NCT03257865

Brief Summary

To demonstrate the efficacy of brexpiprazole for the acute treatment of manic episodes, with or without mixed features, in participants with a diagnosis of bipolar I disorder.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
333

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Sep 2017

Shorter than P25 for phase_3

Geographic Reach
3 countries

38 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 4, 2017

Completed
18 days until next milestone

First Posted

Study publicly available on registry

August 22, 2017

Completed
28 days until next milestone

Study Start

First participant enrolled

September 19, 2017

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 22, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 22, 2019

Completed
12 months until next milestone

Results Posted

Study results publicly available

January 2, 2020

Completed
Last Updated

February 11, 2020

Status Verified

February 1, 2020

Enrollment Period

1.3 years

First QC Date

August 4, 2017

Results QC Date

December 13, 2019

Last Update Submit

February 3, 2020

Conditions

Keywords

BrexpiprazoleBipolarManic episode

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline In Young-Mania Rating Scale (YMRS) Score At Week 3

    The YMRS was utilized to assess a participant's level of manic symptoms. It consists of 11 items: 1) elevated mood, 2) increased motor activity-energy, 3) sexual interest, 4) sleep, 5) irritability, 6) speech (rate and amount), 7) language-thought disorder, 8) content, 9) disruptive-aggressive behavior, 10) appearance, and 11) insight. Seven items are rated on a 0- to 4-scale, while four items (Items 5, 6, 8, and 9) are rated on a 0- to 8-scale with 0, 2, 4, 6, and 8 being the possible scores (twice the weight of the other items). For all items, 0 is the "best" rating and the highest score (4 or 8) is the 'worst' rating. The YMRS total score is the sum of ratings for all 11 items; therefore, possible total scores range from 0 to 60, with higher scores signifying more severe manic symptoms. Comparison between treatment groups was carried out using mixed-effect model repeated measure (MRMM).

    Baseline, Week 3

Secondary Outcomes (1)

  • Change From Baseline In Clinical Global Impression-Bipolar (CGI-BP) Severity Score In Mania At Week 3

    Baseline, Week 3

Study Arms (2)

Brexpiprazole

EXPERIMENTAL

Participants received a starting dose of 2 milligrams (mg)/day brexpiprazole from Days 1 to 3, followed by titration to 3 mg/day on Day 4. Participants may have been titrated (or re-titrated) to a higher dose of brexpiprazole, up to a maximum of 4 mg/day, based on treatment response and at the investigator's discretion anytime at Day 7 or thereafter. Participants who were unable to tolerate their current dose could have been titrated down to a minimum of 2 mg/day any time after Day 4.

Drug: Brexpiprazole

Placebo

PLACEBO COMPARATOR

Matching placebo was administered in the same way as brexpiprazole to maintain the blind

Drug: Placebo

Interventions

Brexpiprazole was administered orally with flexible dosing from 2 to 4 mg/day; titrated to a maximum of 4 mg/day for 3 weeks.

Brexpiprazole

Administered orally daily for 3 weeks.

Placebo

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female participants, ages 18 to 65 years, inclusive, at the time of informed consent.
  • Participants willing to discontinue all prohibited medications to meet protocol-required washouts prior to and during the trial period.
  • Participants with a Diagnostic \& Statistical Manual on Mental Disorders, 5th Edition (DSM-5) diagnosis of bipolar I disorder displaying an acute manic episode with or without mixed features requiring hospitalization. Diagnosis confirmed by the MINI International Neuropsychiatric Interview (MINI) and a history of at least one previous manic episode with or without mixed features with manic symptoms of sufficient severity to require one of the following interventions: hospitalization or treatment with a mood stabilizer, or treatment with an antipsychotic agent. "Require" was defined as an intervention that occurred rather than one that was recommended.
  • Young-mania rating scale (YMRS) score of ≥ 24 at screening and baseline

You may not qualify if:

  • Sexually active male or women of childbearing potential (WOCBP) who did not agree to practice 2 different methods of birth control or remain abstinent during the trial and for 30 days after the last dose of investigational medicinal product (IMP).
  • Females who were breastfeeding and/or who had a positive pregnancy test result prior to receiving trial medication.
  • Participants considered unresponsive to clozapine or who were only responsive to clozapine.
  • Participants with a history of DSM-5 diagnosis other than bipolar I disorder, including schizophrenia, schizoaffective disorder, major depressive disorder, attention-deficit/hyperactivity disorder, delirium, dementia, amnestic, or other cognitive disorders. Also, participants with borderline, paranoid, histrionic, schizotypal, schizoid, or antisocial personality disorder. All other current diagnoses must have been discussed with the medical monitor.
  • Participants whose current manic episode had lasted for more than 4 weeks overall, or who had required hospitalization \> 21 days for the current acute episode at the time of the screening visit, excluding hospitalization for psychosocial reasons.
  • Participant with manic symptoms better accounted for by another general medical condition or direct physiological effect of substance (for example, medications).
  • Participants who have had electroconvulsive treatment within the past 2 months.
  • Participants with a positive drug screen for cocaine or other illicit drugs.
  • Abnormal laboratory test results, vital signs or electrocardiogram findings, unless, based on investigator's judgment, the findings are not medically significant and would not impact the safety of the participant or the interpretation of the trial results.
  • Rapid cyclers with more than 6 episodes in the previous year.
  • Participants with hypothyroidism or hyperthyroidism (unless condition has been stabilized with medications for at least the past 90 days) or an abnormal result for free thyroxine at screening.
  • Participants with uncontrolled hypertension or symptomatic hypotension or orthostatic hypotension.
  • Participants with epilepsy or history of seizures.
  • Participants who participated in a clinical trial within the last 60 days or who participated in more than 2 clinical trials within the past year.
  • Use of psychotropic medications (other than benzodiazepines) within 7 days of the baseline YMRS.
  • +2 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (38)

Atria Clinical Research

Little Rock, Arkansas, 72209, United States

Location

Woodland International Research Group, LLC

Little Rock, Arkansas, 72211, United States

Location

CiTrials

Bellflower, California, 90706, United States

Location

CNS Research Science Inc.

Cerritos, California, 90703, United States

Location

Apostle Clinical Trials

Long Beach, California, 90813, United States

Location

CNRI-San Diego

San Diego, California, 92102, United States

Location

Artemis Institute for Clinical Research

San Diego, California, 92103, United States

Location

CiTrials

Santa Ana, California, 92705, United States

Location

Collaborative Neuroscience Network, LLC

Torrance, California, 90502, United States

Location

Shreenath Clinical Service

Yorba Linda, California, 92886, United States

Location

Galiz Research

Hialeah, Florida, 33016, United States

Location

Research Centers of America LLC

Hollywood, Florida, 33024, United States

Location

Optimus U Corporation

Miami, Florida, 33125, United States

Location

South Florida Research Phase I-IV

Miami Springs, Florida, 33166, United States

Location

Meridien Research

Orlando, Florida, 32801, United States

Location

iResearch Atlanta, LLC

Decatur, Georgia, 30030, United States

Location

Uptown Research Institute LLC

Chicago, Illinois, 60640, United States

Location

Neuropsychiatric Research & Associates, LTD

Winfield, Illinois, 60190, United States

Location

Louisiana Clinical Research

Shreveport, Louisiana, 71101, United States

Location

Arch Clinical Trials, LLC

St Louis, Missouri, 63118, United States

Location

St Louis Clinical Trials LLC

St Louis, Missouri, 63141, United States

Location

Hassman Research Institute

Berlin, New Jersey, 08009, United States

Location

CNS Research Science, Inc.

Jamaica, New York, 11432, United States

Location

New Hope Clinical Research

Charlotte, North Carolina, 28211, United States

Location

University of Cincinnati Department of Psychiatry and Behavorial Science

Cincinnati, Ohio, 45219, United States

Location

InSite Clinical Research LLC

DeSoto, Texas, 75115, United States

Location

Pillar Clinical Research, LLC

Richardson, Texas, 75080, United States

Location

Clinical Hospital Centre Rijeka

Rijeka, 51000, Croatia

Location

Communal Institution "Dnipropetrovsk Regional Clinical Hospital named after I.I. Mechnikov

Dnipro, 49005, Ukraine

Location

SI ""Institute of Neurology, Psychiatry and Narcology of National Academy of Medical Sciences of Ukraine

Kharkiv, 61068, Ukraine

Location

Communal Establishment "Kherson Regional Psychiatric Hospital" of Kherson Regional Council

Kherson, 73488, Ukraine

Location

Kyiv Regional Medical Incorporation "Psychiatry", Center for Novel Treatment and Rehabilitation of Psychotic disorders

Kyiv, 04080, Ukraine

Location

Communal Institution of Lviv Regional Council "Lviv Regional Clinical Psychiatric Hospital", Department #20

Lviv, 79021, Ukraine

Location

Communal Institution of Lviv Regional Council "Lviv Regional Clinical Psychiatric Hospital", Department #25

Lviv, 79021, Ukraine

Location

Communal Establishment "Odesa Regional Psychiatric Hospital #2

Oleksandrivka, 67513, Ukraine

Location

O.F. Maltsev Poltava Regional Psychiatric Hospital

Poltava, 36013, Ukraine

Location

Ternopil Regional Municipal Clinical Psychoneurolgical Hospital

Ternopil, 46027, Ukraine

Location

Communal Establishment "Acad. O.I. Iushchenko Vinnytsia Regional Psychoneurologic Hospital"

Vinnytsia, 21005, Ukraine

Location

MeSH Terms

Conditions

Mania

Interventions

brexpiprazole

Condition Hierarchy (Ancestors)

Neurobehavioral ManifestationsNeurologic ManifestationsNervous System DiseasesSigns and SymptomsPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Global Clinical Development
Organization
Otsuka Pharmaceutical Development & Commercialization, Inc.

Study Officials

  • Matthew Leoni, M.D.

    Otsuka Pharmaceutical Development & Commercialization, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Participants received a dose of brexpiprazole or placebo for a maximum of 21 days and were evaluated throughout the duration of the study.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 4, 2017

First Posted

August 22, 2017

Study Start

September 19, 2017

Primary Completion

January 22, 2019

Study Completion

January 22, 2019

Last Updated

February 11, 2020

Results First Posted

January 2, 2020

Record last verified: 2020-02

Data Sharing

IPD Sharing
Will share

Anonymized Individual participant data (IPD) that underlie the results of this study will be shared with researchers to achieve aims pre-specified in a methodologically sound research proposal. Small studies with less than 25 participants are excluded from data sharing.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
Data will be available after marketing approval in global markets, or beginning 1-3 years following article publication. There is no end date to the availability of the data.
Access Criteria
Otsuka will share data on an Otsuka-owned remotely accessible data sharing platform with Python and R analytical software. Research requests should be directed to clinicaltransparency@Otsuka-us.com

Locations