NCT02201901

Brief Summary

The primary objectives of this study are to evaluate the efficacy, safety, and tolerability of sofosbuvir (SOF)/velpatasvir (VEL) fixed dose combination (FDC) with and without ribavirin (RBV) for 12 weeks and SOF/VEL FDC for 24 weeks in adults with chronic hepatitis C virus (HCV) infection and Child-Pugh-Turcotte (CPT) class B cirrhosis.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
268

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jul 2014

Shorter than P25 for phase_3

Geographic Reach
2 countries

50 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2014

Completed
23 days until next milestone

First Submitted

Initial submission to the registry

July 24, 2014

Completed
4 days until next milestone

First Posted

Study publicly available on registry

July 28, 2014

Completed
1 year until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2015

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2015

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

December 14, 2016

Completed
Last Updated

November 15, 2018

Status Verified

October 1, 2016

Enrollment Period

1.1 years

First QC Date

July 24, 2014

Results QC Date

August 24, 2016

Last Update Submit

October 19, 2018

Conditions

Keywords

SofosbuvirVelpatasvirSOF/VELGS-5816Hepatitis CHCVCirrhosisCPT-B

Outcome Measures

Primary Outcomes (2)

  • Percentage of Participants With Sustained Virologic Response (SVR) 12 Weeks After Discontinuation of Therapy (SVR12)

    SVR12 was defined as HCV RNA \< the lower limit of quantitation (LLOQ) 12 weeks following the last dose of study drug.

    Posttreatment Week 12

  • Percentage of Participants Who Permanently Discontinued Any Study Drug Due to an Adverse Event

    Up to 24 weeks plus 30 days

Secondary Outcomes (6)

  • Percentage of Participants With Sustained Virologic Response 4 and 24 Weeks After Discontinuation of Therapy (SVR4 and SVR24)

    Posttreatment Weeks 4 and 24

  • Percentage of Participants With HCV RNA < LLOQ at Weeks 1, 2, 4, 6, 8, 10, 12, 16, 20, and 24

    Weeks 1, 2, 4, 6, 8, 10, 12, 16, 20, and 24

  • Change From Baseline in HCV RNA at Weeks 1, 2, 4, 6, 8, 10, 12, 16, 20, and 24

    Baseline; Weeks 1, 2, 4, 6, 8, 10, 12, 16, 20, and 24

  • Percentage of Participants With Virologic Failure

    Up to Posttreatment Week 24

  • Percentage of Participants With a Decrease, No Change, or Increase Between Baseline and Posttreatment Week 24 in MELD Score

    Baseline to Posttreatment Week 24

  • +1 more secondary outcomes

Study Arms (3)

SOF/VEL 12 weeks

EXPERIMENTAL

Participants will receive SOF/VEL FDC for 12 weeks.

Drug: SOF/VEL

SOF/VEL+RBV 12 weeks

EXPERIMENTAL

Participants will receive SOF/VEL FDC plus RBV for 12 weeks.

Drug: SOF/VELDrug: RBV

SOF/VEL 24 weeks

EXPERIMENTAL

Participants will receive SOF/VEL FDC for 24 weeks.

Drug: SOF/VEL

Interventions

400/100 mg tablets administered orally once daily

Also known as: GS-7977/GS-5816, Epclusa®
SOF/VEL 12 weeksSOF/VEL 24 weeksSOF/VEL+RBV 12 weeks
RBVDRUG

Ribavirin (RBV) tablets administered orally in a divided daily dose according to package insert weight-based dosing recommendations (\< 75 kg = 1000 mg and ≥ 75 kg = 1200 mg)

SOF/VEL+RBV 12 weeks

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Willing and able to provide written informed consent
  • HCV RNA \> 10\^4 IU/mL at screening
  • Chronic HCV infection (≥ 6 months)
  • Confirmed CPT class B (7-9) at screening

You may not qualify if:

  • Current or prior history of solid organ transplantation, significant pulmonary disease, significant cardiac disease, or porphyria
  • Inability to exclude hepatocellular carcinoma (HCC) by imaging within 6 months of baseline/Day 1
  • Infection with hepatitis B virus (HBV) or human immunodeficiency virus (HIV)
  • Screening ECG with clinically significant abnormalities
  • Prior exposure to SOF or any other nucleotide analogue HCV nonstructural protein 5B (NS5B) inhibitor or any HCV NS5A inhibitor
  • Laboratory results outside of acceptable ranges at screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (50)

Unknown Facility

Phoenix, Arizona, United States

Location

Unknown Facility

La Jolla, California, United States

Location

Unknown Facility

Los Angeles, California, 90048, United States

Location

Unknown Facility

Los Angeles, California, United States

Location

Unknown Facility

Pasadena, California, United States

Location

Unknown Facility

San Francisco, California, United States

Location

Unknown Facility

Aurora, Colorado, United States

Location

Unknown Facility

Washington D.C., District of Columbia, United States

Location

Unknown Facility

Gainesville, Florida, United States

Location

Unknown Facility

Jacksonville, Florida, 32256, United States

Location

Unknown Facility

Miami, Florida, United States

Location

Unknown Facility

Tampa, Florida, United States

Location

Unknown Facility

Marietta, Georgia, United States

Location

Unknown Facility

Chicago, Illinois, United States

Location

Unknown Facility

Indianapolis, Indiana, 46202, United States

Location

Unknown Facility

Indianapolis, Indiana, 46237, United States

Location

Unknown Facility

Kansas City, Kansas, United States

Location

Unknown Facility

Monroe, Louisiana, 71280, United States

Location

Unknown Facility

New Orleans, Louisiana, United States

Location

Unknown Facility

Baltimore, Maryland, United States

Location

Unknown Facility

Boston, Massachusetts, United States

Location

Unknown Facility

Ann Arbor, Michigan, United States

Location

Unknown Facility

Detroit, Michigan, United States

Location

Unknown Facility

Rochester, Minnesota, United States

Location

Unknown Facility

Jackson, Mississippi, United States

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Unknown Facility

St Louis, Missouri, United States

Location

Unknown Facility

Santa Fe, New Mexico, 87505, United States

Location

Unknown Facility

New York, New York, 10016, United States

Location

Unknown Facility

New York, New York, 10029, United States

Location

Unknown Facility

New York, New York, 10032, United States

Location

Unknown Facility

Chapel Hill, North Carolina, United States

Location

Unknown Facility

Charlotte, North Carolina, 28204, United States

Location

Unknown Facility

Durham, North Carolina, United States

Location

Unknown Facility

Cleveland, Ohio, 44195, United States

Location

Unknown Facility

Cleveland, Ohio, United States

Location

Unknown Facility

Philadelphia, Pennsylvania, 19104, United States

Location

Unknown Facility

Philadelphia, Pennsylvania, 19107, United States

Location

Unknown Facility

Pittsburgh, Pennsylvania, United States

Location

Unknown Facility

Providence, Rhode Island, 02905, United States

Location

Unknown Facility

Germantown, Tennessee, 38138, United States

Location

Unknown Facility

Nashville, Tennessee, 37211, United States

Location

Unknown Facility

Arlington, Texas, 76012, United States

Location

Unknown Facility

Dallas, Texas, United States

Location

Unknown Facility

San Antonio, Texas, United States

Location

Unknown Facility

Murray, Utah, United States

Location

Unknown Facility

Fairfax, Virginia, United States

Location

Unknown Facility

Norfolk, Virginia, 23502, United States

Location

Unknown Facility

Richmond, Virginia, United States

Location

Unknown Facility

Seattle, Washington, United States

Location

Unknown Facility

San Juan, 00927, Puerto Rico

Location

Related Publications (5)

  • Charlton MR, O'Leary JG, Bzowej NH, Muir AJ, Korenblat KM, Fenkel JM, et al. Sofosbuvir/Velapatasvir Fixed Dose Combination for the Treatment of HCV in Patients with Decompensated Liver Disease: The Phase 3 ASTRAL-4 Study. Hepatology 2015; 62 (6): 1387A-1388A.

    BACKGROUND
  • Curry MP, O'Leary JG, Bzowej N, Muir AJ, Korenblat KM, Fenkel JM, Reddy KR, Lawitz E, Flamm SL, Schiano T, Teperman L, Fontana R, Schiff E, Fried M, Doehle B, An D, McNally J, Osinusi A, Brainard DM, McHutchison JG, Brown RS Jr, Charlton M; ASTRAL-4 Investigators. Sofosbuvir and Velpatasvir for HCV in Patients with Decompensated Cirrhosis. N Engl J Med. 2015 Dec 31;373(27):2618-28. doi: 10.1056/NEJMoa1512614. Epub 2015 Nov 16.

  • Asselah T, Charlton M, Feld J, Foster GR, McNally J, Brainard DM, et al. The ASTRAL Studies: Evaluation of SOF/GS-5816 Single-Tablet Regimen for the Treatment of Genotype 1-6 HCV Infection [Poster P1332]. J Hepatol 2015; 62:S855-S6.

    RESULT
  • Younossi ZM, Stepanova M, Charlton M, Curry MP, O'Leary JG, Brown RS, Hunt S. Patient-reported outcomes with sofosbuvir and velpatasvir with or without ribavirin for hepatitis C virus-related decompensated cirrhosis: an exploratory analysis from the randomised, open-label ASTRAL-4 phase 3 trial. Lancet Gastroenterol Hepatol. 2016 Oct;1(2):122-132. doi: 10.1016/S2468-1253(16)30009-7. Epub 2016 Aug 3.

  • Younossi ZM, Stepanova M, Feld J, Zeuzem S, Sulkowski M, Foster GR, Mangia A, Charlton M, O'Leary JG, Curry MP, Nader F, Henry L, Hunt S. Sofosbuvir and Velpatasvir Combination Improves Patient-reported Outcomes for Patients With HCV Infection, Without or With Compensated or Decompensated Cirrhosis. Clin Gastroenterol Hepatol. 2017 Mar;15(3):421-430.e6. doi: 10.1016/j.cgh.2016.10.037. Epub 2016 Nov 12.

MeSH Terms

Conditions

Hepatitis CFibrosis

Interventions

sofosbuvir-velpatasvir drug combination

Condition Hierarchy (Ancestors)

Blood-Borne InfectionsCommunicable DiseasesInfectionsHepatitis, Viral, HumanVirus DiseasesFlaviviridae InfectionsRNA Virus InfectionsHepatitisLiver DiseasesDigestive System DiseasesPathologic ProcessesPathological Conditions, Signs and Symptoms

Limitations and Caveats

There were no limitations affecting the analysis or results.

Results Point of Contact

Title
Clinical Trial Disclosures
Organization
Gilead Sciences

Study Officials

  • Anu M Osinusi, MD, MPH

    Gilead Sciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 24, 2014

First Posted

July 28, 2014

Study Start

July 1, 2014

Primary Completion

August 1, 2015

Study Completion

November 1, 2015

Last Updated

November 15, 2018

Results First Posted

December 14, 2016

Record last verified: 2016-10

Data Sharing

IPD Sharing
Will share

Qualified external researchers may request IPD for this study after study completion. For more information, please visit our website at http://www.gilead.com/research/disclosure-and-transparency.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
18 months after study completion
Access Criteria
A secured external environment with username, password, and RSA code.
More information

Locations