NCT02696499

Brief Summary

This is a randomized, double blind, placebo-controlled, parallel-arm, multi-center, Phase 2, proof-of-concept efficacy and safety study in patients with end-stage renal disease requiring hemodialysis. The purpose of the study is to determine the efficacy and safety profile of PA101B delivered via eFlow high efficiency nebulizer in patients with uremic pruritus who are symptomatic despite using standard treatments.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
70

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Feb 2016

Shorter than P25 for phase_2

Geographic Reach
1 country

13 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 1, 2016

Completed
24 days until next milestone

First Submitted

Initial submission to the registry

February 25, 2016

Completed
6 days until next milestone

First Posted

Study publicly available on registry

March 2, 2016

Completed
5 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2016

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2016

Completed
Last Updated

April 20, 2018

Status Verified

April 1, 2018

Enrollment Period

6 months

First QC Date

February 25, 2016

Last Update Submit

April 18, 2018

Conditions

Keywords

Uremic pruritusPruritusChronic itchItchHemodialysisEnd-stage renal disease

Outcome Measures

Primary Outcomes (1)

  • Itching intensity

    Numerical rating scale (NRS)

    7 weeks

Secondary Outcomes (4)

  • Pruritus-specific quality of life (QoL)

    7 weeks

  • Pruritus-specific sleep quality

    7 weeks

  • Assessment of depression

    7 weeks

  • Patient Global Impression of Change (PGIC)

    7 weeks

Study Arms (2)

PA101B

EXPERIMENTAL
Drug: PA101B

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

PA101BDRUG

40 mg PA101B administered via inhalation twice daily for 7 weeks

PA101B

Matching placebo administered via inhalation twice daily for 7 weeks

Placebo

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of end-stage renal disease (ESRD) requiring hemodialysis for at least 3 months prior to the Screening Period
  • Receiving conventional hemodialysis (i.e., not hemofiltration or hemodiafiltration)
  • Pruritus present for at least 6 weeks of Screening
  • Mean pruritus severity score on a numerical rating scale (NRS) \> 4
  • Patient-Assessed Disease Severity Scale Type B or C at Screening
  • Documentation of a urea reduction ratio (URR) \>65% or single-pooled Kt/V\> 1.4 during Screening
  • Willing and able to provide written informed consent

You may not qualify if:

  • Current or recent history of clinically significant medical condition, laboratory abnormality, or illness that could put the patient at risk or compromise the quality of the study data as determined by the investigator
  • Myocardial infarction within 6 months or unstable angina, acute coronary syndrome, or interventional coronary procedure within 2 months of Screening
  • Upper or lower respiratory tract infection (including sinus infection) within 4 weeks of Screening
  • Severely symptomatic cardiopulmonary disease defined by the use of home oxygen treatment, dyspnea at rest or with minimal exertion, uncontrolled arrhythmias (e.g. atrial fibrillation with inadequate rate control), or history of life-threatening arrhythmias (e.g. cardiac arrest or syncope related to arrhythmia)
  • Acute exacerbation of asthma or chronic obstructive pulmonary disease resulting in hospitalization or visit to an emergency department or urgent care clinic within 6 months of Screening
  • Hospitalization for any medical reason other than for a pre-planned procedure or dialysis access related procedure within the 2 weeks of Screening
  • Malignancy requiring active treatment with a systemic drug
  • Participation in any other investigation drug study within 4 weeks of Screening
  • Current or anticipated use of baclofen, gabapentin, pregabalin and nalbuphine for the treatment of pruritus
  • Current or anticipated use of glucocorticoids administered intravenously, orally, or transdermally
  • Pregnant or breastfeeding females, or if of child-bearing potential unwilling to practice acceptable means of birth control or abstinence during the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (13)

Arizona Kidney Disease and Hypertension Center

Phoenix, Arizona, 85012, United States

Location

US Renal Care

Pine Bluff, Arkansas, 71603, United States

Location

Valley Renal Medical Group

Northridge, California, 91324, United States

Location

North America Research Institute

San Dimas, California, 91773, United States

Location

Pines Clinical Research, Inc.

Pembroke Pines, Florida, 33028, United States

Location

Genesis Clinical Research

Tampa, Florida, 33614, United States

Location

Boise Kidney and Hypertension Institute

Meridian, Idaho, 83642, United States

Location

Fresenius Medical Care of Evergreen Park

Evergreen Park, Illinois, 60805, United States

Location

Renal Medicine Associates

Albuquerque, New Mexico, 87109, United States

Location

US Renal Care

Gallup, New Mexico, 87313, United States

Location

Ridgewood Dialysis Center

Ridgewood, New York, 11385, United States

Location

Brookview Hills Research Associates LLC

Winston-Salem, North Carolina, 27103, United States

Location

Southeast Renal Research Institute

Chattanooga, Tennessee, 37408, United States

Location

Related Publications (1)

  • Hercz D, Jiang SH, Webster AC. Interventions for itch in people with advanced chronic kidney disease. Cochrane Database Syst Rev. 2020 Dec 7;12(12):CD011393. doi: 10.1002/14651858.CD011393.pub2.

MeSH Terms

Conditions

PruritusKidney Failure, Chronic

Condition Hierarchy (Ancestors)

Skin DiseasesSkin and Connective Tissue DiseasesSkin ManifestationsSigns and SymptomsPathological Conditions, Signs and SymptomsRenal Insufficiency, ChronicRenal InsufficiencyKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesChronic DiseaseDisease AttributesPathologic Processes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 25, 2016

First Posted

March 2, 2016

Study Start

February 1, 2016

Primary Completion

August 1, 2016

Study Completion

December 1, 2016

Last Updated

April 20, 2018

Record last verified: 2018-04

Locations