NCT02923921

Brief Summary

To compare the efficacy of pegilodecakin in combination with FOLFOX versus FOLFOX alone in participants with metastatic pancreatic cancer as measured by overall survival.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
567

participants targeted

Target at P75+ for phase_3 pancreatic-cancer

Timeline
Completed

Started Mar 2017

Geographic Reach
12 countries

126 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 30, 2016

Completed
5 days until next milestone

First Posted

Study publicly available on registry

October 5, 2016

Completed
5 months until next milestone

Study Start

First participant enrolled

March 1, 2017

Completed
2.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 9, 2019

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 5, 2020

Completed
8 months until next milestone

Results Posted

Study results publicly available

October 19, 2020

Completed
Last Updated

October 19, 2020

Status Verified

April 15, 2020

Enrollment Period

2.5 years

First QC Date

September 30, 2016

Results QC Date

August 14, 2020

Last Update Submit

September 24, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • Overall Survival

    Overall survival is defined as the time from date of randomization to the date of death (due to any cause). For participants whose last known status is alive at the data cutoff date for the analysis, time will be censored as the last contact date prior to the data cutoff date.

    Randomization to date of death from any cause (Up To 30 Months)

Secondary Outcomes (5)

  • Progression Free Survival

    Randomization to Progressive Disease (PD) or Date of Death (Up To 30 Months)

  • Percentage of Participants Achieving Complete Response (CR) or Partial Response (PR) [Objective Response Rate (ORR)] That Assessed by Investigator

    Randomization to PD (Up To 30 Months)

  • Percentage of Participants With a Best Overall Response of Complete Response (CR), Partial Response (PR) or Stable Disease (SD): Disease Control Rate (DCR)

    Randomization to Objective Progressive Disease or Start of New Anti-Cancer Therapy (Up To 30 Months)

  • Duration of Response (DOR)

    Randomization to Progressive Disease (PD) or Date of Death (Up To 30 Months)

  • Percentage of Participants Alive at 1 Year (12-Month Survival Rate)

    From randomization to until the date of first documented date of death from any cause within 12 months

Study Arms (2)

Pegilodecakin + FOLFOX

EXPERIMENTAL

Pegilodecakin 5 microgram per kilogram (μg/kg) dosed as one of the following 2 fixed doses: 0.4 milligram (mg) for participants weighing ≤80 kg or 0.8 mg for participants weighing\>80 kg on Days 1-5 and Days 8-12 subcutaneously (SC) plus FOLFOX \[dl-Leucovorin (dl-LV) 400 milligram per meter square (mg/m2) and oxaliplatin 85 mg/m2 followed by bolus 5-fluorouracil (5-FU) 400 mg/m2 and a 46 to 48 hour infusion of 5- FU 2400 mg/m2\] initiated on Day 1 of a 14-day cycles for up to 12 cycles or until disease progression. After discontinuation of FOLFOX in the absence of tumor progression \[that is (i.e., completion of the planned 12 cycles or unacceptable FOLFOX related toxicity\], Pegilodecakin 10µg/kg maintenance treatment administered as one of the 2 fixed doses, either 0.8 mg for participants weighing ≤80 kg or 1.6 mg for participants weighing\>80 kg.

Biological: PegilodecakinDrug: FOLFOX

FOLFOX

ACTIVE COMPARATOR

FOLFOX (dl-LV 400 mg/m2 and oxaliplatin 85 mg/m2 followed by bolus 5-FU 400 mg/m2 and a 46-hour infusion of 5-FU 2400 mg/m2) initiated on Day 1 of a 14-day cycles for up to 12 cycles or until disease progression.

Drug: FOLFOX

Interventions

PegilodecakinBIOLOGICAL

Pegilodecakin plus FOLFOX

Also known as: LY3500518, AM0010
Pegilodecakin + FOLFOX
FOLFOXDRUG

FOLFOX Alone

Also known as: oxaliplatin, 5-FU, leucovorin
FOLFOXPegilodecakin + FOLFOX

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • The presence of metastatic pancreatic adenocarcinoma
  • Measurable disease per RECIST v.1.1
  • Participant must have documented tumor progression during or following a gemcitabine containing regimen to treat metastatic disease as established by CT or MRI scan
  • Eastern Cooperative Oncology Group Performance Status of 0 - 1
  • Participant must have completed prior chemotherapy at least 2 weeks (washout period) prior to randomization and recovered from toxicity to Grade 1 or baseline
  • Participants must not have received previous radiation therapy or investigational therapy for the treatment of advanced metastatic disease.
  • Participants having received cytotoxic doses of gemcitabine or any other chemotherapy in the adjuvant setting are not eligible for this study
  • No peripheral neuropathy
  • No known history of dihydropyrimidine dehydrogenase deficiency

You may not qualify if:

  • Diagnosis of pancreatic islet neoplasm, acinar cell carcinoma, non- adenocarcinoma (i.e., lymphoma, sarcoma), adenocarcinoma originating from the biliary tree, or cystadenocarcinoma
  • Participant on Coumadin and not willing to change to LMWH or oral Factor II or Xa inhibitor with half-life of less than 24 hours.
  • Participant has received prior treatment with pegilodecakin or fluoropyrimidine/platinum containing regimen
  • Participants who were intolerant of a gemcitabine containing regimen.
  • History of positivity for human immunodeficiency virus
  • Chronic active or active viral hepatitis A, B, or C infection
  • Clinically significant bleeding within two weeks prior to randomization (e.g., gastrointestinal (GI) bleeding, intracranial hemorrhage)
  • Pregnant or lactating women
  • Participants with a history of immune-mediated neurological disorders such as multiple sclerosis, Guillain-Barré or inflammatory CNS/PNS disorders
  • Clinically significant ascites defined as requiring ≥ 1 paracentesis every 2- weeks
  • Major surgery, defined as any surgical procedure that involves general anesthesia and a significant incision (i.e., larger than what is required for placement of central venous access, percutaneous feeding tube, or biopsy),within 28 days prior to randomization or anticipated surgery during the study period
  • Prior history of receiving immune modulators including, but not limited to, anti-CTLA4, anti-PD1, anti-PD-L1

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (130)

Banner MD Anderson Cancer Center

Gilbert, Arizona, 85234, United States

Location

Cancer Treatment Centers of America

Goodyear, Arizona, 85338, United States

Location

University of Arizona Cancer Center

Phoenix, Arizona, 85004, United States

Location

Comprehensive Blood and Cancer Center

Bakersfield, California, 93309, United States

Location

St. Joseph Heritage Healthcare

Fullerton, California, 92935, United States

Location

USC Norris Cancer Hospital

Los Angeles, California, 90033, United States

Location

TRIO - Translational Research in Oncology-US, Inc.

Los Angeles, California, 90095, United States

Location

UCLA Medical Center

Los Angeles, California, 90095, United States

Location

Cancer Care Associates Medical Group

Redondo Beach, California, 90277, United States

Location

Central Coast Medical Oncology Corporation

Santa Maria, California, 93454, United States

Location

Rocky Mountain Cancer Center

Denver, Colorado, 80218, United States

Location

Georgetown University Medical Center

Washington D.C., District of Columbia, 20007, United States

Location

Lynn Cancer Institute Ctr for Hem-Onc

Boca Raton, Florida, 33486, United States

Location

Memorial Regional Hospital/Joe Dimaggio Childrens Hospital

Hollywood, Florida, 33021, United States

Location

Baptist Cancer Institute

Jacksonville, Florida, 32207, United States

Location

Watson Clinic

Lakeland, Florida, 33805, United States

Location

Florida Hospital Cancer Institute

Orlando, Florida, 32804, United States

Location

UF Health Cancer Center- Orlando Health

Orlando, Florida, 32806, United States

Location

Northeast Georgia Cancer Care, LLC

Athens, Georgia, 30607, United States

Location

Southeastern Regional Medical Center

Newnan, Georgia, 30265, United States

Location

Saint Alphonsus Regional Medical Center

Caldwell, Idaho, 83605, United States

Location

Decatur Memorial Hospital

Decatur, Illinois, 62526, United States

Location

Fort Wayne Oncology & Hematology

Fort Wayne, Indiana, 46815, United States

Location

St. Elizabeth Medical Center

Edgewood, Kentucky, 41017, United States

Location

Norton Cancer Institute

Louisville, Kentucky, 40202, United States

Location

Hematology Oncology Clinic

Baton Rouge, Louisiana, 70808, United States

Location

New England Cancer Specialists - Scarborough

Scarborough, Maine, 04074, United States

Location

Committee on Clinical Investigations (CCI)- Beth Isreal Deaconess Medical Center IRB

Boston, Massachusetts, 02215, United States

Location

University of Massachusetts Medical Center

Worcester, Massachusetts, 01655, United States

Location

Virginia Piper Cancer Institute

Minneapolis, Minnesota, 55407, United States

Location

St Louis Cancer Care

Bridgeton, Missouri, 63044, United States

Location

Summit Medical Group

Summit, New Jersey, 07902, United States

Location

North Shore Hematology Oncology Associates

East Setauket, New York, 11733, United States

Location

Winthrop University Hospital

Mineola, New York, 11501, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Novant Health, Oncology Research Institute

Winston-Salem, North Carolina, 27103, United States

Location

Gabrail Cancer Center

Canton, Ohio, 44718, United States

Location

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, 73190, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Gettysburg Cancer Center

Gettysburg, Pennsylvania, 17325, United States

Location

Eastern Regional Medical Center

Philadelphia, Pennsylvania, 19124, United States

Location

UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, 15232-1305, United States

Location

Sarah Cannon Research Institute SCRI

Nashville, Tennessee, 37203, United States

Location

Tennessee Oncology PLLC

Nashville, Tennessee, 37203, United States

Location

Texas Oncology-Austin Midtown

Austin, Texas, 78705, United States

Location

Texas Oncology-Plano East

Plano, Texas, 75075, United States

Location

Texas Oncology - San Antonio Medical Center

San Antonio, Texas, 78240, United States

Location

US Oncology

The Woodlands, Texas, 77380, United States

Location

Hope Cancer Center of East Texas

Tyler, Texas, 75701, United States

Location

Texas Oncology - Tyler

Tyler, Texas, 75702, United States

Location

Texas Oncology-Wichital Falls Texoma Cancer Center

Wichita Falls, Texas, 76310, United States

Location

University of Utah School of Medicine

Salt Lake City, Utah, 84132, United States

Location

Virginia Cancer Institute

Richmond, Virginia, 23230, United States

Location

Medical Oncology Associates, PS

Spokane, Washington, 99208, United States

Location

MultiCare Regional Cancer Center - Auburn

Tacoma, Washington, 98002, United States

Location

Aurora West Allis Medical Center

Green Bay, Wisconsin, 54308, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

St Vincent's Hospital

Sydney, New South Wales, 2010, Australia

Location

Warringal Private Hospital

Heidelberg, Victoria, 3084, Australia

Location

Cabrini Hospital Malvern

Malvern, Victoria, 3144, Australia

Location

St John of God Murdoch Hospital

Murdoch, Western Australia, 6150, Australia

Location

Universitätsklinikum Graz

Graz, Styria, 8036, Austria

Location

KH der Barmherzigen Schwestern Linz BetriebsGesmbH

Linz, Upper Austria, 4010, Austria

Location

Universitätsklinikum Salzburg

Salzburg, 5020, Austria

Location

Imeldaziekenhuis

Bonheiden, 2820, Belgium

Location

Hospital Universitaire Erasme Brussel

Brussels, 1070, Belgium

Location

Universitair Ziekenhuis Brussel

Brussels, 1090, Belgium

Location

Grand Hopital de Charleroi-Site Notre-Dame

Charleroi, 6000, Belgium

Location

Universitair Ziekenhuis Antwerpen

Edegem, 2650, Belgium

Location

Universitair Ziekenhuis Gent

Ghent, 9000, Belgium

Location

AZ Groeninge

Kortrijk, 8500, Belgium

Location

Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg

Leuven, 3000, Belgium

Location

Clinique St Elisabeth Namur

Namur, 5000, Belgium

Location

CHU Dinant Godinne - UCL Namur

Yvoir, 5530, Belgium

Location

Toronto Sunnybrook Regional Cancer Center

Toronto, Ontario, M4N 3M5, Canada

Location

McGill University

Montreal, Quebec, H3A 1A1, Canada

Location

CHU de Besancon Hopital Jean Minjoz

Besançon, 25030, France

Location

Hopital de la Pitie Salpetriere

Paris, 75651, France

Location

CHU la Miletrie

Poitiers, 86021, France

Location

Hôpital Nord Franche-Comté

Trévenans, 90400, France

Location

Städtisches Klinikum München

München, Bavaria, 81737, Germany

Location

Kliniken Essen-Mitte Ev. Huyssens-Stiftung

Essen, North Rhine-Westphalia, 45136, Germany

Location

Universitätsklinikum Carl Gustav Carus

Dresden, Saxony, 01307, Germany

Location

Charité Universitätsmedizin Berlin

Berlin, 13353, Germany

Location

St Josef-Hospital Bochum

Bochum, Germany

Location

Universitätsklinikum Freiburg

Freiburg im Breisgau, Germany

Location

Asklepios Klinik Altona

Hamburg, 22763, Germany

Location

Istituto Scientifico Romagnolo - Studio e la Cura dei Tumori

Meldola, Forli, 47014, Italy

Location

Fondazione Piemonte l'Oncologia-Istituto Ricerca Cura Cancro

Candiolo, Torino, Italy

Location

Ospedale le Torrette

Ancona, 60100, Italy

Location

Azienda Ospedaliera Universitaria Ospedale San Martino di Genova

Genova, 16132, Italy

Location

IRCCS Ospedale San Raffaele

Milan, 20132, Italy

Location

Ospedale Niguarda Ca Granda

Milan, 20162, Italy

Location

AOU dell'Università degli Studi della Campania Luigi Vanvitelli

Naples, Italy

Location

Istituto Oncologico Veneto

Padua, 35128, Italy

Location

Policlinico San Matteo

Pavia, 27100, Italy

Location

Arcispedale Santa Maria Nuova Azienda Ospedaliera di Reggio Emilia

Reggio Emilia, 42123, Italy

Location

Universita Campus Biomedico

Roma, 00155, Italy

Location

Uniwersyteckie Centrum Kliniczne

Gdansk, 80-952, Poland

Location

Szp.Kliniczny Przemienienia Panskiego UM im.K.Marcinkowskieg

Poznan, 60-569, Poland

Location

Centrum Medyczne Medyk

Rzeszów, 35-025, Poland

Location

Wojewodzki Szpital Zespolony

Torun, 87-100, Poland

Location

Dong-A University Medical Center

Busan, Busan Gwang'yeogsi, 49201, South Korea

Location

Chonnam National University Hwasun Hospital

Hwasun-gun, Jeollanam-do, 519-809, South Korea

Location

Severance Hospital Yonsei University Health System

Seoul, Korea, 03722, South Korea

Location

Samsung Medical Center

Seoul, Korea, 06351, South Korea

Location

Seoul St. Mary's Hospital

Seoul, Korea, 06591, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Hospital Duran I Reynals

Hospitaled de Llobre, Barcelona, 08907, Spain

Location

Hospital Clinico Universitario de Santiago

Santiago de Compostela, La Coruna, 15706, Spain

Location

Hospital General Universitario Alicante

Alicante, 03010, Spain

Location

Hospital de la Santa Creu i Sant Pau

Barcelona, 08025, Spain

Location

Hospital Universitari Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Universitario Germans Trias i Pujol

Barcelona, Spain

Location

Hospital General Yague

Burgos, 9005, Spain

Location

C.H. Regional Reina Sofia

Córdoba, 14001, Spain

Location

Hospital General Universitario Gregorio Marañon

Madrid, 28007, Spain

Location

Hospital Universitario Ramon y Cajal

Madrid, 28034, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Hospital Madrid Norte Sanchinarro

Madrid, 28050, Spain

Location

Regional University Hospital in Malaga

Málaga, 29011, Spain

Location

Hospital Universitario Virgen del Rocio

Seville, 41013, Spain

Location

Tri-Service General Hospital

Neihu Taipei, 11490, Taiwan

Location

National Cheng Kung University Hospital

Tainan, 704, Taiwan

Location

Taipei Veterans General Hospital

Taipei, 11217, Taiwan

Location

Addenbrookes Hospital

Cambridge, Cambridgeshire, CB2 0QQ, United Kingdom

Location

Hammersmith Hospital

Acton, London, W12 0HS, United Kingdom

Location

Velindre Hospital

Cardiff, South Glamorgan, CF14 2TL, United Kingdom

Location

University College London Hospital Foundation Trust

London, Surrey, NW1 2BU, United Kingdom

Location

Guys/St. Thomas Hospital

London, Surrey, SE1 9RT, United Kingdom

Location

Related Publications (1)

  • Hecht JR, Lonardi S, Bendell J, Sim HW, Macarulla T, Lopez CD, Van Cutsem E, Munoz Martin AJ, Park JO, Greil R, Wang H, Hozak RR, Gueorguieva I, Lin Y, Rao S, Ryoo BY. Randomized Phase III Study of FOLFOX Alone or With Pegilodecakin as Second-Line Therapy in Patients With Metastatic Pancreatic Cancer That Progressed After Gemcitabine (SEQUOIA). J Clin Oncol. 2021 Apr 1;39(10):1108-1118. doi: 10.1200/JCO.20.02232. Epub 2021 Feb 8.

MeSH Terms

Conditions

Pancreatic Neoplasms

Interventions

pegilodecakinAM0010Folfox protocolOxaliplatinFluorouracilLeucovorin

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

Coordination ComplexesOrganic ChemicalsUracilPyrimidinonesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsFormyltetrahydrofolatesTetrahydrofolatesFolic AcidPterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingCoenzymesEnzymes and Coenzymes

Results Point of Contact

Title
Chief Medical Officer
Organization
Eli Lilly and Company

Study Officials

  • Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 9 AM - 5 PM Eastern time (UTC/GMT - 5 hours, EST)

    Eli Lilly and Company

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 30, 2016

First Posted

October 5, 2016

Study Start

March 1, 2017

Primary Completion

September 9, 2019

Study Completion

March 5, 2020

Last Updated

October 19, 2020

Results First Posted

October 19, 2020

Record last verified: 2020-04-15

Data Sharing

IPD Sharing
Will share

Anonymized individual patient level data will be provided in a secure access environment upon approval of a research proposal and a signed data sharing agreement.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
Data are available 6 months after the primary publication and approval of the indication studied in the US and EU, whichever is later. Data will be indefinitely available for requesting.
Access Criteria
A research proposal must be approved by an independent review panel and researchers must sign a data sharing agreement.
More information

Locations