NCT02161185

Brief Summary

The purpose of this study is to examine the long-term safety and tolerability of USL261 in the treatment of seizure clusters.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
7

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started May 2014

Shorter than P25 for phase_3

Geographic Reach
1 country

16 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2014

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

June 9, 2014

Completed
2 days until next milestone

First Posted

Study publicly available on registry

June 11, 2014

Completed
11 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2015

Completed
3.7 years until next milestone

Results Posted

Study results publicly available

January 14, 2019

Completed
Last Updated

October 10, 2019

Status Verified

October 1, 2019

Enrollment Period

1 year

First QC Date

June 9, 2014

Results QC Date

September 25, 2018

Last Update Submit

October 8, 2019

Conditions

Keywords

Epilepsyseizure clusteracute repetitive seizuresopen-labelintranasal MidazolamUSL261Upsher-Smith

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Death, Serious Adverse Events, Treatment Emergent Adverse Events (TEAEs) Leading to Discontinuation

    Number of Participants with Death, Serious Adverse Events, Treatment emergent adverse events (TEAEs) leading to subject discontinuation from study

    Duration of individual subject participation was open-ended. Study ended early. Longest subject participation approximately 6 months.

Secondary Outcomes (1)

  • Treatment Success

    Duration of individual subject participation was open-ended. Study ended early. Longest subject participation approximately 6 months.

Study Arms (1)

USL261

OTHER
Drug: USL261

Interventions

USL261DRUG

5 mg, intranasal dose for seizure cluster, may repeat as indicated by protocol

Also known as: Intranasal Midazolam
USL261

Eligibility Criteria

Age12 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Has a competent, adult caregiver(s) who is able to recognize and observe the subject's seizure cluster episodes
  • Has an established diagnosis of partial or generalized epilepsy that includes all the following:
  • A documented history of seizure clusters lasting a minimum of 10 minutes, seizure cluster pattern is observable, stereotyped, and recognizably different from the subject's other non-cluster seizure activity (if any)
  • A second seizure in the seizure cluster typically occurs within 6 hours from the time of recognition
  • A seizure cluster pattern composed of multiple (≥ 2) partial or generalized seizures
  • A seizure cluster pattern established \>3 months before Visit 1
  • A frequency of ≥ 3 stereotyped seizure clusters during the year before Visit 1
  • At least 1 stereotyped seizure cluster occuring ≤ 4 months before Visit 1
  • Currently on a stable regimen of AED(s) that includes a benzodiazepine
  • Weight is 40 kg to 125 kg, inclusive

You may not qualify if:

  • Has a neurological disorder that is likely to progress in the next year
  • Has a severe chronic cardio-respiratory disease
  • Has a psychogenic, non-epileptic seizure(s) within the 5 years before Visit 1
  • Has a history of their stereotypical seizure cluster progressing to status epilepticus within 2 years before Visit 1
  • Has a history of acute narrow-angle glaucoma
  • Has had active suicidal plan/intent or active suicidal thoughts in the 6 months before Visit 1 or a suicide attempt in the past 5 years

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (16)

Unknown Facility

Tucson, Arizona, United States

Location

Unknown Facility

Fresno, California, United States

Location

Unknown Facility

Ventura, California, United States

Location

Unknown Facility

Aurora, Colorado, United States

Location

Unknown Facility

Port Charlotte, Florida, United States

Location

Unknown Facility

Tampa, Florida, United States

Location

Unknown Facility

Boise, Idaho, United States

Location

Unknown Facility

Chicago, Illinois, United States

Location

Unknown Facility

Lexington, Kentucky, United States

Location

Unknown Facility

Saint Paul, Minnesota, United States

Location

Unknown Facility

Reno, Nevada, United States

Location

Unknown Facility

Philadelphia, Pennsylvania, United States

Location

Unknown Facility

Nashville, Tennessee, United States

Location

Unknown Facility

Dallas, Texas, United States

Location

Unknown Facility

Houston, Texas, United States

Location

Unknown Facility

San Antonio, Texas, United States

Location

MeSH Terms

Conditions

Epilepsy

Condition Hierarchy (Ancestors)

Brain DiseasesCentral Nervous System DiseasesNervous System Diseases

Limitations and Caveats

Early termination due to poor enrollment leading to small numbers of subjects analyzed for safety. Efficacy was not analyzed.

Results Point of Contact

Title
David Sequeira,
Organization
Proximagen, LLC

Study Officials

  • TzeChiang Meng, MD

    Proximagen, LLC

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 9, 2014

First Posted

June 11, 2014

Study Start

May 1, 2014

Primary Completion

May 1, 2015

Study Completion

May 1, 2015

Last Updated

October 10, 2019

Results First Posted

January 14, 2019

Record last verified: 2019-10

Locations