NCT02116361

Brief Summary

This study will evaluate the safety and efficacy of onabotulinumtoxinA (BOTOX®) compared with placebo as treatment for major depressive disorder (MDD) in adult females.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
258

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Apr 2014

Geographic Reach
1 country

35 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 15, 2014

Completed
1 day until next milestone

First Posted

Study publicly available on registry

April 16, 2014

Completed
6 days until next milestone

Study Start

First participant enrolled

April 22, 2014

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 25, 2016

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 22, 2016

Completed
12 months until next milestone

Results Posted

Study results publicly available

December 19, 2017

Completed
Last Updated

December 19, 2017

Status Verified

November 1, 2017

Enrollment Period

2.3 years

First QC Date

April 15, 2014

Results QC Date

November 21, 2017

Last Update Submit

November 21, 2017

Conditions

Outcome Measures

Primary Outcomes (2)

  • Baseline Values for the Clinic 10-Item Montgomery-Asberg Depression Rating Scale (MADRS) Total Score

    The MADRS is a 10-item scale completed by clinic personnel that assesses the subject's symptoms of depression. Each question is answered on a 7-point scale ranging from no symptoms to worst possible symptoms. The total score is summed for all responses and ranges from 0 to 60. A negative change from baseline indicates an improvement in symptoms and a positive change from baseline indicates a worsening.

    Baseline

  • Change From Baseline Values in the Clinic 10-Item Montgomery-Asberg Depression Rating Scale (MADRS) Total Score

    The MADRS is a 10-item scale completed by clinic personnel that assesses the subject's symptoms of depression. Each question is answered on a 7-point scale ranging from no symptoms to worst possible symptoms. The total score is summed for all responses and ranges from 0 to 60. A negative change from baseline indicates an improvement in symptoms and a positive change from baseline indicates a worsening.

    Week 6

Secondary Outcomes (4)

  • Baseline Values for the 7-Item Clinical Global Impression of Severity of Illness (CGI-S) Score

    Baseline

  • Change From Baseline Values in the 7-Item Clinical Global Impression of Severity of Illness (CGI-S) Score

    24 Weeks

  • Baseline Values in the Clinic Hamilton Depression Rating Scale 17-Item Version (HAM-D17)

    Baseline

  • Change From Baseline Values in the Clinic Hamilton Depression Rating Scale 17-Item Version (HAM-D17)

    24 Weeks

Study Arms (4)

Placebo for onabotulinumtoxinA 50 U

PLACEBO COMPARATOR

Placebo (normal saline) for onabotulinumtoxinA 50 U injected into protocol-specified areas on Day 1.

Drug: Normal Saline

onabotulinumtoxinA 50 U

EXPERIMENTAL

OnabotulinumtoxinA 50 U injected into protocol-specified areas on Day 1.

Biological: onabotulinumtoxinA

Placebo for onabotulinumtoxinA 30 U

PLACEBO COMPARATOR

Placebo (normal saline) for onabotulinumtoxinA 30 U injected into protocol-specified areas on Day 1.

Drug: Normal Saline

onabotulinumtoxinA 30 U

EXPERIMENTAL

OnabotulinumtoxinA 30 U injected into protocol-specified areas on Day 1.

Biological: onabotulinumtoxinA

Interventions

OnabotulinumtoxinA injected into protocol-specified areas on Day 1.

Also known as: BOTOX®, botulinum toxin Type A
onabotulinumtoxinA 30 UonabotulinumtoxinA 50 U

Placebo (normal saline) injected into protocol-specified areas on Day 1.

Placebo for onabotulinumtoxinA 30 UPlacebo for onabotulinumtoxinA 50 U

Eligibility Criteria

Age18 Years - 65 Years
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Moderate to severe major depressive disorder

You may not qualify if:

  • Prior treatment with botulinum toxin of any serotype for any reason
  • Use of antidepressant medication for depression within 2 weeks of study
  • Diagnosis of Myasthenia gravis, Eaton-Lambert Syndrome, Amyotrophic Lateral Sclerosis

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (35)

Woodland International Research Group

Little Rock, Alaska, 72211, United States

Location

CITrials

Bellflower, California, 90706, United States

Location

Radiant Research/Comprehensive Clinical Development, Inc.

Cerritos, California, 90703, United States

Location

Collaborative Neuroscience Network Inc.

Garden Grove, California, 92845, United States

Location

Behavioral Research Specialists, LLC

Glendale, California, 91206, United States

Location

Excell Research, Inc.

Oceanside, California, 92056, United States

Location

NRC Research Institute

Orange, California, 92868, United States

Location

Artemis Institute for Clinical Research

San Diego, California, 92103, United States

Location

Schuster Medical Research Institute

Sherman Oaks, California, 91403, United States

Location

Sarkis Clinical Trials

Gainesville, Florida, 32607, United States

Location

Clinical Neuroscience Solutions, Inc.

Jacksonville, Florida, 32256, United States

Location

Compass Research LLC-North Clinic

Leesburg, Florida, 34748, United States

Location

Research Centers of America, LLC

Oakland Park, Florida, 33334, United States

Location

Clinical Neuroscience Solutions, Inc

Orlando, Florida, 32801, United States

Location

Compass Research, LLC

Orlando, Florida, 32806, United States

Location

Stedman Clinical Trials

Tampa, Florida, 33613, United States

Location

Institute for Advanced Medical Research

Alpharetta, Georgia, 30005, United States

Location

Atlanta Center for Medical Research

Atlanta, Georgia, 30331, United States

Location

iResearch Atlanta, LLC

Decatur, Georgia, 30030, United States

Location

Uptown Research Institute, LLC

Chicago, Illinois, 60640, United States

Location

Psychiatric Medicine Associates, LLC

Skokie, Illinois, 60076, United States

Location

St. Louis Clinical Trials, LLC

St Louis, Missouri, 63141, United States

Location

Integrative Clinical Trials

Brooklyn, New York, 11229, United States

Location

SPRI Clinical Trials

Brooklyn, New York, 11235, United States

Location

Finger Lakes Clinical Research

Rochester, New York, 14618, United States

Location

Midwest Clinical Research Center

Dayton, Ohio, 45417, United States

Location

IPS Research Company

Oklahoma City, Oklahoma, 73103, United States

Location

Oklahoma Clinical Research Center

Oklahoma City, Oklahoma, 73112, United States

Location

Summit Research Network (Oregon) Inc.

Portland, Oregon, 97210, United States

Location

Clinical Neuroscience Solutions, INC

Memphis, Tennessee, 38119, United States

Location

KRK Medical Research

Dallas, Texas, 75230, United States

Location

InSite Clinical Research

DeSoto, Texas, 75115, United States

Location

Virginia Commonwealth University Clinical Research Services Unit

Richmond, Virginia, 23298, United States

Location

Northwest Clinical Research Center

Bellevue, Washington, 98007, United States

Location

Zain Research LLC

Richland, Washington, 99352, United States

Location

Related Publications (1)

  • Brin MF, Durgam S, Lum A, James L, Liu J, Thase ME, Szegedi A. OnabotulinumtoxinA for the treatment of major depressive disorder: a phase 2 randomized, double-blind, placebo-controlled trial in adult females. Int Clin Psychopharmacol. 2020 Jan;35(1):19-28. doi: 10.1097/YIC.0000000000000290.

MeSH Terms

Conditions

Depressive Disorder, Major

Interventions

Botulinum Toxins, Type ASaline Solution

Condition Hierarchy (Ancestors)

Depressive DisorderMood DisordersMental Disorders

Intervention Hierarchy (Ancestors)

Botulinum ToxinsMetalloendopeptidasesEndopeptidasesPeptide HydrolasesHydrolasesEnzymesEnzymes and CoenzymesMetalloproteasesBacterial ProteinsProteinsAmino Acids, Peptides, and ProteinsBacterial ToxinsToxins, BiologicalBiological FactorsCrystalloid SolutionsIsotonic SolutionsSolutionsPharmaceutical Preparations

Results Point of Contact

Title
Arlene Lum, PMP
Organization
Allergan, Inc

Study Officials

  • Shobhal Patel

    Allergan

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 15, 2014

First Posted

April 16, 2014

Study Start

April 22, 2014

Primary Completion

August 25, 2016

Study Completion

December 22, 2016

Last Updated

December 19, 2017

Results First Posted

December 19, 2017

Record last verified: 2017-11

Data Sharing

IPD Sharing
Will not share

Locations