unable to obtain parental or guardian consent

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (16)

University of Alabama at Birmingham

Birmingham, Alabama, 35233, United States

Location

Stanford University

Palo Alto, California, 94304, United States

Location

Emory University

Atlanta, Georgia, 30303, United States

Location

University of Iowa

Iowa City, Iowa, 52242, United States

Location

University of New Mexico

Albuquerque, New Mexico, 87131, United States

Location

University of Rochester

Rochester, New York, 14642, United States

Location

RTI International

Durham, North Carolina, 27705, United States

Location

Duke University

Durham, North Carolina, 27710, United States

Location

Cincinnati Children's Medical Center

Cincinnati, Ohio, 45267, United States

Location

Case Western Reserve University, Rainbow Babies and Children's Hospital

Cleveland, Ohio, 44106, United States

Location

Research Institute at Nationwide Children's Hospital

Columbus, Ohio, 43205, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Brown University, Women & Infants Hospital of Rhode Island

Providence, Rhode Island, 02905, United States

Location

University of Texas Southwestern Medical Center at Dallas

Dallas, Texas, 75235, United States

Location

University of Texas Health Science Center at Houston

Houston, Texas, 77030, United States

Location

University of Utah

Salt Lake City, Utah, 84108, United States

Location

Related Publications (1)

  • Carlo WA, Eichenwald EC, Carper BA, Bell EF, Keszler M, Patel RM, Sanchez PJ, Goldberg RN, D'Angio CT, Van Meurs KP, Hibbs AM, Ambalavanan N, Cosby SS, Newman NS, Vohr BR, Walsh MC, Das A, Ohls RK, Fuller J, Rysavy MA, Ghavam S, Brion LP, Puopolo KM, Moore R, Baack ML, Colaizy TT, Baserga M, Osman AF, Merhar SL, Poindexter BB, DeMauro SB, Kumar V, Cotten CM; Eunice Kennedy Shriver National Institute of Child Health and Human Development Neonatal Research Network. Extended Caffeine for Apnea in Moderately Preterm Infants: The MoCHA Randomized Clinical Trial. JAMA. 2025 Jun 24;333(24):2154-2163. doi: 10.1001/jama.2025.5791.

MeSH Terms

Conditions

Apnea

Interventions

caffeine citrate

Condition Hierarchy (Ancestors)

Respiration DisordersRespiratory Tract DiseasesSigns and Symptoms, RespiratorySigns and SymptomsPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Abhik Das
Organization
RTI International

Study Officials

  • Waldemar Carlo, MD

    University of Alabama at Birmingham

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Sample size for this trial will be flexible: the trial will be stopped for efficacy or futility based on pre-determined statistical thresholds or based on study drug availability.
Sponsor Type
NETWORK
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 3, 2017

First Posted

November 13, 2017

Study Start

February 27, 2019

Primary Completion

January 23, 2023

Study Completion

March 20, 2023

Last Updated

July 31, 2024

Results First Posted

June 28, 2024

Record last verified: 2024-07

Data Sharing

IPD Sharing
Will share

Per NIH Data Sharing Plan

Locations