NCT03202992

Brief Summary

This study evaluates the use of ABI-1968, a topical cream, in the treatment of anal precancerous lesions in adults with and without human immunodeficiency virus (HIV) infection.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
57

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Aug 2017

Geographic Reach
2 countries

6 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 24, 2017

Completed
5 days until next milestone

First Posted

Study publicly available on registry

June 29, 2017

Completed
1 month until next milestone

Study Start

First participant enrolled

August 11, 2017

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 4, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 4, 2019

Completed
Last Updated

February 7, 2019

Status Verified

February 1, 2019

Enrollment Period

1.5 years

First QC Date

June 24, 2017

Last Update Submit

February 5, 2019

Conditions

Outcome Measures

Primary Outcomes (1)

  • Maximum Tolerated Dose (MTD) of ABI-1968 for the treatment of aHSIL

    Number of participants with Adverse Events related to treatment

    SAD portion is 29 days/MAD portion is 84 days

Secondary Outcomes (2)

  • Systemic exposure to ABI-1968 Topical Cream following topical application to the anal canal.

    SAD portion is 29 days/MAD portion is 84 days

  • Histopathology of areas with biopsy-proven disease following single and multiple doses of ABI-1968 Topical Cream.

    SAD portion is 29 days/MAD portion is 84 days

Study Arms (10)

Dose 1 -Single Ascending Dose (SAD)

EXPERIMENTAL

SAD Dose Level 1 of ABI-1968 topical cream applied on Day 1 of the study

Drug: ABI-1968

Dose 2 -Single Ascending Dose (SAD)

EXPERIMENTAL

SAD Dose Level 2 of ABI-1968 topical cream applied on Day 1 of the study

Drug: ABI-1968

Dose 3 -Single Ascending Dose(SAD)

EXPERIMENTAL

SAD Dose Level 3 of ABI-1968 topical cream applied on Day 1 of the study

Drug: ABI-1968

Dose 4 -Single Ascending Dose(SAD)

EXPERIMENTAL

SAD Dose Level 4 of ABI-1968 topical cream applied on Day 1 of the study

Drug: ABI-1968

Dose 5 -Single Ascending Dose(SAD)

EXPERIMENTAL

SAD Dose Level 5 of ABI-1968 topical cream applied on Day 1 of the study

Drug: ABI-1968

Dose 1 - Multiple Ascending Dose(MAD)

EXPERIMENTAL

MAD Dose Level 1 of ABI-1968 topical cream applied at Day 1, Day 8, Day 15, Day 22 and Day 29

Drug: ABI-1968

Dose 2 -Multiple Ascending Dose(MAD)

EXPERIMENTAL

MAD Dose Level 2 of ABI-1968 topical cream applied at Day 1, Day 8, Day 15, Day 22 and Day 29

Drug: ABI-1968

Dose 3 -Multiple Ascending Dose(MAD)

EXPERIMENTAL

MAD Dose Level 3 of ABI-1968 topical cream applied at Day 1, Day 8, Day 15, Day 22 and Day 29

Drug: ABI-1968

Multiple Ascending Dose (MAD) Cohort Expansion

EXPERIMENTAL

MAD Cohort Expansion of ABI-1968 applied at Day 1, Day 8, Day 15, Day 22 and Day 29

Drug: ABI-1968

Dose 4-Multiple Ascending Dose(MAD)

EXPERIMENTAL

MAD Dose Level 3 of ABI-1968 topical cream applied at Day 1, Day 8, Day 15, Day 22 and Day 29

Drug: ABI-1968

Interventions

Topical cream applied at Day 1 for the SAD portion and applied at Day 1, Day 8, Day 15, Day 22 and Day 29 for the MAD portion

Dose 1 - Multiple Ascending Dose(MAD)Dose 1 -Single Ascending Dose (SAD)Dose 2 -Multiple Ascending Dose(MAD)Dose 2 -Single Ascending Dose (SAD)Dose 3 -Multiple Ascending Dose(MAD)Dose 3 -Single Ascending Dose(SAD)Dose 4 -Single Ascending Dose(SAD)Dose 4-Multiple Ascending Dose(MAD)Dose 5 -Single Ascending Dose(SAD)Multiple Ascending Dose (MAD) Cohort Expansion

Eligibility Criteria

Age27 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Female or male subjects, at least 27 years old.
  • Confirmed diagnosis of intra-anal HSIL at least 3 months prior to screening and confirmed by histopathology (with p16 positive staining)
  • Intra-anal HSIL are visible and evaluable by HRA at the time of screening, and no lesion(s) is suspicious for invasive cancer.
  • For HIV-positive subjects, CD4 count must be at least 200/mm3 with undetectable (\<50 copies/mL) viral load within the 3 months prior to enrollment. Subjects must be on a stable regimen of antiretroviral drugs for the 3 months prior to enrollment.

You may not qualify if:

  • Women who are pregnant, plan to become pregnant in the next 3 months, or lactating females.
  • Received topical treatment or ablative procedures for aHSIL in the 6 months prior to enrolment.
  • History of cancer, including anal cancer (with the exception of basal cell or squamous cell carcinoma of the skin), or currently undergoing treatment for any skin cancer.
  • History of genital herpes with \> 3 outbreaks per year.
  • Plan to have excision or ablation of the lesion(s) within 3 months of enrolment.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (6)

Research Center

San Francisco, California, 94115, United States

Location

Research Center

Orlando, Florida, 32803, United States

Location

Research Center

Chicago, Illinois, 60614, United States

Location

Research Center

New York, New York, 10011, United States

Location

Research Center

Winston-Salem, North Carolina, 27157, United States

Location

Research Center

Sydney, Darlinghurst, 2010, Australia

Location

MeSH Terms

Conditions

Squamous Intraepithelial LesionsPapillomavirus InfectionsHIV InfectionsAnus Neoplasms

Condition Hierarchy (Ancestors)

Morphological and Microscopic FindingsPathological Conditions, Signs and SymptomsSexually Transmitted Diseases, ViralSexually Transmitted DiseasesCommunicable DiseasesInfectionsDNA Virus InfectionsVirus DiseasesTumor Virus InfectionsGenital DiseasesUrogenital DiseasesDisease AttributesPathologic ProcessesBlood-Borne InfectionsLentivirus InfectionsRetroviridae InfectionsRNA Virus InfectionsImmunologic Deficiency SyndromesImmune System DiseasesRectal NeoplasmsColorectal NeoplasmsIntestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesIntestinal DiseasesAnus DiseasesRectal Diseases

Study Officials

  • Clinical Operations

    Choosing to participate in a study is an important personal decision. Talk with your doctor and family members or friends about deciding to join a study. To learn more about this study, you or your doctor may use the contacts provided below.

    STUDY CHAIR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Model Details: The study will be conducted in 2 Phases: Part A, up to 5 cohorts of 3 subjects each will receive a single dose of ABI-1968 Topical Cream. In Part B, three cohorts (3 subjects per cohort) will receive multiple doses in 3 ascending dose strengths of ABI-1968 Topical Cream. After completing the ascending dose multiple-dosing cohorts, a multiple-dosing Cohort Expansion group of 30 subjects will be initiated.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 24, 2017

First Posted

June 29, 2017

Study Start

August 11, 2017

Primary Completion

February 4, 2019

Study Completion

February 4, 2019

Last Updated

February 7, 2019

Record last verified: 2019-02

Data Sharing

IPD Sharing
Will not share

Locations