NCT02544633

Brief Summary

MGCD265 is an orally administered receptor tyrosine kinase inhibitor that targets MET and other receptors. This study is a Phase 2 trial of MGCD265 in patients with locally advanced, unresectable or metastatic non-small cell lung cancer (NSCLC) that has activating genetic changes of the MET gene (mutation or amplification \[increase number of gene copies\]). Testing for tumor gene changes can be performed in tumor tissue or blood samples. Patients must have previously received treatment with chemotherapy. The number of patients to be enrolled will depend on how many enrolled patients experience tumor size reduction. MGCD265 will be administered orally, twice daily. The study is designed to evaluate whether the number of patients experiencing tumor size reduction is substantially higher than would be expected with other available treatments.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
68

participants targeted

Target at P50-P75 for phase_2 nonsmall-cell-lung-cancer

Timeline
Completed

Started Oct 2015

Geographic Reach
9 countries

94 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 4, 2015

Completed
5 days until next milestone

First Posted

Study publicly available on registry

September 9, 2015

Completed
22 days until next milestone

Study Start

First participant enrolled

October 1, 2015

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 30, 2018

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2019

Completed
8 months until next milestone

Results Posted

Study results publicly available

September 10, 2019

Completed
Last Updated

March 4, 2020

Status Verified

February 1, 2020

Enrollment Period

2.6 years

First QC Date

September 4, 2015

Results QC Date

April 30, 2019

Last Update Submit

February 19, 2020

Conditions

Keywords

MiratiMGCD265METNSCLC

Outcome Measures

Primary Outcomes (1)

  • Objective Response Rate

    Objective disease response is defined as the percent of patients documented by investigator assessment to have a confirmed Complete Response (CR) or Partial Response (PR) in accordance with the Response Evaluation Criteria in Solid Tumors (RECIST 1.1) for target and non-target lesions as assessed by CT or MRI. CR is defined as complete disappearance of all target lesions with the exception of nodal disease; PR is defined as \>=30% decrease under baseline of the sum of diameters of all target measurable lesions; Stable Disease (SD) is concluded when the response does not qualify for CR, PR or Progression; Progressive Disease (PD) is defined as a 20% increase in the sum of diameters of target measurable lesions above the smallest sum observed with a minimum absolute increase of 5 mm, or unequivocal progression of pre-existing non-target lesions.

    Up to 3 months

Secondary Outcomes (16)

  • Duration of Response

    From date of the first documentation of objective tumor response (CR or PR) to the first documentation of Objective Progression of Disease (PD) or to death due to any cause in the absence of documented PD, assessed up to 24 months.

  • Progression Free Survival

    The time from date of first study treatment to first PD or death due to any cause in the absence of documented PD, up to 24 months.

  • 1-Year Survival Rate

    From date of first study treatment to death due to any cause, assessed up to 12 months

  • Overall Survival

    From date of first study treatment to death due to any cause, assessed up to 24 months.

  • Number of Patients Experiencing Treatment-emergent Adverse Events

    Date of first dose to 28 days after the last dose, up to an average of 5.1 months on treatment.

  • +11 more secondary outcomes

Study Arms (4)

Arm 1

EXPERIMENTAL

MGCD265 in patients with MET activating mutations in tumor tissue

Drug: MGCD265

Arm 2

EXPERIMENTAL

MGCD265 in patients with MET gene amplifications in tumor tissue

Drug: MGCD265

Arm 3

EXPERIMENTAL

MGCD265 in patients with MET activating mutations in blood (circulating tumor DNA)

Drug: MGCD265

Arm 4

EXPERIMENTAL

MGCD265 in patients with MET gene amplifications in blood (circulating tumor DNA)

Drug: MGCD265

Interventions

MGCD265 is a small molecule multi-targeted receptor tyrosine kinase inhibitor

Arm 1Arm 2Arm 3Arm 4

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of non-small cell lung cancer
  • Metastatic or locally advanced disease
  • Prior platinum chemotherapy or immunotherapy
  • Test result showing genetic change in MET tumor gene
  • At least one tumor that can be measured on a radiographic scan

You may not qualify if:

  • Prior treatment with inhibitor of MET or HGF
  • Prior positive test for EGFR mutation or ALK gene rearrangement
  • Uncontrolled tumor in the brain

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (94)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Clearview Cancer Institute

Huntsville, Alabama, 35805, United States

Location

Fowler Family Center for Cancer Care

Jonesboro, Arkansas, 72401, United States

Location

Providence Saint Joseph Medical Center

Burbank, California, 91505, United States

Location

Saint Joseph Heritage Healthcare

Fullerton, California, 92835-3825, United States

Location

University of California San Diego

La Jolla, California, 92121, United States

Location

Loma Linda University Medical Center

Loma Linda, California, 92354, United States

Location

University of California, San Francisco

San Francisco, California, 94143, United States

Location

Innovative Clinical Reseach Institute

Whittier, California, 90603, United States

Location

St. Mary's Regional Cancer Center

Grand Junction, Colorado, 81501, United States

Location

Eastern Connecticut Hematology and Oncology Associates

Norwich, Connecticut, 06360, United States

Location

Georgetown University Medical Center

Washington D.C., District of Columbia, 20007, United States

Location

Boca Raton Regional Hospital - Eugene M. & Christine E. Lynn Cancer Institute

Boca Raton, Florida, 33486, United States

Location

Sylvester Comprehensive Cancer Center

Deerfield Beach, Florida, 33442-7753, United States

Location

Florida Cancer Specialists

Fort Myers, Florida, 33916, United States

Location

Mount Sinai Medical Center

Miami Beach, Florida, 33140, United States

Location

Memorial Hospital West

Pembroke Pines, Florida, 33028, United States

Location

Florida Cancer Specialists

St. Petersburg, Florida, 33705, United States

Location

Robert H. Lurie Comprehensive Cancer Center of Northwestern University

Chicago, Illinois, 60611, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

NorthShore University HealthSystem

Evanston, Illinois, 60201, United States

Location

Loyola University Medical Center

Maywood, Illinois, 60153, United States

Location

Goshen Center for Cancer Care

Goshen, Indiana, 46526, United States

Location

Mercy Cancer Center

Mason City, Iowa, 50401, United States

Location

Oncology-Hematology Associates, PA

Danville, Kentucky, 40422-2534, United States

Location

Lexington Oncology Associates, LLC

Lexington, Kentucky, 40503, United States

Location

Kentuckyone Health Cancer and Blood Speacialists

Louisville, Kentucky, 40245, United States

Location

Christus Saint Frances Cabrini Hospital

Alexandria, Louisiana, 71301, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

Henry Ford Health System

Detroit, Michigan, 48202, United States

Location

University of Minnesota Masonic Cancer Center

Minneapolis, Minnesota, 55455, United States

Location

Washington University

St Louis, Missouri, 63110, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

The University of New Mexico Cancer Research and Treatment Center

Albuquerque, New Mexico, 87102, United States

Location

Queens Cancer Center

Jamaica, New York, 11430, United States

Location

Clinical Research Alliance

New York, New York, 10021, United States

Location

Montefiore Medical Center

The Bronx, New York, 10467, United States

Location

University Hospitals of Cleveland

Cleveland, Ohio, 44106, United States

Location

Fox Chase Cancer Center

Philadelphia, Pennsylvania, 19111, United States

Location

Guthrie Cancer Center

Sayre, Pennsylvania, 18840, United States

Location

Greenville Health System

Greenville, South Carolina, 29615, United States

Location

Sarah Cannon Research Institute

Nashville, Tennessee, 37203, United States

Location

Mary Crowley Cancer Research Centers

Dallas, Texas, 752010, United States

Location

MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Seattle Cancer Care Alliance

Seattle, Washington, 98109, United States

Location

Concord Repatriation General Hospital

Concord, New South Wales, 2139, Australia

Location

Saint George Hospital

Kogarah, New South Wales, 2217, Australia

Location

Royal North Shore Hospital

Saint Leonards, New South Wales, 2065, Australia

Location

Royal Hobart Hospital

Hobart, Tasmania, 7000, Australia

Location

Monash Cancer Centre

Clayton, Victoria, 3165, Australia

Location

Austin Health

Heidelberg, Victoria, 3084, Australia

Location

Flinders Medical Centre

Bedford Park, 5042, Australia

Location

Monash Health

Clayton, 3165, Australia

Location

The Tweed Hospital

Tweed Heads, 2485, Australia

Location

Princess Alexandra Hospital

Woolloongabba, 4102, Australia

Location

McGill University Health Centre

Montreal, H2W 1S6, Canada

Location

Szent Borbála Kórház

Tatabánya, Komárom-Esztergom, 2800, Hungary

Location

Országos Korányi TBC és Pulmonológiai Intézet

Budapest, 1121, Hungary

Location

Országos Onkológiai Intézet

Budapest, 1122, Hungary

Location

Semmelweis Egyetem

Budapest, 1125, Hungary

Location

Azienda Ospedaliero-Universitaria Careggi

Florence, 50139, Italy

Location

Ospedale Unico Versilia

Lucca, 55041, Italy

Location

IRCCS Ospedale San Raffaele

Milan, 20132, Italy

Location

Istituto Europeo di Oncologia Milano

Milan, 20132, Italy

Location

Ospedale San Raffaele

Milan, 20132, Italy

Location

Azienda Unità Sanitaria Locale di Piacenza-Ospedale Guglielmo da Saliceto

Piacenza, 29100, Italy

Location

Azienda Unita Sanitaria Locale di Ravenna

Ravenna, 48121, Italy

Location

Azienda Ospedaliera Città della Salute e della Scienza di Torino

Torino, 10126, Italy

Location

Med Polonia Sp. z o.o.

Poznan, Greater Poland Voivodeship, 60-693, Poland

Location

Uniwersyteckie Centrum Kliniczne

Gdansk, Pomeranian Voivodeship, 80-952, Poland

Location

Samodzielny Publiczny Zespól Gruzlicy i Chorób Pluc w Olsztynie

Olsztyn, Warmian-Masurian Voivodeship, 10-357, Poland

Location

National Cancer Center

Goyang-si, Gyeonggi-do, 410-769, South Korea

Location

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, 463-707, South Korea

Location

Saint Vincent Hospital

Suwon, Gyeonggi-do, 442-723, South Korea

Location

The Catholic University of Korea Saint Vincent's Hospital

Suwon, Gyeonggi-do, 442-723, South Korea

Location

Chungbuk National University Hospital

Cheongju-si, North Chungcheong, 361-271, South Korea

Location

Keimyung University Dongsan Medical Center

Daegu, 700-712, South Korea

Location

Seoul National University Hospital

Seoul, 110-744, South Korea

Location

Severance Hospital, Yonsei University Health System

Seoul, 120-752, South Korea

Location

Veterans Health Service Medical Center

Seoul, 134-791, South Korea

Location

Samsung Medical Center

Seoul, 135-710, South Korea

Location

Asan Medical Center

Seoul, 138-736, South Korea

Location

National Cheng Kung University

Tainan, Tainan CITY, 70403, Taiwan

Location

Chi Mei Hospital Liouying

Tainan, Tainan, 73657, Taiwan

Location

Hualien Tzu Chi Hospital, Buddhist Tzu Chi Medical Foundation

Hualien City, 970, Taiwan

Location

Kaohsiung Medical University Hospital

Kaohsiung City, 807, Taiwan

Location

Taichung Veterans General Hospital

Taichung, 40705, Taiwan

Location

Taipei Veterans General Hospital

Taipei, 11217, Taiwan

Location

North Bristol NHS Trust, Westbury on Trym

Bristol, England, BS10 5NB, United Kingdom

Location

University College London Hospitals NHS Foundation Trust

London, England, NW1 2PQ, United Kingdom

Location

East and North Hertordshire NHS Trust

Northwood, England, HA6 2RN, United Kingdom

Location

Royal Free London NHS Foundation Trust

London, NW3 2QG, United Kingdom

Location

Related Publications (2)

  • Hong DS, Cappuzzo F, Chul Cho B, Dowlati A, Hussein M, Kim DW, Percent I, Christensen JG, Morin J, Potvin D, Faltaos D, Tassell V, Der-Torossian H, Chao R. Phase II study investigating the efficacy and safety of glesatinib (MGCD265) in patients with advanced NSCLC containing MET activating alterations. Lung Cancer. 2024 Apr;190:107512. doi: 10.1016/j.lungcan.2024.107512. Epub 2024 Feb 22.

  • Kollmannsberger C, Hurwitz H, Bazhenova L, Cho BC, Hong D, Park K, Reckamp KL, Sharma S, Der-Torossian H, Christensen JG, Faltaos D, Potvin D, Tassell V, Chao R, Shapiro GI. Phase I Study Evaluating Glesatinib (MGCD265), An Inhibitor of MET and AXL, in Patients with Non-small Cell Lung Cancer and Other Advanced Solid Tumors. Target Oncol. 2023 Jan;18(1):105-118. doi: 10.1007/s11523-022-00931-9. Epub 2022 Dec 2.

MeSH Terms

Conditions

Carcinoma, Non-Small-Cell Lung

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract Diseases

Limitations and Caveats

Early closure of the study is due to sponsor portfolio prioritization and not due to any patient safety issues.

Results Point of Contact

Title
Vanessa Tassell, Vice President, Clinical Science
Organization
Mirati Therapeutics, Inc.

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 4, 2015

First Posted

September 9, 2015

Study Start

October 1, 2015

Primary Completion

April 30, 2018

Study Completion

January 1, 2019

Last Updated

March 4, 2020

Results First Posted

September 10, 2019

Record last verified: 2020-02

Data Sharing

IPD Sharing
Will not share

Locations