NCT03295760

Brief Summary

The main purpose of this study is the comparison of frequency of vomiting episodes (number of episodes per year) observed during the year after the begin of Q10 coenzyme treatment to frequency observed during the year before the begin of this treatment in children with cyclic vomiting syndrome. Secondary purposes are the evaluation of life quality of parents and children, of treatment safety and its economic cost compared to other recommended treatments.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
15

participants targeted

Target at below P25 for all trials

Timeline
Completed

Started Dec 2016

Shorter than P25 for all trials

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 1, 2016

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 31, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 31, 2017

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

September 21, 2017

Completed
7 days until next milestone

First Posted

Study publicly available on registry

September 28, 2017

Completed
Last Updated

September 28, 2017

Status Verified

September 1, 2017

Enrollment Period

8 months

First QC Date

September 21, 2017

Last Update Submit

September 25, 2017

Conditions

Outcome Measures

Primary Outcomes (2)

  • Frequency of vomiting episodes

    measured by number of episodes per year

    from date of inclusion (start of Q10 coenzyme treatment) up to 1 year

  • Frequency of vomiting episodes

    measured by number of episodes per year

    from 1 year before date of inclusion until date of inclusion (start of Q10 coenzyme treatment)

Secondary Outcomes (5)

  • Intensity of vomiting episodes

    from 1 year before date of inclusion until date of inclusion (start of Q10 coenzyme treatment)

  • Intensity of vomiting episodes

    from date of inclusion (start of Q10 coenzyme treatment) up to 1 year

  • Number of child hospitalizations

    from 1 year before date of inclusion until date of inclusion (start of Q10 coenzyme treatment)

  • Number of child hospitalizations

    from date of inclusion (start of Q10 coenzyme treatment) up to 1 year

  • Cost of Q10 coenzyme treatment and other recommended treatments for cyclic vomiting syndrome

    baseline

Study Arms (1)

Children with cyclic vomiting syndrome

Children followed at Children's Hospital of Nancy treated with Q10 coenzyme for cyclic vomiting syndrome

Drug: Q10 Coenzyme

Interventions

Children with cyclic vomiting syndrome

Eligibility Criteria

AgeUp to 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)
Sampling MethodNon-Probability Sample
Study Population

Children followed at Children's Hospital of Nancy treated with Q10 coenzyme for cyclic vomiting syndrome

You may qualify if:

  • Cyclic vomiting syndrome as defined by Rome IV criteria
  • Treated with Q10 coenzyme treatment for cyclic vomiting syndrome
  • Q10 coenzyme treatment started between January 2000 and July 2006

You may not qualify if:

  • \- Refusal of processing of personal data reported in patient medical files

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Children's Hospital - CHRU de Nancy

Vandœuvre-lès-Nancy, France

Location

MeSH Terms

Conditions

Familial cyclic vomiting syndrome

Interventions

Ubiquinone

Intervention Hierarchy (Ancestors)

BenzoquinonesQuinonesOrganic ChemicalsCoenzymesEnzymes and Coenzymes

Study Design

Study Type
observational
Observational Model
CASE CROSSOVER
Time Perspective
RETROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 21, 2017

First Posted

September 28, 2017

Study Start

December 1, 2016

Primary Completion

July 31, 2017

Study Completion

July 31, 2017

Last Updated

September 28, 2017

Record last verified: 2017-09

Data Sharing

IPD Sharing
Will not share

Locations