NCT02229981

Brief Summary

This is a sequential Phase I and IIa study to identify the maximum tolerated dose and to evaluate safety, tolerability, toxicity, pharmacokinetics and pharmacodynamics of the oral sphingosine kinase inhibitor ABC294640 specifically in patients with diffuse large B-cell lymphoma (DLBCL), including virus-associated (e.g., KSHV- or EBV-associated) DLBCL or Kaposi Sarcoma (KS) after failure of or intolerance to initial standard therapy.

Trial Health

30
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Timeline
Completed

Started Jul 2014

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
withdrawn

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2014

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

August 28, 2014

Completed
6 days until next milestone

First Posted

Study publicly available on registry

September 3, 2014

Completed
4.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2019

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2019

Completed
Last Updated

December 7, 2017

Status Verified

December 1, 2017

Enrollment Period

4.9 years

First QC Date

August 28, 2014

Last Update Submit

December 5, 2017

Conditions

Keywords

LymphomaB-cell LymphomasDiffuse Large B-cell LymphomaLymphosarcomaKaposi's Sarcoma-associated HerpesvirusKHSVHuman Immunodeficiency VirusHIVEpstein-Barr VirusEBVKaposi sarcoma

Outcome Measures

Primary Outcomes (2)

  • Determine Maximum tolerated dose (MTD) of ABC294640 in patients with refractory/relapsed DLBCL or KS and determine tolerability at MTD.

    Patients will be followed until a dose limiting toxicity (DLT) is experienced, if present, expected within the first 8 weeks

  • Evaluate safety of ABC294640 in patients with refractory/relapsed DLBCL or KS

    If present, expected within 8 weeks

Secondary Outcomes (4)

  • Measure plasma levels of ABC294640 (pharmacokinetics) in patients with DLBCL or KS

    Days 1 and 28, 1,2, 4, 8 and 24 hours post drug administration

  • Measure plasma levels of sphingosine-1-phosphate in response to ABC294640 in patients with DLBCL or KS

    Days 1,8,15 and 28 in Cycle 1, Days 14 and 28 for all subsequent cycles and at the end of treatment study

  • Measure levels of circulating CD4+ T cell count, KSHV/EBV viral loads, and HIV viral load (if applicable) in response to ABC294640 in patients with DLBCL or KS

    Days 1, 8, 15 and 22 for cycles 1-3 and Days 1, 8, 15, 22 and 28 for Cycle 4

  • Evaluate antitumor activity of ABC294640 in virus-associated DLBCL or KS patients by objective radiographic assessment using PET (DLBCL) or CT (KS) criteria, or measurement of clinically evident skin lesions (KS)

    Within 14 Days of Treatment Day 1 and then on Day 28 of Cycles 2, 4, 6, 8, etc., stopping if tumor progression is observed

Study Arms (1)

ABC294640

EXPERIMENTAL

Patients will receive ABC294640 orally in gelatin capsules BID.

Drug: ABC294640

Interventions

Also known as: Yeliva
ABC294640

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may not qualify if:

  • For patients with DLBCL, the patient is not a candidate for hematopoietic stem cell transplantation (as determined by medical oncologists at participating institutions) or has failed stem cell transplantation.
  • Tumor progression after receiving standard/approved chemotherapy, or lack of candidacy for standard therapy.
  • One or more tumors measurable on PET-CT scan (DLBCL), CT scan (KS), or by clinical exam of skin (KS).
  • Eastern Cooperative Oncology Group (ECOG) performance status ≤ 3.
  • Life expectancy of at least 3 months.
  • Age ≥ 18 years.
  • Signed, written IRB-approved informed consent.
  • A negative pregnancy test (if female).
  • Acceptable liver function:
  • Bilirubin ≤ 3 times upper limit of normal (CTCAE Grade 2 baseline)
  • AST (SGOT), ALT (SGPT) ≤ 3 x ULN (CTCAE Grade 1 baseline)
  • Serum creatinine ≤ 1.5 X ULN (CTCAE Grade 1 baseline)
  • Acceptable hematologic status:
  • Absolute neutrophil count ≥ 1000 cells/mm3
  • Platelet count ≥ 75,000 (plt/mm3) (CTCAE Grade 1 baseline)
  • +20 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Louisiana State University Health Sciences Center

New Orleans, Louisiana, 70112, United States

Location

Related Publications (3)

  • Qin Z, Dai L, Trillo-Tinoco J, Senkal C, Wang W, Reske T, Bonstaff K, Del Valle L, Rodriguez P, Flemington E, Voelkel-Johnson C, Smith CD, Ogretmen B, Parsons C. Targeting sphingosine kinase induces apoptosis and tumor regression for KSHV-associated primary effusion lymphoma. Mol Cancer Ther. 2014 Jan;13(1):154-64. doi: 10.1158/1535-7163.MCT-13-0466. Epub 2013 Oct 18.

    PMID: 24140934BACKGROUND
  • Dai L, Plaisance-Bonstaff K, Voelkel-Johnson C, Smith CD, Ogretmen B, Qin Z, Parsons C. Sphingosine kinase-2 maintains viral latency and survival for KSHV-infected endothelial cells. PLoS One. 2014 Jul 10;9(7):e102314. doi: 10.1371/journal.pone.0102314. eCollection 2014.

    PMID: 25010828BACKGROUND
  • Dai L, Trillo-Tinoco J, Bai A, Chen Y, Bielawski J, Del Valle L, Smith CD, Ochoa AC, Qin Z, Parsons C. Ceramides promote apoptosis for virus-infected lymphoma cells through induction of ceramide synthases and viral lytic gene expression. Oncotarget. 2015 Sep 15;6(27):24246-60. doi: 10.18632/oncotarget.4759.

    PMID: 26327294BACKGROUND

MeSH Terms

Conditions

Lymphoma, Large B-Cell, DiffuseSarcoma, KaposiLymphomaLymphoma, B-CellLymphoma, Non-HodgkinAcquired Immunodeficiency SyndromeEpstein-Barr Virus Infections

Interventions

3-(4-chlorophenyl)-adamantane-1-carboxylic acid (pyridin-4-ylmethyl)amide

Condition Hierarchy (Ancestors)

Neoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesHerpesviridae InfectionsDNA Virus InfectionsVirus DiseasesInfectionsSarcomaNeoplasms, Connective and Soft TissueNeoplasms, Vascular TissueHIV InfectionsBlood-Borne InfectionsCommunicable DiseasesSexually Transmitted Diseases, ViralSexually Transmitted DiseasesLentivirus InfectionsRetroviridae InfectionsRNA Virus InfectionsSlow Virus DiseasesGenital DiseasesUrogenital DiseasesImmunologic Deficiency SyndromesTumor Virus Infections

Study Officials

  • Suki Subbiah, MD

    Louisiana State University Health Sciences Center

    PRINCIPAL INVESTIGATOR
0

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 28, 2014

First Posted

September 3, 2014

Study Start

July 1, 2014

Primary Completion

June 1, 2019

Study Completion

December 1, 2019

Last Updated

December 7, 2017

Record last verified: 2017-12

Locations