NCT02576301

Brief Summary

Phase 1 will investigate maximum tolerated dose of OXi4503 as a single agent and in combination with intermediate-dose cytarabine in subjects with relapsed/refractory AML or MDS. Phase 2 will investigate overall response rate of OXi4503 in combination with intermediate-dose cytarabine in 1) subjects with MDS after failure of 1 prior hypomethylating agent (Arm A) and 2) subjects with relapsed and refractory AML after treatment failure of up to 1 prior chemotherapy regimen (Arm B).

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
105

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Oct 2015

Longer than P75 for phase_1

Geographic Reach
1 country

4 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2015

Completed
12 days until next milestone

First Submitted

Initial submission to the registry

October 13, 2015

Completed
2 days until next milestone

First Posted

Study publicly available on registry

October 15, 2015

Completed
4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2019

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2020

Completed
Last Updated

June 4, 2018

Status Verified

September 1, 2017

Enrollment Period

4 years

First QC Date

October 13, 2015

Last Update Submit

June 1, 2018

Conditions

Keywords

AMLMDS

Outcome Measures

Primary Outcomes (2)

  • Phase 1b:MTD of OXi4503 as a single agent and in combination with intermediate-dose cytarabine in subjects with relapsed/refractory AML or MDS

    1 year

  • Phase 2: Overall response rate of OXi4503 in combination with intermediate-dose cytarabine in subjects with MDS after failure of 1 prior hypomethylating agent (Arm A), and subjects with relapsed and refractory AML after treatment failure of up

    2 years

Study Arms (4)

Phase 2 AML

EXPERIMENTAL

OXi4503 at MTD plus cytarabine 1g/m2/day

Drug: Phase 2 - OXi4503 + cytarabine

Phase 2 MDS

EXPERIMENTAL

OXi4503 at MTD plus cytarabine 1g/m2/day

Drug: Phase 2 - OXi4503 + cytarabine

OXi4503 dose escalation

EXPERIMENTAL

MTD for OXi4503 will be determined

Drug: Phase 1 - OXi4503

OXi4503 + cytarabine dose escalation

EXPERIMENTAL

MTD of the combination of OXi4503 + cytarbine will be determined

Drug: Phase 1 - OXi4503 + cytarabine

Interventions

Determination of MTD of OXi4503

Also known as: CA1P, combretastatin A1-diphosphate
OXi4503 dose escalation

Determination of MTD of the combination of OXi4503 + cytarabine

Also known as: CA1P, combretastatin A1-diphosphate
OXi4503 + cytarabine dose escalation

Safety and efficacy of the combination of OXi4503 + cytarabine in subjects with AML

Also known as: CA1P, combretastatin A1-diphosphate
Phase 2 AML

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Provide informed consent
  • ≥ 18 years of age
  • Phase 1 (dose escalation) subjects must have either:
  • AML that has failed to achieve complete remission or morphologic complete remission or
  • MDS - Marrow blasts must be \> 5% and disease failed at least 1 prior hypomethylating agent
  • Phase 2 (expansion) subjects must have either MDS or relapsed/refractory AML
  • Eastern Cooperative Oncology Group performance status 0, 1, or 2
  • Total bilirubin ≤ 2
  • Serum aspartate aminotransferase (AST) and alanine aminotransferase (ALT) levels ≤ 2.5 times upper limit of normal (ULN)
  • Serum creatinine \< 2.5 times ULN
  • Prothrombin time (PT)/international normalized ratio and (PTT) in normal range ± 25%
  • Women of child-bearing potential
  • Males with female partners of child-bearing potential must agree to use physician-approved contraceptive methods

You may not qualify if:

  • Acute promyelocytic leukemia
  • Absolute peripheral blood myeloblast count greater than 20,000/mm3
  • Uncontrolled hypertension
  • History of congenital long QT syndrome or torsades de pointes
  • Pathologic bradycardia or heart block
  • Prolonged baseline QTc
  • Hiistory of ventricular arrhythmia
  • Myocardial infarction and/or new ST elevation
  • Any history of hemorrhagic stroke
  • Symptomatic congestive heart failure
  • Major hemorrhagic event within 28 days
  • Suggestive central nervous system involvement with leukemia
  • Any open wound
  • Pregnant and nursing subjects are excluded
  • Treatment with any anticancer therapy
  • +2 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (4)

David Geffen School of Medicine at UCLA

Los Angeles, California, 90095, United States

RECRUITING

University of Florida

Gainesville, Florida, 32610, United States

RECRUITING

University of Miami Sylvester Comprehensive Cancer Center

Miami, Florida, 33136, United States

RECRUITING

University of Kansas Cancer Center and Medical Pavilion

Westwood, Kansas, 66205, United States

RECRUITING

Related Publications (1)

  • Johnson SP, Ogunlade O, Lythgoe MF, Beard P, Pedley RB. Longitudinal Photoacoustic Imaging of the Pharmacodynamic Effect of Vascular Targeted Therapy on Tumors. Clin Cancer Res. 2019 Dec 15;25(24):7436-7447. doi: 10.1158/1078-0432.CCR-19-0360. Epub 2019 Sep 24.

MeSH Terms

Conditions

Leukemia, Myeloid, AcuteMyelodysplastic Syndromes

Interventions

Cytarabine

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesBone Marrow Diseases

Intervention Hierarchy (Ancestors)

CytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsArabinonucleosidesNucleosidesNucleic Acids, Nucleotides, and Nucleosides

Central Study Contacts

Rachel Couchenour

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 13, 2015

First Posted

October 15, 2015

Study Start

October 1, 2015

Primary Completion

October 1, 2019

Study Completion

October 1, 2020

Last Updated

June 4, 2018

Record last verified: 2017-09

Locations