NCT02392624

Brief Summary

This multicenter, randomized, double-blind, placebo-controlled study will evaluate the efficacy and safety of subcutaneous (SC) omalizumab (Xolair) as an add-on therapy through 48 weeks for treatment of H1 antihistamine refractory chronic idiopathic urticaria (CIU). After completing an initial 24-week open-label treatment period with omalizumab 300 milligrams (mg) every 4 weeks (Q4W), participants responding to omalizumab will be randomized at a 3:2 ratio (omalizumab:placebo) to either continue omalizumab or be transitioned to placebo for a further 24 weeks.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
206

participants targeted

Target at P75+ for phase_4

Timeline
Completed

Started May 2015

Geographic Reach
1 country

40 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 13, 2015

Completed
6 days until next milestone

First Posted

Study publicly available on registry

March 19, 2015

Completed
2 months until next milestone

Study Start

First participant enrolled

May 18, 2015

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 9, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 9, 2017

Completed
1 year until next milestone

Results Posted

Study results publicly available

March 26, 2018

Completed
Last Updated

March 29, 2018

Status Verified

March 1, 2018

Enrollment Period

1.8 years

First QC Date

March 13, 2015

Results QC Date

February 21, 2018

Last Update Submit

March 26, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants Who Experienced Clinical Worsening in CIU as Assessed by Urticaria Activity Score Over 7 Days (UAS7) (Clinical Worsening: UAS7 Greater Than or Equal to [>/=] 12, Maintained for At Least 2 Consecutive Weeks)

    Urticaria activity score (UAS) is a composite diary-recorded score with numeric severity ratings (0=none to 3=intense) for the number of wheals (hives) per 24 hours and the intensity of the pruritus (itch). The total UAS score (sum of the wheal and pruritus scores) ranges from 0 to 6. Due to variations in chronic urticaria disease intensity, assessment of disease activity was based on a weekly (7 days) UAS score called UAS7, that is, the sum of the daily average UASs (average of morning and evening scores), ranging from 0 to 42 per week. A higher score indicates worse disease. Clinical worsening in CIU was defined as UAS7 \>/=12 for at least 2 consecutive weeks post-randomization between Weeks 24 and 48.

    From randomization (Week 24) to Week 48

Secondary Outcomes (4)

  • Time to Clinical Worsening in CIU as Assessed by UAS7 (Clinical Worsening: UAS7 >/=12, Maintained for At Least 2 Consecutive Weeks)

    From randomization (Week 24) to Week 48

  • Percentage of Participants Who Experienced Clinical Worsening in CIU as Assessed by UAS7 (Clinical Worsening: UAS7 Greater Than [>] 6, Maintained for At Least 2 Consecutive Weeks)

    From randomization (Week 24) to Week 48

  • Change From Randomization (Week 24) to Week 48 in UAS7 Among Participants Who Received Total 48 Weeks Treatment With Omalizumab

    Week 24 (randomization) and Week 48

  • Retreatment Efficacy: Change From Time of Retreatment to 12 Weeks After Retreatment in UAS7 Among Participants Randomized to Placebo and Who Were Retreated With Open-Label Omalizumab After Randomization

    At start of retreatment (any time between Weeks 24 and Week 48) and 12 weeks after retreatment (up to Week 60)

Study Arms (2)

Omalizumab

EXPERIMENTAL

Participants will receive open-label omalizumab treatment at 300 mg SC Q4W for 24 weeks. After 24 weeks open-label treatment, eligible participants will be randomized to receive omalizumab treatment at 300 mg SC Q4W for next 24 weeks (up to Week 48). Participants randomized to omalizumab may, at the discretion of the investigator, be transitioned from blinded study drug to open-label omalizumab at 300 mg SC Q4W if they experience clinically significant worsening in their CIU (as judged by the investigator). Participants who are transitioned to open-label omalizumab will continue to receive open-label omalizumab as study drug until Week 48.

Drug: Omalizumab

Placebo

PLACEBO COMPARATOR

Participants will receive open-label omalizumab treatment at 300 mg SC Q4W for 24 weeks. After 24 weeks open-label treatment, eligible participants will be randomized to receive placebo SC Q4W for next 24 weeks (up to Week 48). Participants randomized to placebo may, at the discretion of the investigator, be transitioned from blinded study drug to open-label omalizumab at 300 mg SC Q4W if they experience clinically significant worsening in their CIU (as judged by the investigator). Participants who are transitioned to open-label omalizumab will continue to receive open-label omalizumab as study drug until Week 48.

Drug: OmalizumabDrug: Placebo

Interventions

Omalizumab 300 mg administered SC Q4W.

Also known as: Xolair; RO5489789
OmalizumabPlacebo

Placebo matched to omalizumab administered SC Q4W.

Placebo

Eligibility Criteria

Age12 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of CIU refractory to H1 antihistamines at baseline
  • Presence of itch and hives for at least 8 consecutive weeks at any time prior to enrollment despite current use of H1 antihistamine treatment (up to four times the approved dose) during this time period
  • UAS7 score (range 0-42) ≥ 16 and itch component of UAS7 (range 0-21) ≥ 8 during 7 days prior to baseline
  • Participants must have been on a non-sedating H1 antihistamine treatment (up to four times the approved dose) for CIU for at least 3 consecutive days immediately prior to screening visit with continued current use on the day of the initial screening visit
  • CIU diagnosis for ≥ 6 months
  • Willing and able to complete a daily symptom eDiary for the duration of the study

You may not qualify if:

  • Treatment with an investigational agent within 30 days of the initial screening visit
  • Body weight less than 20 kilograms
  • Clearly defined underlying etiology for chronic urticarias other than CIU
  • Evidence of a parasitic infection
  • Atopic dermatitis, bullous pemphigoid, dermatitis herpetiformis, senile pruritus or other skin disease associated with itch
  • Previous treatment with omalizumab within 1 year prior to the initial screening visit
  • Participants may not have taken during treatment period or have been taking within 30 days before the initial screening visit any of the following medications or treatments:
  • regular (daily/every other day during 5 or more consecutive days) systemic corticosteroids, hydroxychloroquine, methotrexate, mycophenolate, cyclosporine, cyclophosphamide, intravenous immunoglobulin G or plasmapheresis
  • Regular (daily/every other day) oral doxepin use within 14 days prior to the initial screening visit
  • Pregnant or lactating women, or women intending to become pregnant during the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (40)

Allergy and Asthma Relief Experts

Granada Hills, California, 91344, United States

Location

Allergy & Asthma Care Center of Southern California

Long Beach, California, 90808, United States

Location

Dermatology Research Associate

Los Angeles, California, 90045, United States

Location

Southern California Research Center

Mission Viejo, California, 92691, United States

Location

Choc Psf, Amc

Orange, California, 92868, United States

Location

Allergy & Asthma Consultants

Redwood City, California, 94063, United States

Location

Allergy and Asthma Clinical Research, Inc.

Walnut Creek, California, 94598, United States

Location

IMMUNOe Research Centers

Centennial, Colorado, 80112, United States

Location

Colorado Allergy & Asthma Centers, Pc

Denver, Colorado, 80230, United States

Location

Florida Center for Allergy and Asthma Research

Aventura, Florida, 33180, United States

Location

Florida Ctr-Allergy & Asthma

Miami, Florida, 33173, United States

Location

Sarasota Clinical Research

Sarasota, Florida, 34239, United States

Location

University of South Florida

Tampa, Florida, 33613, United States

Location

Clinical Research Center of Southern Illinois LLC

Shiloh, Illinois, 62269, United States

Location

Deaconess Clinic

Evansville, Indiana, 47713, United States

Location

Dawes Fretzin Clinical Res LLC

Indianapolis, Indiana, 46256, United States

Location

Abraham Research PLLC

Fort Mitchell, Kentucky, 41017, United States

Location

Dermatology Specialists Research, LLC

Louisville, Kentucky, 40241, United States

Location

Allergy & Asthma Specialists, PSC

Owensboro, Kentucky, 42301, United States

Location

Asthma, Allergy & Sinus Center

Baltimore, Maryland, 21236, United States

Location

Institute for Asthma & Allergy

Chevy Chase, Maryland, 20815, United States

Location

Respiratory Medicine Research; Institue of Michigan P.L.C.

Ypsilanti, Michigan, 48197, United States

Location

James Q. Del Rosso, DO, LLC

Las Vegas, Nevada, 89117, United States

Location

Ocean Allergy & Resp Res Ctr

Brick, New Jersey, 08724, United States

Location

Winthrop University Hospital

Mineola, New York, 11501, United States

Location

Aair Research Center

Rochester, New York, 14618, United States

Location

University of Rochester Medical Center; University Dermatology Associates

Rochester, New York, 14642, United States

Location

Montefiore Medical Group;Department of Medicine

The Bronx, New York, 10461, United States

Location

Allergy Partners of Western NC

Asheville, North Carolina, 28801, United States

Location

Allergy & Respiratory Center

Canton, Ohio, 44718, United States

Location

Bernstein Clinical Research Center Llc

Cincinnati, Ohio, 45231, United States

Location

Toledo Inst of Clin Research

Toledo, Ohio, 43617, United States

Location

Vital Prospects Clin Res Pc

Tulsa, Oklahoma, 74136, United States

Location

Asthma, Nasal Disease, and Allergy Research Center of New England

East Providence, Rhode Island, 02914, United States

Location

National Allergy and Asthma Research

Charleston, South Carolina, 29407, United States

Location

Live Oak Allergy & Asthma Clinic

Live Oak, Texas, 78233, United States

Location

Allergy & Asthma Research Center

San Antonio, Texas, 78229, United States

Location

Timber Lane Allergy-Asth Res

South Burlington, Vermont, 05403, United States

Location

O & O Alpan, LLC

Fairfax, Virginia, 22030, United States

Location

Premier Clinical Research

Spokane, Washington, 99202, United States

Location

Related Publications (1)

  • Casale TB, Murphy TR, Holden M, Rajput Y, Yoo B, Bernstein JA. Impact of omalizumab on patient-reported outcomes in chronic idiopathic urticaria: Results from a randomized study (XTEND-CIU). J Allergy Clin Immunol Pract. 2019 Sep-Oct;7(7):2487-2490.e1. doi: 10.1016/j.jaip.2019.04.020. Epub 2019 Apr 26. No abstract available.

MeSH Terms

Conditions

Urticaria

Interventions

Omalizumab

Condition Hierarchy (Ancestors)

Skin Diseases, VascularSkin DiseasesSkin and Connective Tissue DiseasesHypersensitivity, ImmediateHypersensitivityImmune System Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Anti-IdiotypicAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsAntibodies, Monoclonal, HumanizedAntibodies, MonoclonalSerum GlobulinsGlobulins

Results Point of Contact

Title
Medical Communications
Organization
Hoffmann-La Roche

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 13, 2015

First Posted

March 19, 2015

Study Start

May 18, 2015

Primary Completion

March 9, 2017

Study Completion

March 9, 2017

Last Updated

March 29, 2018

Results First Posted

March 26, 2018

Record last verified: 2018-03

Locations