NCT03287869

Brief Summary

This study evaluated the safety and evaluate the safety and tolerability of open-label brexpiprazole (2 - 4 mg/day, with a starting dose of 2 mg/day) for the treatment of adult subjects with bipolar I disorder. All participants received a starting dose of brexpiprazole.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
381

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Oct 2017

Geographic Reach
6 countries

73 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 24, 2017

Completed
26 days until next milestone

First Posted

Study publicly available on registry

September 19, 2017

Completed
1 month until next milestone

Study Start

First participant enrolled

October 24, 2017

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 31, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 31, 2019

Completed
1 year until next milestone

Results Posted

Study results publicly available

August 17, 2020

Completed
Last Updated

August 17, 2020

Status Verified

August 1, 2020

Enrollment Period

1.8 years

First QC Date

August 24, 2017

Results QC Date

July 29, 2020

Last Update Submit

August 14, 2020

Conditions

Keywords

BipolarManiaBrexpiprazole

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With at Least One Treatment Emergent Adverse Event (TEAE) by Severity

    An adverse event (AE) was defined as any untoward medical occurrence in a clinical investigation participant administered a drug; it does not necessarily have to have a causal relationship with this treatment. An AE can therefore be any unfavorable and unintended sign (eg, a clinically significant abnormal laboratory finding), symptom, or disease temporally associated with the use of a drug, whether or not it is considered related to the drug. A TEAE is defined as an adverse event with an onset that occurs after receiving study drug. AEs severity were graded on a 3-point scale as: 1 = mild; discomfort noticed, but no disruption to daily activity, 2 = moderate; discomfort sufficient to reduce or affect normal daily activity, and 3 = severe; inability to work or perform normal daily activity.

    From Day 1 (after dosing) through 29 weeks (26 weeks treatment, 3 weeks safety follow-up)

Study Arms (1)

Brexpiprazole

EXPERIMENTAL

Brexpiprazole was administered in participants orally with flexible dosing from 2 mg/day from Days 1 to 3 regardless of treatment assignment in the previous double-blind trial, followed by titration to 3 mg/day on Day 4. Participants may have been titrated (or re-titrated) to a higher dose of brexpiprazole, up to a maximum of 4 mg/day, based on treatment response and at the investigator's discretion anytime at Day 7 or thereafter. Participants who were unable to tolerate their current dose could have been titrated down to a minimum of 2 mg/day any time after Day 4.

Drug: Brexpiprazole

Interventions

Brexpiprazole tablets

Also known as: OPC-34712
Brexpiprazole

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants remaining in hospital at the Day 21 visit of trial 331-201-00080 or 331-201-00081 were permitted to enroll in the 331-201-00083 trial at the week 3 visit of the double-blind trial if they were planned to be discharged from the hospital before the week 1 visit of trial 331-201-0083. Participants not discharged by the week 1 visit of trial 331-201-0083 were withdrawn.
  • Participants who, in the opinion of the investigator, could potentially benefit from administration of oral brexpiprazole for the treatment of bipolar I disorder and who completed 3 weeks of post-randomization treatment in Trial 331-201-00080 \& Trial 331-201-00081.

You may not qualify if:

  • Participants with a major protocol violation during the course of their participation in the double-blind phase 3 trials (331-201-00080 or 331-201-00081).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (73)

Woodland International Research Group

Little Rock, Arkansas, 72211, United States

Location

Woodland Research Northwest, LLC

Rogers, Arkansas, 72758, United States

Location

Citrials Inc.

Bellflower, California, 90706, United States

Location

Radiant Research

Cerritos, California, 90703, United States

Location

ProScience Research Group

Culver City, California, 90230, United States

Location

Collaborative Neuroscience Network, LLC

Garden Grove, California, 92845, United States

Location

Behavioral Research Specialists, LLC

Glendale, California, 91206, United States

Location

Apostle Clinical Trials

Long Beach, California, 90813, United States

Location

Pacific Research Partners, LLC

Oakland, California, 94607, United States

Location

NRC Research Institute

Orange, California, 92868, United States

Location

Asclepes Research Centers, PC

Panorama City, California, 91402, United States

Location

CI Trials

Riverside, California, 92705, United States

Location

CNRI-San Diego

San Diego, California, 92102, United States

Location

Artemis Institute for Clinical Research

San Diego, California, 92103, United States

Location

Sharp Mesa Vista Hospital

San Diego, California, 92123, United States

Location

CI Trials

Santa Ana, California, 92705, United States

Location

Collaborative Neuroscience Network, LLC

Torrance, California, 90502, United States

Location

Shreenath Clinical Service

Yorba Linda, California, 92886, United States

Location

Optimus U Corp

Coral Gables, Florida, 33134, United States

Location

Segal Trials

Fort Lauderdale, Florida, 33308, United States

Location

Galiz Research

Hialeah, Florida, 33016, United States

Location

Research Centers of America, LLC

Hollywood, Florida, 33024, United States

Location

Florida Behavioral Medicine

Largo, Florida, 33770, United States

Location

University of South Florida Board of Trustees

Tampa, Florida, 33613, United States

Location

iResearch Atlanta, LLC

Decatur, Georgia, 30030, United States

Location

Alexian Brothers Center for Psychiatric Research

Hoffman Estates, Illinois, 60169, United States

Location

NeuroPsychiatric Research

Winfield, Illinois, 60190, United States

Location

Louisiana Clinical Research

Shreveport, Louisiana, 71101, United States

Location

CBH Health

Gaithersburg, Maryland, 20877, United States

Location

St. Charles Psychiatric Associates

Saint Charles, Missouri, 63304, United States

Location

Arch Clinical Trials, LLC

St Louis, Missouri, 63118, United States

Location

St. Louis Clinical Trials

St Louis, Missouri, 63141, United States

Location

Hassman Research Institute, LLC

Berlin, New Jersey, 08009, United States

Location

Clinical Trials of America-NC, LLC

Hickory, North Carolina, 28601, United States

Location

Richard H Weisler, MD PA Associates

Raleigh, North Carolina, 27609, United States

Location

SP Research PLLC

Oklahoma City, Oklahoma, 73112, United States

Location

Cutting Edge Research Group

Oklahoma City, Oklahoma, 73116, United States

Location

Community Clinical Research, Inc.

Austin, Texas, 78754, United States

Location

InSite Clinical Research

DeSoto, Texas, 75115, United States

Location

North Texas Clinical Trials

Fort Worth, Texas, 76104, United States

Location

Pillar Clinical Research LLC

Garland, Texas, 75042, United States

Location

Pillar Clinical Research, LLC

Richardson, Texas, 75080, United States

Location

Core Clinical Research

Everett, Washington, 98201, United States

Location

Mid Columbia Research

Richland, Washington, 99352, United States

Location

Mental Health Center Prof. Dr. Ivan Temkov - Burgas EOOD, Department for Treatment of Emergency Psychiatric Condition

Burgas, 8000, Bulgaria

Location

State Psychiatry Hospital - Kardzhali,Third Male Department, First Female Department

Kardzhali, 6600, Bulgaria

Location

State Psychiatry Hospital Sv. Ivan Rilski, First Male department, First Female Department

Novi Iskar, 1282, Bulgaria

Location

University Multiprofile Hospital for Active Treatment Sveti Georgi EAD, Clinic of Psychiatry

Plovdiv, 4002, Bulgaria

Location

"Mental Health Centre-Ruse" EOOD, Male department for persons with severe mental disorders, Female department for persons with severe mental disorders

Rousse, 7003, Bulgaria

Location

University Multiprofile Hospital for Active Treatment -Alexandrovska EAD, Clinic of Psychiatry, First Department of Psychiatry

Sofia, 1431, Bulgaria

Location

Multiprofile Hospital for Active Treatment - Targovishte AD, Department of Psychiatry

Targovishte, 7700, Bulgaria

Location

Mental Health Center - Veliko Tarnovo EOOD, Department of Psychiatry for Active Treatment of Persons with Severe Mental Disorders

Veliko Tarnovo, 5000, Bulgaria

Location

Mental Health Center - Vratsa EOOD, Department of Psychiatry

Vratsa, 3000, Bulgaria

Location

CHC Rijeka-Clinic for Psychiatrics

Rijeka, 51000, Croatia

Location

Poliklinika Neuron /Polyclinic Neuron

Zagreb, 10000, Croatia

Location

Indywidualna Specjalistyczna Praktyka Lekarska Wieslaw Jerzy Cubala

Gdansk, 80-438, Poland

Location

NZOZ Prywatna Klinika Psychiatryczna Inventiva

Tuszyn, 95-080, Poland

Location

CHC Dr Dragisa Misovic

Belgrade, 11000, Serbia

Location

Clinic for Psychiatric Disorders, Dr Laza Lazarevic

Belgrade, 11000, Serbia

Location

Clinic for Psychiatry

Belgrade, 11000, Serbia

Location

Specialized Hospital for Psychiatry Diseases Kovin

Kovin, 26220, Serbia

Location

Clinical Center Kragujevac, Clinic of Psychiatry

Kragujevac, 34000, Serbia

Location

Klinika za psihijariju, Klinicki Centar Vojvodine

Novi Sad, 21000, Serbia

Location

Regional Clinical Hospital n.a I.I. Mechnicov

Dnipro, 49005, Ukraine

Location

SI of Neurology Psychiatry and Narcology NAMS

Kharkiv, 61068, Ukraine

Location

Kherson Regional Psychiatric Hospital

Kherson, 73488, Ukraine

Location

Kyiv Regional Medical Incorporation Psychiatry

Kyiv, 04080, Ukraine

Location

CI of LOR Lviv Regional Clinical Psychiatric Hospital, Department #25

Lviv, 79021, Ukraine

Location

Communal Institution of Lviv Regional Council "Lviv Regional Clinical Psychiatric Hospital", department #20

Lviv, 79021, Ukraine

Location

Odesa Regional Psychiatric Hospital 2

Odesa, 67513, Ukraine

Location

Maltsev Regional Clinical Psychiatric Hospital

Poltava, 36013, Ukraine

Location

Ternopil Regional Municipal Clinical Psychoneurological Hospital

Ternopil, 46027, Ukraine

Location

O.I. Yushenko Vinnitsa Regional Clinic

Vinnitsa, 21018, Ukraine

Location

MeSH Terms

Conditions

Mania

Interventions

brexpiprazole

Condition Hierarchy (Ancestors)

Neurobehavioral ManifestationsNeurologic ManifestationsNervous System DiseasesSigns and SymptomsPathological Conditions, Signs and Symptoms

Limitations and Caveats

As predefined in the protocol, there were no primary or secondary efficacy endpoints in this trial.

Results Point of Contact

Title
Global Clinical Development
Organization
Otsuka Pharmaceutical Development & Commercialization, Inc.

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Group composed of eligible rollover participants who completed one of the double-blind, phase 3 efficacy trials (331-201-00080 (NCT03259555) or 331-201-00081 (NCT03257865)).
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 24, 2017

First Posted

September 19, 2017

Study Start

October 24, 2017

Primary Completion

July 31, 2019

Study Completion

July 31, 2019

Last Updated

August 17, 2020

Results First Posted

August 17, 2020

Record last verified: 2020-08

Data Sharing

IPD Sharing
Will share

Anonymized Individual participant data (IPD) that underlie the results of this study will be shared with researchers to achieve aims pre-specified in a methodologically sound research proposal. Small studies with less than 25 participants are excluded from data sharing.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
Data will be available after marketing approval in global markets, or beginning 1-3 years following article publication. There is no end date to the availability of the data.
Access Criteria
Otsuka will share data on an Otsuka-owned remotely accessible data sharing platform with Python and R analytical software. Research requests should be directed to clinicaltransparency@Otsuka-us.com
More information

Locations