NCT02968368

Brief Summary

To evaluate the efficacy of oral ferric maltol compared with placebo in the treatment of IDA in subjects with CKD

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
167

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Dec 2016

Geographic Reach
1 country

27 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 30, 2016

Completed
3 months until next milestone

First Posted

Study publicly available on registry

November 18, 2016

Completed
13 days until next milestone

Study Start

First participant enrolled

December 1, 2016

Completed
1.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 18, 2018

Completed
9 months until next milestone

Study Completion

Last participant's last visit for all outcomes

October 10, 2018

Completed
1.6 years until next milestone

Results Posted

Study results publicly available

May 1, 2020

Completed
Last Updated

November 2, 2020

Status Verified

October 1, 2020

Enrollment Period

1.1 years

First QC Date

August 30, 2016

Results QC Date

November 19, 2019

Last Update Submit

October 5, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change in Hb Concentration From Baseline to Week 16

    Change in hemoglobin concentration from baseline to Week 16.

    16 weeks

Secondary Outcomes (11)

  • Number of Subjects That Achieve an Increase in Hb Concentration of ≥1 g/dL at Week 16

    16 weeks

  • Number of Subjects That Achieve a Hb Concentration of ≥11 g/dL at Week 16

    16 weeks

  • Change in Hb Concentration From Baseline to Week 8

    8 weeks

  • Number of Subjects That Achieve an Increase in Hb Concentration of ≥2 g/dL at Week 16

    16 weeks

  • Changes in Ferritin From Baseline to Week 16

    baseline to week 16

  • +6 more secondary outcomes

Study Arms (2)

Oral ferric maltol

EXPERIMENTAL

30mg capsules BID

Drug: Ferric maltol

Oral placebo

PLACEBO COMPARATOR

Matching placebo capsules BID

Other: Placebo

Interventions

Also known as: Feraccru
Oral ferric maltol
PlaceboOTHER
Oral placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Ability to understand the information given in the Independent Ethics Committee (IEC) or Institutional Review Board (IRB) approved information sheet and consent form. Must sign and date the informed consent and authorization to use protected health information (PHI) in accordance with national and local subject privacy regulations prior to any study mandated procedure.
  • Willing and able to comply with study requirements.
  • Age ≥ 18 years at the time of informed consent.
  • A current diagnosis of CKD with an estimated glomerular filtration rate (eGFR) of \<60 mL/min/1.73m2 and ≥15 mL/min/1.73m2, as calculated using the abbreviated version of the Modified Diet in Renal Disease equation (MDRD) assessed via screening laboratory results.
  • Iron deficiency anemia defined by the following criteria assessed via screening laboratory results:
  • Hb \<11.0g/dL and ≥8.0g/dL
  • AND ferritin \<250ng/mL with a Transferrin saturation (TSAT) \<25% OR ferritin \<500ng/mL with a TSAT of \<15%
  • Female subjects of childbearing potential (including perimenopausal females who have had a menstrual period within 1 year prior to screening) must agree to use a reliable method of contraception until study completion and for at least 4 weeks following their final study visit. Reliable contraception is defined as a method which results in a low failure rate, i.e., less than 1% per year when used consistently and correctly, such as implants, injectables, some intrauterine contraceptive devices (IUDs), complete sexual abstinence, a vasectomized partner and oral contraceptive medications. Female subjects who are surgically sterile (bilateral tubal ligation, bilateral oophorectomy or hysterectomy) or postmenopausal (defined as no menstrual period within 1 year of screening) are also allowed to participate.

You may not qualify if:

  • Anemia due to any cause other than iron deficiency, including, but not limited to:
  • Untreated or untreatable severe malabsorption syndrome.
  • Myelosuppression use (permitted if taken at a stable dose and frequency for at least 12 weeks prior to randomization and are expected to stay stable throughout the double-blind treatment period so long as there is no clinical evidence of the myelosuppression contributing to the subject's anemia).
  • Administration with any of the following prior to randomization:
  • IV iron injection within the previous 4 weeks or administration of intramuscular or depot iron preparation within the previous 12 weeks.
  • Single agent oral iron supplementation, taken specifically to treat anemia (e.g. ferrous sulfate, fumarate and gluconate) within the previous 2 weeks. Multivitamins are permitted.
  • Use if ferric citrate and sucroferric oxyhydroxide within the previous 1 week.
  • ESAs within the previous 4 weeks
  • Blood transfusion or donation within the previous 12 weeks.
  • Dimercaprol or cloramphenicol within the previous 7 days.
  • Current use of methyldopa.
  • Currently receiving dialysis or initiation of dialysis is considered likely during the study.
  • Renal transplant within 12 months prior to randomization or is considered likely during the study.
  • Known hypersensitivity or allergy to the active substance or excipients of ferric maltol or placebo capsules.
  • Contraindication for treatment with iron preparations, e.g. hemochromatosis, chronic hemolytic disease, sideroblastic anemia, thalassemia, or lead intoxication induced anemia.
  • +8 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (27)

Unknown Facility

Peoria, Arizona, United States

Location

Unknown Facility

Phoenix, Arizona, United States

Location

Unknown Facility

Prescott, Arizona, United States

Location

Unknown Facility

Tucson, Arizona, United States

Location

Unknown Facility

La Mesa, California, United States

Location

Unknown Facility

Long Beach, California, United States

Location

Unknown Facility

Roseville, California, United States

Location

Unknown Facility

Sacramento, California, United States

Location

Unknown Facility

Denver, Colorado, United States

Location

Unknown Facility

Coral Springs, Florida, United States

Location

Unknown Facility

Edgewater, Florida, United States

Location

Unknown Facility

Lauderdale Lakes, Florida, United States

Location

Unknown Facility

Miami, Florida, United States

Location

Unknown Facility

Macon, Georgia, United States

Location

Unknown Facility

Shreveport, Louisiana, United States

Location

Unknown Facility

Pontiac, Michigan, United States

Location

Unknown Facility

Roseville, Michigan, United States

Location

Unknown Facility

Las Vegas, Nevada, United States

Location

Unknown Facility

Asheville, North Carolina, United States

Location

Unknown Facility

Charlotte, North Carolina, United States

Location

Unknown Facility

Wilmington, North Carolina, United States

Location

Unknown Facility

Bethlehem, Pennsylvania, United States

Location

Unknown Facility

Knoxville, Tennessee, United States

Location

Unknown Facility

Nashville, Tennessee, United States

Location

Unknown Facility

El Paso, Texas, United States

Location

Unknown Facility

San Antonio, Texas, United States

Location

Unknown Facility

Hampton, Virginia, United States

Location

Related Publications (1)

  • Pergola PE, Kopyt NP. Oral Ferric Maltol for the Treatment of Iron-Deficiency Anemia in Patients With CKD: A Randomized Trial and Open-Label Extension. Am J Kidney Dis. 2021 Dec;78(6):846-856.e1. doi: 10.1053/j.ajkd.2021.03.020. Epub 2021 May 23.

MeSH Terms

Conditions

Renal Insufficiency, ChronicAnemia, Iron-Deficiency

Interventions

ferric maltol

Condition Hierarchy (Ancestors)

Renal InsufficiencyKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsAnemia, HypochromicAnemiaHematologic DiseasesHemic and Lymphatic DiseasesIron DeficienciesIron Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Results Point of Contact

Title
Jackie Mitchell MA DPhil
Organization
Shield Therapeutics

Study Officials

  • Mark Sampson, MBChB

    Shield Therapeutics

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 30, 2016

First Posted

November 18, 2016

Study Start

December 1, 2016

Primary Completion

January 18, 2018

Study Completion

October 10, 2018

Last Updated

November 2, 2020

Results First Posted

May 1, 2020

Record last verified: 2020-10

Data Sharing

IPD Sharing
Will not share

Locations