NCT03240991

Brief Summary

This study aims to describe quality of life in hereditary or acquired non drug-related bradykinin-mediated angioedema patients, using validated questionnaires

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
45

participants targeted

Target at P25-P50 for all trials

Timeline
Completed

Started Jul 2016

Shorter than P25 for all trials

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 11, 2016

Completed
5 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2016

Completed
8 months until next milestone

First Submitted

Initial submission to the registry

July 27, 2017

Completed
11 days until next milestone

First Posted

Study publicly available on registry

August 7, 2017

Completed
Last Updated

April 17, 2018

Status Verified

April 1, 2018

Enrollment Period

5 months

First QC Date

July 27, 2017

Last Update Submit

April 13, 2018

Conditions

Keywords

bradykinin-mediated angiodemaquality of life

Outcome Measures

Primary Outcomes (2)

  • Dermatology Life Quality Index (DLQI)

    Description of Quality of Life (QoL) using DLQI

    6 months

  • Angioedema Quality of Life (AE-QoL) Questionnaire

    Description of QoL using AE-QOL questionnnaire

    6 months

Study Arms (1)

Quality of life questionnaires

Data will be collected retrospectively and prospectively.

Other: Quality of life

Interventions

Dermatology Life Quality Index, Angioedema Quality of Life Questionnaire, Angioedema Activity Score

Quality of life questionnaires

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Hereditary or Acquired non drug-induced bradykinin-mediated angioedema patients

You may qualify if:

  • Clinically documented angioedema due to C1 inhibitor deficiency, hereditary (type I et II) or acquired
  • Clinically documented angioedema with normal C1 inhibitor activity (hereditary type III)

You may not qualify if:

  • Acquired angioedema with normal C1 inhibitor activity (former "drug-induced")
  • Minor subjects
  • Vulnerable subjects (under guardianship/curatorship/tutorship)
  • Pregnant women

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

CHU Besançon

Besançon, 25000, France

Location

MeSH Terms

Conditions

Angioedema

Interventions

Quality of Life

Condition Hierarchy (Ancestors)

Vascular DiseasesCardiovascular DiseasesUrticariaSkin Diseases, VascularSkin DiseasesSkin and Connective Tissue DiseasesHypersensitivity, ImmediateHypersensitivityImmune System Diseases

Intervention Hierarchy (Ancestors)

Health StatusDemographyEpidemiologic MeasurementsPublic HealthEnvironment and Public Health

Study Design

Study Type
observational
Observational Model
CASE ONLY
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 27, 2017

First Posted

August 7, 2017

Study Start

July 11, 2016

Primary Completion

December 1, 2016

Study Completion

December 1, 2016

Last Updated

April 17, 2018

Record last verified: 2018-04

Locations