NCT02877615

Brief Summary

The purpose of this study is to assess the efficacy and safety of S 44819 in enhancing functional recovery after an ischemic stroke.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
585

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Dec 2016

Geographic Reach
15 countries

121 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 20, 2016

Completed
1 month until next milestone

First Posted

Study publicly available on registry

August 24, 2016

Completed
4 months until next milestone

Study Start

First participant enrolled

December 19, 2016

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 10, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 10, 2019

Completed
Last Updated

March 11, 2020

Status Verified

March 1, 2020

Enrollment Period

2.2 years

First QC Date

July 20, 2016

Last Update Submit

March 9, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • Modified Rankin Scale (mRS)

    Up to 90 days

Secondary Outcomes (10)

  • National Institutes of Health Stroke Scale (NIHSS) total score

    Selection visit Day 0 Day 5 Day 30 Day 60 Day 90 Day 105

  • Barthel Index (BI) total score

    Day 30 Day 60 Day 90 Day 105

  • Montreal Cognitive Assessment scale (Moca) total score

    Day 30 Day 90

  • Trail Making Test (TMT) time for part A

    Day 30 Day 90

  • Adverse events

    Through study completion, an average of 3 months

  • +5 more secondary outcomes

Study Arms (3)

S 44819 150 mg twice a day

EXPERIMENTAL
Drug: S 44819 150 mg twice a day

S 44819 300 mg twice a day

EXPERIMENTAL
Drug: S 44819 300 mg twice a day

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

One sachet of S 44819 150 mg and one sachet of placebo twice a day

S 44819 150 mg twice a day

Two sachets of S 44819 150 mg twice a day

S 44819 300 mg twice a day

Two sachets of placebo twice a day

Placebo

Eligibility Criteria

Age18 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients aged between 18 and 85 years (both inclusive)

You may not qualify if:

  • Any non-selection criteria, which could have occurred after the selection visit
  • Positive urinary or blood pregnancy test (for female patients of child bearing potential)
  • Any clinically significant findings from the local laboratory test likely to interfere with the ability to participate in the study and / or with the study outcome
  • Severe renal impairment detected in the local laboratory test
  • Severe hepatic impairment or liver enzymes abnormalities found in the local laboratory test
  • Stroke due to cerebral venous thrombosis
  • Brain MRI showing a severe microangiopathy
  • Brain imaging showing an acute haemorrhagic stroke or a symptomatic haemorrhagic transformation of the brain infarct
  • Any clinically relevant abnormalities detected during the examinations likely to interfere with study procedures or study outcome,
  • Repeated prolongation of ECG QTcF
  • Patient or authorised representative refusing to attend study visits or to take part in the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (121)

Royal Adelaide Hospital Department of Neurology

Adelaide, 5000, Australia

Location

Sunshine Coast Hospital

Birtinya, 4575, Australia

Location

Monash Medical Centre Department of Neurology

Clayton, 3168, Australia

Location

Lyell McEwin Hospital Neurology Department

Elizabeth Vale, 5112, Australia

Location

Gosford Hospital Neurosciences Department

Gosford, 2250, Australia

Location

Austin Health Neurology Department

Heidelberg, VIC 3084, Australia

Location

Royal Brisbane & Women's Hospital Department of Neurology

Herston, 4029, Australia

Location

Alfred Health

Melbourne, 3004, Australia

Location

Royal Melbourne Hospital Department of Neurology

Parkville, 3050, Australia

Location

Gold Coast University Hospital

Southport, QLD 4215, Australia

Location

AZ Sint-Lucas Neurologie

Bruges, 8000, Belgium

Location

AZ. St. Jan

Bruges, 8000, Belgium

Location

Universitair Ziekenhuis Antwerpen

Edegem, 2650, Belgium

Location

Jessa Ziekenhuis Dienst Neurologie

Hasselt, 3500, Belgium

Location

UZ Leuven Campus Gasthuisberg

Leuven, 3000, Belgium

Location

Les Cliniques Saint-Joseph

Liège, 4000, Belgium

Location

Sint Andries Ziekenhuis Dienst Neurologie

Tielt, 8700, Belgium

Location

Hospital das Clinicas da Faculdade de Medicina de Botucatu

Botucatu, 18618-970, Brazil

Location

Clínica Neurológica e Neurocirúrgica de Joinville

Joinville, 89202-165, Brazil

Location

Hospital Carlos Fernando Malzone Departamento de Neurologia

Matão, 15990-000, Brazil

Location

IMV Pesquisa Neurológica Setor de Pesquisa Clinica

Porto Alegre, 90110-270, Brazil

Location

Hospital Sao Lucas da Pontificia Universidade Catolica RS Setor de Pesquisa Clínica

Porto Alegre, 90610-000, Brazil

Location

Hospital das Clinicas da Fac. de Med. de Ribeirao Preto Unidade de Emergencia - Centro de Estudo

Ribeirão Preto, 14015-130, Brazil

Location

Hospital das Clinicas da Fac. de med. de Ribeirao Preto Unidade de Emergiancia

Ribeirão Preto, 14015-130, Brazil

Location

Hospital Quinta D'or Departamento de Neurologia

Rio de Janeiro, 20941-150, Brazil

Location

Irmandade Santa Casa de Misericordia de Sao Paulo Ambulatório de Neurologia

São Paulo, 01221-020, Brazil

Location

UNIFESP - Universidade Federal de Sao Paulo Centro de Pesquisa em Neurologia

São Paulo, 04039-032, Brazil

Location

University of Alberta

Edmonton, T6G 2G3, Canada

Location

Charles LeMoyne Hospital-CISSS de la Monteregie-Centre

Greenfield Park, J4V 2H1, Canada

Location

Montreal General Hospital

Montreal, H3G 1A4, Canada

Location

Saint John Regional Hospital

Saint John, E2L 4L2, Canada

Location

Fakultni nemocnice Brno Neurologicka klinika

Brno, 625 00, Czechia

Location

Fakultni nemocnice u sv. Anny Neurologicka klinika

Brno, 656 91, Czechia

Location

Nemocnice Jihlava

Jihlava, 586 33, Czechia

Location

Vseobecna fakultni nemocnice II. interni klinika VFN a 1. LF UK

Prague, 128 08, Czechia

Location

CHU Bdx-Hôpital Pellegrin-Tripode Service de Neurologie

Bordeaux, 33076, France

Location

Hôpital Sud-Francilien Unité Neurovasculaire

Corbeil-Essonnes, 91106, France

Location

CHU Henri Mondor Service de Neurologie

Créteil, 94010, France

Location

CHU de Bicêtre Service de neurologie

Le Kremlin-Bicêtre, 94270, France

Location

CHRU-Hôpital Roger Salengro Service de Neurologie

Lille, 59037, France

Location

CHU-Hôpital Gui de Chaulliac Unité de Neuropshysiologie Clinique

Montpellier, 34295, France

Location

Hôpital Lariboisière, Fernand-Vidal Service de Neurologie

Paris, 75010, France

Location

Hôpital Sainte-Anne Service de Neurologie

Paris, 75674, France

Location

CHU-Hôpital de la Milétrie Service de Neurologie

Poitiers, 86021, France

Location

Klinikum Altenburger Land GmbH Neurologische Klinik

Altenburg, 04600, Germany

Location

Neurologische Klinik GmbH, Bad Neustadt

Bad Neustadt an der Saale, 97616, Germany

Location

Vivantes Klinikum Neukölln Klinik für Neurologie mit Stroke Unit

Berlin, 12351, Germany

Location

Universitätsklinikum Erlangen Neurologische Klinik

Erlangen, 91054, Germany

Location

Universitaetsklinikum Essen Neurologische Universitätsklinik Essen

Essen, 45147, Germany

Location

Universitätsmedizin der Johannes Gutenberg-Universität Klinik und Poliklinik für

Mainz, 55131, Germany

Location

Johannes Wesling Klinik Minden Klinik für Neurologie

Minden, 32429, Germany

Location

Kreisklinikum Siegen Klinik fuer Neurologie

Siegen, 57076, Germany

Location

Universitätsklinik der Eberhard-Karls Universtiät Tübingen Hertie-Institut für Klinische Hirnforschung

Tübingen, 72076, Germany

Location

Universitätsklinikum Ulm Neurologische Klinik (RKU)

Ulm, 89081, Germany

Location

Semmelweis Egyetem Neurologiai Klinika

Budapest, 1083, Hungary

Location

Bajcsy-Zsilinszky Korhaz es Rendelointezet Neurologiai Osztaly

Budapest, 1106, Hungary

Location

Szent Janos Korhaz Neurologiai osztaly

Budapest, 1125, Hungary

Location

Honved Korhaz Stroke reszleg

Budapest, 1134, Hungary

Location

Orszagos Idegsebeszeti Tudomanyos Intezet

Budapest, 1145, Hungary

Location

Petz Aladar Megyei Oktato Korhaz Neurologiai Osztaly

Győr, 9024, Hungary

Location

Somogy Megyei Kaposi Mor Oktato Korhaz Neurologiai Osztaly

Kaposvár, 7400, Hungary

Location

Flor Ferenc Korhaz Neurologia

Kistarcsa, 2143, Hungary

Location

B-A-Z Megyei Korhaz es Egyetemi Oktato Korhaz Stroke, Er- es Neurologiai, Toxikologiai Osztaly

Miskolc, 3526, Hungary

Location

Kanizsai Dorottya Korhaz Neurologiai Osztaly

Nagykanizsa, 8800, Hungary

Location

Josa Andras Oktatokorhaz Neurologiai Osztaly

Nyíregyháza, 4400, Hungary

Location

Pecsi Tudomanyegyetem Klinikai Kozpont Neurologiai Klinika

Pécs, 7623, Hungary

Location

Soproni Erzsebet Oktato Korhaz Neurologiai Osztaly

Sopron, 9400, Hungary

Location

Szegedi Tudomanyegyetem Szent-Gyorgy Albert Klinikai Kozpont

Szeged, 6725, Hungary

Location

Vito FAZZI U.O. semplice Stroke Unit

Lecce, 73100, Italy

Location

Ospedale San Giuseppe UOC di Neurologia e Stroke Unit

Milan, 20123, Italy

Location

Ospedale San Raffaele

Milan, 20132, Italy

Location

Ospedale Sacro Cuore Don Calabria Negrar NEUROLOGY DEPT

Negrar, 37020, Italy

Location

Istituto Neurologico mediterraneo NEUROMED Dipartimento di Medicina Riabilitativa e Specialistica Repar

Pozzilli, 86077, Italy

Location

Policlinico Umberto I Emergency Department Stroke Unit

Rome, 00161, Italy

Location

Zuyderland Medisch Centrum Afdeling Neurologie

Heerlen, 6419 PC, Netherlands

Location

UMC St Radboud Afdeling Neurologie

Nijmegen, 6525 GA, Netherlands

Location

Canisius Wilhelmina Ziekenhuis Afdeling Neurologie

Nijmegen, 6532 SZ, Netherlands

Location

Erasmus MC Afdeling Neurologie

Rotterdam, 3015 GD, Netherlands

Location

Isala Klinieken Afdeling Neurologie

Zwolle, 8011 JW, Netherlands

Location

Samodzielny Publiczny Wojewodzki Szpital Specjalistyczny Oddzial Neurologiczny i Oddzial Udarowy

Chełm, 22-100, Poland

Location

M. Kopernika Provincial Specialist Hospital Dpt of Neurology

Gdansk, 80-803, Poland

Location

Szpital Specjalistyczny sw. Lukasza Oddzial Neurologii i Oddzial Udarowy

Gmina Końskie, 26-200, Poland

Location

Samodzielny Publiczny Szpital Kliniczny nr7 SUM w Katowicach Oddzial Neurologii z Pododdzialem Udarowym

Katowice, 40-635, Poland

Location

Miejskie Centrum Medyczne Jonscher Szpital Dr K. Jonschera

Lodz, 93-113, Poland

Location

Samodzielny Publiczny Szpital Kliniczny nr 4 w Lublinie Oddzial Neurologii

Lublin, 20-954, Poland

Location

Wojewodzki Szpital Specjalistyczny SPZOZ nr 3 w Rybniku

Rybnik, 44-200, Poland

Location

Szpital Specjalistyczny Ducha Swietego w Sandomierzu Oddzial Neurologii

Sandomierz, 27-600, Poland

Location

Instytut Psychiatrii i Neurologii II Klinika Neurologiczna

Warsaw, 02-957, Poland

Location

Inje University Busan Paik Hospital

Busan, 47392, South Korea

Location

Dong-A University Medical Center Department of Neurology

Busan, 49201, South Korea

Location

Kyungpook National University Hospital Department of Neurology

Daegu, 41944, South Korea

Location

Chonnam National University Hospital Department of Neurology

Gwangju, 61469, South Korea

Location

Seoul National University Bundang Hospital Department of Orthopaedic

Seongnam, 13620, South Korea

Location

Kyung Hee University Hospital

Seoul, 02447, South Korea

Location

ASAN Medical Center Department of Neurology

Seoul, 05505, South Korea

Location

H. General de Albacete Servicio de Neurología

Albacete, 02006, Spain

Location

H. Germans Trias I Pujol Servicio de Neurología

Badalona, 08916, Spain

Location

H. del Mar Neurología

Barcelona, 08003, Spain

Location

H. Valle de Hebrón Servicio de Neurología

Barcelona, 08035, Spain

Location

H. Clinic de Barcelona Comprehensive Stroke Center

Barcelona, 08036, Spain

Location

Hospital Universitari de Bellvitge Servicio de Neurología-Unidad de Ictus-Planta 9

Barcelona, 08907, Spain

Location

H. Universitario de Donosti Servicio de Neurología

Donostia / San Sebastian, 20080, Spain

Location

H. Josep Trueta Servicio de Neurología

Girona, 17007, Spain

Location

H. Universitario La Princesa Servicio de Neurología

Madrid, 28006, Spain

Location

H. Ramón y Cajal Servicio de Neurología

Madrid, 28034, Spain

Location

H. Virgen del Rocío Servicio de Neurología

Seville, 41013, Spain

Location

Hospital Universitario La Fe Servicio de Neurología

Valencia, 46026, Spain

Location

Hassleholms Sjukhus Stroke- och rehabiliteringsavdelningen 9

Hässleholm, 281 25, Sweden

Location

University Hospital Department of Neurology

Linköping, 581 85, Sweden

Location

Skaraborgs Sjukhus Skovde Strokenheten

Skövde, 541 85, Sweden

Location

Danderyds Sjukhus Medicinmottagningen

Stockholm, 182 88, Sweden

Location

Akademiska Sjukhuset Strokeavdelningen 85B

Uppsala, 751 85, Sweden

Location

Royal United Hospital Older People's Unit

Bath, BA1 3NG, United Kingdom

Location

Queen Elizabeth University Hospital

Glasgow, United Kingdom

Location

Northwick Park Hospital Neurology

Harrow, HA1 3UJ, United Kingdom

Location

Leicester Royal Infirmary Dpt of Neurology

Leicester, LE1 5WW, United Kingdom

Location

St George's University Hospitals Stroke Research office

London, SW17 0QT, United Kingdom

Location

Nottingham City Hospital

Nottingham, NG5 1PB, United Kingdom

Location

Poole NHS Foundation Trust Stroke Unit

Poole, BH15 2JB, United Kingdom

Location

Sheffield Teaching Hospitals NHS Foundation Trust Royal Hallamshire Hospital

Sheffield, S10 2JF, United Kingdom

Location

Royal Stoke University Hospital Stroke Team Office

Stoke-on-Trent, ST4 6QG, United Kingdom

Location

Related Publications (2)

  • Chabriat H, Bassetti CL, Marx U, Picarel-Blanchot F, Sors A, Gruget C, Saba B, Wattez M, Audoli ML, Hermann DM. Randomized Efficacy and Safety Trial with Oral S 44819 after Recent ischemic cerebral Event (RESTORE BRAIN study): a placebo controlled phase II study. Trials. 2020 Feb 3;21(1):136. doi: 10.1186/s13063-020-4072-2.

    PMID: 32014032BACKGROUND
  • Chabriat H, Bassetti CL, Marx U, Audoli-Inthavong ML, Sors A, Lambert E, Wattez M, Hermann DM; RESTORE BRAIN study investigators. Safety and efficacy of GABAA alpha5 antagonist S44819 in patients with ischaemic stroke: a multicentre, double-blind, randomised, placebo-controlled trial. Lancet Neurol. 2020 Mar;19(3):226-233. doi: 10.1016/S1474-4422(20)30004-1.

Related Links

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 20, 2016

First Posted

August 24, 2016

Study Start

December 19, 2016

Primary Completion

March 10, 2019

Study Completion

March 10, 2019

Last Updated

March 11, 2020

Record last verified: 2020-03

Data Sharing

IPD Sharing
Will share

Qualified scientific and medical researchers can request access to anonymized patient-level and study-level clinical trial data. They can ask all interventional clinical studies: * submitted for new medicines and new indications approved after 1 January 2014 in the European Economic Area (EEA) or the United States (US). * Where Servier or an affiliate are the Marketing Authorization Holders (MAH). The date of the first Marketing Authorization of the new medicine (or the new indication) in one of the EEA Member States will be considered within this scope.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR
Time Frame
After Marketing Authorisation in EEA or US if the study is used for the approval.
Access Criteria
Researchers should register on Servier Data Portal and fill in the research proposal form. This form in four parts should be fully documented. The Research Proposal Form will not be reviewed until all mandatory fields are completed.
More information

Available IPD Datasets

Study Protocol Access
Individual Participant Data Set Access
Statistical Analysis Plan Access
Informed Consent Form Access
Clinical Study Report Access
Study-level clinical trial data Access

Locations