NCT03043651

Brief Summary

This was an open-label study to evaluate the safety of continued therapy with oral treprostinil in subjects who completed Study TDE-HF-301. This study provided long-term, open-label data regarding the effect of continued long-term oral treprostinil therapy for the treatment of pulmonary hypertension (PH) associated with heart failure with preserved ejection fraction (HFpEF). Subject visits occurred at Baseline, Weeks 6, 12, 18, 24, and every 12 weeks thereafter until either oral treprostinil was commercially available to treat PH associated with HFpEF or the study was discontinued by the Sponsor. The Sponsor terminated Studies TDE-HF-301 and TDE-HF-302 on 14 October 2019 due to slow enrollment. Safety data from the final subject in Study TDE-HF-302 were recorded on 02 March 2020. Due to the lower than expected number of subjects enrolled, the planned secondary efficacy-related endpoints were not analyzed.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
48

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Jan 2018

Geographic Reach
1 country

82 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 31, 2017

Completed
6 days until next milestone

First Posted

Study publicly available on registry

February 6, 2017

Completed
12 months until next milestone

Study Start

First participant enrolled

January 30, 2018

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 2, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 2, 2020

Completed
8 months until next milestone

Results Posted

Study results publicly available

October 22, 2020

Completed
Last Updated

October 22, 2020

Status Verified

September 1, 2020

Enrollment Period

2.1 years

First QC Date

January 31, 2017

Results QC Date

September 25, 2020

Last Update Submit

September 25, 2020

Conditions

Keywords

Pulmonary HypertensionHFpEF6-Minute Walk TestOral Treprostinil

Outcome Measures

Primary Outcomes (1)

  • Long-term Safety of Oral Treprostinil in Subjects With PH Associated With HFpEF for Subjects Who Completed Study TDE-HF-301

    The primary objective of this study was to evaluate the long-term safety of oral treprostinil in subjects with PH associated with HFpEF for subjects who completed Study TDE-HF-301. The number of subjects with adverse events during the study is reported as the primary outcome measure, which was the only outcome measurement reported for this Sponsor-terminated study.

    Baseline through study completion, up to approximately 25 months

Study Arms (1)

Oral treprostinil

EXPERIMENTAL

Sustained-release tablets for TID administration

Drug: Oral treprostinil

Interventions

Sustained-release oral tablets for TID administration

Also known as: Treprostinil diethanolamine, Treprostinil diolamine
Oral treprostinil

Eligibility Criteria

Age18 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • \. The subject participated in Study TDE-HF-301, remained on study drug, was compliant with study procedures and assessments during Study TDE-HF-301, and completed through Week 24 of that study.

You may not qualify if:

  • The subject was pregnant or lactating.
  • The subject was prematurely discontinued from Study TDE-HF-301 for any reason.
  • The subject developed a concurrent illness or condition during Study TDE-HF-301, which, in the opinion of the Investigator, represented a risk to the subject's overall health if they enrolled in this study.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (82)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Banner University Medical Center Phoenix

Phoenix, Arizona, 85006, United States

Location

University of Arizona

Tucson, Arizona, 85724, United States

Location

VA Healthcare System of Greater Los Angeles

Los Angeles, California, 90073, United States

Location

University of California Los Angeles Pulmonary Division

Los Angeles, California, 90095, United States

Location

Cedars-Sinai Medical Center

Los Angeles, California, 90211, United States

Location

University of California - Davis Medical Center

Sacramento, California, 95817, United States

Location

Santa Barbara Cottage Hospital

Santa Barbara, California, 93105, United States

Location

Aurora Denver Cardiology Associates

Aurora, Colorado, 80012, United States

Location

University of Colorado Denver

Aurora, Colorado, 80045, United States

Location

National Jewish Health

Denver, Colorado, 80206, United States

Location

South Denver Cardiology

Littleton, Colorado, 80120, United States

Location

MedStar Georgetown University Hospital

Washington D.C., District of Columbia, 20007, United States

Location

Medical Faculty Associates, George Washington University

Washington D.C., District of Columbia, 20037, United States

Location

Bay Area Cardiology Associates

Brandon, Florida, 33511, United States

Location

Mayo Clinic - Jacksonville

Jacksonville, Florida, 32224, United States

Location

St. Vincent's Lung, Sleep, and Critical Care Specialists

Jacksonville, Florida, 33204, United States

Location

Central Florida Pulmonary Group, P.A.

Orlando, Florida, 32803, United States

Location

Florida Hospital

Orlando, Florida, 32806, United States

Location

University of South Florida ; Tampa General Hospital

Tampa, Florida, 33606, United States

Location

Cleveland Clinic of Florida

Weston, Florida, 33331, United States

Location

Emory University Hospital

Atlanta, Georgia, 30322, United States

Location

Augusta University

Augusta, Georgia, 30912, United States

Location

Piedmont Physicians Georgia Lung

Austell, Georgia, 30309, United States

Location

WellStar Medical Group

Marietta, Georgia, 30060, United States

Location

University of Illinois at Chicago Hospital

Chicago, Illinois, 60612, United States

Location

Loyola University Medical Center

Maywood, Illinois, 60153, United States

Location

Advocate Christ Medical Center

Oak Lawn, Illinois, 60453, United States

Location

OSF HealthCare

Peoria, Illinois, 61614, United States

Location

Indiana University Health Methodist Research Institute, INC

Indianapolis, Indiana, 46202, United States

Location

Community Heart and Vascular Hospital

Indianapolis, Indiana, 46250, United States

Location

Saint Vincent Hospital and Health Services

Indianapolis, Indiana, 46260, United States

Location

University of Iowa Hospitals and Clinics

Iowa City, Iowa, 55242, United States

Location

Iowa Heart Center

West Des Moines, Iowa, 50266, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

University of Kentucky Medical Center

Lexington, Kentucky, 40536, United States

Location

Kentuckiana Pulmonary Associates

Louisville, Kentucky, 40202, United States

Location

University of Louisville Physicians Outpatient Center

Louisville, Kentucky, 40202, United States

Location

Chest Medicine Associates

South Portland, Maine, 04106, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

St. Elizabeth's Medical Center

Brighton, Massachusetts, 02135, United States

Location

Henry Ford Health System

Detroit, Michigan, 48202, United States

Location

Spectrum Health Medical Group

Grand Rapids, Michigan, 49503, United States

Location

University of Minnesota

Minneapolis, Minnesota, 55455, United States

Location

St. Luke's Hospital

Chesterfield, Missouri, 63017, United States

Location

Saint Luke's Hospital of Kansas City

Kansas City, Missouri, 64111, United States

Location

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, 03756, United States

Location

Barnabas Health Lung Center

Newark, New Jersey, 07112, United States

Location

Albany Medical College

Albany, New York, 12208, United States

Location

Mount Sinai Medical Center

New York, New York, 10029, United States

Location

Pulmonary Health Physicians, PC

Syracuse, New York, 13066, United States

Location

Montefiore Medical Center

The Bronx, New York, 10461, United States

Location

Asheville Cardiology Associates

Asheville, North Carolina, 28803, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Pinehurst Medical Clinic

Pinehurst, North Carolina, 28374, United States

Location

The Lindner Research Center The Christ Hospital Health Network

Cincinnati, Ohio, 45219, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

The Ohio State University Wexner Medical Center

Columbus, Ohio, 43210, United States

Location

University of Toldedo Medical Center

Toledo, Ohio, 43614, United States

Location

The Oregon Clinic

Portland, Oregon, 97225, United States

Location

Lancaster General Hospital

Lancaster, Pennsylvania, 17601, United States

Location

Allegheny General Hospital

Pittsburgh, Pennsylvania, 15212, United States

Location

AnMed Health Pulmonary and Sleep Medicine

Anderson, South Carolina, 29621, United States

Location

VitaLink Research - Anderson

Anderson, South Carolina, 29621, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

Stern Cardiovascular Foundation

Germantown, Tennessee, 38138, United States

Location

Summit Medical Group

Knoxville, Tennessee, 37909, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232-2650, United States

Location

Baylor University Medical Center

Dallas, Texas, 75246, United States

Location

Houston Methodist Research Institute

Houston, Texas, 77030, United States

Location

The University of Texas Health Science Center at Houston

Houston, Texas, 77030, United States

Location

Texas Tech University Health Sciences Center

Lubbock, Texas, 79905, United States

Location

Intermountain Medical Center

Murray, Utah, 84143, United States

Location

Inova Heart and Vascular Institute

Falls Church, Virginia, 22042, United States

Location

Sentara Cardiovascular Research Institute

Norfolk, Virginia, 23507, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23298, United States

Location

Carilion Clinic

Roanoke, Virginia, 24014, United States

Location

Providence Medical Research Center

Spokane, Washington, 99204, United States

Location

West Virginia University Hospital

Morgantown, West Virginia, 26506, United States

Location

Aurora St. Luke's Medical Center

Milwaukee, Wisconsin, 53215, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

MeSH Terms

Conditions

Hypertension, Pulmonary

Interventions

treprostinil

Condition Hierarchy (Ancestors)

Lung DiseasesRespiratory Tract DiseasesHypertensionVascular DiseasesCardiovascular Diseases

Results Point of Contact

Title
Louis Holdstock
Organization
United Therapeutics

Study Officials

  • Mardi Gomberg-Maitland, MD

    George Washington University

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 31, 2017

First Posted

February 6, 2017

Study Start

January 30, 2018

Primary Completion

March 2, 2020

Study Completion

March 2, 2020

Last Updated

October 22, 2020

Results First Posted

October 22, 2020

Record last verified: 2020-09

Data Sharing

IPD Sharing
Will not share

Locations