NCT04172831

Brief Summary

This is a Phase 3, randomized, parallel-group, double-blind, placebo-controlled, 14-week study designed to evaluate the efficacy and safety of TNX-102 SL 5.6 mg (2 x 2.8 mg tablets) taken daily at bedtime for the treatment of fibromyalgia.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
503

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Dec 2019

Shorter than P25 for phase_3

Geographic Reach
1 country

39 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 20, 2019

Completed
1 day until next milestone

First Posted

Study publicly available on registry

November 21, 2019

Completed
18 days until next milestone

Study Start

First participant enrolled

December 9, 2019

Completed
11 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 29, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 29, 2020

Completed
1.8 years until next milestone

Results Posted

Study results publicly available

August 8, 2022

Completed
Last Updated

August 8, 2022

Status Verified

July 1, 2022

Enrollment Period

11 months

First QC Date

November 20, 2019

Results QC Date

June 2, 2022

Last Update Submit

July 13, 2022

Conditions

Keywords

PainSleepFibromyalgiaFM

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline to Week 14 in the Numerical Rating Scale (NRS) Weekly Average of Daily Self-reported Average Pain Severity Scores.

    Patients provide a daily numeric assessment of their average pain (24-hour recall), via an electronic diary, using an 11-point NRS. Scores range from 0 (no pain) to 10 (worst possible pain).

    14 weeks

Secondary Outcomes (6)

  • Number of Patients With a Patient's Global Impression of Change (PGIC) Rating of "Very Much Improved" or "Much Improved"

    14 weeks

  • Change From Baseline to Week 14 in the Fibromyalgia Impact Questionnaire - Revised (FIQR) Symptoms Domain Score

    14 weeks

  • Change From Baseline to Week 14 in the FIQR Function Domain Score

    14 weeks

  • Change From Baseline to Week 14 in the Patient Reported Outcomes Measurement Information System (PROMIS) Score for Sleep Disturbance

    14 weeks

  • Change From Baseline to Week 14 in the PROMIS Score for Fatigue

    14 weeks

  • +1 more secondary outcomes

Study Arms (2)

TNX-102 SL Tablets, 5.6 mg

EXPERIMENTAL

1 x TNX-102 SL 2.8 mg Tablet taken sublingually each day at bedtime for 2 weeks then 2 x TNX-102 SL 2.8 mg (5.6 mg) Tablet taken sublingually each day at bedtime for 12 weeks.

Drug: TNX-102 SL

Placebo SL Tablet

PLACEBO COMPARATOR

1 x Placebo Tablet taken sublingually each day at bedtime for 2 weeks then 2 x Placebo Tablet taken sublingually each day at bedtime for 12 weeks.

Drug: Placebo SL Tablet

Interventions

Patients will take 1 tablet of randomly assigned study drug sublingually starting on Day 1 for 2 weeks. At the Week 2 visit, all patients will have the dose increased to 2 tablets for 12 weeks.

Also known as: Low dose cyclobenzaprine sublingual tablets
TNX-102 SL Tablets, 5.6 mg

Patients will take 1 tablet of randomly assigned study drug sublingually starting on Day 1 for 2 weeks. At the Week 2 visit, all patients will have the dose increased to 2 tablets for 12 weeks.

Also known as: Placebo sublingual tablets
Placebo SL Tablet

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • The patient is male or female 18 to 65 years of age, inclusive.
  • The patient has a diagnosis of primary FM as defined by the 2016 Revisions to the 2010/2011 fibromyalgia diagnostic criteria (American College of Rheumatology Preliminary Diagnostic Criteria)
  • The in-clinic 7-day recall NRS average daily pain intensity score at Screening Visit within protocol specified range.

You may not qualify if:

  • History of or evidence for a diagnosis of borderline personality disorder (BPD).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (39)

Tonix Clinical Site

Birmingham, Alabama, 35216, United States

Location

Tonix Clinical Site

Phoenix, Arizona, 85016, United States

Location

Tonix Clinical Site

Oceanside, California, 92056, United States

Location

Tonix Clinical Site

Sacramento, California, 95831, United States

Location

Tonix Clinical Site

San Diego, California, 92103, United States

Location

Tonix Clinical Site

Temecula, California, 32591, United States

Location

Tonix Clinical Site

Cromwell, Connecticut, 06416, United States

Location

Tonix Clinical Site

Fort Myers, Florida, 33912, United States

Location

Tonix Clinical Site

Jacksonville, Florida, 32256, United States

Location

Tonix Clinical Site

North Miami, Florida, 33161, United States

Location

Tonix Clinical Site

Ocala, Florida, 34470, United States

Location

Tonix Clinical Site

Orlando, Florida, 32801, United States

Location

Tonix Clinical Site

Atlanta, Georgia, 30341, United States

Location

Tonix Clinical Site

Evansville, Indiana, 47714, United States

Location

Tonix Clinical Site

West Des Moines, Iowa, 50265, United States

Location

Tonix Clinical Site

Prairie Village, Kansas, 66208, United States

Location

Tonix Clinical Site

New Orleans, Louisiana, 70115, United States

Location

Tonix Clinical Site

Boston, Massachusetts, 02131, United States

Location

Tonix Clinical Site

North Dartmouth, Massachusetts, 02747, United States

Location

Tonix Clinical Site

Las Vegas, Nevada, 89102, United States

Location

Tonix Clinical Site

Williamsville, New York, 14221, United States

Location

Tonix Clinical Site

High Point, North Carolina, 27262, United States

Location

Tonix Clinical Site

Raleigh, North Carolina, 27612, United States

Location

Tonix Clinical Site

Fargo, North Dakota, 58104, United States

Location

Tonix Clinical Site

Cincinnati, Ohio, 45219, United States

Location

Tonix Clinical Site

Dayton, Ohio, 45417, United States

Location

Tonix Clinical Site

North Canton, Ohio, 44720, United States

Location

Tonix Clinical Site

Oklahoma City, Oklahoma, 73112, United States

Location

Tonix Clinical Site

Tulsa, Oklahoma, 74133, United States

Location

Tonix Clinical Site

Portland, Oregon, 97210, United States

Location

Tonix Clinical Site

Allentown, Pennsylvania, 18104, United States

Location

Tonix Clinical Site

Warwick, Rhode Island, 02886, United States

Location

Tonix Clinical Site

Chattanooga, Tennessee, 37421, United States

Location

Tonix Clinical Site

Memphis, Tennessee, 38119, United States

Location

Tonix Clinical Site

Austin, Texas, 78737, United States

Location

Tonix Clinical Site

Dallas, Texas, 75231, United States

Location

Tonix Clinical Site

Salt Lake City, Utah, 84102, United States

Location

Tonix Clinical Site

Charlottesville, Virginia, 22911, United States

Location

Tonix Clinical Site

Kenosha, Wisconsin, 53144, United States

Location

Related Publications (1)

  • Lederman S, Arnold LM, Vaughn B, Kelley M, Sullivan GM. Efficacy and Safety of Sublingual Cyclobenzaprine for the Treatment of Fibromyalgia: Results From a Randomized, Double-Blind, Placebo-Controlled Trial. Arthritis Care Res (Hoboken). 2023 Nov;75(11):2359-2368. doi: 10.1002/acr.25142. Epub 2023 Jul 4.

MeSH Terms

Conditions

FibromyalgiaPain

Condition Hierarchy (Ancestors)

Muscular DiseasesMusculoskeletal DiseasesRheumatic DiseasesNeuromuscular DiseasesNervous System DiseasesNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Limitations and Caveats

Recruitment during COVID-19 pandemic

Results Point of Contact

Title
Gregory Sullivan, MD
Organization
Tonix Pharmaceuticals

Study Officials

  • Gregory Sullivan, MD

    Tonix Pharmaceuticals

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 20, 2019

First Posted

November 21, 2019

Study Start

December 9, 2019

Primary Completion

October 29, 2020

Study Completion

October 29, 2020

Last Updated

August 8, 2022

Results First Posted

August 8, 2022

Record last verified: 2022-07

Locations