NCT02104245

Brief Summary

This study (ARD-3150-1202, ORBIT-4) will evaluate the safety and efficacy of inhaled Pulmaquin (ciprofloxacin dispersion for inhalation) compared to inhaled placebo in subjects who have a confirmed diagnosis of non-cystic fibrosis (non-CF) bronchiectasis with a history of pulmonary exacerbations and chronic P. aeruginosa infections.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
304

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started May 2014

Geographic Reach
16 countries

95 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 28, 2014

Completed
7 days until next milestone

First Posted

Study publicly available on registry

April 4, 2014

Completed
2 months until next milestone

Study Start

First participant enrolled

May 28, 2014

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 11, 2016

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2016

Completed
Last Updated

March 26, 2021

Status Verified

March 1, 2021

Enrollment Period

2.2 years

First QC Date

March 28, 2014

Last Update Submit

March 23, 2021

Conditions

Keywords

Non Cystic Fibrosis Bronchiectasis, Pulmaquin, Ciprofloxacin, Pseudomonas aeruginosa

Outcome Measures

Primary Outcomes (1)

  • Time to first pulmonary exacerbation (from baseline)

    48 weeks

Study Arms (2)

Ciprofloxacin dispersion for inhalation

EXPERIMENTAL

Liquid mixture of liposomally encapsulated and unencapsulated ciprofloxacin

Drug: Ciprofloxacin dispersion for inhalation

Placebo

PLACEBO COMPARATOR

Liquid formulation of empty liposomes

Drug: Placebo

Interventions

Ciprofloxacin dispersion for inhalation
Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Confirmed diagnosis of non-CF bronchiectasis
  • History of P. aeruginosa respiratory infections
  • At least two pulmonary exacerbations treated with antibiotics in the previous year

You may not qualify if:

  • Have a clinical diagnosis of CF
  • Are pregnant

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (95)

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Phoenix, Arizona, United States

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Scottsdale, Arizona, United States

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Sacramento, California, United States

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San Diego, California, United States

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Torrance, California, United States

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Danbury, Connecticut, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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Winter Park, Florida, United States

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Decatur, Georgia, United States

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Duluth, Georgia, United States

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Port Huron, Michigan, United States

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Omaha, Nebraska, United States

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Lebanon, New Hampshire, United States

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Summit, New Jersey, United States

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Albuquerque, New Mexico, United States

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New York, New York, United States

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Chapel Hill, North Carolina, United States

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Columbus, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Rock Hill, South Carolina, United States

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Spartanburg, South Carolina, United States

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Tyler, Texas, United States

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Seattle, Washington, United States

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Milwaukee, Wisconsin, United States

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Greenslopes, Queensland, Australia

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Adelaide, South Australia, Australia

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Nedlands, Western Australia, Australia

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Perth, Western Australia, Australia

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Vancouver, British Columbia, Canada

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Toronto, Ontario, Canada

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Windsor, Ontario, Canada

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Saint-Jérôme, Quebec, Canada

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Créteil, France

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Grenoble, France

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Nice, France

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Pessac, France

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Rouen, France

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Toulouse, France

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Kutaisi, Georgia

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Tbilisi, Georgia

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Budapest, Hungary

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Nyíregyháza, Hungary

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Székesfehérvár, Hungary

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Törökbálint, Hungary

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Jerusalem, Israel

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Petah Tikva, Israel

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Ramat Gan, Israel

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Tel Aviv, Israel

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Avellino, Italy

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Napoli, Italy

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Parma, Italy

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Pisa, Italy

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San Gerardo, Italy

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Terni, Italy

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Trieste, Italy

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Otahuhu, Auckland, New Zealand

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Hamilton, Waikato Region, New Zealand

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Tauranga, New Zealand

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Jesus Maria, Lima region, Peru

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La Victoria, Lima region, Peru

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Pueblo Libre, Lima region, Peru

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San Juan de Miraflores, Lima region, Peru

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Bialystok, Poland

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Krakow, Poland

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Ruda Śląska, Poland

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Warsaw, Poland

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Arad, Romania

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Bucharest, Romania

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Cluj-Napoca, Romania

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Craiova, Romania

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Iași, Romania

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Belgrade, Serbia and Montenegro

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Knez Selo, Serbia and Montenegro

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Kragujevac, Serbia and Montenegro

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Sremska Kamenica, Serbia and Montenegro

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Suwon, Gyeonggi-do, South Korea

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Daegu, South Korea

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Seoul, South Korea

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A Coruña, Spain

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Barcelona, Spain

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Lleida, Spain

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Valencia, Spain

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Stockton-on-Trees, Cleveland, United Kingdom

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Wigan, Greater Manchester, United Kingdom

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Cambridge, United Kingdom

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Colchester, United Kingdom

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Cottingham, United Kingdom

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Lancaster, United Kingdom

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Leeds, United Kingdom

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London, United Kingdom

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Manchester, United Kingdom

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North Sheilds, United Kingdom

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Southampton, United Kingdom

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Telford, United Kingdom

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Related Publications (2)

  • Chalmers JD, Cipolla D, Thompson B, Davis AM, O'Donnell A, Tino G, Gonda I, Haworth C, Froehlich J. Changes in respiratory symptoms during 48-week treatment with ARD-3150 (inhaled liposomal ciprofloxacin) in bronchiectasis: results from the ORBIT-3 and -4 studies. Eur Respir J. 2020 Oct 22;56(4):2000110. doi: 10.1183/13993003.00110-2020. Print 2020 Oct.

  • Haworth CS, Bilton D, Chalmers JD, Davis AM, Froehlich J, Gonda I, Thompson B, Wanner A, O'Donnell AE. Inhaled liposomal ciprofloxacin in patients with non-cystic fibrosis bronchiectasis and chronic lung infection with Pseudomonas aeruginosa (ORBIT-3 and ORBIT-4): two phase 3, randomised controlled trials. Lancet Respir Med. 2019 Mar;7(3):213-226. doi: 10.1016/S2213-2600(18)30427-2. Epub 2019 Jan 15.

MeSH Terms

Conditions

Pseudomonas Infections

Interventions

Inhalation

Condition Hierarchy (Ancestors)

Gram-Negative Bacterial InfectionsBacterial InfectionsBacterial Infections and MycosesInfections

Intervention Hierarchy (Ancestors)

Respiratory MechanicsRespirationRespiratory Physiological PhenomenaCirculatory and Respiratory Physiological Phenomena

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 28, 2014

First Posted

April 4, 2014

Study Start

May 28, 2014

Primary Completion

August 11, 2016

Study Completion

October 1, 2016

Last Updated

March 26, 2021

Record last verified: 2021-03

Locations