NCT03053050

Brief Summary

The primary objective of this study is to evaluate whether selonsertib (SEL; GS-4997) can cause fibrosis regression and reduce progression to cirrhosis and associated complications in adults with NASH and bridging (F3) fibrosis.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
808

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Feb 2017

Geographic Reach
26 countries

296 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 10, 2017

Completed
3 days until next milestone

Study Start

First participant enrolled

February 13, 2017

Completed
1 day until next milestone

First Posted

Study publicly available on registry

February 14, 2017

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 19, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 19, 2019

Completed
1 year until next milestone

Results Posted

Study results publicly available

June 29, 2020

Completed
Last Updated

June 29, 2020

Status Verified

June 1, 2020

Enrollment Period

2.3 years

First QC Date

February 10, 2017

Results QC Date

June 10, 2020

Last Update Submit

June 10, 2020

Conditions

Outcome Measures

Primary Outcomes (2)

  • Percentage of Participants Who Achieved a ≥ 1-Stage Improvement in Fibrosis According to the Nonalcoholic Steatohepatitis (NASH) Clinical Research Network (CRN) Classification Without Worsening of NASH at Week 48

    Fibrosis improvement was defined as ≥ 1-stage decrease from baseline in fibrosis according to the NASH CRN classification. NASH CRN fibrosis stages range from 0 to 4, with higher scores indicating greater fibrosis (0=None, 4=Cirrhosis). Worsening of NASH was defined as ≥ 1 point increase from baseline in hepatocellular ballooning or lobular inflammation according to the Non-Alcoholic Fatty Liver Disease (NAFLD) Activity Score (NAS) criteria. As defined by NAS, hepatocellular ballooning ranges from 0-2 and lobular inflammation ranges from 0-3, with higher scores indicating more severe hepatocellular ballooning or lobular inflammation.

    Week 48

  • Event-Free Survival (EFS) at Week 240 as Assessed by Time to First Clinical Event

    EFS was assessed by the time to the first clinical event, including progression to cirrhosis on liver biopsy, liver decompensation events, liver transplantation, and all-cause mortality.

    Week 240

Secondary Outcomes (6)

  • Percentage of Participants Who Had Progression to Cirrhosis at Week 48

    Week 48

  • Percentage of Participants Who Had a ≥ 1-Stage Improvement in Fibrosis Without Worsening of NASH at Week 240

    Week 240

  • Percentage of Participants Who Had a ≥ 1-Stage Improvement in Fibrosis at Week 48

    Week 48

  • Percentage of Participants Who Had a ≥ 1-Stage Improvement in Fibrosis at Week 240

    Week 240

  • Percentage of Participants Who Had NASH Resolution Without Worsening of Fibrosis at Week 48

    Week 48

  • +1 more secondary outcomes

Study Arms (3)

SEL 18 mg

EXPERIMENTAL

Randomized Phase: Selonsertib (SEL) 18 mg tablet + placebo to match SEL 6 mg tablet for 240 weeks Open-Label (OL) Phase: Participants who experience a hepatic clinical event or have biopsy confirmed progression to cirrhosis during the randomized phase, prior to completing the Week 240 visit, will be offered the option to roll over into an OL phase to receive OL SEL 18 mg for a total treatment duration of 240 weeks inclusive of the randomized phase.

Drug: SELDrug: Placebo to match SEL 6 mg

SEL 6 mg

EXPERIMENTAL

Randomized Phase: SEL 6 mg tablet + placebo to match SEL 18 mg tablet for 240 weeks OL Phase: Participants who experience a hepatic clinical event or have biopsy confirmed progression to cirrhosis during the randomized phase, prior to completing the Week 240 visit, will be offered the option to roll over into an OL phase to receive OL SEL 18 mg for a total treatment duration of 240 weeks inclusive of the randomized phase.

Drug: SELDrug: Placebo to match SEL 18 mg

Placebo

PLACEBO COMPARATOR

Randomized Phase: Placebo to match SEL 6 mg tablet + placebo to match SEL 18 mg tablet for 240 weeks OL Phase: Participants who experience a hepatic clinical event or have biopsy confirmed progression to cirrhosis during the randomized phase, prior to completing the Week 240 visit, will be offered the option to roll over into an OL phase to receive OL SEL 18 mg for a total treatment duration of 240 weeks inclusive of the randomized phase.

Drug: Placebo to match SEL 6 mgDrug: Placebo to match SEL 18 mg

Interventions

SELDRUG

Tablets administered orally once daily

Also known as: selonsertib, GS-4997
SEL 18 mgSEL 6 mg

Tablets administered orally once daily

PlaceboSEL 18 mg

Tablets administered orally once daily

PlaceboSEL 6 mg

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Liver biopsy consistent with NASH and bridging (F3 fibrosis) according to the NASH Clinical Research Network (CRN) classification in the opinion of the central reader
  • Has the following laboratory parameters at the screening visit:
  • Alanine aminotransferase (ALT) ≤ 8 x upper limit of normal (ULN)
  • Creatinine Clearance (CLcr) ≥ 30 milliliter/minute (mL/min), as calculated by the Cockcroft-Gault equation
  • Hemoglobin A1c (HbA1c) ≤ 9.5% (or serum fructosamine ≤ 381 μmol if HbA1c is unable to be resulted)
  • Total bilirubin ≤ 1.3 x ULN (unless an alternate etiology such as Gilbert's syndrome or hemolytic anemia is present)

You may not qualify if:

  • Prior history of decompensated liver disease including clinical ascites, hepatic encephalopathy (HE), or variceal bleeding
  • Child-Pugh (CP) score \> 6, as determined at screening, unless due to therapeutic anti-coagulation
  • Model for End-stage Liver Disease (MELD) score \> 12, as determined at screening, unless due to therapeutic anti-coagulation
  • Other causes of liver disease including, but not limited to, alcoholic liver disease, hepatitis B, hepatitis C, autoimmune disorders, drug-induced hepatotoxicity, Wilson disease, iron overload, and alpha-1-antitryspin deficiency, based on medical history and/ or centralized review of liver histology.
  • History of liver transplantation
  • Current or history of hepatocellular carcinoma (HCC)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (298)

Institute of Liver Health

Chandler, Arizona, 85224, United States

Location

Banner University Medical Center-Phoenix

Phoenix, Arizona, 85006, United States

Location

St. Joseph's Hospital and Medical Center

Phoenix, Arizona, 85013, United States

Location

Mayo Clinic

Phoenix, Arizona, 85054, United States

Location

University of Arizona

Tucson, Arizona, 85724, United States

Location

Baptist Medical Center

Little Rock, Arkansas, 72204, United States

Location

Arkansas Gastroenterology

North Little Rock, Arkansas, 72204, United States

Location

eStudySite

Chula Vista, California, 91911, United States

Location

Southern California Liver Centers

Coronado, California, 92673, United States

Location

United Gastroenterologists

Costa Mesa, California, 92626, United States

Location

TriWest Research Associates, LLC

El Cajon, California, 92020, United States

Location

Fresno Clinical Research Center

Fresno, California, 93720, United States

Location

University of California San Diego (UCSD)

La Jolla, California, 92103, United States

Location

Ruane Clinical Research Group

Los Angeles, California, 90036, United States

Location

Cedars Sinai Medical Center

Los Angeles, California, 90048, United States

Location

VA Greater Los Angeles Healthcare System

Los Angeles, California, 90073, United States

Location

eStudySite

Oceanside, California, 92056, United States

Location

California Liver Institute

Pasadena, California, 91105, United States

Location

Inland Empire Liver Foundation

Rialto, California, 92377, United States

Location

University of California, Davis Medical Center

Sacramento, California, 95817, United States

Location

Medical Associates Research Group

San Diego, California, 92123, United States

Location

Kaiser Permanente

San Diego, California, 92514, United States

Location

California Pacific Medical Center - Sutter Pacific Medical Foundation San Francisco Center for Liver Disease Dept. of Transplant

San Francisco, California, 94115, United States

Location

Mission Gastroenterology and Hepatology

San Francisco, California, 94115, United States

Location

University of California San Francisco (UCSF)

San Francisco, California, 94143, United States

Location

Silicon Valley Research Institute

San Jose, California, 95128, United States

Location

University of Colorado

Aurora, Colorado, 80045, United States

Location

Yale University School of Medicine

New Haven, Connecticut, 06510, United States

Location

Integrity Clinical Research, LLC

Doral, Florida, 33166, United States

Location

UF Hepatology Research at CTRB

Gainesville, Florida, 32610, United States

Location

UF Health Jacksonville-Gastroenterology Emerson

Jacksonville, Florida, 32207, United States

Location

Florida Research Institute

Lakewood Rch, Florida, 34211, United States

Location

Sunrise Medical Research, Inc

Lauderdale Lakes, Florida, 33319, United States

Location

Sunrise Research Institute

Miami, Florida, 33130, United States

Location

Schiff Center for Liver Diseases/University of Miami

Miami, Florida, 33136, United States

Location

Genoma Research Group, Inc

Miami, Florida, 33165, United States

Location

Advanced Research Institute

New Port Richey, Florida, 34653, United States

Location

Avail Clinical Research, LLC

Orange City, Florida, 32763, United States

Location

South Florida Center of Gastroenterology, PA

Wellington, Florida, 33414, United States

Location

Florida Medical Clinic, PA

Zephyrhills, Florida, 33540, United States

Location

Digestive Healthcare of Georgia

Atlanta, Georgia, 30309, United States

Location

Piedmont Transplant Institute

Atlanta, Georgia, 30309, United States

Location

Gastrointestinal Specialists of Georgia, PC

Marietta, Georgia, 30060, United States

Location

Northwestern Memorial Hospital; Clinical Research Unit

Chicago, Illinois, 60611, United States

Location

The University of Chicago Medical Center

Chicago, Illinois, 60615, United States

Location

NorthShore University Healthsystem

Glenview, Illinois, 60026, United States

Location

Indiana University Health - University Hospital

Indianapolis, Indiana, 46202, United States

Location

Indianapolis Gastroenterology Research Foundation

Indianapolis, Indiana, 46237, United States

Location

University of Iowa Hospitals and Clinics

Iowa City, Iowa, 52242, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Gastroenterology Associates of Hazard

Hazard, Kentucky, 41707, United States

Location

Delta Research Partners, LLC

Bastrop, Louisiana, 71021, United States

Location

Tulane University Health Sciences Center

New Orleans, Louisiana, 70112, United States

Location

Ocshner Medical Center

New Orleans, Louisiana, 70121, United States

Location

Louisiana Research Center, LLC

Shreveport, Louisiana, 71105, United States

Location

Mercy Medical Center

Baltimore, Maryland, 21202, United States

Location

Walter Reed National Military Medical Center

Bethesda, Maryland, 20889, United States

Location

Digestive Disease Associates, PA

Catonsville, Maryland, 21228, United States

Location

Meritus Center for Clinical Research

Hagerstown, Maryland, 21472, United States

Location

Henry Ford Health System

Detroit, Michigan, 48202, United States

Location

Gastroenterology Associates of Western Michigan, P.L.C.

Wyoming, Michigan, 49519, United States

Location

Huron Gastroenterology Associates/Center for Digestive Care

Ypsilanti, Michigan, 48197, United States

Location

University of Minnesota Medical Center - Fairview

Minneapolis, Minnesota, 55455, United States

Location

Mayo Clinic

Rochester, Minnesota, 55095, United States

Location

Southern Therapy and Advanced Research LLC (STAR)

Ridgeland, Mississippi, 39157, United States

Location

Saint Luke's Hospital of Kansas City

Kansas City, Missouri, 64111, United States

Location

Kansas City Gastroenterology and Hepatology

Kansas City, Missouri, 64131, United States

Location

Saint Louis University

St Louis, Missouri, 63104, United States

Location

eStudySite

Las Vegas, Nevada, 89109, United States

Location

Rutgers New Jersey Medical School- Doctors Office Center

Newark, New Jersey, 07102, United States

Location

University of Buffalo, Clinical and Translational Research Center

Buffalo, New York, 14230, United States

Location

Northwell Health - Sandra Atlas Bass Center for Liver Diseases

Manhasset, New York, 11030, United States

Location

Icahn School of Medicine at Mount Sinai Beth Israel

New York, New York, 10003, United States

Location

University of Rochester Medical Center

Rochester, New York, 14642, United States

Location

University of North Carolina at Chapel Hill / UNC School of Medicine

Chapel Hill, North Carolina, 27599, United States

Location

Duke University Medical Center - Duke South Clinics

Durham, North Carolina, 27710, United States

Location

Cumberland Research Associates, LLC

Fayetteville, North Carolina, 28304, United States

Location

Triad Clinical Trials LLC

Greensboro, North Carolina, 27410, United States

Location

Piedmont HealthCare, d/b/a Carolinas Center for Liver Disease

Huntersville, North Carolina, 28078, United States

Location

PMG Research of Rocky Mount, LLC

Rocky Mount, North Carolina, 27804, United States

Location

Piedmont HealthCare, d/b/a Carolinas Center for Liver Disease

Statesville, North Carolina, 28625, United States

Location

Digestive Health Specialists, PA

Winston-Salem, North Carolina, 27103, United States

Location

Consultants for Clinical Research

Cincinnati, Ohio, 45249, United States

Location

UC Health/Holmes Hospital

Cincinnati, Ohio, 45267, United States

Location

Northeast Clinical Research Center, LLC

Bethlehem, Pennsylvania, 18017, United States

Location

Hospital of the University of Pennsylvania- Perelman Center for Advanced Medicine

Philadelphia, Pennsylvania, 19104, United States

Location

Thomas Jefferson University

Philadelphia, Pennsylvania, 19107, United States

Location

UPMC - Center for Liver Diseases at the Thomas E. Starlz Institute

Pittsburgh, Pennsylvania, 15213, United States

Location

VA Pittsburgh Healthcare System

Pittsburgh, Pennsylvania, 15240, United States

Location

eStudySite

Pittsburgh, Pennsylvania, 15251, United States

Location

Guthrie Medical Group, PC

Sayre, Pennsylvania, 18840, United States

Location

University Gastroenterology

Providence, Rhode Island, 02905, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29245, United States

Location

Greenville Health System - Gastroenterology and Liver Center

Greenville, South Carolina, 29605, United States

Location

WR-ClinSearch, LLC

Chattanooga, Tennessee, 37421, United States

Location

Gastro One

Germantown, Tennessee, 38138, United States

Location

Quality Medical Research PLLC

Nashville, Tennessee, 37211, United States

Location

Vanderbilt University Medical Center - Digestive Disease Center

Nashville, Tennessee, 37212, United States

Location

Texas Clinical Research Institute, LLC

Arlington, Texas, 76012, United States

Location

Pinnacle Clinical Research, PLLC

Austin, Texas, 78746, United States

Location

Austin Center for Clinical Research

Austin, Texas, 78756, United States

Location

The Liver Institute at Methodist Dallas Medical Center

Dallas, Texas, 75203, United States

Location

Texas Digestive Disease Consultants

Dallas, Texas, 75246, United States

Location

Baylor Scott & White All Saints Medical Center

Fort Worth, Texas, 76104, United States

Location

Kelsey-Seybold Clinic

Houston, Texas, 77025, United States

Location

Baylor College of Medicine - Advanced Liver Therapies

Houston, Texas, 77030, United States

Location

VAMC & Baylor College

Houston, Texas, 77030, United States

Location

Pinnacle Clinical Research, PLLC

Live Oak, Texas, 78233, United States

Location

American Research Corporation, The Texas Liver Institute

San Antonio, Texas, 78215, United States

Location

Intermountain Liver Disease and Transplant Center

Murray, Utah, 84107, United States

Location

University of Utah Hospital

Salt Lake City, Utah, 84132, United States

Location

The University of Vermont Medical Center

Burlington, Vermont, 05401, United States

Location

University of Virginia Medical Center

Charlottesville, Virginia, 22908, United States

Location

Verity Research, Inc.

Fairfax, Virginia, 22031, United States

Location

Inova Fairfax Medical Campus

Falls Church, Virginia, 22042, United States

Location

Emeritas Research Group

Lansdowne Town Center, Virginia, 20716, United States

Location

Bon Secours St. Mary's Hospital of Richmond, Inc. d/b/a Bon Secours Liver Institute of Virginia

Newport News, Virginia, 23602, United States

Location

Digestive and Liver Disease Specialists

Norfolk, Virginia, 23502, United States

Location

Bon Secours St. Mary's Hospital of Richmond, Inc. d/b/a Bon Secours Liver Institute of Virginia

Richmond, Virginia, 23226, United States

Location

McGuire VA Medical Center

Richmond, Virginia, 23249, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23298, United States

Location

Virginia Mason

Seattle, Washington, 98101, United States

Location

Swedish Organ Transplant and Liver Center

Seattle, Washington, 98104, United States

Location

Froedtert Memorial Lutheran Hospital

Milwaukee, Wisconsin, 53226, United States

Location

Hospital Italiano de Buenos Aires

Buenos Aires, 450, Argentina

Location

Instituto Oulton

Córdoba, X5000JJS, Argentina

Location

St. Vincent's Hospital Sydney

Darlinghurst, New South Wales, 2010, Australia

Location

St. George's Hospital

Kogarah, New South Wales, 2217, Australia

Location

Westmead Hospital

Westmead, New South Wales, 2145, Australia

Location

Royal Brisbane & Women's Hospital

Herston, Queensland, 4029, Australia

Location

Royal Adelaide Hospital

Adelaide, South Australia, 5000, Australia

Location

Monash Health, Monash Medical Centre

Clayton, Victoria, 3168, Australia

Location

St. Vincent's Hospital Melbourne

Fitzroy, Victoria, 3065, Australia

Location

Austin Hospital

Heidelberg, Victoria, 3084, Australia

Location

The Alfred Hospital, Alfred Health

Melbourne, Victoria, 3004, Australia

Location

Royal Perth Hospital

Perth, Western Australia, 6000, Australia

Location

Medizinische Universitat Graz, Universitatsklinik fue Innere Medizin

Graz, A-8036, Austria

Location

Allgemeines Krankenhaus Wien

Vienna, 1090, Austria

Location

CUB Hopital Erasme

Brussels, 1070, Belgium

Location

UZ Brussel

Brussels, 1090, Belgium

Location

Universitaire Ziekenhuizen Leuven

Leuven, 3000, Belgium

Location

Hospital das Clínicas da Faculdade de Medicina de Botucatu - FMB/Universidade Estadual Paulista Julio de Mesquita Filho - UNESP

Botucatu, 18618-000, Brazil

Location

Hospital de Clínicas de Porto Alegre - HCPA/UFRGS

Porto Alegre, CEP 90035-903, Brazil

Location

Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto - USP

Ribeirão Preto, 14048-900, Brazil

Location

Hospital Das Clinicas Da Faculdade De Medicina Da Universidade De Sao Paulo

São Paulo, 01246-903, Brazil

Location

Universidade Federal de São Paulo / Unidade Ambulatorial de Pesquisa Clínica - I (UAPC-I)

São Paulo, 04040-003, Brazil

Location

University of Calgary Liver Unit (Heritage Medical Research Clinic)

Calgary, Alberta, T2N 4Z6, Canada

Location

University of Alberta Hospital - Walter C. Mackenzie Health Sciences Centre (WMC)

Edmonton, Alberta, T6G 2X8, Canada

Location

LAIR Centre

Vancouver, British Columbia, V5Z 1H2, Canada

Location

Gordon and Leslie Diamond Health Care Centre

Vancouver, British Columbia, V5Z 1M9, Canada

Location

(G.I.R.I.) GI Research Institute

Vancouver, British Columbia, V6Z 2K5, Canada

Location

PerCuro Clinical Research Ltd.

Victoria, British Columbia, V8T 5G4, Canada

Location

South Shore Medical Arts

Bridgewater, Nova Scotia, B4V 3N2, Canada

Location

William Osler Health System-Brampton Civic Hospital

Brampton, Ontario, Canada

Location

South Shore Medical Arts

London, Ontario, N6A 5A5, Canada

Location

Toronto Center for Liver Diseases (TCLD), Toronto General Hospital

Toronto, Ontario, M5G 2C4, Canada

Location

Chronic Viral Illness Service/Royal Victoria Hospital/McGill University Health Centre (MUHC)

Montreal, Quebec, H4A 3JI, Canada

Location

Centre Hospitalier Universitaire d'Angers

Angers, 49033, France

Location

Centre Hospitalier Universitaire Estaing

Clermont-Ferrand, 63003, France

Location

Hopital Henri Mondor

Créteil, 94010, France

Location

CHU de Grenoble- Hopital Michallon

Grenoble, 38043, France

Location

Centre Hospitalier Regional Universitaire- Hopital Claude Huriez

Lille, 59000, France

Location

CHU de Limoges- Hopital Dupuytren- Federation Hepatologie

Limoges, 87000, France

Location

Hopital de la Croix Rousse

Lyon, 69317, France

Location

Hôpital Saint Joseph

Marseille, 13008, France

Location

Centre Hospitalier Universitaire de Nice- Hopital l'Archet 2

Nice, 06200, France

Location

Hopital Cochin

Paris, 75014, France

Location

Hopital Beaujon

Pessac, 33600, France

Location

Centre Hospitalier Universitaire de Bordeaux

Pessac, 33604, France

Location

Centre Hospitalier Universitaire de Strasbourg- Nouvel Hopital Civil

Strasbourg, 67091, France

Location

Centre Hospitalier Universitaire de Toulouse- Hopital Purpan

Toulouse, 31059, France

Location

Hopital Paul Brousse

Villejuif, 94800, France

Location

Uniklinik RWTH Aachen, Medizinische Klinik III

Aachen, 52074, Germany

Location

Zentrum fur Infektiologie Berlin Prenzlauer Berg GmbH (zibp)

Berlin, 13353, Germany

Location

Universitatsklinikum Bonn (AoR)

Bonn, 53105, Germany

Location

Universitatsklinikum Frankfurt der Goethe-Universitat

Frankfurt, 60590, Germany

Location

Medizinische Hochschule Hannover

Hanover, 30625, Germany

Location

Uniklinikum des Saarlandes- Klinik fur Innere Medizin II

Homburg, 66421, Germany

Location

Gastroenterologisch- Hepatologisches Zentrum Kiel

Kiel, 24146, Germany

Location

Eugastro Gmbh

Leipzig, 04103, Germany

Location

Johannes Gutenberg-Universitat

Mainz, 55131, Germany

Location

Alice Ho Miu Ling Nethersole Hospital

Tai Po, Hong Kong

Location

Tuen Mun Hospital

Tuenmen, Hong Kong

Location

Midas Multispecialty Hospital

Nagpur, Maharashtra, 440010, India

Location

Institute of Post Graduate Medical Education and Research / SSKM Hospital

Kolkata, 700020, India

Location

Kasturba Medical College (KMC) Hospital

Mangalore, 575001, India

Location

Global Hospital-Super Speciality & Transplant Centre (A Unit of Centre for Digestive and Kidney Diseases (India) Pvt. Ltd.)

Mumbai, 400012, India

Location

Maharaja Agrasen Hospital

New Delhi, 110026, India

Location

All India Institute of Medical Sciences

New Delhi, 110029, India

Location

Fortis Flt. Lt. Rajan Dhall Hospital

New Delhi, 110070, India

Location

Institute of Liver & Biliary Sciences

New Delhi, 110070, India

Location

Rambam Health Care Campus

Haifa, 30196, Israel

Location

The Lady Davis Carmel Medical Center

Haifa, 3436212, Israel

Location

Holy Family hospital

Nazareth, 91008, Israel

Location

The Chaim Sheba Medical Center

Ramat Gan, 52621, Israel

Location

Tel-Aviv Sourasky Medical Center

Tel Aviv, 64239, Israel

Location

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, 20122, Italy

Location

Azienda Ospedaliera Universitaria Pisana

Pisa, 56124, Italy

Location

IRCCS Ospedale Casa Sollievo Della Soferrenza

San Giovanni Rotondo, 71013, Italy

Location

Chiba University Hospital

Chiba, 260-8670, Japan

Location

Fukui-Ken Saiseikai Hospital

Fukui-shi, 918-8503, Japan

Location

Hiroshima Red Cross Hospital & Atomic-bomb Survivors Hospital

Hiroshima, 730-8619, Japan

Location

Hiroshima University Hospital

Hiroshima, 734-8551, Japan

Location

Tokyo Medical University Ibaraki Medical Center

Ibaraki, 300-0395, Japan

Location

Juntendo University Shizuoka Hospital

Izunokuni, 410-2295, Japan

Location

Kagoshima University Medical And Dental Hospital

Kagoshima, 890-8520, Japan

Location

Kanazawa University Hospital

Kanagawa, 920-8641, Japan

Location

Nara Medical University Hospital

Kashihara, 634-8522, Japan

Location

Toranomon Hospital Kajigaya

Kawasaki, 105-8470, Japan

Location

Shinkokura Hospital

Kitakyushu, 803-8505, Japan

Location

Kumamoto Shinto General Hospital

Kumamoto, 862-8655, Japan

Location

Kurume University Hospital

Kurume, 830-0011, Japan

Location

University Hospital, Kyoto Prefectural University of Medicine

Kyoto, 602-8566, Japan

Location

Shinshu University Hospital

Matsumoto, 390-8621, Japan

Location

Toranomon Hospital

Minato, 105-8470, Japan

Location

Miyazaki Medical Center Hospital

Miyazaki, 880-0003, Japan

Location

Japanese Red Cross Musashino Hospital

Musashino, 180-8610, Japan

Location

Aichi Medical University Hospital

Nagakute, 480-1195, Japan

Location

Heart Life Hospital

Nakagami, 901-2492, Japan

Location

Nara City Hospital

Nara, 630-8305, Japan

Location

Hyogo College of Medicine Hospital

Nishinomiya, 663-8501, Japan

Location

Kawasaki Medical School General Medical Center

Okayama, 700-808, Japan

Location

Okayama University Hospital

Okayama, 700-8558, Japan

Location

National Hospital Organization Osaka National Hospital

Osaka, 540-0006, Japan

Location

National Hospital Organization Nagasaki Medical Center

Ōmura, 856-8562, Japan

Location

Hirakata Kohsai Hospital

Ōsaka, 573-0153, Japan

Location

Saga University Hospital

Saga, 849-8501, Japan

Location

Hokkaido P.W.F.A.C. Sapporo-Kosei General Hospital

Sapporo, 600-0033, Japan

Location

Tohoku Rosai Hospital

Sendai, 981-8563, Japan

Location

National Center for Global Health and Medicine Hospital

Shinjuku-ku, 162-8655, Japan

Location

Saiseikai Suita Hospital

Suita, 564-0013, Japan

Location

Kagawa Prefectural Central Hospital

Takamatsu, 760-8557, Japan

Location

Ehime University Hospital

Tōno, 7190295, Japan

Location

Mie University Hospital

Tsu, 514-8507, Japan

Location

Yamagata University Hospital

Yamagata, 990-9585, Japan

Location

Yokohama City University Hospital

Yokohama, 236-0004, Japan

Location

Hospital Selayang

Batu Caves, 68100, Malaysia

Location

University of Malaya Medical Centre

Kuala Lumpur, 50603, Malaysia

Location

Phylasis Clinicas Research S. de RL de CV.

Cuautitlán, 54769, Mexico

Location

Consultorio Médico

Mexico City, 6700, Mexico

Location

Investigaciones Medicas Cisneros SC

Monterrey, 64000, Mexico

Location

University Medical Center Utrecht

Utrecht, 3508 GA, Netherlands

Location

Auckland City Hospital

Grafton, 1023, New Zealand

Location

Szpital Specjalistyczny Nr 1 w Bytomiu, Oddzial Obserwacyjno-Zakazny i Hepatologii

Bytom, 41-902, Poland

Location

Wojewodzki Specjalistyczny Szpital im. W. Bieganskiego

Lodz, 91-347, Poland

Location

Centro Hospitalar de Tras-os-Montes e Alto Douro, E.P.E

Vila Real, 5000, Portugal

Location

Klinical Investigations Group, LLC

San Juan, 00907, Puerto Rico

Location

VA Caribbean Healthcare System

San Juan, 00921, Puerto Rico

Location

Fundacion de Investigacion de Diego

San Juan, 00927, Puerto Rico

Location

National University Hospital

Singapore, 119074, Singapore

Location

Singapore General Hospital

Singapore, 169856, Singapore

Location

Tan Tock Seng Hospital

Singapore, 308433, Singapore

Location

Changi General Hospital Pte Ltd.

Singapore, 529889, Singapore

Location

Khoo Teck Puat Hospital

Singapore, 768828, Singapore

Location

Keimyung University Dongsan Medical Center

Daegu, 41931, South Korea

Location

Kyungpook National University Hospital

Daegu, 700-721, South Korea

Location

National Health Insurance Service- Ilsan Hospital

Goyang-si, 10444, South Korea

Location

Hanyang University Seoul Hospital

Seoul, 04763, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Chung-Ang University Hospital

Seoul, 06973, South Korea

Location

Severance Hospital, Yonsei University Health System

Seoul, 120-752, South Korea

Location

Gangnam Severance Hospital

Seoul, 135-720, South Korea

Location

Korea University Guro Hospital

Seoul, 152-703, South Korea

Location

SMG-SNU Boramae Medical Center

Seoul, 37061, South Korea

Location

Yonsei University Wonju Severance Christian Hospital

Wŏnju, 26426, South Korea

Location

Hospital del Mar

Barcelona, 08003, Spain

Location

Hospital Universitari Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Clinic de Barcelona

Barcelona, 08036, Spain

Location

Hospital Universitario La Paz

Madrid, 28046, Spain

Location

Hospital Puerto de Hierro Majadahonda

Majadahonda, 28220, Spain

Location

CHOP_Complejo Hospitalrio Universitario de Pontevedra

Pontevedra, 36071, Spain

Location

Hospital Universitario Marques de Valdecilla

Santander, 39008, Spain

Location

Hospital Universitario Virgen del Rocio

Seville, 41013, Spain

Location

Hospital Universitari i Politecnic La Fe de Valencia

Valencia, 46026, Spain

Location

Universitätsklinik für Viszerale Chirurgie und Medizin, Inselspital, Hepatologie

Bern, 3010, Switzerland

Location

Istituto Cantonale di Patologia Locarno

Lugano, 6900, Switzerland

Location

Changhua Christian Hospital

Chang-hua, 500, Taiwan

Location

Ditmanson Medical Foundation Chia-Yi Christian Hospital

Chiayi City, 60002, Taiwan

Location

Kaohsiung Medical University Chung-Ho Memorial Hospital

Kaohsiung City, 80099, Taiwan

Location

E-DA Hospital

Kaohsiung City, 82445, Taiwan

Location

Chang Gung Medical Foundation, Keelung Chang Gung Memorial Hospital

Keelung, 20401, Taiwan

Location

Taichung Veterans General Hospital

Taichung, 40705, Taiwan

Location

National Cheng Kung University Hospitalv

Tainan, 7428, Taiwan

Location

National Taiwan University Hospital

Taipei, 10002, Taiwan

Location

Mackay Memorial Hospital

Taipei, 10449, Taiwan

Location

Cathay General Hospital

Taipei, 10630, Taiwan

Location

Taipei Veterans General Hospital

Taipei, 11217, Taiwan

Location

Chang Gung Medical Foundation, Linkou Chang Gung Memorial Hospital

Taoyuan District, 33305, Taiwan

Location

Cambridge University Hospitals NHS Foundation Trust

Cambridge, CB2 0QQ, United Kingdom

Location

Derby Teaching Hospitals NHS FT

Derby, DE22 3NE, United Kingdom

Location

University Hospitals Birmingham NHS Foundation Trust

Edgbaston, B15 2TH, United Kingdom

Location

King's College Hospital NHS Foundation Trust

London, SE5 9RS, United Kingdom

Location

Imperial College Healthcare NHS Trust

London, W21NY, United Kingdom

Location

The Newcastle upon Tyne Hospitals NHS Foundation Trust

Newcastle upon Tyne, NE2 3HH, United Kingdom

Location

Norfolk and Norwich University Hospitals NHS Foundation Trust

Norwich, NR4 7UY, United Kingdom

Location

Nottingham University Hospitals NHS Trust

Nottingham, NG7 2UH, United Kingdom

Location

Portsmouth Hospitals NHS Trust

Portsmouth, PO6 3LY, United Kingdom

Location

Abertawe Bro Morgannwg University Health Board

Swansea, SA2 8QA, United Kingdom

Location

Related Publications (11)

  • Anstee QM, Lawitz EJ, Alkhouri N, Wong VW, Romero-Gomez M, Okanoue T, Trauner M, Kersey K, Li G, Han L, Jia C, Wang L, Chen G, Subramanian GM, Myers RP, Djedjos CS, Kohli A, Bzowej N, Younes Z, Sarin S, Shiffman ML, Harrison SA, Afdhal NH, Goodman Z, Younossi ZM. Noninvasive Tests Accurately Identify Advanced Fibrosis due to NASH: Baseline Data From the STELLAR Trials. Hepatology. 2019 Nov;70(5):1521-1530. doi: 10.1002/hep.30842. Epub 2019 Aug 19.

  • Alkhouri N, Younossi ZM, Lawitz EJ, Wong VWS, Romero-Gomez M, et al. Impact of age on routinely available noninvasive tests for the discrimination of advanced fibrosis due to NASH in the phase 3 STELLAR trials of the ASK1 inhibitor selonsertib [Poster SAT-273]. European Association for the Study of the Liver (EASL); 2019; Vienna Austria.

    RESULT
  • Younossi ZM, Stepanova M, Anstee QM, Lawitz EJ, Wai-Sun Wong V, Romero-Gomez M, Kersey K, Li G, Subramanian GM, Myers RP, Djedjos CS, Okanoue T, Trauner M, Goodman Z, Harrison SA. Reduced Patient-Reported Outcome Scores Associate With Level of Fibrosis in Patients With Nonalcoholic Steatohepatitis. Clin Gastroenterol Hepatol. 2019 Nov;17(12):2552-2560.e10. doi: 10.1016/j.cgh.2019.02.024. Epub 2019 Feb 16.

  • Anstee QM, Lawitz EJ, Alkhouri N, Wai Sun Wong V, Romero-Gomez M, et al. Routinely available noninvasive tests discriminate advanced fibrosis due to NASH in the Phase 3 STELLAR trials of the ASK1 inhibitor selonsertib [poster]. American Association for the Study of Liver Diseases (AASLD); 2018, San Francisco, CA.

    RESULT
  • Younossi ZM, Lawitz E, Alkhouri N, Wong VWS, Romero-Gomez M, et al. Algorithms using noninvasive tests can accurately identify patients with advanced fibrosis due to NASH: Data From the STELLAR clinical trials [Poster LB-10]. AASLD; 2018; San Francisco, CA.

    RESULT
  • Younossi ZM, Stepanova M, Anstee QM, Lawitz EJ, Wai-Sun Wong V, et al. Severe impairment of patient-reported outcomes in patients with advanced fibrosis due to non-alcoholic steatohepatitis (NASH) [Poster]. AASLD; 2018; San Francisco, CA.

    RESULT
  • Younossi ZM, Stepanova M, Anstee QM, Lawitz EJ, Wai Sun Wong V, et al. Advanced fibrosis based on noninvasive tests in nonalcoholic steatohepatitis (NASH) is associated with impairment of patient-reported outcomes [Poster]. AASLD; 2018; San Francisco, CA.

    RESULT
  • Loomba R, Huang DQ, Sanyal AJ, Anstee QM, Trauner M, Lawitz EJ, Ding D, Ma L, Jia C, Billin A, Huss RS, Chung C, Goodman Z, Wong VW, Okanoue T, Romero-Gomez M, Abdelmalek MF, Muir A, Afdhal N, Bosch J, Harrison S, Younossi ZM, Myers RP. Liver stiffness thresholds to predict disease progression and clinical outcomes in bridging fibrosis and cirrhosis. Gut. 2023 Mar;72(3):581-589. doi: 10.1136/gutjnl-2022-327777. Epub 2022 Sep 9.

  • Younossi ZM, Anstee QM, Wai-Sun Wong V, Trauner M, Lawitz EJ, Harrison SA, Camargo M, Kersey K, Subramanian GM, Myers RP, Stepanova M. The Association of Histologic and Noninvasive Tests With Adverse Clinical and Patient-Reported Outcomes in Patients With Advanced Fibrosis Due to Nonalcoholic Steatohepatitis. Gastroenterology. 2021 Apr;160(5):1608-1619.e13. doi: 10.1053/j.gastro.2020.12.003. Epub 2020 Dec 8.

  • Harrison SA, Wong VW, Okanoue T, Bzowej N, Vuppalanchi R, Younes Z, Kohli A, Sarin S, Caldwell SH, Alkhouri N, Shiffman ML, Camargo M, Li G, Kersey K, Jia C, Zhu Y, Djedjos CS, Subramanian GM, Myers RP, Gunn N, Sheikh A, Anstee QM, Romero-Gomez M, Trauner M, Goodman Z, Lawitz EJ, Younossi Z; STELLAR-3; STELLAR-4 Investigators. Selonsertib for patients with bridging fibrosis or compensated cirrhosis due to NASH: Results from randomized phase III STELLAR trials. J Hepatol. 2020 Jul;73(1):26-39. doi: 10.1016/j.jhep.2020.02.027. Epub 2020 Mar 6.

  • Younossi ZM, Stepanova M, Younossi I, Racila A. Validation of Chronic Liver Disease Questionnaire for Nonalcoholic Steatohepatitis in Patients With Biopsy-Proven Nonalcoholic Steatohepatitis. Clin Gastroenterol Hepatol. 2019 Sep;17(10):2093-2100.e3. doi: 10.1016/j.cgh.2019.01.001. Epub 2019 Jan 11.

MeSH Terms

Conditions

Non-alcoholic Fatty Liver Disease

Interventions

selonsertib

Condition Hierarchy (Ancestors)

Fatty LiverLiver DiseasesDigestive System Diseases

Limitations and Caveats

Based on the results of the Week 48 analysis, the study was terminated early for lack of efficacy as prespecified in the clinical study protocol.

Results Point of Contact

Title
Gilead Clinical Study Information Center
Organization
Gilead Sciences

Study Officials

  • Gilead Study Director

    Gilead Sciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, CARE PROVIDER
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 10, 2017

First Posted

February 14, 2017

Study Start

February 13, 2017

Primary Completion

June 19, 2019

Study Completion

June 19, 2019

Last Updated

June 29, 2020

Results First Posted

June 29, 2020

Record last verified: 2020-06

Data Sharing

IPD Sharing
Will not share

Locations