NCT02431260

Brief Summary

This was a study of INCB054329 given to patients with advanced malignancies that were conducted in three treatment groups. Each treatment group had a dose escalation (Part 1) and a dose expansion (Part 3), two of the treatment groups also had an intra-patient dose titration (Part 2).

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
69

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Apr 2015

Typical duration for phase_1

Geographic Reach
1 country

12 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 14, 2015

Completed
13 days until next milestone

First Submitted

Initial submission to the registry

April 27, 2015

Completed
3 days until next milestone

First Posted

Study publicly available on registry

April 30, 2015

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 31, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 31, 2018

Completed
1.4 years until next milestone

Results Posted

Study results publicly available

June 14, 2019

Completed
Last Updated

June 14, 2019

Status Verified

May 1, 2019

Enrollment Period

2.8 years

First QC Date

April 27, 2015

Results QC Date

January 29, 2019

Last Update Submit

May 17, 2019

Conditions

Keywords

solid tumorlymphomaBET bromodomain inhibitorBRDDiffuse large B-cell lymphoma (DLBCL)Burkitt's lymphomac-MYCcolorectal cancerNon-small cell lung cancerPancreatic adenocarcinomacastration-resistant prostate cancerbreast cancerNUT midline carcinomaleukemiaacute myeloid leukemia (AML)myelodysplastic syndrome (MDS)myeloproliferative neoplasmsmyelofibrosis (MF)multiple myeloma (MM)MDS/MPN

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With a Treatment-emergent Adverse Event (TEAE)

    TEAE is defined as an adverse event reported for the first time or worsening of a pre-existing event after the first dose of study treatment.

    up to 30 days

Secondary Outcomes (10)

  • Maximum Plasma Concentration (Cmax) Analysis of INCB054329

    Summary of steady-state PK parameters by dosing regimen at Day 15

  • Time to Maximum Plasma Concentration (Tmax) Analysis of INCB054329

    Summary of steady-state PK parameters by dosing regimen at Day 15

  • Minimum Observed Plasma Concentration Over the Dose Interval (Cmin) Analysis of INCB054329

    Summary of steady-state PK parameters by dosing regimen at Day 15

  • AUC0-t Analysis of INCB054329

    Summary of steady-state PK parameters by dosing regimen at Day 15

  • Cl/F Analysis of INCB054329

    Summary of steady-state PK parameters by dosing regimen at Day 15

  • +5 more secondary outcomes

Study Arms (1)

INCB054329 Monotherapy

EXPERIMENTAL
Drug: INCB054329 Monotherapy

Interventions

Initial cohort dose of INCB054329 monotherapy at the protocol-specified starting dose in the treatment group A (TGA), with subsequent cohort escalations in the three treatment groups (TGA, TGB, and TGC) based on protocol-specific criteria

INCB054329 Monotherapy

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Confirmed diagnosis of advanced malignancy:
  • Treatment Group A (TGA): Part 1 and Part 2: Any advanced solid tumor or lymphoma; Part 3: Histologically confirmed disease in specific solid tumors and lymphomas
  • Treatment Group B (TGB): Acute Leukemia (Part 3 - acute myeloid leukemia \[AML\] only), myelodysplastic syndrome (MDS), myelodysplastic /myeloproliferative neoplasms (MDS/MPN) and myelofibrosis (MF)
  • Treatment Group C (TGC): Multiple myeloma
  • Progressed following at least 1 line of prior therapy and there is no further approved therapy available that has been demonstrated to prolong survival (including subjects who are intolerant to the approved therapy)
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1 in Parts 1 and 2 dose escalation and titration, and 0, 1, 2 in Part 3 dose expansion

You may not qualify if:

  • Inadequate hematopoietic, liver, endocrine or renal function
  • Receipt of anticancer medications or investigational drugs within the following interval before the first administration of study drug:
  • \< 6 weeks for mitomycin-C or nitrosoureas
  • \< 5 half-lives or 14 days, whichever is longer, for any investigational agent (for any indication)
  • \< 28 days for any antibodies or biological therapies
  • \< 5 half-lives for all other anticancer medications, or sponsor approval
  • Prior radiotherapy within 2 weeks prior to first dose of study drug
  • Untreated brain or central nervous system (CNS) metastases
  • Type 1 diabetes or uncontrolled Type 2 diabetes
  • Any sign of clinically significant bleeding

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (12)

Cedars-Sinai Medical Center

Los Angeles, California, 90048, United States

Location

University of California, San Francisco, Medical Center at Mount Zion

San Francisco, California, 94115, United States

Location

Sarah Cannon Research Institute Research Center

Denver, Colorado, 80218, United States

Location

Northwestern Memorial Hospital

Chicago, Illinois, 60611, United States

Location

The University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

Horizon Oncology Center

Lafayette, Indiana, 47905, United States

Location

John Hopkins

Baltimore, Maryland, 21287-0013, United States

Location

University of Michigan Comprehensive Cancer Center

Ann Arbor, Michigan, 48109, United States

Location

Washington University School of Medicine in St. Louis

St Louis, Missouri, 63110, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232-0021, United States

Location

The University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Seattle Cancer Care Alliance

Seattle, Washington, 98109, United States

Location

Related Publications (1)

  • Falchook G, Rosen S, LoRusso P, Watts J, Gupta S, Coombs CC, Talpaz M, Kurzrock R, Mita M, Cassaday R, Harb W, Peguero J, Smith DC, Piha-Paul SA, Szmulewitz R, Noel MS, Yeleswaram S, Liu P, Switzky J, Zhou G, Zheng F, Mehta A. Development of 2 Bromodomain and Extraterminal Inhibitors With Distinct Pharmacokinetic and Pharmacodynamic Profiles for the Treatment of Advanced Malignancies. Clin Cancer Res. 2020 Mar 15;26(6):1247-1257. doi: 10.1158/1078-0432.CCR-18-4071. Epub 2019 Sep 16.

MeSH Terms

Conditions

Hematologic NeoplasmsLymphomaLymphoma, Large B-Cell, DiffuseBurkitt LymphomaColorectal NeoplasmsCarcinoma, Non-Small-Cell LungBreast NeoplasmsLeukemiaLeukemia, Myeloid, AcuteMyelodysplastic SyndromesMyeloproliferative DisordersPrimary MyelofibrosisMultiple Myeloma

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesNeoplasms by Histologic TypeLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesLymphoma, B-CellLymphoma, Non-HodgkinEpstein-Barr Virus InfectionsHerpesviridae InfectionsDNA Virus InfectionsVirus DiseasesInfectionsTumor Virus InfectionsIntestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal DiseasesCarcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsLung DiseasesRespiratory Tract DiseasesBreast DiseasesSkin DiseasesSkin and Connective Tissue DiseasesLeukemia, MyeloidBone Marrow DiseasesNeoplasms, Plasma CellHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHemorrhagic Disorders

Results Point of Contact

Title
Study Director
Organization
Incyte Corporation

Study Officials

  • Fred Zheng, M.D.

    Incyte Corporation

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 1
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR
Expanded Access
Yes

Study Record Dates

First Submitted

April 27, 2015

First Posted

April 30, 2015

Study Start

April 14, 2015

Primary Completion

January 31, 2018

Study Completion

January 31, 2018

Last Updated

June 14, 2019

Results First Posted

June 14, 2019

Record last verified: 2019-05

Data Sharing

IPD Sharing
Will not share

Locations