NCT03175705

Brief Summary

This study enrolls patients who have relapsed/advanced hepatocellular carcinoma (HCC, BCLC stage C). The HCC tumor relapsed or metastasized through the body after standard treatment or the patients cannot receive standard treatment under current conditions. This research study uses specific HCC antigens CD8+ T cells, a new experimental treatment. The purpose of this study is to evaluate the safety and tolerance as well as the potential clinical efficacy of an adoptive transfer of CD8+ T cells, sorted with human leukocyte antigen (HLA)-peptide multimers and specific for Glypican (GPC)-3 /New York Esophageal Squamous-1 (NY-ESO-1) /alpha-fetoprotein (AFP) antigens and cultured in vitro, to patients suffering from relapsed/advanced hepatocellular carcinoma (HCC).

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
18

participants targeted

Target at P25-P50 for phase_1 hepatocellular-carcinoma

Timeline
Completed

Started May 2017

Shorter than P25 for phase_1 hepatocellular-carcinoma

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2017

Completed
23 days until next milestone

First Submitted

Initial submission to the registry

May 24, 2017

Completed
12 days until next milestone

First Posted

Study publicly available on registry

June 5, 2017

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 30, 2018

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 30, 2019

Completed
Last Updated

January 18, 2018

Status Verified

January 1, 2018

Enrollment Period

1.7 years

First QC Date

May 24, 2017

Last Update Submit

January 17, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • Incidence of Treatment-Emergent Adverse Events [Safety]

    Defined as signs/symptoms, laboratory toxicities, and clinical events that are possibly, likely, or definitely related to study treatment Adverse events assessed according to NCI-CTCAE v4.0 criteria 2.

    4 weeks

Secondary Outcomes (1)

  • Biological activity of infused T cells

    4 weeks

Other Outcomes (2)

  • Progress Free Survival (PFS)

    12 weeks or up to death

  • Disease Control Rate (DCR)

    12 weeks or up to death

Study Arms (1)

Autologous T cell therapy+Tegafur+Interleukin-2 (IL-2)

EXPERIMENTAL

Autologous in vitro expanded HCC antigens-specific CD8+ T lymphocytes in conjunction with IL-2 and along with lymphodepleting chemotherapy (Tegafur) will be administered to patients with relapsed/advanced HCC.

Biological: HCC antigens-specific CD8+ T lymphocytesDrug: IL-2Drug: Tegafur

Interventions

Three different dosing schedules will be evaluated. Three patients will be evaluated on each dosing schedule. The following dose levels will be evaluated: Loading Dose 1: 3x10\^7/m2 Loading Dose 2: 6x10\^7/m2 Loading Dose 3: 9x10\^7/m2 The doses are calculated according to the actual number of GPC3/NY-ESO-1/AFP specific cytotoxic lymphocytes (CTLs)

Autologous T cell therapy+Tegafur+Interleukin-2 (IL-2)
IL-2DRUG

IL-2 will be given at a dose of 25000 IU/kg/day for 5-14 days.

Also known as: Human recombinated Interleukin-2
Autologous T cell therapy+Tegafur+Interleukin-2 (IL-2)

Tegafur will be given at a dose of 40\~60 mg bis in die (BID) 2 weeks.

Also known as: Gimeracil and Oteracil potassium Capsules
Autologous T cell therapy+Tegafur+Interleukin-2 (IL-2)

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age 18-80 years
  • Patients with relapsed/advanced HCC (BCLC, stage C) proved by histopathology or proved by CT or MRI imaging system, proven GPC3/NY-ESO-1/AFP(+), relapsed after previous therapy and no effective therapies known at this time.
  • Life expectancy of ≥ 12 weeks.
  • WBC\>3.5×10\^9/L, LYMPH\> 0.8×10\^9/L, Hb\>85g/L, PLT\>50×10\^9/L, Cre\<1.5×the upper limit of normal value.
  • Able to understand and sign the informed consent.

You may not qualify if:

  • Any uncontrolled systematic disease: hypertension, heart disease, and et al.;
  • Portal vein tumor thrombus, central nervous system tumor metastasis, or combined with other tumors;
  • Receiving radiochemotherapy, local therapy, or targeting drugs within 4 weeks prior to this treatment;
  • Unstable immune systematic diseases or Infectious diseases;
  • Combined with AIDS or syphilis;
  • Patients with history of stem cell or organ transplantation;
  • Patients with allergic history to related drugs and immunotherapy;
  • Patients with complications associated with liver diseases: moderate or severe pleural effusion, pericardial effusion, ascites, or gastrointestinal hemorrhage;
  • Pregnant or lactating subjects;
  • Unsuitable subjects considered by clinicians.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Beijing Youan Hospital,Capital Medical University

Beijing, Beijing Municipality, 100069, China

RECRUITING

MeSH Terms

Conditions

Carcinoma, Hepatocellular

Interventions

Interleukin-2Tegafurgimeracilpotassium oxonate

Condition Hierarchy (Ancestors)

AdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsLiver NeoplasmsDigestive System NeoplasmsNeoplasms by SiteDigestive System DiseasesLiver Diseases

Intervention Hierarchy (Ancestors)

InterleukinsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsLymphokinesProteinsBiological FactorsFluorouracilUracilPyrimidinonesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Central Study Contacts

Jun Lu, Director

CONTACT

Xuli Bao, Clinician

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Director of Hepatology and Cancer Biotherapy Ward

Study Record Dates

First Submitted

May 24, 2017

First Posted

June 5, 2017

Study Start

May 1, 2017

Primary Completion

December 30, 2018

Study Completion

March 30, 2019

Last Updated

January 18, 2018

Record last verified: 2018-01

Locations