NCT03052751

Brief Summary

The purpose of the study is to evaluate the clinical efficacy of UCB7665 as a chronic-intermittent treatment in subjects with generalized myasthenia gravis (MG) who are classified as moderate to severe.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
43

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started May 2017

Shorter than P25 for phase_2

Geographic Reach
7 countries

20 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 10, 2017

Completed
4 days until next milestone

First Posted

Study publicly available on registry

February 14, 2017

Completed
3 months until next milestone

Study Start

First participant enrolled

May 15, 2017

Completed
1 year until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 31, 2018

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 6, 2018

Completed
3 years until next milestone

Results Posted

Study results publicly available

August 3, 2021

Completed
Last Updated

August 3, 2021

Status Verified

July 1, 2021

Enrollment Period

1 year

First QC Date

February 10, 2017

Results QC Date

May 28, 2021

Last Update Submit

July 12, 2021

Conditions

Keywords

UCB7665Myasthenia Gravis

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline in Quantitative Myasthenia Gravis (QMG) Score to Visit 9

    The total QMG score was obtained by summing the responses to each individual item (13 items; Responses: None=0, Mild=1, Moderate=2, Severe=3). The score ranges from 0 to 39, with lower scores indicating lower disease activity. The change from Baseline is calculated, a negative value indicating improvement and a positive value worsening.

    From Baseline to Visit 9 (up to Day 29)

Secondary Outcomes (2)

  • Change From Baseline in Myasthenia Gravis-Composite Score to Visit 9

    From Baseline to Visit 9 (up to Day 29)

  • Change From Baseline in Myasthenia Gravis-Activities of Daily Living (MGADL) Score to Visit 9

    From Baseline to Visit 9 (up to Day 29)

Study Arms (2)

Dosage Regimen 1

EXPERIMENTAL

Subjects randomized in dosage regimen 1 will receive 3 doses of UCB7655 (dose 1) in dosing period 1 and will then be re-randomized into dosing period 2 to receive 3 doses of UCB7665 (dose 1 or dose 2).

Drug: UCB7665

Dosage Regimen 2

EXPERIMENTAL

Subjects randomized in dosage regimen 2 will receive 3 doses of placebo in dosing period 1 and will then be re-randomized into dosing period 2 to receive 3 doses of UCB7665 (dose 1 or dose 2).

Drug: UCB7665Other: Placebo

Interventions

UCB7665 will be administered in 2 different dosages (dose 1 and dose 2). UCB7665 (INN: Rozanolixizumab) is a humanized monoclonal antibody that is being developed for treatment of IgG autoantibody-mediated conditions such as myasthenia gravis (MG)

Also known as: Rozanolixizumab
Dosage Regimen 1Dosage Regimen 2
PlaceboOTHER

Placebo will be administered in period 1 of dosage regimen 2.

Dosage Regimen 2

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subject has a well-documented diagnosis of myasthenia gravis (MG) at Visit 1 (Screening), based on subject history and supported by previous evaluations
  • Subject would currently be considered for treatment with immunological therapy (immunoglobulin/plasma exchange (IVIG/PLEX)) by the investigator
  • Subject has a well-documented record of autoantibodies against anti-acetylcholine receptor (Anti-AChR) or anti-muscle specific kinase (Anti-MuSK) prior to Screening
  • Female subjects must either be: postmenopausal, permanently sterilized or if childbearing potential applicable will use a highly effective method of birth control
  • Male subjects must be willing to use a method of contraception

You may not qualify if:

  • Subject has previously received treatment in this study or subject has previously been exposed to UCB7665
  • Subject has participated in another study of an investigational medicinal product (IMP; or a medical device) within the previous 30 days of Screening or is currently participating in another study of an investigational medicinal product (IMP; or a medical device)
  • Subject has a known hypersensitivity to any components of the IMP
  • Subject has a history of hyperprolinemia, since L-proline is a constituent of the UCB7665 IMP
  • Subjects with Myasthenia Gravis (MG) only affecting the ocular muscles
  • Subjects with severe weakness affecting oropharyngeal or respiratory muscles, or who have myasthenic crisis at Screening or impending crisis
  • Subject has quantitative myasthenia gravis (QMG) score of \<11 at Baseline
  • Subject has a serum total immunoglobulin G (IgG) level \<= 6g/L at Screening
  • Absolute neutrophil count \<1500 cells/mm\^3
  • Subject has any medical condition (acute or chronic illness) or psychiatric condition that, in the opinion of the investigator, could jeopardize or would compromise the subject's ability to participate in this study
  • Subject has any laboratory abnormality that, in the opinion of the investigator, is clinically significant, has not resolved at randomization, and could jeopardize or would compromise the subject's ability to participate in this study
  • Subject has received a live vaccination within 8 weeks prior to the Baseline Visit; or intends to have a live vaccination during the course of the study or within 7 weeks following the final dose of IMP
  • Subject has received any experimental biological agent within or outside of a clinical study in the past 3 months or within 5 half-lives prior to Baseline (whichever is longer)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (20)

Mg0002 712

Los Angeles, California, 90033, United States

Location

Mg0002 701

Orange, California, 92868, United States

Location

Mg0002 713

Miami, Florida, 33136, United States

Location

Mg0002 708

Tampa, Florida, 33612, United States

Location

Mg0002 707

Augusta, Georgia, 30912, United States

Location

Mg0002 704

Columbus, Ohio, 43210, United States

Location

Mg0002 102

Brussels, Belgium

Location

Mg0002 103

Ghent, Belgium

Location

Mg0002 101

Leuven, Belgium

Location

Mg0002 203

London, Canada

Location

Mg0002 202

Montreal, Canada

Location

Mg0002 201

Toronto, Canada

Location

Mg0002 302

Ostrava-Poruba, Czechia

Location

Mg0002 401

Aarhus, Denmark

Location

Mg0002 402

Copenhagen, Denmark

Location

Mg0002 505

Düsseldorf, Germany

Location

Mg0002 502

Gummersbach, Germany

Location

Mg0002 501

Jena, Germany

Location

Mg0002 601

Barcelona, Spain

Location

Mg0002 602

Barcelona, Spain

Location

Related Publications (4)

  • Matic A, Alfaidi N, Bril V. An evaluation of rozanolixizumab-noli for the treatment of anti-AChR and anti-MuSK antibody-positive generalized myasthenia gravis. Expert Opin Biol Ther. 2023 Jul-Dec;23(12):1163-1171. doi: 10.1080/14712598.2023.2296126. Epub 2023 Dec 28.

  • Regnault A, Morel T, de la Loge C, Mazerolle F, Kaminski HJ, Habib AA. Measuring Overall Severity of Myasthenia Gravis (MG): Evidence for the Added Value of the MG Symptoms PRO. Neurol Ther. 2023 Oct;12(5):1573-1590. doi: 10.1007/s40120-023-00464-x. Epub 2023 May 11.

  • Bril V, Benatar M, Andersen H, Vissing J, Brock M, Greve B, Kiessling P, Woltering F, Griffin L, Van den Bergh P; MG0002 Investigators. Efficacy and Safety of Rozanolixizumab in Moderate to Severe Generalized Myasthenia Gravis: A Phase 2 Randomized Control Trial. Neurology. 2021 Feb 9;96(6):e853-e865. doi: 10.1212/WNL.0000000000011108. Epub 2020 Nov 20.

  • Smith B, Kiessling A, Lledo-Garcia R, Dixon KL, Christodoulou L, Catley MC, Atherfold P, D'Hooghe LE, Finney H, Greenslade K, Hailu H, Kevorkian L, Lightwood D, Meier C, Munro R, Qureshi O, Sarkar K, Shaw SP, Tewari R, Turner A, Tyson K, West S, Shaw S, Brennan FR. Generation and characterization of a high affinity anti-human FcRn antibody, rozanolixizumab, and the effects of different molecular formats on the reduction of plasma IgG concentration. MAbs. 2018 Oct;10(7):1111-1130. doi: 10.1080/19420862.2018.1505464. Epub 2018 Sep 12.

MeSH Terms

Conditions

Myasthenia Gravis

Interventions

rozanolixizumab

Condition Hierarchy (Ancestors)

Paraneoplastic Syndromes, Nervous SystemNervous System NeoplasmsNeoplasms by SiteNeoplasmsParaneoplastic SyndromesAutoimmune Diseases of the Nervous SystemNervous System DiseasesNeurodegenerative DiseasesNeuromuscular Junction DiseasesNeuromuscular DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
UCB
Organization
Cares

Study Officials

  • UCB Cares

    +1 877 822 9493 (UCB)

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
This is an Investigator- and Subject-Blind study.
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 10, 2017

First Posted

February 14, 2017

Study Start

May 15, 2017

Primary Completion

May 31, 2018

Study Completion

August 6, 2018

Last Updated

August 3, 2021

Results First Posted

August 3, 2021

Record last verified: 2021-07

Locations