NCT02245568

Brief Summary

The purpose of this study is to provide subjects who have completed participation in a Phase 2 or Phase 3 trial of LMTM continued access to therapy and to evaluate the long-term safety of LMTM.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
913

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Aug 2014

Typical duration for phase_3

Geographic Reach
17 countries

135 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

August 1, 2014

Completed
26 days until next milestone

First Submitted

Initial submission to the registry

August 27, 2014

Completed
23 days until next milestone

First Posted

Study publicly available on registry

September 19, 2014

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2017

Completed
3.1 years until next milestone

Results Posted

Study results publicly available

June 2, 2020

Completed
Last Updated

May 24, 2023

Status Verified

May 1, 2023

Enrollment Period

2.8 years

First QC Date

August 27, 2014

Results QC Date

May 15, 2020

Last Update Submit

May 22, 2023

Conditions

Keywords

DementiaAlzheimer DiseasebvFTDFrontotemporal DementiaNeurodegenerative DiseasesBrain DiseasesCognitive Disorders

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Serious or Non-serious Adverse Events

    Study-emergent adverse events (including the onset of new adverse events or worsening of pre-existing adverse events) were recorded from the time of first dose in this study to the end of study participation. All laboratory test, vital sign, or electrocardiogram parameter abnormalities deemed clinically significant by the Investigator were to be reported as adverse events.

    Up to 34 months

Study Arms (1)

LMTM

EXPERIMENTAL
Drug: LMTM

Interventions

LMTMDRUG

The initial LMTM dose was 200 mg/day (one 100-mg tablet twice daily), except in subjects with bvFTD who were taking a reduced dose (i.e., 100 mg/day) upon entering this extension study. The dose could be increased (after at least 13 weeks of treatment) or decreased (at any time at or after 2 weeks of treatment) by the Investigator in 100-mg increments or decrements. The maximum allowable dose was 300 mg/day (or in those countries where limited by a Competent Authority or Ethics Committee, 200 mg/day).

LMTM

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Subjects with all cause dementia and probable Alzheimer's disease at enrollment and who completed participation in one of the following three TauRx studies (inclusive of the 4-week post-treatment follow-up visit): TRx-237-005, TRx-237-008, or TRx-237-015.
  • Subjects with a diagnosis of probable bvFTD at enrollment and who completed participation in TauRx study TRx-237-007 through Visit 9 (Week 52).
  • Females, if of child-bearing potential, must practice true abstinence or continue to use adequate contraception and agree to maintain this throughout the study
  • Subject, and/or, in the case of reduced decision-making capacity, legally acceptable representative(s) consistent with national law and ethics approval is/are able to read, understand, and provide written informed consent
  • Has an identified adult caregiver who is willing to provide written informed consent for his/her own participation; is able to read, understand, and speak the designated language at the study site; either lives with the subject or sees the subject for ≥1 hour/day ≥3 days/week; agrees to accompany the subject to each study visit; and is able to verify daily compliance with study drug
  • Able to comply with the study procedures

You may not qualify if:

  • History of swallowing difficulties
  • Pregnant or breastfeeding
  • Clinically significant laboratory, pulse co-oximetry, electrocardiogram, or imaging abnormality (in originating study) or emergent intercurrent illness that, in the judgment of the principal investigator, could result in the risk of participation outweighing the potential benefit
  • Current participation in, or intent to enroll in, another clinical trial of a drug, biologic, device, or medical food
  • In Germany, subjects mandated to reside in a continuous care or assisted living facility or those whose willingness to participate in the clinical trial may be unduly influenced

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (135)

Xenoscience, Inc / 21st Century Neurology

Phoenix, Arizona, 85004, United States

Location

Southern California Research, LLC

Fountain Valley, California, 92708, United States

Location

Feldman, Robert MD

Laguna Hills, California, 92653, United States

Location

Collaborative Neuroscience Network

Long Beach, California, 90806, United States

Location

The Shankle Clinic

Newport Beach, California, 92663, United States

Location

Neuro-Therapeutics, Inc.

Pasadena, California, 91105, United States

Location

Pacific Research Network

San Diego, California, 92103, United States

Location

San Francisco Clinical Research Center

San Francisco, California, 94118, United States

Location

Memory and Aging Centre

San Francisco, California, 94158, United States

Location

Schuster Medical Research Institute

Sherman Oaks, California, 91403, United States

Location

Mile High Research Center

Denver, Colorado, 80218, United States

Location

Institute for Neurodegenerative Disorders

New Haven, Connecticut, 06510, United States

Location

Yale University School of Medicine

New Haven, Connecticut, 06510, United States

Location

Coastal Connecticut Research, LLC

New London, Connecticut, 06320, United States

Location

JEM Research

Atlantis, Florida, 33462, United States

Location

Bradenton Research Center

Bradenton, Florida, 34205, United States

Location

Meridien Research

Brooksville, Florida, 34601, United States

Location

Brain Matters Research

Delray Beach, Florida, 33445, United States

Location

MD Clinical

Hallandale, Florida, 33009, United States

Location

Mayo Clinic

Jacksonville, Florida, 32224, United States

Location

CNS Healthcare, Inc

Jacksonville, Florida, 32256, United States

Location

Miami Research Associates

Miami, Florida, 33143, United States

Location

Compass Research, LLC

Orlando, Florida, 32806, United States

Location

The Roskamp Institute, Inc.

Sarasota, Florida, 34243, United States

Location

Axiom Clinical Research of Florida

Tampa, Florida, 33609, United States

Location

University of South Florida

Tampa, Florida, 33613, United States

Location

Compass Research, LLC - North Clinic

The Villages, Florida, 32162, United States

Location

iResearch Atlanta

Decatur, Georgia, 30030, United States

Location

Neurostudies.net

Decatur, Georgia, 30033, United States

Location

Alexian Brothers Neurosciences Institute

Elk Grove Village, Illinois, 60007, United States

Location

Ruan Neurology Clinic and Research Center

Des Moines, Iowa, 50314, United States

Location

ActivMed Practices & Research

Methuen, Massachusetts, 01844, United States

Location

Mayo Clinic, Alzheimer's Disease Research Center

Rochester, Minnesota, 55905, United States

Location

Neurological Research Center - Hattiesburg Clinic

Hattiesburg, Mississippi, 39401, United States

Location

Millennium Psychiatric Associates

Creve Coeur, Missouri, 63141, United States

Location

Memory Enhancement Center of America, Inc

Eatontown, New Jersey, 07724, United States

Location

The Atlantic Neuroscience Institute

Springfield, New Jersey, 07801, United States

Location

Advanced Memory Research Institute of NJ PC

Toms River, New Jersey, 08757, United States

Location

Neurological Associates of Albany, P. C.

Albany, New York, 12208, United States

Location

SPRI

Brooklyn, New York, 11235, United States

Location

Columbia University Taub Institute

New York, New York, 10032, United States

Location

Research Foundation for Mental Hygiene, Inc.

Orangeburg, New York, 10962, United States

Location

UNC Department of Neurology, Physicians Office Building

Chapel Hill, North Carolina, 27599, United States

Location

Clinical Trials of America, Inc

Winston-Salem, North Carolina, 27103, United States

Location

Neurobehavioral Clinical Research

Canton, Ohio, 44718, United States

Location

University Hospitals Case Medical Center, Neurology Clinical Trials Unit

Cleveland, Ohio, 44106, United States

Location

Rivus Wellness and Research Institute

Oklahoma City, Oklahoma, 73112, United States

Location

The Clinical Trial Center, LLC

Jenkintown, Pennsylvania, 19046, United States

Location

Hospital of the University of Pennsylvania, Department of Neurology

Philadelphia, Pennsylvania, 19104, United States

Location

RI Hospital

Providence, Rhode Island, 02903, United States

Location

Neurology Clinic, P.C.

Cordova, Tennessee, 38018, United States

Location

Clinical Neuroscience Solutions CNS Healthcare

Memphis, Tennessee, 38119, United States

Location

FutureSearch Trials of Neurology

Austin, Texas, 78731, United States

Location

Senior Adults Specialty Research, Inc.

Austin, Texas, 78757, United States

Location

FutureSearch Trials of Dallas, LP

Dallas, Texas, 75231, United States

Location

University of Virginia Adult Neurology, Primary Care Center

Charlottesville, Virginia, 22903, United States

Location

Independent Psychiatric Consultants

Waukesha, Wisconsin, 53188, United States

Location

Frontotemporal Research Group

Camperdown, New South Wales, 2000, Australia

Location

Division of Rehabilitation and Aged Care

Hornsby, New South Wales, 2077, Australia

Location

Southern Neurology Pty Limited

Kogarah, New South Wales, 2217, Australia

Location

Discipline of Psychiatry, University of Queensland

Herston, Queensland, 4006, Australia

Location

Royal Adelaide Hospital Memory Trials Centre

Adelaide, South Australia, 5000, Australia

Location

Box Hill Hospital

Box Hill, Victoria, 3128, Australia

Location

Medical and Cognitive Research Unit, Austin Health Heidelberg Repatriation Hospital

Heidelberg West, Victoria, 3081, Australia

Location

McCusker Alzheimer's Research Foundation Inc

Nedlands, Western Australia, 6009, Australia

Location

Neurodegenerative Disorders Research Pty Ltd

Subiaco, Western Australia, 6008, Australia

Location

University Hospital Ghent Department of Neurology

Ghent, 9000, Belgium

Location

Jessa Hospital

Hasselt, 3500, Belgium

Location

GZA Sint-Augustinus

Wilrijk, 2610, Belgium

Location

Heritage Medical Research Clinic

Calgary, Alberta, T2N 4Z6, Canada

Location

Okanagan Clinical Trials

Kelowna, British Columbia, V1Y 1Z9, Canada

Location

University of British Columbia Hospital, Clinic for Alzheimer Disease and Related Disorders

Vancouver, British Columbia, V6T 1Z3, Canada

Location

Vancouver Island Health Authority

Victoria, British Columbia, V8R 1J8, Canada

Location

True North Clinical Research Halifax Inc

Halifax, Nova Scotia, B3S 1M7, Canada

Location

True North Clinical Research Kentville Inc

Kentville, Nova Scotia, B4N 4K9, Canada

Location

Geriatric Clinical Trials Group, St. Joseph's Health Care, Parkwood Hospital Site

London, Ontario, N6C 0A7, Canada

Location

Toronto Memory Program

Toronto, Ontario, M3B 2S7, Canada

Location

Jewish General Hospital

Montreal, Quebec, H3T 1E2, Canada

Location

McGill Centre for Studies in Aging, Alzheimer Disease Research Unit

Verdun, Quebec, H4H 1R3, Canada

Location

University Hospital Centre Zagreb, Department of Neurology

Zagreb, 10000, Croatia

Location

University Psychiatric Hospital Vrapče

Zagreb, 10090, Croatia

Location

University of Eastern Finland, Brain Research Unit Mediteknia

Kuopio, 70210, Finland

Location

Clinical Research Services Turku (CRST)

Turku, 20520, Finland

Location

Hôpitaux Civils de Colmar

Colmar, Cedex, 68024, France

Location

Centre de Recherche Clinique

Toulouse, 31059, France

Location

Hôpital de Charpennes

Villeurbanne, 69100, France

Location

Charité, University Medicine Berlin, CBF, Neurology

Berlin, 12200, Germany

Location

Arzeneimittelforschung Leipzig GmbH

Leipzig, 04107, Germany

Location

University Kuala Lumpur Royal College of Medicine

Ipoh, 30450, Malaysia

Location

Hospital Sultan Ismail

Johor Bahru, 81100, Malaysia

Location

University Malaya Medical Centre

Kuala Lumpur, 50603, Malaysia

Location

Erasmus University Medical Center

Rotterdam, 3015, Netherlands

Location

Psychiatry Hospital "Dr. Gheorghe Preda", Department of Psychiatry III

Sibiu, 550082, Romania

Location

Non-governmental Healthcare Institution "Central Clinical Hospital #6 of the JSC "Russian Railways"

Moscow, 109388, Russia

Location

Mental Health Research Center of the Russian Academy of Medical Sciences, Gerontopsychiatry department

Moscow, 115522, Russia

Location

Mental Health Research Center of the Russian Academy of Medical Sciences

Moscow, 115522, Russia

Location

City Clinical Hospital #34, City Scientific Practical Neurological Center

Novosibirsk, 630054, Russia

Location

City Geriatric Medical and Social Center

Saint Petersburg, 190103, Russia

Location

Saint Petersburg Psychoneurological Research Institute n. a. V.M. Bekhterev

Saint Petersburg, 192019, Russia

Location

State Budgetary Healthcare Institution of Sverdlovsk region "Sverdlovsk Regional Clinical Psychiatric Hospital"

Yekaterinburg, 620030, Russia

Location

National University Hospital (NUH)

Singapore, 119228, Singapore

Location

National Neuroscience Institute (NNI)

Singapore, 308433, Singapore

Location

Dong-A University Hospital

Busan, 602-715, South Korea

Location

Gachon University Gil Medical Center

Incheon, 405-760, South Korea

Location

Samsung Medical Center

Seoul, 135-710, South Korea

Location

Seoul National University Boramae Medical Center

Seoul, 156-707, South Korea

Location

Seoul National University Hospital

Seoul, South Korea

Location

Fundació ACE

Barcelona, 08028, Spain

Location

Hospital Clinico San Carlos

Madrid, 28040, Spain

Location

Hospital Universitario La Paz

Madrid, 28046, Spain

Location

Hospital Viamed Montecanal

Zaragoza, 50006, Spain

Location

Chang Gung Memorial Hospital, Kaohsiung

Kaohsiung City, Taiwan

Location

China Medical University Hospital

Taichung, Taiwan

Location

National Taiwan University Hospital

Taipei, Taiwan

Location

Taipei Veterans General Hospital

Taipei, Taiwan

Location

Chang Gung Memorial Hospital, Linkou

Taoyuan District, Taiwan

Location

Grampian NHS, Royal Cornhill Hospital

Aberdeen, AB25 2ZH, United Kingdom

Location

RICE - The Research Institute for the Care of Older People

Bath, BA1 3NG, United Kingdom

Location

Belfast Health and Social Care Trust (BHSCT)

Belfast, BT12 6BA, United Kingdom

Location

The Barberry Centre

Birmingham, B15 2SG, United Kingdom

Location

MAC Clinical Research Ltd

Blackpool, FY2 0JH, United Kingdom

Location

MAC Clinical Research Ltd

Cannock, WS11 0BN, United Kingdom

Location

Sussex Partnership NHS Foundation Trust, Cognitive Treatment and Research Unit

Crowborough, TN6 1HB, United Kingdom

Location

St Margaret's Hospital Mental Health Unit

Epping, CM16 6TN, United Kingdom

Location

Cognition Health Ltd

Guildford, GU27YD, United Kingdom

Location

MAC Clinical Research Ltd

Leeds, LS10 1DU, United Kingdom

Location

Cognition Health Ltd.

London, W1G 9JF, United Kingdom

Location

Imperial College Healthcare NHS Trust - Charing Cross Hospital

London, W6 8RF, United Kingdom

Location

Leonard Wolfson Experimental Neurology Centre

London, WC1N 3BG, United Kingdom

Location

MAC Clinical Research Ltd

Manchester, M13 9NQ, United Kingdom

Location

Nuffield Department of Clinical Neurosciences

Oxford, OX3 9DU, United Kingdom

Location

Redwoods Centre

Shrewsbury, SY3 8DS, United Kingdom

Location

Wessex Neurological Centre, Southampton General Hospital

Southampton, SO16 6YD, United Kingdom

Location

Memory Assessment and Research Centre (MARC)

Southampton, SO30 3JB, United Kingdom

Location

Kingshill Research Centre, Victoria Hospital

Swindon, SN3 6BW, United Kingdom

Location

MeSH Terms

Conditions

Alzheimer DiseaseDementiaFrontotemporal DementiaNeurodegenerative DiseasesBrain DiseasesCognitive Dysfunction

Condition Hierarchy (Ancestors)

Central Nervous System DiseasesNervous System DiseasesTauopathiesNeurocognitive DisordersMental DisordersFrontotemporal Lobar DegenerationTDP-43 ProteinopathiesProteostasis DeficienciesMetabolic DiseasesNutritional and Metabolic DiseasesCognition Disorders

Results Point of Contact

Title
Dr. Diane Downie
Organization
TauRx Therapeutics Ltd

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR
Expanded Access
Yes

Study Record Dates

First Submitted

August 27, 2014

First Posted

September 19, 2014

Study Start

August 1, 2014

Primary Completion

May 1, 2017

Study Completion

May 1, 2017

Last Updated

May 24, 2023

Results First Posted

June 2, 2020

Record last verified: 2023-05

Locations