NCT02610140

Brief Summary

The main purpose of the 15743 study is to assess efficacy and safety of anetumab ravtansine versus vinorelbine in progression free survival in patients with stage IV mesothelin overexpressing malignant pleural mesothelioma (MPM). 210 eligible patients will be randomized to receive either anetumab ravtansine every three weeks or weekly vinorelbine. Treatment will continue until centrally confirmed disease progression or until another criterion is met for withdrawal from the study. Patients will enter follow up phase to capture safety and endpoint data as required. Efficacy will be measured by evaluating progression free survival from randomization. Radiological tumor assessments will be performed at defined time points until the patient's disease progresses. Blood samples will be collected for safety, pharmacokinetic and biomarker analysis. Archival or fresh biopsy tissue may also be collected for central pathology review and biomarkers.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
248

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Dec 2015

Typical duration for phase_2

Geographic Reach
14 countries

75 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 9, 2015

Completed
11 days until next milestone

First Posted

Study publicly available on registry

November 20, 2015

Completed
13 days until next milestone

Study Start

First participant enrolled

December 3, 2015

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 31, 2017

Completed
2.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

September 6, 2019

Completed
11 months until next milestone

Results Posted

Study results publicly available

July 17, 2020

Completed
Last Updated

November 4, 2020

Status Verified

October 1, 2020

Enrollment Period

1.5 years

First QC Date

November 9, 2015

Results QC Date

May 22, 2020

Last Update Submit

October 28, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • Progression-free Survival (PFS), [95% CI]

    Progression-free survival (PFS), defined as time from randomization until disease progression according to mRECIST (Modified Response Evaluation Criteria in Solid Tumors) for Malignant pleural mesothelioma (MPM) per blinded central radiology review, or death. Only descriptive analysis of OS was repeated in the follow-up period.

    From randomization till approximately 117 PFS events observed, up to approx. 30 months (data cut-off: 31-May-2017)

Secondary Outcomes (12)

  • Overall Survival (OS), [95% CI]

    Up to approx. 40 months (data cut-off: 06-Apr-2018) - Time from randomization until death from any cause; one-sided log-rank test stratified by time to progression (TTP) on first line treatment.

  • Objective Response Rate (ORR)

    up to approx. 30 months (data cut-off: 31-May-2017) - Time from randomization until death from any cause.

  • Disease Control Rate (DCR)

    Up to approx. 40 months (data cut-off: 06-Apr-2018) - Time from randomization until death from any cause.

  • Duration of Response (DOR)

    Up to approx. 40 months (data cut-off: 06-Apr-2018) - Time from randomization until death from any cause.

  • Durable Response Rate (DRR)

    Up to approx. 40 months (data cut-off: 06-Apr-2018) - Time from randomization until death from any cause.

  • +7 more secondary outcomes

Study Arms (2)

BAY94-9343

EXPERIMENTAL

Drug Anetumab ravtansine given Intravenously (IV)

Drug: Anetumab ravtansine (BAY94-9343)

Vinorelbine

ACTIVE COMPARATOR

Drug Vinorelbine given Intravenously

Drug: Vinorelbine

Interventions

Starting dose: 6.5 mg/kg administered as IV infusion over 1 h every 3 weeks until disease progression or treatment withdrawal for any reason. Dose reductions are permitted.

BAY94-9343

Starting dose: 30mg/m\^2 administered as an IV infusion over 6 to 10 min every week until disease progression or treatment withdrawal for any reason. Dose reductions are permitted per standard practise.

Vinorelbine

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histological documentation of malignant pleural mesothelioma (MPM) overexpressing mesothelin
  • Unresectable locally advanced or metastatic MPM after locally confirmed progression on 1st line treatment with platinum in combination with pemetrexed.
  • Patients must have measurable disease
  • Eastern Cooperative Oncology Group Performance Status (ECOG PS) of 0 or 1
  • Life expectancy of at least 3 months.
  • Adequate bone marrow, liver and renal function
  • Left ventricular ejection fraction (LVEF) ≥ 50% or the lower limit of normal (LLN) according to local institution ranges of normality.

You may not qualify if:

  • More than 1 previous systemic anti-cancer therapy line
  • Patients with corneal epitheliopathy or any eye disorder that may predispose the patients to this condition at the discretion of the investigator in consultation with the ophthalmologist.
  • Brain metastases, meningeal tumours or other metastases in the central nervous system
  • Evidence of history of bleeding diathesis.
  • Ongoing or active infection (bacterial, fungal, or viral) of National Cancer Institute's Common Terminology Criteria for Adverse Events (NCI-CTCAE) version 4.03 Grade \> 2.
  • Pre-existing cardiac conditions

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (75)

Unknown Facility

La Jolla, California, 92093-1503, United States

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Aurora, Colorado, 80045, United States

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Norwich, Connecticut, 06360, United States

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Tampa, Florida, 33612, United States

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Chicago, Illinois, 60612, United States

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Chicago, Illinois, 60637, United States

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New Orleans, Louisiana, 70121, United States

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Bethesda, Maryland, 20814, United States

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Rochester, Minnesota, 55905, United States

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Buffalo, New York, 14263-0001, United States

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New York, New York, 10016, United States

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Durham, North Carolina, 27710, United States

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Cleveland, Ohio, 44195, United States

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Dallas, Texas, 75251, United States

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Houston, Texas, 77030, United States

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St Leonards, New South Wales, 2065, Australia

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Woolloogabba, Queensland, 4102, Australia

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Adelaide, South Australia, 5043, Australia

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Richmond, Victoria, 3122, Australia

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Nedlands, Western Australia, 6009, Australia

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Bruxelles - Brussel, 1200, Belgium

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Edegem, 2650, Belgium

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Ghent, 9000, Belgium

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Leuven, 3000, Belgium

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Liège, 4000, Belgium

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Sint-Niklaas, 9100, Belgium

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Calgary, Alberta, T2N 4N2, Canada

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Hamilton, Ontario, L8V 5C2, Canada

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London, Ontario, N6A 4L6, Canada

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Toronto, Ontario, M5G 2M9, Canada

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Helsinki, 00290, Finland

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Turku, 20520, Finland

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Vaasa, 65130, Finland

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Bordeaux, 33076, France

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Caen, 14076, France

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Lille, 59037, France

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Marseille, 13915, France

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Paris, 75018, France

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Paris, 75020, France

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Pierre-Bénite, 69495, France

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Pordenone, Friuli Venezia Giulia, 33081, Italy

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Bergamo, Lombardy, 24125, Italy

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Milan, Lombardy, 20089, Italy

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Milan, Lombardy, 20133, Italy

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Monza Brianza, Lombardy, 20900, Italy

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Turin, Piedmont, 10043, Italy

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Siena, Tuscany, 53100, Italy

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Amsterdam, 1066 CX, Netherlands

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Rotterdam, 3015 CE, Netherlands

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Gdansk, 80-952, Poland

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Krakow, 31-202, Poland

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Krakow, 31-501, Poland

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Szczecin, 70-891, Poland

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Omsk, 644013, Russia

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Yekaterinburg, 620036, Russia

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Seoul, 05505, South Korea

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Seoul, 06351, South Korea

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A Coruña, 15006, Spain

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Alicante, 03010, Spain

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Barcelona, 08035, Spain

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Madrid, 28041, Spain

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Málaga, 29010, Spain

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Adana, 01330, Turkey (Türkiye)

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Ankara, 06100, Turkey (Türkiye)

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Eskişehir, 26480, Turkey (Türkiye)

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Istanbul, 34899, Turkey (Türkiye)

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Malatya, 44280, Turkey (Türkiye)

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Yenimahalle, 06200, Turkey (Türkiye)

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Plymouth, Devon, PL6 8DH, United Kingdom

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Maidstone, Kent, ME16 9QQ, United Kingdom

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Leicester, Leicestershire, LE1 5WW, United Kingdom

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Glasgow, G12 0YN, United Kingdom

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London, SE1 9RT, United Kingdom

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Manchester, M23 9LT, United Kingdom

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Newcastle upon Tyne, NE7 7DN, United Kingdom

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Related Publications (1)

  • Kindler HL, Novello S, Bearz A, Ceresoli GL, Aerts JGJV, Spicer J, Taylor P, Nackaerts K, Greystoke A, Jennens R, Calabro L, Burgers JA, Santoro A, Cedres S, Serwatowski P, Ponce S, Van Meerbeeck JP, Nowak AK, Blumenschein G Jr, Siegel JM, Kasten L, Kochert K, Walter AO, Childs BH, Elbi C, Hassan R, Fennell DA. Anetumab ravtansine versus vinorelbine in patients with relapsed, mesothelin-positive malignant pleural mesothelioma (ARCS-M): a randomised, open-label phase 2 trial. Lancet Oncol. 2022 Apr;23(4):540-552. doi: 10.1016/S1470-2045(22)00061-4.

Related Links

MeSH Terms

Conditions

Mesothelioma

Interventions

anetumab ravtansineVinorelbine

Condition Hierarchy (Ancestors)

AdenomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsNeoplasms, Mesothelial

Intervention Hierarchy (Ancestors)

Vinca AlkaloidsSecologanin Tryptamine AlkaloidsIndole AlkaloidsAlkaloidsHeterocyclic CompoundsIndolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingIndolizidinesIndolizines

Results Point of Contact

Title
Therapeutic Area Head
Organization
Bayer AG

Study Officials

  • Bayer Study Director

    Bayer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 9, 2015

First Posted

November 20, 2015

Study Start

December 3, 2015

Primary Completion

May 31, 2017

Study Completion

September 6, 2019

Last Updated

November 4, 2020

Results First Posted

July 17, 2020

Record last verified: 2020-10

Locations