NCT03252548

Brief Summary

This study is a prospective cohort study of children diagnosed with primary immunodeficiency disease (PID). The aim is to investigate the clinical characteristics and prognosis of PID in Chinese children.

Trial Health

35
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
400

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Jan 2018

Longer than P75 for all trials

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 15, 2017

Completed
2 days until next milestone

First Posted

Study publicly available on registry

August 17, 2017

Completed
5 months until next milestone

Study Start

First participant enrolled

January 1, 2018

Completed
4.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2022

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2022

Completed
Last Updated

January 3, 2018

Status Verified

May 1, 2017

Enrollment Period

4.6 years

First QC Date

August 15, 2017

Last Update Submit

January 1, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • Frequencies of severe infection of children with PID

    Times of severe infection attack will be recorded every year from baseline to 60 months, assessed by questionnaire

    60 months

Secondary Outcomes (3)

  • Life quality of children with PID

    60 months

  • Complications of children with PID

    60 months

  • Long-term changes on lung function of children with PID

    60 months

Eligibility Criteria

Age1 Day - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)
Sampling MethodProbability Sample
Study Population

Children who was confirmed diagnosis as PID at the certain hospitals

You may qualify if:

  • Age: from neonates to 18 years old
  • Fulfilling the one of the followings:
  • Severe infection after vaccination (BCG, polio arthritis pill)
  • Chronic/recurrent ear infection, sinus infections and respiratory tract infection
  • Recurrent, deep skin or deep-seated infections
  • Boys with early period and refractory thrombocytopenia
  • Infants with obviously decreased absolute number of lymphocytes
  • Severe allergy with infection
  • Infant diabetes with severe diarrhea
  • Boys with severe Epstein-Barr virus infection
  • Infants with hepatosplenomegaly and generalized lymphadenopathy
  • Infantile hemophagocytic syndrome
  • Failure of an infant to gain weight or grow normally
  • Persistent thrush in mouth or fungalinfection on skin
  • Family history of primary immunodeficiency
  • +3 more criteria

You may not qualify if:

  • Subject will be excluded if she or he would not enroll into this study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

MeSH Terms

Conditions

Primary Immunodeficiency Diseases

Condition Hierarchy (Ancestors)

Genetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesImmunologic Deficiency SyndromesImmune System Diseases

Study Officials

  • kunling shen, MD,PhD

    Beijing Children's Hospital, Capital Medical University, China

    STUDY DIRECTOR
  • jianxin he, MD,PhD

    Beijing Children's Hospital, Capital Medical University, China

    PRINCIPAL INVESTIGATOR

Central Study Contacts

baoping xu, MD,PhD

CONTACT

Study Design

Study Type
observational
Observational Model
CASE ONLY
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Chief of China National Clinical Research Center for Respiratory Diseases

Study Record Dates

First Submitted

August 15, 2017

First Posted

August 17, 2017

Study Start

January 1, 2018

Primary Completion

August 1, 2022

Study Completion

August 1, 2022

Last Updated

January 3, 2018

Record last verified: 2017-05

Data Sharing

IPD Sharing
Will not share