NCT03096314

Brief Summary

Vitamin D deficiency is a common, potentially reversible contributor to morbidity and mortality among critically ill patients. We conducted a randomized, double-blind, placebo-controlled, phase 3 trial of early vitamin D3 supplementation in critically ill, vitamin D-deficient patients who were at high risk for death. Patients screened as vitamin D deficient (\<20 ng/mL) were randomized. Randomization occurred within 12 hours after the decision to admit the patient to an intensive care unit. Eligible patients received a single enteral dose of 540,000 IU of vitamin D3 or matched placebo. The primary end point was 90-day all-cause, all-location mortality.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,358

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Apr 2017

Geographic Reach
1 country

47 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 21, 2017

Completed
1 month until next milestone

First Posted

Study publicly available on registry

March 30, 2017

Completed
28 days until next milestone

Study Start

First participant enrolled

April 27, 2017

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 11, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 11, 2018

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

January 27, 2020

Completed
Last Updated

January 27, 2020

Status Verified

January 1, 2020

Enrollment Period

1.6 years

First QC Date

February 21, 2017

Results QC Date

December 10, 2019

Last Update Submit

January 24, 2020

Conditions

Keywords

ARDSVitamin D

Outcome Measures

Primary Outcomes (1)

  • All-cause, All-location Mortality to Day 90

    Vital status of the patient at day 90 was determined using any of the following methods: medical record review, phone calls to patient, proxy or healthcare facility, review of obituaries, or information from the Centers for Disease Control and Prevention's National Death Index (NDI).

    90 days after randomization

Secondary Outcomes (21)

  • All-cause, All Location Mortality to Day 28

    Up to 28 days after randomization

  • Hospital Mortality to Day 90

    Up to 90 days after randomization

  • Alive and Home (Prior Level of Care) at Day 90

    90 days post randomization

  • Hospital Length of Stay to Day 90

    90 days after randomization

  • Healthcare Facility Length of Stay to Day 90

    90 days after randomization

  • +16 more secondary outcomes

Study Arms (2)

High dose vitamin D formulation

ACTIVE COMPARATOR

A single dose of 540,000 IU vitamin D3 will be administered within 2 hours of randomization time.

Drug: Vitamin D3

Placebo

PLACEBO COMPARATOR

A single, liquid enteral placebo dose administered either orally or via naso/orogastric tube will be administered within 2 hours of randomization time.

Drug: Placebo

Interventions

540,000 IU vitamin D3 delivered as a single, liquid enteral dose administered either orally or via naso/orogastric tube

Also known as: cholecalciferol
High dose vitamin D formulation

A single, liquid enteral dose identical in appearance and consistency to cholecalciferol administered either orally or via naso/orogastric tube.

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age ≥ 18 years
  • Intention to admit to ICU from emergency department, hospital ward, operating room, or outside facility
  • One or more of the following acute risk factors for ARDS and mortality contributing directly to the need for ICU admission:
  • Pulmonary
  • Pneumonia
  • Aspiration
  • Smoke Inhalation
  • Lung contusion
  • Mechanical ventilation for acute hypoxemic or hypercarbic respiratory failure Extra-Pulmonary
  • Shock
  • Sepsis
  • Pancreatitis
  • Vitamin D deficiency (screening 25OHD level \<20 ng/mL)

You may not qualify if:

  • Inability to obtain informed consent
  • Unable to randomize within 12 hours of ICU admission decision
  • Unable to take study medication by mouth or enteral tube
  • Baseline serum calcium \>10.2 mg/dL (2.54 mmol/L) or ionized calcium \>5.2 mg/dL (1.30 mmol/L)
  • Known kidney stone in past year or history of multiple (\>1) prior kidney stone episodes
  • Decision to withhold or withdraw life-sustaining treatment (patients are still eligible if they are committed to full support except cardiopulmonary resuscitation if a cardiac arrest occurs)
  • Expect \<48 hour survival
  • Prisoner
  • Pregnancy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (47)

UCSF Fresno

Fresno, California, 93701, United States

Location

Ronald Reagan UCLA Medical Center

Los Angeles, California, 90095, United States

Location

UC Davis Medical Center

Sacramento, California, 95817, United States

Location

UCSF Medical Center

San Francisco, California, 94143, United States

Location

Stanford University

Stanford, California, 94305, United States

Location

Medical Center of Aurora

Aurora, Colorado, 80045, United States

Location

University of Colorado Hospital

Aurora, Colorado, 80045, United States

Location

St. Joseph Hospital

Del Norte, Colorado, 80218, United States

Location

Denver Health Medical Center

Denver, Colorado, 80204, United States

Location

Swedish Medical Center

Englewood, Colorado, 80113, United States

Location

IU Health Methodist Hospital

Indianapolis, Indiana, 46202, United States

Location

University of Kentucky

Lexington, Kentucky, 40506, United States

Location

University Medical Center

New Orleans, Louisiana, 70112, United States

Location

Maine Medical Center

Portland, Maine, 04102, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02214, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Baystate Medical Center

Springfield, Massachusetts, 01199, United States

Location

St. Vincent's Hospital

Worcester, Massachusetts, 01608, United States

Location

University of Michigan Medical Center

Ann Arbor, Michigan, 48109, United States

Location

Henry Ford Medical Center

Detroit, Michigan, 48025, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

Mt. Sinai Hospital

New York, New York, 10029, United States

Location

Montefiore Medical Center

The Bronx, New York, 10467, United States

Location

Wake Forest Baptist Medical Center

Winston-Salem, North Carolina, 27157, United States

Location

Summa Akron City Hospital

Akron, Ohio, 44304, United States

Location

University of Cincinnati Medical Center

Cincinnati, Ohio, 45219, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

OSU Hospital East Campus

Columbus, Ohio, 43203, United States

Location

Ohio State University Wexner Medical Center

Columbus, Ohio, 43210, United States

Location

Providence Portland Medical Center

Portland, Oregon, 97213, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Penn State Hershey Medical Center

Hershey, Pennsylvania, 17033, United States

Location

UPMC Presbyterian/Mercy/Shadyside

Pittsburgh, Pennsylvania, 15261, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37221, United States

Location

Intermountain Medical Center

Murray, Utah, 84107, United States

Location

McKay-Dee Hospital

Ogden, Utah, 84403, United States

Location

Utah Valley Regional Medical Center

Provo, Utah, 84604, United States

Location

University of Utah Hospital

Salt Lake City, Utah, 84132, United States

Location

LDS Hospital

Salt Lake City, Utah, 84143, United States

Location

University of Virginia Health System

Charlottesville, Virginia, 22903, United States

Location

VCU Medical Center

Richmond, Virginia, 23298, United States

Location

Harborview Medical Center

Seattle, Washington, 98104, United States

Location

University of Washington Medical Center

Seattle, Washington, 98104, United States

Location

Swedish Hospital Cherry Hill

Seattle, Washington, 98122, United States

Location

Swedish Hospital First Hill

Seattle, Washington, 98122, United States

Location

Related Publications (1)

  • National Heart, Lung, and Blood Institute PETAL Clinical Trials Network; Ginde AA, Brower RG, Caterino JM, Finck L, Banner-Goodspeed VM, Grissom CK, Hayden D, Hough CL, Hyzy RC, Khan A, Levitt JE, Park PK, Ringwood N, Rivers EP, Self WH, Shapiro NI, Thompson BT, Yealy DM, Talmor D. Early High-Dose Vitamin D3 for Critically Ill, Vitamin D-Deficient Patients. N Engl J Med. 2019 Dec 26;381(26):2529-2540. doi: 10.1056/NEJMoa1911124. Epub 2019 Dec 11.

Related Links

MeSH Terms

Conditions

Respiratory Distress SyndromeVitamin D DeficiencyCritical Illness

Interventions

Cholecalciferol

Condition Hierarchy (Ancestors)

Lung DiseasesRespiratory Tract DiseasesRespiration DisordersAvitaminosisDeficiency DiseasesMalnutritionNutrition DisordersNutritional and Metabolic DiseasesDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

CholestenesCholestanesSteroidsFused-Ring CompoundsPolycyclic CompoundsSterolsVitamin DSecosteroidsMembrane LipidsLipids

Limitations and Caveats

The Data and Safety Monitoring Board recommended that the trial be stopped at the first interim analysis when the primary outcome of the study crossed a protocol specified futility boundary. This adaptive design element resulted in a completed study.

Results Point of Contact

Title
Nancy Ringwood, CCC Project Manager
Organization
Massachusetts General Hospital

Study Officials

  • Boyd Taylor Thompson, MD

    Massachusetts General Hospital

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Co-Prinicipal Investigator PETAL CCC

Study Record Dates

First Submitted

February 21, 2017

First Posted

March 30, 2017

Study Start

April 27, 2017

Primary Completion

December 11, 2018

Study Completion

December 11, 2018

Last Updated

January 27, 2020

Results First Posted

January 27, 2020

Record last verified: 2020-01

Data Sharing

IPD Sharing
Will share

Data will be collected electronically and stored at the Clinical Coordinating Center at Massachusetts General Hospital (MGH). A de-identified database of all data will be available for use 3 years after the primary publication. Data can be accessed at that point via the National Heart Lung Blood Institute (NHLBI) BioLINCC data and biospecimen repository.

Locations