NCT02436096

Brief Summary

The use of low-dose CBP dosed nightly at bedtime for FM was supported by the results of Tonix' TNX-CY-F202 Phase 2b study (also referred to as the BESTFIT Study). The TNX-CY-F202 study provided evidence that TNX-102 SL 2.8 mg dosed nightly results in beneficial effects upon pain, sleep and other FM symptomatology. The present trial is designed to assess the safety and efficacy of TNX-102 SL 2.8 mg tablets, taken daily at bedtime over 12 weeks to treat fibromyalgia.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
519

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Apr 2015

Geographic Reach
1 country

35 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 2015

Completed
27 days until next milestone

First Submitted

Initial submission to the registry

April 28, 2015

Completed
8 days until next milestone

First Posted

Study publicly available on registry

May 6, 2015

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2016

Completed
8.4 years until next milestone

Results Posted

Study results publicly available

February 7, 2025

Completed
Last Updated

February 7, 2025

Status Verified

February 1, 2025

Enrollment Period

1.4 years

First QC Date

April 28, 2015

Results QC Date

August 21, 2024

Last Update Submit

February 5, 2025

Conditions

Keywords

PainSleep

Outcome Measures

Primary Outcomes (1)

  • Proportion of Patients With ≥30% Pain Improvement

    The primary efficacy endpoint is the proportion of patients with a ≥30% improvement (responder criteria) from baseline to Week 12 in the weekly mean of the daily self-reported 24-hour recall average pain intensity score using an 11-point (0-10) NRS. Scores range from 0 (no pain) to 10 (worst possible pain).

    Day 1, Week 12

Secondary Outcomes (7)

  • Patient's Global Impression of Change (PGIC)

    Week 12

  • Change From Baseline to Week 12 in the Fibromyalgia Impact Questionnaire - Revised (FIQR) Symptoms Domain Score

    Day 1, Week 12

  • Change From Baseline to Week 12 in the FIQR Function Domain Score

    Day 1, Week 12

  • Patient Reported Outcomes Measurement System (PROMIS) Sleep Disturbance

    Day 1, Week 12

  • Weekly Average of Daily Sleep Quality Diary

    Baseline (Day -7 to Day -1), Week 12

  • +2 more secondary outcomes

Study Arms (2)

TNX-102 SL Tablet, 2.8 mg

EXPERIMENTAL

1 x TNX-102 SL 2.8mg Tablet taken sublingually each day at bedtime for 12 weeks

Drug: TNX-102 SL Tablet, 2.8mg

Placebo SL Tablet

PLACEBO COMPARATOR

1 x Placebo Tablet taken sublingually each day at bedtime for 12 weeks

Drug: Placebo SL Tablet

Interventions

Patients will take 1 tablet of randomly assigned study drug sublingually each day at bedtime starting on Day 1 for 12 weeks.

Also known as: Low dose cyclobenzaprine sublingual tablets
TNX-102 SL Tablet, 2.8 mg

Patients will take 1 tablet of randomly assigned study drug sublingually each day at bedtime starting on Day 1 for 12 weeks.

Also known as: Placebo sublingual tablets
Placebo SL Tablet

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of Primary Fibromyalgia (2010 ACR criteria)
  • Male or female 18-75 years old
  • For patients with major depressive disorders only: clinically stable, no suicidal risk and stable anti-depressant therapy
  • Willing and able to withdraw specific therapies (ask PI)
  • Medically acceptable form of contraception (female only)
  • Signed informed consent

You may not qualify if:

  • Arthritis, lupus and other systemic auto-immune diseases
  • Regional or persistent pain that could interfere with assessment of fibromyalgia pain
  • Bipolar and psychotic disorders
  • Increased risk of suicide
  • Significant clinical (cardiac, systemic infection, systemic corticosteroid requirement, drug/alcohol abuse) or laboratory abnormalities.
  • Inability to wash-out specific medications (ask PI)
  • Known hypersensitivity to cyclobenzaprine
  • Others: seizure disorders, severe/untreated sleep apnea, BMI\>40

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (35)

Unknown Facility

Birmingham, Alabama, 35216, United States

Location

Unknown Facility

Phoenix, Arizona, 85032, United States

Location

Unknown Facility

Sacramento, California, 95825, United States

Location

Unknown Facility

San Diego, California, 92103, United States

Location

Unknown Facility

Brandon, Florida, 33511, United States

Location

Unknown Facility

DeLand, Florida, 32720, United States

Location

Unknown Facility

Lakeland, Florida, 33805, United States

Location

Unknown Facility

Ocala, Florida, 34471, United States

Location

Unknown Facility

Orlando, Florida, 32806, United States

Location

Unknown Facility

Tampa, Florida, 33613, United States

Location

Unknown Facility

Tampa, Florida, 33614, United States

Location

Unknown Facility

West Palm Beach, Florida, 33409, United States

Location

Unknown Facility

Columbus, Georgia, 31904, United States

Location

Unknown Facility

Smyrna, Georgia, 30080, United States

Location

Unknown Facility

Evansville, Indiana, 47714, United States

Location

Unknown Facility

North Dartmouth, Massachusetts, 02747, United States

Location

Unknown Facility

Ann Arbor, Michigan, 48104, United States

Location

Unknown Facility

Jackson, Mississippi, 39202, United States

Location

Unknown Facility

Williamsville, New York, 14221, United States

Location

Unknown Facility

Cincinnati, Ohio, 45206, United States

Location

Unknown Facility

Columbus, Ohio, 43212, United States

Location

Unknown Facility

Middleburg Heights, Ohio, 44130, United States

Location

Unknown Facility

Medford, Oregon, 97504, United States

Location

Unknown Facility

Portland, Oregon, 97210, United States

Location

Unknown Facility

Allentown, Pennsylvania, 18104, United States

Location

Unknown Facility

Warwick, Rhode Island, 02888, United States

Location

Unknown Facility

Greer, South Carolina, 29650, United States

Location

Unknown Facility

Mt. Pleasant, South Carolina, 29464, United States

Location

Unknown Facility

Dallas, Texas, 75231, United States

Location

Unknown Facility

Salt Lake City, Utah, 84102, United States

Location

Unknown Facility

Charlottesville, Virginia, 22911, United States

Location

Unknown Facility

Norfolk, Virginia, 23507, United States

Location

Unknown Facility

Bellevue, Washington, 98007, United States

Location

Unknown Facility

Seattle, Washington, 98104, United States

Location

Unknown Facility

Kenosha, Wisconsin, 53142, United States

Location

MeSH Terms

Conditions

FibromyalgiaMyofascial Pain SyndromesMuscular DiseasesMusculoskeletal DiseasesNervous System DiseasesNeuromuscular DiseasesRheumatic DiseasesPain

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Gregory Sullivan, MD
Organization
Tonix Pharmaceuticals

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 28, 2015

First Posted

May 6, 2015

Study Start

April 1, 2015

Primary Completion

September 1, 2016

Study Completion

September 1, 2016

Last Updated

February 7, 2025

Results First Posted

February 7, 2025

Record last verified: 2025-02

Locations