NCT03134222

Brief Summary

The primary objective of this study is to evaluate the efficacy of filgotinib and lanraplenib (formerly GS-9876) in females with moderately-to-severely active cutaneous lupus erythematosus (CLE).

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
47

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started May 2017

Geographic Reach
2 countries

16 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 25, 2017

Completed
3 days until next milestone

First Posted

Study publicly available on registry

April 28, 2017

Completed
26 days until next milestone

Study Start

First participant enrolled

May 24, 2017

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 13, 2019

Completed
9 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 18, 2019

Completed
4 months until next milestone

Results Posted

Study results publicly available

April 8, 2020

Completed
Last Updated

June 9, 2020

Status Verified

June 1, 2020

Enrollment Period

1.8 years

First QC Date

April 25, 2017

Results QC Date

March 9, 2020

Last Update Submit

June 1, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change in Cutaneous Lupus Erythematosus Disease Area and Severity Index (CLASI) Activity Score From Baseline to Week 12

    CLASI Activity is scored based on erythema, scale/hyperkeratosis, mucous membrane involvement, acute hair loss and nonscarring alopecia. Evaluation of erythema and scale/hyperkeratosis is based on a table: rows represent anatomical areas and columns represent major clinical symptoms. The extent of involvement for each of the skin symptoms is documented for each anatomic area. The total score ranges from 0-70, with higher scores indicating more severe skin disease.

    Baseline; Week 12

Secondary Outcomes (4)

  • Percentage of Participants at Week 12 With Decrease of ≥ 5 Points in CLASI Activity Score From Baseline

    Baseline; Week 12

  • Percentage of Participants at Week 12 With No Worsening in CLASI Activity Score From Baseline

    Baseline; Week 12

  • Percentage of Participants at Week 24 With Decrease of ≥ 5 Points in CLASI Activity Score From Baseline

    Baseline; Week 24

  • Percentage of Participants at Week 24 With No Worsening in CLASI Activity Score From Baseline

    Baseline; Week 24

Study Arms (5)

Lanraplenib 30 mg

EXPERIMENTAL

Lanraplenib + filgotinib placebo for 48 weeks

Drug: LanraplenibDrug: Filgotinib placebo

Filgotinib 200 mg

EXPERIMENTAL

Filgotinib + lanraplenib placebo for 48 weeks

Drug: FilgotinibDrug: Lanraplenib placebo

Placebo

PLACEBO COMPARATOR

Filgotinib placebo + lanraplenib placebo for 12 weeks

Drug: Lanraplenib placeboDrug: Filgotinib placebo

Placebo to Lanraplenib 30 mg

EXPERIMENTAL

After Week 12 Visit, participants on placebo will be rerandomized 1:1 and receive lanraplenib + filgotinib placebo in a blinded fashion through Week 48.

Drug: LanraplenibDrug: Filgotinib placebo

Placebo to Filgotinib 200 mg

EXPERIMENTAL

After Week 12 Visit, participants on placebo will be rerandomized 1:1 and receive filgotinib + lanraplenib placebo in a blinded fashion through Week 48.

Drug: FilgotinibDrug: Lanraplenib placebo

Interventions

30 mg tablets administered orally once daily with or without food

Also known as: GS-9876
Lanraplenib 30 mgPlacebo to Lanraplenib 30 mg

200 mg tablets administered orally once daily with or without food

Also known as: GS-6034
Filgotinib 200 mgPlacebo to Filgotinib 200 mg

Tablets administered orally once daily with or without food

Filgotinib 200 mgPlaceboPlacebo to Filgotinib 200 mg

Tablets administered orally once daily with or without food

Lanraplenib 30 mgPlaceboPlacebo to Lanraplenib 30 mg

Eligibility Criteria

Age18 Years - 75 Years
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Must have a diagnosis of CLE, either chronic (e.g., discoid) or subacute CLE per investigator evaluation, with the following:
  • Moderately-to-severely active CLE (Cutaneous lupus erythematosus disease area and severity index \[CLASI\] activity score ≥ 10) at screening and Day 1
  • Prior intolerance or inadequate response to at least one of the listed medications for the treatment of CLE
  • Stable dose (defined as no change in prescription for at least 28 days prior to Day 1) of antimalarials and/or topical or oral corticosteroids is permitted during the study. Individuals who are not planning to continue these medications during the study must have discontinued them at least 28 days prior to Day 1

You may not qualify if:

  • Use of prohibited concomitant medications per study protocol

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (16)

Wallace Rheumatic Studies Center

Beverly Hills, California, 90211, United States

Location

St. Jude Hospital Yorba Linda DBA Dr. Joseph Heritage Healthcare

Fullerton, California, 92835, United States

Location

Dermatology Research Associates

Los Angeles, California, 90045, United States

Location

Desert Medical Advances

Palm Desert, California, 92260, United States

Location

Medderm Associates

San Diego, California, 92103, United States

Location

Inland Rheumatology Clinical Trials

Upland, California, 91786, United States

Location

Clinical Research of West Florida, Inc.

Clearwater, Florida, 33765, United States

Location

Omega Research Consultants LLC

DeBary, Florida, 32713, United States

Location

DJL Clinical Research, PLLC

Charlotte, North Carolina, 28210, United States

Location

Wake Forest University Health Sciences

Winston-Salem, North Carolina, 27104, United States

Location

Penn State Hershey Medical Center

Hershey, Pennsylvania, 17033, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Metroplex Clinical Research Center

Dallas, Texas, 75231, United States

Location

Dermatology Ottawa Research Centre

Ottawa, K2C 3N2, Canada

Location

University Health Network (UHN) - Toronto Western Hospital

Toronto, M5T 2S8, Canada

Location

K.Papp Clinical Research

Waterloo, N2J 1C4, Canada

Location

Related Publications (1)

  • Werth VP, Fleischmann R, Robern M, Touma Z, Tiamiyu I, Gurtovaya O, Pechonkina A, Mozaffarian A, Downie B, Matzkies F, Wallace D. Filgotinib or lanraplenib in moderate to severe cutaneous lupus erythematosus: a phase 2, randomized, double-blind, placebo-controlled study. Rheumatology (Oxford). 2022 May 30;61(6):2413-2423. doi: 10.1093/rheumatology/keab685.

MeSH Terms

Conditions

Lupus Erythematosus, Cutaneous

Interventions

GLPG0634

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesSkin Diseases

Results Point of Contact

Title
Gilead Clinical Study Information Center
Organization
Gilead Sciences

Study Officials

  • Gilead Study Director

    Gilead Sciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 25, 2017

First Posted

April 28, 2017

Study Start

May 24, 2017

Primary Completion

March 13, 2019

Study Completion

December 18, 2019

Last Updated

June 9, 2020

Results First Posted

April 8, 2020

Record last verified: 2020-06

Data Sharing

IPD Sharing
Will not share

Locations