NCT02371720

Brief Summary

The purpose of this research study is to learn about ways to help children and adults with sickle cell disease who are taking the medication, hydroxyurea.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
164

participants targeted

Target at P75+ for not_applicable

Timeline
Completed

Started Jun 2014

Longer than P75 for not_applicable

Geographic Reach
1 country

4 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2014

Completed
9 months until next milestone

First Submitted

Initial submission to the registry

February 19, 2015

Completed
7 days until next milestone

First Posted

Study publicly available on registry

February 26, 2015

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2018

Completed
Last Updated

March 5, 2021

Status Verified

March 1, 2021

Enrollment Period

4.6 years

First QC Date

February 19, 2015

Last Update Submit

March 3, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Medication Possession Ratio (MPR)

    Proportion of days the patient is in possession of the medication in the study period

    12 months

Secondary Outcomes (7)

  • Change in Hemoglobin (Hb) levels

    Baseline, 24 months

  • Change in mean cell volume (MCV)

    Baseline, 24 months

  • Change in fetal hemoglobin (HbF) levels

    Baseline, 24 months

  • Impact of adherence on clinical outcomes and healthcare utilization

    Baseline, 24 months

  • Impact of adherence on patients' lives

    Baseline, 24 months

  • +2 more secondary outcomes

Study Arms (4)

Adults - Mobile DOT

EXPERIMENTAL

Subjects with SCD that are older than 21 years old will receive comprehensive medication adherence management (Mobile DOT) after 1 month assessment period. The subjects will receive the Mobile DOT intervention for 24 months.

Behavioral: Mobile DOT

Adults - standard of care then Mobile DOT

ACTIVE COMPARATOR

Subjects with SCD that are older than 21 years old will receive standard of care for the first 12 months. They will then crossover to the comprehensive medication adherence management plan (Mobile DOT) after 1 month assessment period for the remaining 12 months.

Behavioral: Mobile DOT

Children - Mobile DOT

EXPERIMENTAL

Subjects with SCD that are younger than 21 years old will receive comprehensive medication adherence management (Mobile DOT) after 1 month assessment period. The subjects will receive the Mobile DOT intervention for 24 months.

Behavioral: Mobile DOT

Children - standard of care then Mobile DOT

ACTIVE COMPARATOR

Subjects with SCD that are younger than 21 years old will receive standard of care for the first 12 months. They will then crossover to the comprehensive medication adherence management plan (Mobile DOT) after 1 month assessment period for the remaining 12 months.

Behavioral: Mobile DOT

Interventions

Mobile DOTBEHAVIORAL

Daily reminders via text or email to send a video of themselves taking their Hydroxyurea, positive feedback, and be encouraged to contact the research coordinator with any questions, concerns, etc.

Also known as: Comprehensive medication adherence management
Adults - Mobile DOTAdults - standard of care then Mobile DOTChildren - Mobile DOTChildren - standard of care then Mobile DOT

Eligibility Criteria

Age2 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • be \>2 years of age up to 65 years of age, inclusive
  • have a diagnosis of SCD, with either βS/βS, βS/βC, βS/βD, βS/β0, βS/βO-Arab, or βS/β+ genotype
  • prescribed Hydroxyurea for at least the 6 months prior to study entry
  • have daily access to a smart phone, tablet, personal computer or other device capable of producing and transmitting videos over the internet
  • be willing and able to record and transmit videos

You may not qualify if:

  • patient or caregiver refuses to take Hydroxyurea as treatment for SCD
  • diagnosis of significant psychiatric disorder of the subject that could seriously impede the ability to participate in the study
  • an assessment by the investigator that the subject will not comply with the study procedures outlined in the study protocol
  • patients receiving automatic home delivery of medications since medication possession ratio is reflective of the patient initiation the refill when they have exhausted the home supply of HU

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (4)

Children's National Medical Center

Washington D.C., District of Columbia, 20010, United States

Location

Children's Healthcare of Atlanta

Atlanta, Georgia, 30322, United States

Location

University of Illinois at Chicago

Chicago, Illinois, 60607, United States

Location

Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, 15224, United States

Location

MeSH Terms

Conditions

Anemia, Sickle Cell

Condition Hierarchy (Ancestors)

Anemia, Hemolytic, CongenitalAnemia, HemolyticAnemiaHematologic DiseasesHemic and Lymphatic DiseasesHemoglobinopathiesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Study Officials

  • Lakshmanan Krishnamurti, MD

    Emory University/Children's Healthcare of Atlanta

    STUDY CHAIR

Study Design

Study Type
interventional
Phase
not applicable
Allocation
RANDOMIZED
Masking
NONE
Purpose
HEALTH SERVICES RESEARCH
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Professor

Study Record Dates

First Submitted

February 19, 2015

First Posted

February 26, 2015

Study Start

June 1, 2014

Primary Completion

December 31, 2018

Study Completion

December 31, 2018

Last Updated

March 5, 2021

Record last verified: 2021-03

Locations