NCT02889978

Brief Summary

GRAIL is using deep sequencing of circulating cell-free nucleic acids (cfNAs) to develop assays to detect cancer early in blood. The purpose of this study is to collect biological samples from participants with a new diagnosis of cancer (blood and tumor tissue) and from participants who do not have a diagnosis of cancer (blood) in order to characterize the population heterogeneity in cancer and non-cancer participants and to develop models for distinguishing cancer from non-cancer.

Trial Health

47
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
15,254

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Aug 2016

Longer than P75 for all trials

Geographic Reach
2 countries

140 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

August 4, 2016

Completed
14 days until next milestone

First Submitted

Initial submission to the registry

August 18, 2016

Completed
20 days until next milestone

First Posted

Study publicly available on registry

September 7, 2016

Completed
7.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2024

Completed
Last Updated

September 13, 2023

Status Verified

September 1, 2023

Enrollment Period

7.6 years

First QC Date

August 18, 2016

Last Update Submit

September 11, 2023

Conditions

Keywords

Cancer ScreeningHigh-Throughput Nucleotide SequencingDeep SequencingCirculating cell-free tumor DNA

Outcome Measures

Primary Outcomes (3)

  • To collect and study clinically-annotated biospecimens, specifically peripheral blood and contemporary tumor tissue when available, to characterize cfNA profiles from deep sequencing and to estimate the population heterogeneity in two arms of the study.

    30 months

  • To develop and evaluate models for discriminating cancer versus non-cancer and tissue of origin.

    30 months

  • To evaluate concordance of variants identified in sequencing of tumor tissue and cfNA sequencing results in plasma from the same subject.

    30 months

Secondary Outcomes (2)

  • To explore the relationship between genomic results and clinical outcomes based on collection of longitudinal information (at least annually for up to 5 years) from medical records for all consenting participants.

    Year 1, 2, 3, 4, 5

  • To enable assessment of the performance of an analytically validated clinical laboratory version of the NGS assay (under development) to detect circulating tumor DNA (ctDNA) in plasma.

    Year 1, 2, 3, 4, 5

Study Arms (2)

Cancer arm

Participants with new diagnosis of cancer (multiple tumor types) from which a blood sample and contemporaneous FFPE tumor tissue will be collected.

Non-cancer arm

Participants with no known diagnosis or past history of cancer from which a blood sample will be collected.

Eligibility Criteria

Age20 Years+
Sexall
Healthy VolunteersYes
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Eligible study participants will be recruited from participating medical centers in a ratio of 3 non-cancer participants for every 7 cancer participants within each individual research center. Non-cancer subject recruitment will be monitored to achieve demographic characteristics (eg, age, gender, ethnicity, smoking status) reflective of those of the cancer participants.

You may qualify if:

  • Age 20 years or older
  • Able to provide a written informed consent

You may not qualify if:

  • Known current or prior diagnosis of cancer except non-melanoma skin cancer
  • Oral or IV corticosteroid use in past 14 days prior to blood draw
  • Pregnancy (by self-report)
  • Current febrile illness
  • Acute exacerbation or flare of an inflammatory condition requiring escalation in medical therapy within 14 days prior to blood draw.
  • Recipient of organ transplant or prior non-autologous (allogeneic) bone marrow or stem cell transplant
  • Poor health status or unfit to tolerate blood draw
  • Age 20 years or older
  • Able to provide a written informed consent
  • Have either of the following:
  • A. Confirmed cancer diagnosis (any stage I-IV, as well as carcinoma in situ (CIS) within 90 days prior to or up to 42 days after study blood draw, based upon assessment of a pathological specimen
  • B. A high suspicion for a cancer diagnosis by clinical and/or radiological assessment, with planned biopsy or surgical resection to establish a definitive diagnosis within 6 weeks (42 days) after study blood draw
  • Known prior diagnosis of cancer except non-melanoma skin cancer
  • Currently receiving, or ever received, any of the following therapies to treat their current cancer: surgical management of the cancer beyond that required to establish the cancer diagnosis; local, regional or systemic chemotherapy including chemoembolization; targeted therapy, immunotherapy including cancer vaccines; hormone therapy; or radiation therapy
  • Pregnancy (by self-report)
  • +4 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (140)

Southern Cancer Center, PC - Daphne

Daphne, Alabama, 36526, United States

Location

Southern Cancer Center, P.C. - Mobile Infirmary

Mobile, Alabama, 36607, United States

Location

Southern Cancer Center, PC - Mobile Airport

Mobile, Alabama, 36608, United States

Location

Southern Cancer Center, PC - Springhill Medical Center

Mobile, Alabama, 36608, United States

Location

Mayo Clinic - Arizona

Phoenix, Arizona, 85054, United States

Location

Mercy Fort Smith

Fort Smith, Arkansas, 72903, United States

Location

Sansum Clinic - 540

Santa Barbara, California, 93105, United States

Location

Sansum Clinic- 317

Santa Barbara, California, 93105, United States

Location

Sansum Clinic - Viborg

Solvang, California, 93463, United States

Location

Rocky Mountain Cancer Centers

Aurora, Colorado, 80012, United States

Location

Rocky Mountain Cancer Center

Boulder, Colorado, 80303, United States

Location

Rocky Mountain Cancer Centers

Centennial, Colorado, 80112, United States

Location

Rocky Mountain Cancer Center

Colorado Springs, Colorado, 80907, United States

Location

Rocky Mountain Cancer Centers

Denver, Colorado, 80218, United States

Location

Rocky Mountain Cancer Centers

Denver, Colorado, 80220, United States

Location

Rocky Mountain Cancer Centers

Englewood, Colorado, 80113, United States

Location

Rocky Mountain Cancer Center

Lakewood, Colorado, 80228, United States

Location

Rocky Mountain Cancer Centers

Littleton, Colorado, 80120-4413, United States

Location

Rocky Mountain Cancer Centers

Lone Tree, Colorado, 80124, United States

Location

Rocky Mountain Cancer Centers

Longmont, Colorado, 80501, United States

Location

Rocky Mountain Cancer Center

Pueblo, Colorado, 81008, United States

Location

Rocky Mountain Cancer Centers

Thornton, Colorado, 80260, United States

Location

Hartford HealthCare Cancer Institute at Hartford Hospital

Hartford, Connecticut, 06102, United States

Location

Hartford New Britain

New Britain, Connecticut, 06052, United States

Location

UMHC Lennar Foundation - Coral Gables

Coral Gables, Florida, 33146, United States

Location

UMHC Sylvester- Coral Springs

Coral Springs, Florida, 33065, United States

Location

University of Miami Sylvester at Deerfield Beach

Deerfield Beach, Florida, 33442, United States

Location

University of Miami Sylvester at Hollywood

Hollywood, Florida, 33021, United States

Location

Mayo Clinic - Florida

Jacksonville, Florida, 32224, United States

Location

University of Miami Sylvester at Kendall

Kendall, Florida, 33176, United States

Location

University of Miami Sylvester Comprehensive Cancer Center

Miami, Florida, 33136, United States

Location

Florida Cancer Affiliates - Ocala

Ocala, Florida, 34471, United States

Location

Woodlands Medical Specialists, PA

Pensacola, Florida, 32503, United States

Location

University of Miami Sylvester at Plantation

Plantation, Florida, 33324, United States

Location

Illinois Cancer Specialists

Arlington Heights, Illinois, 60005, United States

Location

Illinois Cancer Specialists

Niles, Illinois, 60714, United States

Location

Baptist Health Lexington

Lexington, Kentucky, 40503, United States

Location

Baptist Health Louisville

Louisville, Kentucky, 40207, United States

Location

Baptist Health Paducah

Paducah, Kentucky, 42003, United States

Location

Maryland Oncology Hematology, P.A.

Bethesda, Maryland, 20817, United States

Location

Maryland Oncology Hematology, P.A.

Brandywine, Maryland, 20613, United States

Location

Maryland Oncology Hematology, P.A.

Clinton, Maryland, 20735, United States

Location

Maryland Oncology Hematology, P.A.

Columbia, Maryland, 21044, United States

Location

Maryland Oncology Hematology, P.A.

Rockville, Maryland, 20850, United States

Location

Maryland Oncology Hematology, P.A.

Silver Spring, Maryland, 20904, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

Lahey Hospital & Medical Center

Burlington, Massachusetts, 01805, United States

Location

Lahey Hospital & Medical Center - Peabody

Peabody, Massachusetts, 01960, United States

Location

Minnesota Oncology Hematology, P.A. - Main

Coon Rapids, Minnesota, 55433, United States

Location

Minnesota Oncology Hematology, P.A. - Edina

Edina, Minnesota, 55435, United States

Location

Minnesota Oncology Hematology, P.A. - Woodbury

Minneapolis, Minnesota, 55404, United States

Location

Mayo Clinic - Rochester

Rochester, Minnesota, 32224, United States

Location

Minnesota Oncology Hematology, P.A. - Coon Rapids

Woodbury, Minnesota, 55125, United States

Location

Mercy Joplin

Joplin, Missouri, 64804, United States

Location

Mercy Research - Springfield

Springfield, Missouri, 65804, United States

Location

Memorial Sloan Kettering - Basking Ridge

Basking Ridge, New Jersey, 07920, United States

Location

Memorial Sloan Kettering, NY - Monmouth

Middletown, New Jersey, 07748, United States

Location

New York Oncology Hematology, P.C.

Albany, New York, 12206, United States

Location

New York Oncology Hematology, P.C.

Albany, New York, 12208, United States

Location

Broome Oncology, LLC

Binghamton, New York, 13905, United States

Location

New York Oncology Hematology, P.C.

Clifton Park, New York, 12065, United States

Location

Broome Oncology, LLC

Johnson City, New York, 13790, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

Memorial Sloan Kettering - Rockville Center

New York, New York, 10065, United States

Location

Memorial Sloan Kettering, NY - Commack

New York, New York, 10065, United States

Location

Memorial Sloan Kettering, NY - West Harrison

New York, New York, 10065, United States

Location

Memorial Sloan Kettering

New York, New York, 10065, United States

Location

Oncology Hematology Care, Inc. - Reading Road

Cincinnati, Ohio, 45202, United States

Location

Oncology Hematology Care, Inc. - Fairfield

Cincinnati, Ohio, 45211, United States

Location

Christ Hospital Health Network - The Lindner Center Cancer Research Division

Cincinnati, Ohio, 45219, United States

Location

Oncology Hematology Care, Inc. - Mercy Health

Cincinnati, Ohio, 45230, United States

Location

Oncology Hematology Care, Inc. - E. Galbraith

Cincinnati, Ohio, 45236, United States

Location

Oncology Hematology Care, Inc. - Malsbary

Cincinnati, Ohio, 45242, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

Oncology Hematology Care, Inc. - Five Mile Road

Fairfield, Ohio, 45014, United States

Location

Oregon Health & Science University Knight Cancer Institute

Portland, Oregon, 97201, United States

Location

Northwest Cancer Specialists, P.C. dba Compass Oncology

Portland, Oregon, 97213-2982, United States

Location

Northwest Cancer Specialists, P.C. dba Compass Oncology

Portland, Oregon, 97225, United States

Location

Northwest Cancer Specialists, P.C. dba Compass Oncology

Portland, Oregon, 97227, United States

Location

Northwest Cancer Specialists, P.C. dba Compass Oncology

Tualatin, Oregon, 97062, United States

Location

Lehigh Valley Hospital - Cedar Crest

Allentown, Pennsylvania, 18101, United States

Location

Cancer Center at Lehigh Valley Hospital - Muhlenberg

Bethlehem, Pennsylvania, 18017, United States

Location

Bon Secours Saint Francis Cancer Center

Greenville, South Carolina, 29607, United States

Location

Prisma Health - Upstate

Seneca, South Carolina, 29672, United States

Location

Spartanburg Regional Healthcare System

Spartanburg, South Carolina, 29303, United States

Location

Avera Research Institute

Sioux Falls, South Dakota, 57105, United States

Location

Tennessee Oncology Medical Park II

Chattanooga, Tennessee, 37404, United States

Location

Tennessee Oncology Memorial Plaza

Chattanooga, Tennessee, 37404, United States

Location

Tennessee Oncology Cleveland Clinic

Cleveland, Tennessee, 37311, United States

Location

Tennessee Oncology CMC

Crossville, Tennessee, 38555, United States

Location

Tennessee Oncology Dickson

Dickson, Tennessee, 37055, United States

Location

Tennessee Oncology Franklin

Franklin, Tennessee, 37067, United States

Location

Tennessee Oncology Gallatin

Gallatin, Tennessee, 37066, United States

Location

Tennessee Oncology Summit

Hermitage, Tennessee, 37076, United States

Location

Tennessee Oncology Lebanon

Lebanon, Tennessee, 37090, United States

Location

Tennessee Oncology Murfreesboro

Murfreesboro, Tennessee, 37129, United States

Location

Tennessee Oncology Midtown

Nashville, Tennessee, 37203, United States

Location

Tennessee Oncology Nashville

Nashville, Tennessee, 37203, United States

Location

Tennessee Oncology SCCBC

Nashville, Tennessee, 37203, United States

Location

Tennessee Oncology St. Thomas West

Nashville, Tennessee, 37205, United States

Location

Tennessee Oncology Skyline

Nashville, Tennessee, 37207, United States

Location

Tennessee Oncology Southern Hills

Nashville, Tennessee, 37211, United States

Location

Tennessee Oncology Shelbyville

Shelbyville, Tennessee, 37160, United States

Location

Tennessee Oncology Stonecrest

Smyrna, Tennessee, 37167, United States

Location

Texas Oncology - West Texas

Amarillo, Texas, 79106, United States

Location

Texas Oncology-Bedford

Bedford, Texas, 76022, United States

Location

TXO - Methodist Dallas Cancer Center

Dallas, Texas, 75203, United States

Location

Texas Oncology - Dallas Forest Ln

Dallas, Texas, 75230, United States

Location

Texas Oncology - Presbyterian Cancer Center Dallas

Dallas, Texas, 75231, United States

Location

Texas Oncology - Baylor Charles A. Sammons Cancer Center

Dallas, Texas, 75246, United States

Location

Texas Oncology-Fort Worth

Fort Worth, Texas, 76104, United States

Location

Texas Oncology-Southwest Fort Worth

Fort Worth, Texas, 76132, United States

Location

Texas Oncology - Grapevine

Grapevine, Texas, 76051, United States

Location

Texas Oncology Cancer Care and Research Center - Harlingen

Harlingen, Texas, 78550, United States

Location

Texas Oncology - Longview Cancer Center

Longview, Texas, 75601, United States

Location

Texas Oncology - McAllen

McAllen, Texas, 78503, United States

Location

Texas Oncology - Mesquite

Mesquite, Texas, 75150, United States

Location

Texas Oncology-New Braunfels

New Braunfels, Texas, 78130, United States

Location

Texas Oncology - Plano East

Plano, Texas, 75075, United States

Location

Texas Oncology - Plano West

Plano, Texas, 75093, United States

Location

Texas Oncology - Rockwall

Rockwall, Texas, 75032, United States

Location

Texas Oncology-San Antonio Downtown

San Antonio, Texas, 78212, United States

Location

Texas Oncology - San Antonio Northeast

San Antonio, Texas, 78217, United States

Location

Texas Oncology-San Antonio Medical Center

San Antonio, Texas, 78229, United States

Location

Texas Oncology-San Antonio Stone Oak

San Antonio, Texas, 78258, United States

Location

Texas Oncology - Sherman

Sherman, Texas, 75090, United States

Location

Texas Oncology-The Woodlands

The Woodlands, Texas, 77380, United States

Location

Texas Oncology - Tyler

Tyler, Texas, 75702, United States

Location

Texas Oncology - Weslaco

Weslaco, Texas, 78503, United States

Location

Texas Oncology - West Texas

Wichita Falls, Texas, 76310, United States

Location

Virginia Cancer Specialists, PC

Alexandria, Virginia, 22304, United States

Location

Virginia Cancer Specialists, PC

Arlington, Virginia, 22205, United States

Location

Virginia Cancer Specialists, PC

Fairfax, Virginia, 22031, United States

Location

Virginia Cancer Specialists, PC

Gainesville, Virginia, 20155, United States

Location

Virginia Cancer Specialists, PC

Leesburg, Virginia, 20176, United States

Location

Virginia Cancer Specialists, PC

Woodbridge, Virginia, 22191, United States

Location

Benaroya Research Institute at Virginia Mason

Seattle, Washington, 98101, United States

Location

Northwest Cancer Specialists, P.C. dba Compass Oncology

Vancouver, Washington, 98684, United States

Location

Yakima Valley Memorial Hospital/North Star Lodge

Yakima, Washington, 98902, United States

Location

UHN Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2M9, Canada

Location

Related Publications (8)

  • Mahal BA, Margolis M, Hubbell E, Chen C, Venstrom JM, Abran J, Kartlitz JJ, Wyatt AW, Klein EA. A Targeted Methylation-Based Multicancer Early Detection Blood Test Preferentially Detects High-Grade Prostate Cancer While Minimizing Overdiagnosis of Indolent Disease. JCO Precis Oncol. 2024 Aug;8:e2400269. doi: 10.1200/PO.24.00269.

  • Bryce AH, Thiel DD, Seiden MV, Richards D, Luan Y, Coignet M, Zhang Q, Zhang N, Hubbell E, Kurtzman KN, Klein EA. Performance of a Cell-Free DNA-Based Multi-cancer Detection Test in Individuals Presenting With Symptoms Suspicious for Cancers. JCO Precis Oncol. 2023 Jul;7:e2200679. doi: 10.1200/PO.22.00679.

  • Tang WHW, Yimer H, Tummala M, Shao S, Chung G, Clement J, Chu BC, Hubbell E, Kurtzman KN, Swanton C, Roberts LR. Performance of a targeted methylation-based multi-cancer early detection test by race and ethnicity. Prev Med. 2023 Feb;167:107384. doi: 10.1016/j.ypmed.2022.107384. Epub 2022 Dec 7.

  • Shao SH, Allen B, Clement J, Chung G, Gao J, Hubbell E, Liu MC, Swanton C, Tang WHW, Yimer H, Tummala M. Multi-cancer early detection test sensitivity for cancers with and without current population-level screening options. Tumori. 2023 Jun;109(3):335-341. doi: 10.1177/03008916221133136. Epub 2022 Oct 31.

  • Bredno J, Lipson J, Venn O, Aravanis AM, Jamshidi A. Clinical correlates of circulating cell-free DNA tumor fraction. PLoS One. 2021 Aug 25;16(8):e0256436. doi: 10.1371/journal.pone.0256436. eCollection 2021.

  • Klein EA, Richards D, Cohn A, Tummala M, Lapham R, Cosgrove D, Chung G, Clement J, Gao J, Hunkapiller N, Jamshidi A, Kurtzman KN, Seiden MV, Swanton C, Liu MC. Clinical validation of a targeted methylation-based multi-cancer early detection test using an independent validation set. Ann Oncol. 2021 Sep;32(9):1167-1177. doi: 10.1016/j.annonc.2021.05.806. Epub 2021 Jun 24.

  • Larson MH, Pan W, Kim HJ, Mauntz RE, Stuart SM, Pimentel M, Zhou Y, Knudsgaard P, Demas V, Aravanis AM, Jamshidi A. A comprehensive characterization of the cell-free transcriptome reveals tissue- and subtype-specific biomarkers for cancer detection. Nat Commun. 2021 Apr 21;12(1):2357. doi: 10.1038/s41467-021-22444-1.

  • Liu MC, Oxnard GR, Klein EA, Swanton C, Seiden MV; CCGA Consortium. Sensitive and specific multi-cancer detection and localization using methylation signatures in cell-free DNA. Ann Oncol. 2020 Jun;31(6):745-759. doi: 10.1016/j.annonc.2020.02.011. Epub 2020 Mar 30.

Biospecimen

Retention: SAMPLES WITH DNA

Plasma, white blood cells, formalin fixed, paraffin embedded (FFPE) tumor tissue

MeSH Terms

Conditions

Neoplasms

Study Officials

  • Eric Fung, MD, PhD

    GRAIL, Inc.

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 18, 2016

First Posted

September 7, 2016

Study Start

August 4, 2016

Primary Completion

March 1, 2024

Study Completion

March 1, 2024

Last Updated

September 13, 2023

Record last verified: 2023-09

Locations