NCT02338843

Brief Summary

This is a Phase 3, double-blind, randomized study of LJPC-501 (angiotensin II) in adult patients diagnosed with catecholamine-resistant hypotension (CRH) conducted in multiple centers globally.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
344

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Mar 2015

Geographic Reach
10 countries

115 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 1, 2015

Completed
13 days until next milestone

First Posted

Study publicly available on registry

January 14, 2015

Completed
2 months until next milestone

Study Start

First participant enrolled

March 1, 2015

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2016

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

February 18, 2017

Completed
11 months until next milestone

Results Posted

Study results publicly available

January 17, 2018

Completed
Last Updated

March 27, 2018

Status Verified

January 1, 2018

Enrollment Period

1.8 years

First QC Date

January 1, 2015

Results QC Date

November 28, 2017

Last Update Submit

February 27, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • An Increased MAP, Defined as Achievement of a Day 1 MAP at 3 Hours Following the Initiation of Study Drug, of ≥ 75 mmHg OR a 10 mmHg Increase in Baseline MAP

    Response with respect to mean arterial pressure (MAP) at hour 3 after the start of infusion was defined as an increase from baseline of at least 10 mm Hg or an increase to at least 75 mm Hg, without an increase in the dose of background vasopressors.

    Hour 3

Study Arms (2)

LJPC-501 (angiotensin II)

EXPERIMENTAL

Treatment arm

Drug: LJPC-501

Placebo (0.9% sodium chloride solution)

PLACEBO COMPARATOR

Placebo arm

Drug: Placebo

Interventions

Treatment arm

Also known as: angiotensin II
LJPC-501 (angiotensin II)

PBO

Also known as: 0.9% Sodium Chloride Solution USP
Placebo (0.9% sodium chloride solution)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Adult patients ≥ 18 years of age with CRH, defined as those who require a total sum catecholamine dose of \> 0.2 mcg/kg/min for a minimum of 6 hours and a maximum of 48 hours, to maintain a MAP between 55-70 mmHg.
  • Patients are required to have central venous access and an arterial line present, and these are expected to remain present for at least the initial 48 hours of study.
  • Patients are required to have an indwelling urinary catheter present, and it is expected to remain present for at least the initial 48 hours of study.
  • Patients must have received at least 25 mL/kg of crystalloid or colloid equivalent over the previous 24-hour period, and be adequately volume resuscitated in the opinion of the treating investigator.
  • Patients must have clinical features of high-output shock by meeting one of the following criteria.
  • Central venous oxygen saturation (ScvO2) \> 70% (either by oximetry catheter or by central venous blood gas) and central venous pressure (CVP) \> 8 mmHg.
  • Cardiac Index (CI) \> 2.3 L/min/1.73 m2. Patient must meet 5a or 5b to be eligible.
  • Patient or legal surrogate is willing and able to provide written informed consent and comply with all protocol requirements.

You may not qualify if:

  • Patients who are \< 18 years of age.
  • Any patient with burns covering \> 20% of total body surface area (TBSA).
  • Patients with a Cardiovascular (CV) SOFA score ≤ 3.
  • Patients diagnosed with acute occlusive coronary syndrome requiring intervention.
  • Patients on veno-arterial (VA) ECMO.
  • Patients who have been on ECMO for less than 12 hours.
  • Patients in liver failure with a Model for End-Stage Liver Disease (MELD) score of ≥ 30.
  • Patients with a history of asthma or who are currently experiencing bronchospasm requiring the use of inhaled bronchodilators, if not mechanically ventilated.
  • Patients with acute mesenteric ischemia or a history of mesenteric ischemic.
  • Patients with a history of, presence of, or highly-suspected of having an aortic dissection or abdominal aortic aneurysm.
  • Patients requiring more than 500 mg daily of hydrocortisone or equivalent glucocorticoid medication as a standing dose.
  • Patients with Raynaud's phenomenon, systemic sclerosis or vasospastic disease.
  • Patients with an expected lifespan of \< 12 hours.
  • Patients with active bleeding AND an anticipated need (within 48 hours of initiation of the study) for transfusion of \> 4 units of packed red blood cells.
  • Patients with active bleeding AND hemoglobin \< 7g/dL or any other condition that would contraindicate serial blood sampling.
  • +4 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (115)

Pulmonary Associates of Mobile, PC

Mobile, Alabama, 36608, United States

Location

Mayo Clinic Arizona

Phoenix, Arizona, 85054, United States

Location

Loma Linda University Medical Center

Loma Linda, California, 92354, United States

Location

Keck Hospital of USC

Los Angeles, California, 90033, United States

Location

Los Angeles County + University of Southern California Medical Center

Los Angeles, California, 90033, United States

Location

University of California, Los Angeles

Los Angeles, California, 90095, United States

Location

University of California, Irvine Medical Center

Orange, California, 92868, United States

Location

University of California, Davis

Sacramento, California, 95817, United States

Location

University of Florida

Gainesville, Florida, 32610, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

Joseph M. Still Research Foundation, Inc.

Augusta, Georgia, 30909, United States

Location

Eastern Idaho Regional Medical Center

Idaho Falls, Idaho, 83404, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Methodist Hospital, Indiana University Health Physicians

Indianapolis, Indiana, 46202, United States

Location

Kentucky Lung Clinic

Hazard, Kentucky, 41701, United States

Location

University of Louisville

Louisville, Kentucky, 40292, United States

Location

University of Maryland Medical Center

Baltimore, Maryland, 21201, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

Hennepin County Medical Center

Minneapolis, Minnesota, 55415, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

St. Paul Regions Hospital

Saint Paul, Minnesota, 55101, United States

Location

Saint Louis University

St Louis, Missouri, 63104, United States

Location

Sunrise Hospital/eStudySite

Las Vegas, Nevada, 89109, United States

Location

Englewood Hospital & Medical Center

Englewood, New Jersey, 07631, United States

Location

Rutgers Robert Wood Johnson Medical Center

New Brunswick, New Jersey, 08901, United States

Location

Montefiore Medical Center, Weiler Division

The Bronx, New York, 10461, United States

Location

Montefiore Medical Center

The Bronx, New York, 10467, United States

Location

Duke Regional Hospital

Durham, North Carolina, 27704, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Moses Cone Health

Greensboro, North Carolina, 27403, United States

Location

Wesley Long Hospital

Greensboro, North Carolina, 27403, United States

Location

University of Cincinnati Medical Center

Cincinnati, Ohio, 45267, United States

Location

Cleveland Clinic - Fairview Hospital

Cleveland, Ohio, 44195, United States

Location

The Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

Riverside Methodist Hospital

Columbus, Ohio, 43215, United States

Location

University of Oklahoma Medical Center

Oklahoma City, Oklahoma, 73104, United States

Location

Oregon Health & Sciences University

Portland, Oregon, 97239, United States

Location

Lehigh Valley Health Network

Allentown, Pennsylvania, 18103, United States

Location

Geisinger Medical Center

Danville, Pennsylvania, 17822, United States

Location

Penn Presbyterian Medical Center

Philadelphia, Pennsylvania, 19104, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15261, United States

Location

Erlanger Hospital

Chattanooga, Tennessee, 37408, United States

Location

Memorial Hospital

Chattanooga, Tennessee, 37408, United States

Location

Baylor University

Dallas, Texas, 75246, United States

Location

John Peter Smith Hospital - JPS Health Network

Fort Worth, Texas, 76104, United States

Location

U.S. Army Military Medical Center

San Antonio, Texas, 78234, United States

Location

Inova Fairfax Hospital

Falls Church, Virginia, 22042, United States

Location

Virginia Commonwealth University Medical Center

Richmond, Virginia, 23298, United States

Location

Canberra Hospital

Garran, Australian Capital Territory, 2605, Australia

Location

John Hunter Hospital

New Lambton Heights, New South Wales, 2305, Australia

Location

Nepean Hospital

Penrith, New South Wales, 2751, Australia

Location

Royal North Shore Hospital

St Leonards, New South Wales, 2065, Australia

Location

The Wesley Hospital

Auchenflower, Queensland, 4066, Australia

Location

Royal Brisbane & Women's Hospital

Herston, Queensland, 4029, Australia

Location

Gold Coast University Hospital

Southport, Queensland, 4215, Australia

Location

Princess Alexandra Hospital

Woolloongabba, Queensland, 4102, Australia

Location

Flinders Medical Centre

Bedford Park, South Australia, 5042, Australia

Location

Royal Hobart Hospital

Hobart, Tasmania, 7000, Australia

Location

Monash Medical Centre

Clayton, Victoria, 3168, Australia

Location

Frankston Hospital

Frankston, Victoria, 3199, Australia

Location

Austin Hospital

Heidelberg, Victoria, 3084, Australia

Location

St. Vincent's Hospital

Melbourne, Victoria, 3065, Australia

Location

Royal Melbourne Hospital

Parkville, Victoria, 3050, Australia

Location

Fiona Stanley Hospital

Murdoch, Western Australia, 6150, Australia

Location

Royal Perth Hospital

Perth, Western Australia, 6000, Australia

Location

Royal Adelaide Hospital

Adelaide, 5000, Australia

Location

UZ Antwerpen

Antwerp, 2650, Belgium

Location

Brugmann University Hospital

Brussels, 1020, Belgium

Location

Erasme University Hospital

Brussels, 1070, Belgium

Location

UZ Brussel

Brussels, 1090, Belgium

Location

UZ Gent

Ghent, 9000, Belgium

Location

South Health Campus & Rockyview General Hospital

Calgary, Alberta, T2N 2T9, Canada

Location

Royal Alexandra Hospital

Edmonton, Alberta, T5H 3V9, Canada

Location

University of Alberta Hospital

Edmonton, Alberta, T6G 2B7, Canada

Location

St. Paul's Hospital

Vancouver, British Columbia, V6Z 1Y6, Canada

Location

Royal Jubilee Hospital

Victoria, British Columbia, V8R 1J8, Canada

Location

Victoria General Hospital

Victoria, British Columbia, V8Z 6R5, Canada

Location

Kingston General Hospital

Kingston, Ontario, K7I 2V7, Canada

Location

The Ottawa Hospital - Civic Campus

Ottawa, Ontario, KIH 8L6, Canada

Location

The Ottawa Hospital - General Campus

Ottawa, Ontario, KIH 8L6, Canada

Location

St. Michael's Hospital

Toronto, Ontario, M5B1W8, Canada

Location

Helsinki University Central Hospital

Helsinki, 00290, Finland

Location

Kuopio University Hospital

Kuopio, 70210, Finland

Location

Tampere University Hospital

Tampere, 33520, Finland

Location

Turku University Hospital

Turku, 20521, Finland

Location

Jean Minjoz Hospital

Besançon, 25030, France

Location

Hospital Roger Salengro, CHRU de Lille

Lille, 59037, France

Location

CHU Nice

Nice, 06202, France

Location

Bordeaux Hospital University Center

Pessac, 33604, France

Location

University Medical Center, Berlin

Berlin, 10117, Germany

Location

University Hospital Münster

Münster, 48149, Germany

Location

Auckland City Hospital

Grafton, Auckland, 1023, New Zealand

Location

Middlemore Hospital

Otahuhu, Auckland, New Zealand

Location

Wellington Hospital

Newtown, Wellington Region, 6021, New Zealand

Location

Bern University Hospital

Bern, CH-3010, Switzerland

Location

Southampton General Hospital

Southampton, Hampshire, SO16 6YD, United Kingdom

Location

Norfolk and Norwich University Hospitals

Norwich, Norfolk, NR4 7UY, United Kingdom

Location

Sunderland Royal Hospital

Sunderland, Tyne and Wear, SR4 7TP, United Kingdom

Location

Birmingham Heartlands Hospital

Birmingham, West Midlands, B9 5SS, United Kingdom

Location

Queen Elizabeth Hospital

Birmingham, West Midlands, B15 2WB, United Kingdom

Location

Bristol Royal Infirmary

Bristol, BS2 8HW, United Kingdom

Location

Addenbrooke's Hospital

Cambridge, CB2 0QQ, United Kingdom

Location

Hull Royal Infirmary

Hull, HU3 2JZ, United Kingdom

Location

Royal London Hospital

London, E1 1BB, United Kingdom

Location

St. Thomas Hospital

London, SE1 7EH, United Kingdom

Location

St. George's University Hospital

London, SW17 0QT, United Kingdom

Location

Charing Cross Hospital

London, W6 8RF, United Kingdom

Location

Hammersmith Hospital

London, W6 8RF, United Kingdom

Location

Royal Liverpool Hospital

Merseyside, L7 8XP, United Kingdom

Location

Northampton General Hospital

Northampton, NN1 5BD, United Kingdom

Location

Derriford Hospital

Plymouth, PL6 8DH, United Kingdom

Location

Related Publications (9)

  • Leisman DE, Wieruszewski PM, Busse LW, Chawla LS, Hibbert KA, Handisides DR, Khanna AK, Ostermann M, McCurdy MT, Adams CD, Hodges TN, Bellomo R; ATHOS-3 Investigators. An index of the initial blood pressure response to angiotensin II treatment and its association with clinical outcomes in vasodilatory shock. Crit Care. 2025 Feb 19;29(1):81. doi: 10.1186/s13054-025-05311-z.

  • Leisman DE, Handisides DR, Busse LW, Chappell MC, Chawla LS, Filbin MR, Goldberg MB, Ham KR, Khanna AK, Ostermann M, McCurdy MT, Adams CD, Hodges TN, Bellomo R; ATHOS-3 Investigators. ACE inhibitors and angiotensin receptor blockers differentially alter the response to angiotensin II treatment in vasodilatory shock. Crit Care. 2024 Apr 18;28(1):130. doi: 10.1186/s13054-024-04910-6.

  • Leisman DE, Handisides DR, Chawla LS, Albertson TE, Busse LW, Boldt DW, Deane AM, Gong MN, Ham KR, Khanna AK, Ostermann M, McCurdy MT, Thompson BT, Tumlin JS, Adams CD, Hodges TN, Bellomo R. Angiotensin II treatment is associated with improved oxygenation in ARDS patients with refractory vasodilatory shock. Ann Intensive Care. 2023 Dec 16;13(1):128. doi: 10.1186/s13613-023-01227-5.

  • Wieruszewski PM, Bellomo R, Busse LW, Ham KR, Zarbock A, Khanna AK, Deane AM, Ostermann M, Wunderink RG, Boldt DW, Kroll S, Greenfeld CR, Hodges T, Chow JH; Angiotensin II for the Treatment of High-Output Shock 3 (ATHOS-3) Investigators. Initiating angiotensin II at lower vasopressor doses in vasodilatory shock: an exploratory post-hoc analysis of the ATHOS-3 clinical trial. Crit Care. 2023 May 5;27(1):175. doi: 10.1186/s13054-023-04446-1.

  • Bellomo R, Forni LG, Busse LW, McCurdy MT, Ham KR, Boldt DW, Hastbacka J, Khanna AK, Albertson TE, Tumlin J, Storey K, Handisides D, Tidmarsh GF, Chawla LS, Ostermann M. Renin and Survival in Patients Given Angiotensin II for Catecholamine-Resistant Vasodilatory Shock. A Clinical Trial. Am J Respir Crit Care Med. 2020 Nov 1;202(9):1253-1261. doi: 10.1164/rccm.201911-2172OC.

  • Bellomo R, Wunderink RG, Szerlip H, English SW, Busse LW, Deane AM, Khanna AK, McCurdy MT, Ostermann M, Young PJ, Handisides DR, Chawla LS, Tidmarsh GF, Albertson TE. Angiotensin I and angiotensin II concentrations and their ratio in catecholamine-resistant vasodilatory shock. Crit Care. 2020 Feb 6;24(1):43. doi: 10.1186/s13054-020-2733-x.

  • Senatore F, Jagadeesh G, Rose M, Pillai VC, Hariharan S, Liu Q, McDowell TY, Sapru MK, Southworth MR, Stockbridge N. FDA Approval of Angiotensin II for the Treatment of Hypotension in Adults with Distributive Shock. Am J Cardiovasc Drugs. 2019 Feb;19(1):11-20. doi: 10.1007/s40256-018-0297-9.

  • Khanna A, English SW, Wang XS, Ham K, Tumlin J, Szerlip H, Busse LW, Altaweel L, Albertson TE, Mackey C, McCurdy MT, Boldt DW, Chock S, Young PJ, Krell K, Wunderink RG, Ostermann M, Murugan R, Gong MN, Panwar R, Hastbacka J, Favory R, Venkatesh B, Thompson BT, Bellomo R, Jensen J, Kroll S, Chawla LS, Tidmarsh GF, Deane AM; ATHOS-3 Investigators. Angiotensin II for the Treatment of Vasodilatory Shock. N Engl J Med. 2017 Aug 3;377(5):419-430. doi: 10.1056/NEJMoa1704154. Epub 2017 May 21.

  • Schmull S, Wang Z, Gao L, Lv J, Li J, Xue S. Angiotensins and Their Receptors in Cardiac and Vascular Injury. Curr Hypertens Rev. 2016;12(3):170-180. doi: 10.2174/1573402112666160302101545.

MeSH Terms

Conditions

Sepsis

Interventions

Angiotensin IAngiotensin II

Condition Hierarchy (Ancestors)

InfectionsSystemic Inflammatory Response SyndromeInflammationPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

AngiotensinsPeptide HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsNeuropeptidesPeptidesAmino Acids, Peptides, and ProteinsOligopeptidesNerve Tissue ProteinsProteinsAutacoidsInflammation MediatorsBiological Factors

Results Point of Contact

Title
George Tidmarsh, MD, PhD
Organization
La Jolla Pharmaceutical Company

Study Officials

  • George F Tidmarsh, MD, PhD

    La Jolla Pharmaceutical Company

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 1, 2015

First Posted

January 14, 2015

Study Start

March 1, 2015

Primary Completion

December 1, 2016

Study Completion

February 18, 2017

Last Updated

March 27, 2018

Results First Posted

January 17, 2018

Record last verified: 2018-01

Locations