NCT03257644

Brief Summary

The purpose of this study is to evaluate the safety, tolerability and the pharmacokinetics (PK) of topical ruxolitinib cream applied to pediatric subjects (age ≥ 2 to 17 years) with atopic dermatitis (AD).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
70

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Sep 2017

Typical duration for phase_1

Geographic Reach
1 country

23 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 18, 2017

Completed
4 days until next milestone

First Posted

Study publicly available on registry

August 22, 2017

Completed
1 month until next milestone

Study Start

First participant enrolled

September 21, 2017

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 7, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 7, 2020

Completed
Last Updated

November 10, 2020

Status Verified

November 1, 2020

Enrollment Period

3 years

First QC Date

August 18, 2017

Last Update Submit

November 9, 2020

Conditions

Keywords

Atopic dermatitisJanus kinase (JAK) inhibitorpediatricinflammation

Outcome Measures

Primary Outcomes (1)

  • Participants with treatment-emergent adverse events (TEAEs)

    A TEAE is any adverse event (AE) either reported for the first time or worsening of a pre-existing event after first application of study drug.

    Screening through 30-37 days after end of treatment, up to approximately 12 weeks.

Secondary Outcomes (2)

  • Plasma concentrations of ruxolitinib for Cohorts 1 and 2

    Day 1, Day 15, and Day 29

  • Plasma concentrations of ruxolitinib for Cohorts 3, 4, 5 and 6

    Day 1, Day 10, and Day 29

Study Arms (6)

Cohort 1

EXPERIMENTAL

Ruxolitinib phosphate cream 0.5%.

Drug: Ruxolitinib phosphate cream

Cohort 2

EXPERIMENTAL

Ruxolitinib phosphate cream 1.5%.

Drug: Ruxolitinib phosphate cream

Cohort 3

EXPERIMENTAL

Ruxolitinib phosphate cream 0.75%.

Drug: Ruxolitinib phosphate cream

Cohort 4

EXPERIMENTAL

Ruxolitinib phosphate cream 1.5%.

Drug: Ruxolitinib phosphate cream

Cohort 5

EXPERIMENTAL

Ruxolitinib phosphate cream 0.75%.

Drug: Ruxolitinib phosphate cream

Cohort 6

EXPERIMENTAL

Ruxolitinib phosphate cream 1.5%.

Drug: Ruxolitinib phosphate cream

Interventions

Ruxolitinib phosphate cream at the protocol-defined dose strength based on cohort assignment.

Also known as: INCB018424
Cohort 1Cohort 2Cohort 3Cohort 4Cohort 5Cohort 6

Eligibility Criteria

Age2 Years - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Pediatric subjects aged ≥ 2 to 17 years, inclusive
  • Subjects diagnosed with AD as defined by the Hanifin and Rajka criteria.
  • Subjects with active inflammation associated with AD.
  • Subjects with an Investigator's Global Assessment (IGA) score of at least 2 at screening and baseline.
  • Subjects with body surface area (BSA) of AD involvement of 8% to 20% at screening and baseline.
  • Subjects who agree to discontinue all agents used to treat AD from screening through the final follow-up visit.
  • Subjects of childbearing potential must agree to take appropriate precautions to avoid pregnancy or fathering a child for the duration of study participation.
  • Written informed consent of the parent(s) or legal guardian and a verbal or written assent from the subject when possible.

You may not qualify if:

  • Unstable course of AD (spontaneously improving or rapidly deteriorating) as determined by the investigator over the previous 4 weeks before baseline.
  • Use of topical treatments for AD (other than bland moisturizer such as Eucerin® cream) within 2 weeks of baseline.
  • Concurrent conditions and history of other diseases:
  • Presence of AD lesions only on the hands or feet without a history of involvement of other classical areas of involvement such as the face or the flexural folds.
  • Other types of eczema.
  • Any other concomitant skin disorder (eg, generalized erythroderma such as Netherton Syndrome, or psoriasis), pigmentation, or extensive scarring that in the opinion of the investigator may interfere with the evaluation of AD lesions or compromise subject safety.
  • Immunocompromised (eg, lymphoma, acquired immunodeficiency syndrome, Wiskott-Aldrich syndrome) or have a history of malignant disease within 5 years before the baseline visit.
  • Chronic or acute infection requiring treatment with systemic antibiotics, antivirals, antiparasitics, antiprotozoals, or antifungals within 4 weeks before the baseline visit.
  • Active acute bacterial, fungal, or viral (eg, herpes simplex, herpes zoster, chicken pox) skin infection within 1 week before the baseline visit.
  • Chronic asthma requiring more than 880 μg of inhaled budesonide or equivalent high dose of other inhaled corticosteroids.
  • Subjects with cytopenias at screening per protocol-defined criteria.
  • Use of the following medications:
  • Systemic immunosuppressive or immunomodulating drugs (eg, oral or injectable corticosteroids, methotrexate, cyclosporine, mycophenolate mofetil, azathioprine) within 4 weeks or 5 half-lives of baseline (whichever is longer).
  • Subjects taking potent systemic cytochrome P450 3A4 inhibitors or fluconazole within 2 weeks or 5 half lives, whichever is longer, before the baseline visit (topical agents with limited systemic availability are permitted).
  • Subjects who have previously received JAK inhibitors, systemic or topical (eg, ruxolitinib, tofacitinib, baricitinib, filgotinib, lestaurtinib, pacritinib).
  • +3 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (23)

Cahaba Dermatology

Hoover, Alabama, 35244, United States

Location

Desert Sky Dermatology

Gilbert, Arizona, 85295, United States

Location

Applied Research Center of Arkansas

Little Rock, Arkansas, 72212, United States

Location

Orange County Research Center

Anaheim, California, 92801, United States

Location

Children'S Hospital Los Angeles Specialt

Los Angeles, California, 90027, United States

Location

Rady Children'S Hospital - San Diego

San Diego, California, 92123, United States

Location

National Jewish Health

Denver, Colorado, 80206, United States

Location

Olympian Clinical Research

Largo, Florida, 33770, United States

Location

Acevedo Clinical Research

Miami, Florida, 33142, United States

Location

Floridian Research Institute Llc

Miami, Florida, 33145, United States

Location

Rm Medical Research Inc

Miami, Florida, 33174, United States

Location

Olympian Clinical Research

Tampa, Florida, 33609, United States

Location

Iact Health

Columbus, Georgia, 31904, United States

Location

Advanced Clinical Research

Boise, Idaho, 83713, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

The Indiana Clincal Trials Center

Plainfield, Indiana, 46168, United States

Location

David Fivenson, Md, Pllc

Ann Arbor, Michigan, 48103, United States

Location

Wake Research Associates Llc

Raleigh, North Carolina, 27612, United States

Location

Ohio Pediatric Research Association

Dayton, Ohio, 45414, United States

Location

Cyn3Rgy Research - Clinedge - Ppds

Gresham, Oregon, 97030, United States

Location

Penn State Hershey Medical Center

Hershey, Pennsylvania, 17033, United States

Location

Progressive Clinical Research

San Antonio, Texas, 78213, United States

Location

Texas Dermatology and Laser Specialists

San Antonio, Texas, 78218, United States

Location

Related Publications (1)

  • Leung DYM, Paller AS, Zaenglein AL, Tom WL, Ong PY, Venturanza ME, Kuligowski ME, Li Q, Gong X, Lee MS. Safety, pharmacokinetics, and efficacy of ruxolitinib cream in children and adolescents with atopic dermatitis. Ann Allergy Asthma Immunol. 2023 Apr;130(4):500-507.e3. doi: 10.1016/j.anai.2022.12.033. Epub 2022 Dec 28.

MeSH Terms

Conditions

Dermatitis, AtopicInflammation

Interventions

ruxolitinib

Condition Hierarchy (Ancestors)

Skin Diseases, GeneticGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesDermatitisSkin DiseasesSkin and Connective Tissue DiseasesSkin Diseases, EczematousHypersensitivity, ImmediateHypersensitivityImmune System DiseasesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • Michael Kuligowski, MD, PhD, MBA

    Incyte Corporation

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 18, 2017

First Posted

August 22, 2017

Study Start

September 21, 2017

Primary Completion

October 7, 2020

Study Completion

October 7, 2020

Last Updated

November 10, 2020

Record last verified: 2020-11

Data Sharing

IPD Sharing
Will not share

Locations