NCT02229383

Brief Summary

Study D5553C00002 is a multicenter, randomized, double-blind, placebo-controlled, parallel group, Phase 3 study to compare the safety and efficacy of exenatide once weekly (EQW) added to titrated basal insulin glargine with or without metformin to placebo added to titrated basal insulin glargine with or without metformin in patients with type 2 diabetes mellitus (T2DM). Eligible patients will be randomized at Visit 5 (Day 1) to receive either EQW added to titrated basal insulin glargine, with or without metformin ≥1500 mg/day, or placebo added to titrated basal insulin glargine, with or without metformin ≥1500 mg/day, during the 28-week treatment period.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
464

participants targeted

Target at P50-P75 for phase_3 diabetes-mellitus

Timeline
Completed

Started Sep 2014

Geographic Reach
6 countries

123 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 28, 2014

Completed
4 days until next milestone

First Posted

Study publicly available on registry

September 1, 2014

Completed
5 days until next milestone

Study Start

First participant enrolled

September 6, 2014

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 29, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 29, 2016

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

September 18, 2017

Completed
Last Updated

January 8, 2019

Status Verified

December 1, 2018

Enrollment Period

2 years

First QC Date

August 28, 2014

Results QC Date

August 18, 2017

Last Update Submit

December 17, 2018

Conditions

Keywords

Diabetes MellitusExenatideDiabetes drugTreatment efficacyPlaceboMetabolismCardiovascilar metabolic

Outcome Measures

Primary Outcomes (1)

  • Change in HbA1c From Baseline to Week 28

    To compare the change from baseline in HbA1c achieved with exenatide once weekly (EQW) added to titrated basal insulin glargine to placebo added to titrated basal insulin glargine, with or without metformin, after 28 weeks of double-blind treatment. SU= sulfonylurea.

    Baseline to Week 28

Secondary Outcomes (6)

  • Change in Body Weight From Baseline to Week 28

    Baseline to Week 28

  • Change From Baseline to Week 28 in 2-hour Postprandial Glucose After a Standard Meal Tolerance Test (MTT)

    Baseline to Week 28

  • Percentage of Participants Achieving HbA1c <7.0% at Week 28

    Baseline to Week 28

  • Change From Baseline to Week 28 in Daily Insulin Dose

    Baseline to Week 28

  • Percentage of Participants Achieving HbA1c <7.0% at Week 28, No Weight Gain at Week 28, and No Major Hypoglycemia Over 28 Weeks

    Baseline to Week 28

  • +1 more secondary outcomes

Study Arms (2)

Exenatide

EXPERIMENTAL

Exenatide 2 mg 1 time per week + titrated basal insulin glargine with or without metformin

Drug: Exenatide

Placebo

PLACEBO COMPARATOR

Placebo 2 mg 1 time per week + titrated basal insulin glargine with or without metformin

Drug: Exenatide matching placebo

Interventions

2 mg weekly suspension injection

Exenatide

Once weekly Placebo injection

Placebo

Eligibility Criteria

Age18 Years - 130 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Has a diagnosis of Type 2 Diabetes Mellitus (T2DM)
  • Has HbA1c of 7.5% to 12.0%, inclusive, at Visit 1 (Screening).
  • Has fasting plasma glucose (FPG) concentration \<280 mg/dL (15.6 mmol/L) at Visit 1 (Screening)
  • Treated with basal insulin glargine at a dose of ≥20 units/day once daily for at least 6 weeks prior to Screening, in combination with diet and exercise alone or in combination with:
  • a stable dose of metformin (≥1500 mg/day) for at least 8 weeks prior to Visit 1
  • a stable dose of metformin (≥1500 mg/day) for at least 8 weeks prior to Visit 1 (Screening) and a stable dose of sulfonylurea for at least 8 weeks prior to the Screening visit

You may not qualify if:

  • Serum calcitonin concentration ≥40 pg/mL (≥40 ng/L) at Visit 1 (Screening)
  • History of, or currently have, acute or chronic pancreatitis, or have triglyceride concentrations ≥500 mg/dL (≥5.65 mmol/L) at Visit 1
  • Positive serological test for hepatitis B or hepatitis C

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (123)

Research Site

Birmingham, Alabama, 35235, United States

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Huntsville, Alabama, 35801, United States

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Muscle Shoals, Alabama, 35662, United States

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Tempe, Arizona, 85283, United States

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Chino, California, 91710, United States

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Chula Vista, California, 91910, United States

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El Cajon, California, 92020, United States

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Fresno, California, 93720, United States

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Long Beach, California, 90807, United States

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Los Angeles, California, 90057, United States

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Mission Hills, California, 91345, United States

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Tustin, California, 92780, United States

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West Hills, California, 91307, United States

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Boynton Beach, Florida, 33437, United States

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Brooksville, Florida, 34601, United States

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Chiefland, Florida, 32626, United States

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Clearwater, Florida, 33765, United States

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Coral Gables, Florida, 33134, United States

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Fort Lauderdale, Florida, 33316, United States

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Hialeah, Florida, 33012, United States

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Jacksonville, Florida, 32256, United States

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Jacksonville, Florida, 32277, United States

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Miami, Florida, 33125, United States

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Miami, Florida, 33126, United States

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Miami, Florida, 33133, United States

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Miami, Florida, 33142, United States

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Miami, Florida, 33175, United States

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North Miami Beach, Florida, 33162, United States

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Orlando, Florida, 32806, United States

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Tampa, Florida, 33603, United States

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Columbus, Georgia, 31406, United States

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Chicago, Illinois, 60607, United States

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Avon, Indiana, 46123, United States

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Evansville, Indiana, 47714, United States

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Franklin, Indiana, 46131, United States

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Newton, Kansas, 67114, United States

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Monroe, Louisiana, 71203, United States

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New Orleans, Louisiana, 70112, United States

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Hazelwood, Missouri, 63042, United States

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Bellevue, Nebraska, 68005, United States

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Omaha, Nebraska, 68114, United States

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Haddon Heights, New Jersey, 08035, United States

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Mooresville, North Carolina, 28117, United States

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Morehead City, North Carolina, 28557, United States

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Morganton, North Carolina, 28655, United States

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Cincinnati, Ohio, 45242, United States

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Cleveland, Ohio, 44122, United States

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Dayton, Ohio, 45417, United States

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Medford, Oregon, 97504, United States

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Philadelphia, Pennsylvania, 91307, United States

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Greer, South Carolina, 29651, United States

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Spartanburg, South Carolina, 29303, United States

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Dakota Dunes, South Dakota, 57049, United States

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Johnson City, Tennessee, 37604, United States

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Kingsport, Tennessee, 37660, United States

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Austin, Texas, 78705, United States

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Dallas, Texas, 75208, United States

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Dallas, Texas, 75230, United States

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Houston, Texas, 77030, United States

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Houston, Texas, 77070, United States

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Houston, Texas, 77079, United States

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Houston, Texas, 77090, United States

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Clinton, Utah, 84015, United States

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Ogden, Utah, 84405, United States

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Salt Lake City, Utah, 84102, United States

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Manassas, Virginia, 20110, United States

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Richmond, Virginia, 23294, United States

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Port Orchard, Washington, 98366, United States

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Baja, 6500, Hungary

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Balatonfüred, 8230, Hungary

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Budapest, 1033, Hungary

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Budapest, 1036, Hungary

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Budapest, 1083, Hungary

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Budapest, 1088, Hungary

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Budapest, 1134, Hungary

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Debrecen, 4032, Hungary

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Eger, 3300, Hungary

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Gödöllő, 2100, Hungary

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Gyula, 5700, Hungary

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Komárom, 2921, Hungary

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Létavértes, 4281, Hungary

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Pécs, 7623, Hungary

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Sátoraljaújhely, 3980, Hungary

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Szeged, 6722, Hungary

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Szekszárd, 7100, Hungary

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Lodz, 94-048, Poland

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Lublin, 20-363, Poland

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Lublin, 20-538, Poland

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Oświęcim, 32-600, Poland

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Poznan, 61-655, Poland

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Torun, 87-100, Poland

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Zamość, 22-400, Poland

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Zgierz, 95-100, Poland

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Baia Mare, 430222, Romania

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Bucharest, 010192, Romania

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Bucharest, 010825, Romania

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Bucharest, 020475, Romania

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Galati, 800578, Romania

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Oradea, 410032, Romania

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Oradea, 410169, Romania

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Ploieşti, 100342, Romania

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Tg Mures, 540142, Romania

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Timișoara, 300456, Romania

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Bardejov, 08501, Slovakia

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Bratislava, 81108, Slovakia

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Bratislava, 82106, Slovakia

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Dolný Kubín, 026 01, Slovakia

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Košice, 04001, Slovakia

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Levice, 934 01, Slovakia

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Levice, 93401, Slovakia

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Lučenec, 984 01, Slovakia

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Nitra, 94901, Slovakia

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Nitra, 94911, Slovakia

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Prešov, 080 01, Slovakia

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Štúrovo, 94301, Slovakia

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Bloemfontein, 9301, South Africa

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Kempton Park, 1619, South Africa

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Krugersdorp, 1739, South Africa

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Paarl, 7646, South Africa

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Pretoria, 0087, South Africa

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Pretoria, 184, South Africa

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Somerset West, 7130, South Africa

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Worcester, 6850, South Africa

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Related Publications (2)

  • Guja C, Frias JP, Suchower L, Hardy E, Marr G, Sjostrom CD, Jabbour SA. Safety and Efficacy of Exenatide Once Weekly in Participants with Type 2 Diabetes and Stage 2/3 Chronic Kidney Disease. Diabetes Ther. 2020 Jul;11(7):1467-1480. doi: 10.1007/s13300-020-00815-z. Epub 2020 Apr 18.

  • Guja C, Frias JP, Somogyi A, Jabbour S, Wang H, Hardy E, Rosenstock J. Effect of exenatide QW or placebo, both added to titrated insulin glargine, in uncontrolled type 2 diabetes: The DURATION-7 randomized study. Diabetes Obes Metab. 2018 Jul;20(7):1602-1614. doi: 10.1111/dom.13266. Epub 2018 Mar 25.

MeSH Terms

Conditions

Diabetes Mellitus

Interventions

Exenatide

Condition Hierarchy (Ancestors)

Glucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

PeptidesAmino Acids, Peptides, and ProteinsVenomsComplex MixturesToxins, BiologicalBiological Factors

Limitations and Caveats

Please note that the data from 4 subjects enrolled at one site were omitted due to potential scientific misconduct at that site. Study conclusions remain unchanged.

Results Point of Contact

Title
Global Clinical Leader
Organization
AstraZeneca

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 28, 2014

First Posted

September 1, 2014

Study Start

September 6, 2014

Primary Completion

August 29, 2016

Study Completion

August 29, 2016

Last Updated

January 8, 2019

Results First Posted

September 18, 2017

Record last verified: 2018-12

Locations