NCT03189160

Brief Summary

This study aims to explore the optimal dose of pegylated recombinant human growth hormone (PEG-rhGH) injection to treat children of Turner syndrome (TS), preliminarily evaluate its safety and efficacy and provide scientific and reliable evidence for the medication dosage in Phase 3 clinical trial.

Trial Health

55
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
180

participants targeted

Target at P75+ for phase_2

Geographic Reach
1 country

9 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 1, 2016

Completed
1.3 years until next milestone

First Submitted

Initial submission to the registry

June 13, 2017

Completed
3 days until next milestone

First Posted

Study publicly available on registry

June 16, 2017

Completed
9 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2018

Completed
Last Updated

December 12, 2017

Status Verified

June 1, 2017

Enrollment Period

2 years

First QC Date

June 13, 2017

Last Update Submit

December 10, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change of height standard deviation score before and after treatment (ΔHT SDS)

    The change of height standard deviation score of chronological age before and after treatment

    52 weeks

Secondary Outcomes (3)

  • Height Velocity

    52 weeks

  • ΔBA/ΔCA

    52 weeks

  • IGF-1(Insulin-like growth factor 1) SDS

    52 weeks

Study Arms (3)

PEG-rhGH low dose

EXPERIMENTAL

PEG-rhGH Injection (27IU/4.5mg/0.5ml/bottle) 0.1 mg/kg/w by subcutaneous injection for 52 weeks.

Biological: PEG-rhGH low doseBiological: PEG-rhGH high doseOther: Non-treatment control group

PEG-rhGH high dose

EXPERIMENTAL

PEG-rhGH Injection (27IU/4.5mg/0.5ml/bottle) 0.2 mg/kg/w by subcutaneous injection for 52 weeks.

Biological: PEG-rhGH low doseBiological: PEG-rhGH high doseOther: Non-treatment control group

Non-treatment control group

NO INTERVENTION

Interventions

PEG-rhGH Injection 0.1 mg/kg/w by subcutaneous injection for 52 weeks.

Also known as: Polyethylene Glycol Recombinant Human Somatropin Injection
PEG-rhGH high dosePEG-rhGH low dose

PEG-rhGH Injection 0.2 mg/kg/w by subcutaneous injection for 52 weeks.

Also known as: Polyethylene Glycol Recombinant Human Somatropin Injection
PEG-rhGH high dosePEG-rhGH low dose
PEG-rhGH high dosePEG-rhGH low dose

Eligibility Criteria

Age2 Years - 18 Years
Sexfemale
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Female
  • Bone age \<12 years
  • Karyotype: 45, X; 45, X / 46, XXqi; 45, X / 46, XXr; 45, X / 46, XX; 46, XXqi; 46, XXpi; 45, X / 47, XXX; 46, XXp-; 45, X / 46, XXp-; 46, XXq-; 45X / 46, XXq-; 45, X / 46, XX / 47, XXX, etc. (count 50 or more cells);
  • Facial appearance and abnormalities: Patients with at least one of the following signs, which include but are not limited to facial pigmented nevus, short neck, webbed neck, low posterior hairline, low-set ears, micrognathia, high-voulted arch, shield-like chest, cubitus valgus, genu valgum, short 4th and 5th metacarpals, nail dysplasia, scoliosis, ptosis and strabismus, cardiovascular abnormalities (such as aortic stenosis, bicuspid aortic valve and hypertension), reproductive abnormalities (such as primary gonadal dysfunction), renal abnormalities, thyroid hypofunction, middle ear lesion, etc.
  • Short stature: height below -2.5SD of the mean height of the same age and gender.
  • Pre-pubertal (Tanner Stage I ) patients
  • No history of growth hormone treatment
  • The subject and his/her guardian sign the informed consent (if the subject is incapable to sign the informed consent, his/her legal guardian shall sign the name of the subject instead)

You may not qualify if:

  • Subjects with abnormal liver and kidney functions (ALT \> upper limit of normal value; Cr \> upper limit of normal value)
  • Subjects positive for anti-HBc, HbsAg or HbeAg in Hepatitis B virus tests;
  • Subjects with highly allergic constitution or allergy to proteins or investigational product or its excipient
  • Subjects with systemic chronic disease and immune deficiency
  • Patients diagnosed with tumor
  • For patients whose tumor markers exceeding normal range in combination with other information, considering as potential high risks of tumor, they may be excluded from the treatment.
  • Patients with mental disease
  • Subjects with impaired glucose regulation (IGR) (including impaired fasting glucose (IFG) and/or impaired glucose tolerance (IGT) ) or diabetes
  • Subjects who took part in other clinical trials within 3 months
  • Subjects who received medicines which may interfere GH secretion or GH function, or other hormones within 3 months (such as sex steroids, glucocorticoids, etc.)
  • Other conditions which are unsuitable for this study in the opinion of the investigator.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (9)

The First Affiliated Hospital with Nanjing Medical University

Nanjing, Jiangsu, China

RECRUITING

Affiliated Hospital of Jiangnan University

Wuxi, Jiangsu, China

RECRUITING

Jiangxi Provincial Children's Hospital

Nanchang, Jiangxi, China

RECRUITING

First Hospital of Jilin University

Changchun, Jilin, China

RECRUITING

The Children's Hospital of Zhejiang University School of Medicine

Hangzhou, Zhejiang, China

RECRUITING

Beijing Children's Hospital,Capital Medical University

Beijing, China

RECRUITING

Children's Hospital of Fudan University

Shanghai, China

RECRUITING

Shanghai Children's Hospital

Shanghai, China

RECRUITING

Xinhua Hospital of Shanghai Jiao Tong University School of Medicine

Shanghai, China

RECRUITING

MeSH Terms

Conditions

Turner Syndrome

Interventions

polyethylene glycol-recombinant human growth hormone

Condition Hierarchy (Ancestors)

Gonadal DysgenesisDisorders of Sex DevelopmentUrogenital AbnormalitiesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesSex Chromosome Disorders of Sex DevelopmentMale Urogenital DiseasesHeart Defects, CongenitalCardiovascular AbnormalitiesCardiovascular DiseasesHeart DiseasesCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesSex Chromosome DisordersChromosome DisordersGenetic Diseases, InbornGonadal DisordersEndocrine System Diseases

Study Officials

  • Chunxiu Gong, PhD

    Beijing Children's Hospital

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 13, 2017

First Posted

June 16, 2017

Study Start

March 1, 2016

Primary Completion

March 1, 2018

Last Updated

December 12, 2017

Record last verified: 2017-06

Locations