NCT02157714

Brief Summary

This multiple ascending dose study is to determine safety, tolerability, pharmacokinetics and immunogenicity of PRX002 in approximately 60 patients with Parkinson's disease.

Trial Health

80
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
64

participants targeted

Target at P75+ for phase_1

Geographic Reach
1 country

8 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2014

Completed
3 days until next milestone

First Submitted

Initial submission to the registry

June 4, 2014

Completed
2 days until next milestone

First Posted

Study publicly available on registry

June 6, 2014

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2016

Completed
Last Updated

October 21, 2016

Status Verified

October 1, 2016

Enrollment Period

2.3 years

First QC Date

June 4, 2014

Last Update Submit

October 19, 2016

Conditions

Outcome Measures

Primary Outcomes (12)

  • Safety and tolerability as determined by number of subjects with adverse events

    up to 6 months

  • Determination of pharmacokinetics parameters

    maximum concentration (Cmax)

    up to 6 months

  • Determination of pharmacokinetics parameters

    time of the maximum measured concentration (Tmax)

    up to 6 months

  • Determination of pharmacokinetics parameters

    area under the concentration-time curve from time zero to the last quantifiable concentration time-point (AUClast)

    up to 6 months

  • Determination of pharmacokinetics parameters

    area under the concentration-time curve from time zero extrapolated to infinity (AUCinf)

    up to 6 months

  • Determination of pharmacokinetics parameters

    elimination rate constant

    up to 6 months

  • Determination of pharmacokinetics parameters

    terminal elimination half life (t½)

    up to 6 months

  • Determination of pharmacokinetics parameters

    clearance (CL)

    up to 6 months

  • Determination of pharmacokinetics parameters

    apparent volume of distribution (Vd)

    up to 6 months

  • Determination of pharmacokinetics parameters

    average concentration over a dosing interval (Cav)

    up to 6 months

  • Determination of pharmacokinetics parameters

    area under the plasma concentration-time curve for a dosing interval (AUCtau)

    up to 6 months

  • Determination of pharmacokinetics parameters

    minimum observed concentration (Cmin)

    up to 6 months

Secondary Outcomes (1)

  • Immunogenicity as determined by measurement of anti-PRX002 antibodies

    up to 3 months

Study Arms (2)

PRX002

EXPERIMENTAL

PRX002

Drug: PRX002

Placebo

PLACEBO COMPARATOR

Placebo

Other: Placebo

Interventions

PRX002DRUG
PRX002
PlaceboOTHER
Placebo

Eligibility Criteria

Age40 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Idiopathic Parkinson's disease, Hoehn and Yahr 1-3
  • Body weight range of ≥ 45kg/99 lbs to ≤ 110 kg/242 lbs
  • Female subjects must be surgically sterile or post-menopausal or if of child-bearing potential must use contraception
  • Male subjects and their partners of childbearing potential must use contraception

You may not qualify if:

  • Significant cardiac history
  • Abnormal MRI
  • Significant laboratory abnormalities

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (8)

Collaborative Neuroscience Network, LLC

Long Beach, California, 90806, United States

Location

Institute for Neurodegenerative Disorders

New Haven, Connecticut, 06510, United States

Location

Parkinson's Disease and Movement Disorders Center of Boca Raton

Boca Raton, Florida, 33486, United States

Location

MD Clinical

Hallandale, Florida, 33009, United States

Location

Compass Research, LLC

Orlando, Florida, 32806, United States

Location

QUEST Research Institute

Bingham Farms, Michigan, 48025, United States

Location

Oregon Health and Science University, Department of Neurology

Portland, Oregon, 97239, United States

Location

Baylor College of Medicine

Houston, Texas, 77030, United States

Location

Related Publications (2)

  • Jankovic J, Goodman I, Safirstein B, Marmon TK, Schenk DB, Koller M, Zago W, Ness DK, Griffith SG, Grundman M, Soto J, Ostrowitzki S, Boess FG, Martin-Facklam M, Quinn JF, Isaacson SH, Omidvar O, Ellenbogen A, Kinney GG. Safety and Tolerability of Multiple Ascending Doses of PRX002/RG7935, an Anti-alpha-Synuclein Monoclonal Antibody, in Patients With Parkinson Disease: A Randomized Clinical Trial. JAMA Neurol. 2018 Oct 1;75(10):1206-1214. doi: 10.1001/jamaneurol.2018.1487.

  • Schenk DB, Koller M, Ness DK, Griffith SG, Grundman M, Zago W, Soto J, Atiee G, Ostrowitzki S, Kinney GG. First-in-human assessment of PRX002, an anti-alpha-synuclein monoclonal antibody, in healthy volunteers. Mov Disord. 2017 Feb;32(2):211-218. doi: 10.1002/mds.26878. Epub 2016 Nov 25.

MeSH Terms

Conditions

Parkinson Disease

Condition Hierarchy (Ancestors)

Parkinsonian DisordersBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative Diseases

Study Officials

  • Jay Soto

    Clinical Trials Prothena Biosciences Inc

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 4, 2014

First Posted

June 6, 2014

Study Start

June 1, 2014

Primary Completion

September 1, 2016

Last Updated

October 21, 2016

Record last verified: 2016-10

Locations