NCT02382016

Brief Summary

24-week study to evaluate the efficacy and safety of macitentan for the treatment of portopulmonary hypertension.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
85

participants targeted

Target at P50-P75 for phase_4

Timeline
Completed

Started Jun 2015

Typical duration for phase_4

Geographic Reach
7 countries

52 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 3, 2015

Completed
3 days until next milestone

First Posted

Study publicly available on registry

March 6, 2015

Completed
4 months until next milestone

Study Start

First participant enrolled

June 23, 2015

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 25, 2017

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

October 31, 2018

Completed
23 days until next milestone

Results Posted

Study results publicly available

November 23, 2018

Completed
Last Updated

March 30, 2025

Status Verified

March 1, 2025

Enrollment Period

2.3 years

First QC Date

March 3, 2015

Results QC Date

October 25, 2018

Last Update Submit

March 28, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Relative Change From Baseline to Week 12 in Pulmonary Vascular Resistance (PVR).

    The relative change from baseline to Week 12 in PVR is expressed as a ratio of Week 12 to baseline PVR.

    From enrollment/baseline to Week 12 in the Double Blind (DB) treatment period

Secondary Outcomes (8)

  • Change From Baseline to Week 12 in 6-minute Walk Distance (6MWD)

    From enrollment/baseline to Week 12 in the DB treatment period

  • Change From Baseline to Week 12 in WHO Functional Class (FC)

    From enrollment/baseline to Week 12 in the DB treatment period

  • Change From Baseline to Week 12 in the Biomarker N-terminal Pro B-type Natriuretic Peptide (NT-proBNP)

    From enrollment/baseline to Week 12 in the DB treatment period

  • Change From Baseline to Week 12 in Mean Right Atrial Pressure (mRAP)

    From enrollment/baseline to Week 12 in the DB treatment period

  • Change From Baseline to Week 12 in Mean Pulmonary Artery Pressure (mPAP)

    From enrollment/baseline to Week 12 in the DB treatment period

  • +3 more secondary outcomes

Study Arms (2)

Investigational treatment

EXPERIMENTAL

Macitentan film-coated tablet 10 mg once daily.

Drug: Macitentan

Placebo

PLACEBO COMPARATOR

Matching placebo tablet once daily.

Other: Placebo

Interventions

Macitentan film-coated tablet 10 mg once daily.

Also known as: ACT-064992
Investigational treatment
PlaceboOTHER

Matching placebo tablet once daily.

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female of at least 18 years of age
  • Confirmed diagnosis of portopulmonary hypertension

You may not qualify if:

  • Severe hepatic impairment
  • Severe obstructive or restrictive lung disease
  • Pulmonary veno-occlusive disease
  • Systolic blood pressure (SBP) \< 90 mmHg at Screening
  • ALT/AST \>= 3 x ULN
  • Bilirubin \>= 3 mg/dL at Screening
  • Any known factor or disease that might interfere with treatment compliance, study conduct, or interpretation of results

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (52)

Mayo Clinic -Clinical Studies Unit

Phoenix, Arizona, 85054, United States

Location

UCSD

La Jolla, California, 92093, United States

Location

David Geffen School of Medicine, UCLA

Los Angeles, California, 90025-1690, United States

Location

Keck School of Medicine

Los Angeles, California, 90033, United States

Location

UCSF

San Francisco, California, 91413-2204, United States

Location

University of Colorado Health Sciences Center Aurora

Aurora, Colorado, 80045, United States

Location

University of Florida - Divison of Pulmonary Critical Care & Sleep

Gainesville, Florida, 32610, United States

Location

University of Florida College of Medicine

Jacksonville, Florida, 32209, United States

Location

Mayo Clinic Florida - Pulmonary Dept.

Jacksonville, Florida, 32224, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

South Miami Hospital

South Miami, Florida, 33143, United States

Location

Emory Healthcare

Atlanta, Georgia, 30322, United States

Location

Piedmont Healthcare

Austell, Georgia, 30106, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Indiana University

Indianapolis, Indiana, 46202, United States

Location

Kentuckiana Pulmonary Associates

Louisville, Kentucky, 40202, United States

Location

Boston University

Boston, Massachusetts, 02118, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

University of New Mexico Health Science Center

Albuquerque, New Mexico, 87131-0001, United States

Location

University of Cincinnati

Cincinnati, Ohio, 45267, United States

Location

Cleveland Clinic - Department of Cardiovascular Medicine

Cleveland, Ohio, 44195, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

UPMC Montefiore

Pittsburgh, Pennsylvania, 15213, United States

Location

Baylor University Medical Center

Dallas, Texas, 75226, United States

Location

University of Texas Southwestern Medical Center Division of NeuroCritical Care 75390-8550

Dallas, Texas, 75390-8550, United States

Location

Methodist Hospital

Houston, Texas, 77030, United States

Location

Methodist Hospital

San Antonio, Texas, 78229, United States

Location

University of Wisconsin-Madison

Madison, Wisconsin, 53705-2281, United States

Location

Servico de Hipertensao Pulmonar - Complexo Hospitalar Santa Casa Irmandade Santa de Misericordia de Porto Alegre

Porto Alegre, 92020-090, Brazil

Location

Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo (HC-FMUSP)

São Paulo, 05403-000, Brazil

Location

Lékařská fakulta a Všeobecná fakultní nemocnice v Praze, II. Interní klinika kardiologie a angiologie U

Prague, 128 08, Czechia

Location

IKEM (Institut klinické a experimentální medicíny, Institute for Clinical and Experimental Medicine)

Prague, 140 21, Czechia

Location

CHRU de Grenoble, Hôpital Albert Michallon

Grenoble, Auvergne-Rhône-Alpes, 38043, France

Location

CHRU Hôpital Cavale Blanche Brest

Brest, Brittany Region, 29609, France

Location

CHU Côte de Nacre, Service de Pneumologie

Caen, 14033, France

Location

Hôpital cardiologique, Service de cardiologie 59037 Lille Cedex"

Lille, 59037, France

Location

Hôpital Cardiologique et Pneumologique Louis Pradel 69677 Bron cedex"

Lyon, 69677, France

Location

Hôpital Kremlin Bicêtre Service de Pneumologie

Paris, 94275, France

Location

Hôpital Pontchaillou - CHU Rennes Service de Cardiologie et des Maladies Vasculaires Rennes Cedex 9 35033"

Rennes, 35033, France

Location

CHU Rouen

Rouen, 76031, France

Location

CHU Toulouse - Hôpital Larrey Hôpital de Jour et Semaine

Toulouse, 31059, France

Location

Universitätsklinikum Carl Gustav Carus an der Technischen Universität Dresden

Dresden, 01307, Germany

Location

Universitätsklinikum Giessen und Marburg GmbH Justus-Liebig Universität Giessen 35392

Giessen, 35392, Germany

Location

Medizinische Hochschule Hannover, Abteilung Pneumologie

Hanover, 30625, Germany

Location

Thoraxklinik des Universitätsklinikums Heidelberg Zentrum für pulmonale Hypertonie Studienkoordination

Heidelberg, 69126, Germany

Location

Universitätsklinikum Leipzig, Department Innere Medizin, Abteilung Pneumologie

Leipzig, 04103, Germany

Location

Hospital Clinico i Provincial Servicio de Neumología

Barcelona, 08036, Spain

Location

Hospital Universitario12 Octubre

Madrid, 28041, Spain

Location

NHS Greater Glasgow and Clyde Trust

Glasgow, Scotland, G11 6NT, United Kingdom

Location

The Royal Free Hospital/ Cardiology Department

London, NW3 2QG, United Kingdom

Location

Sheffield Teaching Hospitals NHS Foundation Trust Royal Hallamshire Hospital

Sheffield, S10 2RX, United Kingdom

Location

Related Publications (2)

  • Raevens S, Fallon MB. PORTICO: First Randomized Controlled Trial of Vasomodulator Therapy in Portopulmonary Hypertension. Hepatology. 2020 May;71(5):1870-1872. doi: 10.1002/hep.31166. No abstract available.

  • Sitbon O, Bosch J, Cottreel E, Csonka D, de Groote P, Hoeper MM, Kim NH, Martin N, Savale L, Krowka M. Macitentan for the treatment of portopulmonary hypertension (PORTICO): a multicentre, randomised, double-blind, placebo-controlled, phase 4 trial. Lancet Respir Med. 2019 Jul;7(7):594-604. doi: 10.1016/S2213-2600(19)30091-8. Epub 2019 Jun 6.

MeSH Terms

Interventions

macitentan

Results Point of Contact

Title
Clinical Trial Disclosure Desk
Organization
Actelion Pharmaceuticals Ltd.

Study Officials

  • Loïc Perchenet, PhD

    Actelion

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 3, 2015

First Posted

March 6, 2015

Study Start

June 23, 2015

Primary Completion

October 25, 2017

Study Completion

October 31, 2018

Last Updated

March 30, 2025

Results First Posted

November 23, 2018

Record last verified: 2025-03

Locations