NCT02092922

Brief Summary

The AfFIRM Study is a Phase 2 study during which patients with advanced multiple myeloma will receive single-agent investigational study drug filanesib (ARRY-520). Patients will be followed to determine the effectiveness of filanesib in treating myeloma. Approximately 160 patients from North America and Europe will be enrolled in this study. Eligible patients will have received at least two prior lines of therapy; have received prior bortezomib and lenalidomide; and have disease refractory to carfilzomib and/or pomalidomide.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
154

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started May 2014

Typical duration for phase_2

Geographic Reach
8 countries

60 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 19, 2014

Completed
1 day until next milestone

First Posted

Study publicly available on registry

March 20, 2014

Completed
1 month until next milestone

Study Start

First participant enrolled

May 1, 2014

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2016

Completed
1.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

September 5, 2017

Completed
Last Updated

October 19, 2020

Status Verified

October 1, 2020

Enrollment Period

2.2 years

First QC Date

March 19, 2014

Last Update Submit

October 13, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • In patients with low Baseline alpha 1-acid glycoprotein (AAG), assess the efficacy of the study drug in terms of objective response rate.

    up to 2 years

Secondary Outcomes (7)

  • In patients with high Baseline AAG, assess the efficacy of the study drug in terms of objective response rate.

    up to 2 years

  • In all patients, assess the efficacy of the study drug in terms of duration of response.

    up to 2 years

  • In all patients, assess the efficacy of the study drug in terms of progression-free survival.

    up to 2 years

  • In all patients, assess the efficacy of study drug in terms of overall survival.

    up to 2 years

  • In all patients, assess the safety of the study drug in terms of adverse events, clinical laboratory tests and electrocardiograms.

    up to 2 years

  • +2 more secondary outcomes

Study Arms (1)

Filanesib

EXPERIMENTAL
Drug: Filanesib, KSP (Eg5) inhibitor; intravenousDrug: Filgrastim, granulocyte-colony stimulating factor (G-CSF); subcutaneous

Interventions

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients with confirmed multiple myeloma whose treatment history must include all of the following:
  • Received at least 2 prior lines of therapy (induction therapy and stem cell transplant ± maintenance are to be considered a single line of therapy).
  • Received at least 2 cycles of a bortezomib-containing regimen and 2 cycles of a lenalidomide-containing regimen, unless intolerant to these agents (defined as requiring discontinuation due to toxicity).
  • Disease refractory to a carfilzomib-containing regimen and/or a pomalidomide containing regimen. Refractory is defined as either failure to achieve a minimal response (MR) or better while on therapy, or development of progressive disease (PD) while on therapy or within 60 days from last dose of therapy.
  • Measurable multiple myeloma disease, defined as meeting at least one of the following criteria within 14 days prior to first dose of study drug:
  • A monoclonal Ig (M-protein) concentration on serum protein electrophoresis (SPEP) of ≥ 1.0 g/dL.
  • Measurable urinary light chain secretion by quantitative analysis using urine protein electrophoresis (UPEP) of ≥ 200 mg/24 hours.
  • Involved serum free light chain (FLC) level ≥ 10 mg/dL, provided the serum FLC ratio is abnormal.
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1 or 2 within 14 days prior to first dose of study drug.
  • Adequate hematology, hepatic and renal function laboratory values within 14 days prior to first dose of study drug.
  • Additional criteria exist.

You may not qualify if:

  • Prior treatment with filanesib (ARRY-520) or any other KSP inhibitor.
  • Past or current plasma cell leukemia.
  • Primary amyloidosis (amyloidosis associated with multiple myeloma is allowed).
  • POEMS syndrome (polyneuropathy, organomegaly, endocrinopathy, monoclonal protein and skin changes).
  • Autologous or allogeneic stem cell or bone marrow transplant within 3 months prior to first dose of study drug.
  • Concomitant malignancies or previous malignancies (other than multiple myeloma) with less than a 2-year disease-free interval at the time of first dose of study drug. Patients with adequately resected basal or squamous cell carcinoma of the skin, carcinoma in situ of the cervix or breast, or Stage 1 prostate cancer are eligible irrespective of the time of diagnosis.
  • Use of an investigational agent that is not expected to be cleared by the time of first dose of study drug or that has been demonstrated to have prolonged side effects. Patients must have recovered from all side effects to a Grade 0 or 1 (except alopecia and neuropathy).
  • Any severe concurrent disease or condition (including severe graft-versus-host disease, requirement for dialysis, symptomatic congestive heart failure \[New York Heart Association Class III or IV\], unstable angina pectoris, cardiac arrhythmia) which, in the judgment of the Investigator, would make the patient inappropriate for study participation.
  • Known positive serology for the human immunodeficiency virus (HIV), active hepatitis B and/or hepatitis C.
  • Acute active infection requiring treatment.
  • Additional criteria exist.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (60)

UAB Comprehensive Cancer Center

Birmingham, Alabama, 35249, United States

Location

City of Hope

Duarte, California, 91010, United States

Location

University of California, San Francisco Medical Center

San Francisco, California, 94143, United States

Location

University of Colorado

Aurora, Colorado, 80045, United States

Location

Colorado Blood Cancer Institute

Denver, Colorado, 80218, United States

Location

Yale Comprehensive Cancer Center

New Haven, Connecticut, 06510, United States

Location

Emory University, Winship Cancer Institute

Atlanta, Georgia, 30322, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Decatur Memorial Hospital

Decatur, Illinois, 62526, United States

Location

University of Kansas Cancer Center and Medical Pavilion

Westwood, Kansas, 66205, United States

Location

University of Kentucky

Lexington, Kentucky, 40536, United States

Location

Norton Cancer Institute

Louisville, Kentucky, 40202, United States

Location

Center for Cancer and Blood Disorders

Bethesda, Maryland, 20817, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

Karmanos Cancer Institute

Detroit, Michigan, 48201, United States

Location

Washington University in St. Louis

St Louis, Missouri, 63130, United States

Location

Nebraska Hematology Oncology, P.C.

Lincoln, Nebraska, 68506, United States

Location

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, 89169, United States

Location

Mount Sinai Medical Center

New York, New York, 10029, United States

Location

NY Presbyterian - Weill Cornell Medical Center

New York, New York, 10065, United States

Location

Levine Cancer Institute

Charlotte, North Carolina, 28204, United States

Location

Duke Cancer Center

Durham, North Carolina, 27710, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Huntsman Cancer Institute

Salt Lake City, Utah, 84112, United States

Location

Cancer Care Northwest

Spokane Valley, Washington, 99216, United States

Location

Institut Jules Bordet

Brussels, Belgium

Location

Universitaire Ziekenhuizen Leuven

Leuven, Belgium

Location

Tom Baker Cancer Centre

Calgary, Alberta, Canada

Location

QEII Health Sciences Center

Halifax, Nova Scotia, Canada

Location

Jewish General Hospital

Montreal, Quebec, Canada

Location

Centre Hospitalier Lyon-Sud

Bierre-Benite Cedex, France

Location

Hopital Claude Huriez

Lille, France

Location

Institut Paoli Calmettes

Marseille, France

Location

CHU Hotel Dieu

Nantes, France

Location

G.H.U Caremeau

Nîmes, France

Location

Institut Universitaire de Cancer

Toulouse, France

Location

CHU tours-Hopital Bretonneau

Tours, France

Location

CHU de Nancy - Hopital de Brabois

Vandœuvre-lès-Nancy, France

Location

TU Dresden Medizinische Fakultat, Medizinische Klinik und Poliklinik I

Dresden, Germany

Location

Asklepios Kliniken Hamburg GmbH

Hamburg, Germany

Location

University Hospital Heidelberg

Heidelberg, Germany

Location

University Hospital Leipzig

Leipzig, Germany

Location

University of Tubingen

Tübingen, Germany

Location

Julius Maximilians Universitat Wurzburg

Würzburg, Germany

Location

General Hospital of Athens "Evangelismos"

Athens, Greece

Location

University of Athens School of Medicine

Athens, Greece

Location

Hospital Germans Trias i Pujol

Badalona, Spain

Location

Hospital Clinic de Barcelona

Barcelona, Spain

Location

Hospital Clinico Universitario de Valencia

Valencia, Spain

Location

Hospital Universitario La Fe

Valencia, Spain

Location

Hospital Quiron de Zaragoza

Zaragoza, Spain

Location

Barts Health NHS Trust

London, United Kingdom

Location

Kings College Hospital NHS Foundation Trust

London, United Kingdom

Location

Southhampton General Hospital

Southhampton, United Kingdom

Location

The Royal Marsden NHS Foundation Trust

Surrey, United Kingdom

Location

New Cross Hospital

Wolverhampton, United Kingdom

Location

MeSH Terms

Interventions

filanesibKIF11 protein, humanFilgrastimGranulocyte Colony-Stimulating FactorInjections, Subcutaneous

Intervention Hierarchy (Ancestors)

Colony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological FactorsInjectionsDrug Administration RoutesDrug TherapyTherapeutics

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 19, 2014

First Posted

March 20, 2014

Study Start

May 1, 2014

Primary Completion

July 1, 2016

Study Completion

September 5, 2017

Last Updated

October 19, 2020

Record last verified: 2020-10

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations