NCT02511431

Brief Summary

Background: \- Chronic hepatitis D is a liver disease caused by the hepatitis D virus (HDV). It can be severe and progressive. Most people with hepatitis D will develop scarring and damage to the liver. There is no FDA approved drug to treat chronic hepatitis D. Researchers want to know if the drugs lonafarnib and ritonavir can help people with chronic hepatitis D. Objective: \- To find out if treatment of hepatitis D with lonafarnib and ritonavir is safe and effective. Eligibility: \- People 18 years of age and older with chronic hepatitis D. They must not have HIV or other major illnesses. Design:

  • Participants will be screened with medical history, physical exams, and blood tests.
  • Participants will have 24 weeks of treatment. They will then have 24 weeks of follow-up.
  • Participants will be in 1 of 6 treatment groups. Those in each group will receive different doses of the study drugs. Some groups will start with placebo but will receive treatment after 3 months of placebo.
  • Participants will also take drugs to treat hepatitis B.
  • Participants will have many visits. These will include:
  • One three-day stay at the Clinical Center
  • Physical exams
  • EKG: small sticky patches will be put on the chest, arms, and legs to trace heart rhythm
  • Ultrasounds of the abdomen
  • Urine and blood tests
  • Stool samples
  • Eye exams
  • Evaluations by a reproductive endocrinologist (women) or urologist (men). Men may provide a sperm sample (optional).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
22

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Jul 2015

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 29, 2015

Completed
Same day until next milestone

Study Start

First participant enrolled

July 29, 2015

Completed
1 day until next milestone

First Posted

Study publicly available on registry

July 30, 2015

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 23, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 23, 2017

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

May 24, 2018

Completed
Last Updated

September 25, 2018

Status Verified

February 23, 2017

Enrollment Period

1.6 years

First QC Date

July 29, 2015

Results QC Date

April 24, 2018

Last Update Submit

August 27, 2018

Conditions

Keywords

Delta HepatitisHepatitis DLiver DiseaseHepatitis D VirusChronic Hepatitis

Outcome Measures

Primary Outcomes (2)

  • Number of Participants With Decline of Hepatitis Delta Virus (HDV) RNA Quantitative Measurements of >2 Logs From Baseline at 12 Weeks of Treatment

    The number of participants who experienced a \> 2 log IU/mL decline in serum HDV RNA at 12 weeks of treatment

    12 weeks

  • Number of Participants With Decline of HDV RNA Quantitative Measurement of > 2 Logs From Baseline at 24 Weeks of Treatment

    The number of participants who experienced a \> 2 log IU/mL decline in serum HDV RNA levels at 24 weeks of treatment

    24 weeks

Study Arms (6)

Group 1

EXPERIMENTAL

Lonafarnib/Ritonavir at 50 mg/100 mg daily for 24 weeks followed by 24 weeks of off therapy follow-up.

Drug: LonafarnibDrug: Ritonavir

Group 2

EXPERIMENTAL

Lonafarnib/Ritonavir at 75 mg/100 mg daily for 24 weeks followed by 24 weeks of off therapy follow-up.

Drug: LonafarnibDrug: Ritonavir

Group 3

EXPERIMENTAL

Lonafarnib/Ritonavir at 100 mg/100 mg daily for 24 weeks followed by 24 weeks of off therapy follow-up.

Drug: LonafarnibDrug: Ritonavir

Group 4

EXPERIMENTAL

Placebo for 12 weeks then Lonafarnib/Ritonavir at 50 mg/100 mg daily for 12 weeks followed by 24 weeks of off therapy follow-up.

Drug: LonafarnibDrug: RitonavirOther: Placebo

Group 5

EXPERIMENTAL

Placebo for 12 weeks then Lonafarnib/Ritonavir at 75 mg/100 mg daily for 12 weeks followed by 24 weeks of off therapy follow-up.

Drug: LonafarnibDrug: RitonavirOther: Placebo

Group 6

EXPERIMENTAL

Placebo for 12 weeks then Lonafarnib/Ritonavir at 100 mg/100 mg daily for 12 weeks followed by 24 weeks of off therapy follow-up.

Drug: LonafarnibDrug: RitonavirOther: Placebo

Interventions

prenylation inhibitor to be administered daily at doses of 50 mg, 75 mg or 100 mg.

Group 1Group 2Group 3Group 4Group 5Group 6

FDA approved drug for use of boosting other drugs. Will be used to boost Lonafarnib as they both use the same cytochrome P450 system. Will be administered at 100 mg daily.

Group 1Group 2Group 3Group 4Group 5Group 6
PlaceboOTHER

Placebo

Group 4Group 5Group 6

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age 18 years or above, male or female.
  • Serum alanine or aspartate aminotransferase (ALT or AST) activities above the upper limit of normal (ALT greater than or equal to 20 or AST greater than or equal to 20 U/L in females and ALT greater than or equal to 30 or AST greater than or equal to 30 U/L in males) on an average of three determinations taken during the previous 6 months at the NIH clinical center. The mean of the three determinations will be defined as baseline levels.
  • Presence of anti-HDV in serum.
  • Presence of quantifiable HDV RNA in serum.

You may not qualify if:

  • Pregnancy, active breast-feeding, or inability to practice adequate contraception, in women of childbearing potential or in spouses of such women. Adequate contraception is defined as vasectomy in men, tubal ligation in women, or use of two barrier methods such as condoms and spermicide combination, birth control pills, an intrauterine device, Depo-Provera, or Norplant. In total, the participant and their partner must utilize two forms of contraception and one method must include a barrier method.
  • Significant systemic or major illnesses other than liver disease, including, but not limited to, congestive heart failure, renal failure (eGFR \<50 ml/min), organ transplantation, serious psychiatric disease or depression (only if felt to be at high risk by the NIH psychiatric consultation service), and active coronary artery disease.
  • Systemic immunosuppressive therapy within the previous 2 months.
  • Evidence of another form of liver disease in addition to viral hepatitis (for example autoimmune liver disease, primary biliary cirrhosis, primary sclerosing cholangitis, Wilson disease, alcoholic liver disease, nonalcoholic steatohepatitis (but not steatosis), hemochromatosis, or alpha-1-antitrypsin deficiency).
  • Active substance abuse, such as alcohol, inhaled or injection drugs within the previous year.
  • Evidence of hepatocellular carcinoma.
  • Evidence of concurrent hepatitis C infection with positive serum hepatitis c virus (HCV) RNA.
  • Any experimental therapy or pegylated interferon therapy within 6 months prior to enrollment.
  • Diagnosis of malignancy in the five years prior to the enrollment with exception granted to superficial dermatologic malignancies.
  • Evidence of HIV co-infection; HIV 1/2 viral RNA or antigen on serum testing.
  • Concurrent usage of statins as these drugs inhibits mevalonate synthesis, which reduces protein prenylation.
  • Concurrent usage of moderate and strong cytochrome p450, family 3, subfamily A (CYP3A) inhibitors and inducers.
  • Use of any prescription, nonprescription or natural medicine (herbal) medications unless the use of medication is medically necessary with appropriate monitoring.
  • Concurrent usage of alpha 1 adrenoreceptor antagonist, antiarrhythmic, pimozide, sildenafil, sedative and hypnotics, ergot and St. John s Wort due to possible effect of ritonavir on hepatic metabolism of these drugs resulting in potentially life threatening side effects.
  • Clinically significant baseline EKG abnormalities.
  • +4 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

National Institutes of Health Clinical Center, 9000 Rockville Pike

Bethesda, Maryland, 20892, United States

Location

Related Publications (1)

  • Kefalakes H, Koh C, Sidney J, Amanakis G, Sette A, Heller T, Rehermann B. Hepatitis D Virus-Specific CD8+ T Cells Have a Memory-Like Phenotype Associated With Viral Immune Escape in Patients With Chronic Hepatitis D Virus Infection. Gastroenterology. 2019 May;156(6):1805-1819.e9. doi: 10.1053/j.gastro.2019.01.035. Epub 2019 Jan 18.

Related Links

MeSH Terms

Conditions

Hepatitis DLiver DiseasesHepatitis, Chronic

Interventions

lonafarnibRitonavir

Condition Hierarchy (Ancestors)

Hepatitis, Viral, HumanVirus DiseasesInfectionsRNA Virus InfectionsHepatitisDigestive System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

ThiazolesSulfur CompoundsOrganic ChemicalsAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Results Point of Contact

Title
Christopher Koh, MD
Organization
NIDDK

Study Officials

  • Theo Heller, M.D.

    National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
NIH
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 29, 2015

First Posted

July 30, 2015

Study Start

July 29, 2015

Primary Completion

February 23, 2017

Study Completion

February 23, 2017

Last Updated

September 25, 2018

Results First Posted

May 24, 2018

Record last verified: 2017-02-23

Locations