NCT01989325

Brief Summary

This is a Phase 2 study during which patients with advanced multiple myeloma will receive either carfilzomib alone (single-agent) or carfilzomib in combination with investigational study drug filanesib (ARRY-520). Patients will be followed to determine the effectiveness of both single-agent carfilzomib and carfilzomib + filanesib in treating myeloma. Patients will be allowed to crossover from single-agent carfilzomib to carfilzomib + filanesib if disease progression occurs. Approximately 75 patients from the US will be enrolled in this study.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
77

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Nov 2013

Geographic Reach
1 country

22 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2013

Completed
4 days until next milestone

First Submitted

Initial submission to the registry

November 5, 2013

Completed
16 days until next milestone

First Posted

Study publicly available on registry

November 21, 2013

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2016

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2016

Completed
Last Updated

September 16, 2020

Status Verified

September 1, 2020

Enrollment Period

2.3 years

First QC Date

November 5, 2013

Last Update Submit

September 14, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • Assess the efficacy of both carfilzomib + study drug and single-agent carfilzomib in terms of progression-free survival.

    18 months

Secondary Outcomes (5)

  • Assess the efficacy of both carfilzomib + study drug and single-agent carfilzomib in terms of objective response rate.

    18 months

  • Assess the safety of both carfilzomib + study drug and single-agent carfilzomib in terms of adverse events, clinical laboratory tests and electrocardiograms.

    18 months

  • Characterize the pharmacokinetics (PK) of study drug, carfilzomib and a carfilzomib metabolite in patients treated with carfilzomib + study drug in terms of plasma concentration-time profiles and model-based PK parameters.

    6 months

  • Following crossover from single-agent carfilzomib, assess the efficacy of carfilzomib + study drug in terms of objective response rate.

    18 months

  • Following crossover from single-agent carfilzomib, assess the safety of carfilzomib + study drug in terms of adverse events, clinical laboratory tests and electrocardiograms.

    18 months

Other Outcomes (1)

  • Evaluate patient serum levels of alpha 1-acid glycoprotein (AAG) at Baseline and during the treatment period.

    18 months

Study Arms (2)

Carfilzomib + Filanesib

EXPERIMENTAL

Single agent + Carfilzomib arm. Patients will be hydrated prior to and following carfilzomib administration and will be premedicated with dexamethasone, per the carfilzomib prescribing information. Filgrastim to be administered per the approved product prescribing information and institutional guidelines.

Drug: Carfilzomib, proteasome inhibitor; intravenousDrug: Filanesib, KSP(Eg5) inhibitor; intravenousDrug: Dexamethasone, steroid; oral or intravenousDrug: Filgrastim, granulocyte-colony stimulating factor (G-CSF); subcutaneous

Carfilzomib

EXPERIMENTAL

Single agent arm. Patients will be hydrated prior to and following carfilzomib administration and will be premedicated with dexamethasone, per the carfilzomib prescribing information.

Drug: Carfilzomib, proteasome inhibitor; intravenousDrug: Dexamethasone, steroid; oral or intravenous

Interventions

multiple dose, single schedule

CarfilzomibCarfilzomib + Filanesib

multiple dose, single schedule

Carfilzomib + Filanesib

as indicated, per the carfilzomib prescribing information

CarfilzomibCarfilzomib + Filanesib

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Confirmed multiple myeloma with measurable disease.
  • Disease refractory to last myeloma regimen.
  • Patients must have received at least 2 prior treatment regimens, including bortezomib and an IMiD (e.g., lenalidomide, thalidomide, pomalidomide). Induction therapy and stem cell transplant ± maintenance are to be considered as a single regimen.
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1 or 2 within 14 days prior to first dose of study treatment.
  • Adequate hematology, liver and renal function laboratory values within 14 days prior to first dose of study treatment.
  • Additional criteria exist.

You may not qualify if:

  • Prior treatment with carfilzomib, filanesib, or any other KSP inhibitor.
  • Past or current plasma cell leukemia.
  • Primary amyloidosis (amyloidosis associated with multiple myeloma is allowed).
  • POEMS syndrome (polyneuropathy, organomegaly, endocrinopathy, monoclonal protein and skin changes).
  • Ongoing Grade 3 or Grade 4 peripheral neuropathy, or Grade 2 peripheral neuropathy with pain despite appropriate interventions, within 28 days prior to first dose of study treatment.
  • Autologous or allogeneic stem cell or bone marrow transplant within 3 months prior to first dose of study treatment.
  • Concomitant malignancies or previous malignancies (other than multiple myeloma) with less than a 2-year disease-free interval at the time of first dose of study treatment. Patients with adequately resected basal or squamous cell carcinoma of the skin, carcinoma in situ of the cervix or breast, or Stage 1 prostate cancer are eligible irrespective of the time of diagnosis.
  • Known pulmonary hypertension of any severity.
  • Concurrent cardiac disease that, in the judgment of the Investigator, would make the patient inappropriate for study participation.
  • Known positive serology for the human immunodeficiency virus (HIV), active hepatitis B and/or hepatitis C.
  • Acute active infection requiring treatment.
  • Additional criteria exist.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (22)

Genesis Cancer Center

Hot Springs, Arkansas, 71913, United States

Location

UCLA

Los Angeles, California, 90095, United States

Location

St. Joseph Heritage Healthcare

Santa Rosa, California, 95403, United States

Location

Florida Cancer Specialists

Fort Myers, Florida, 33905, United States

Location

Robert H. Lurie Comprehensive Cancer Center of Northwestern University

Chicago, Illinois, 60611, United States

Location

Crescent City Research Consortium

Marrero, Louisiana, 70072, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Karmanos Cancer Institute

Detroit, Michigan, 48201, United States

Location

Forrest General Cancer Center

Hattiesburg, Mississippi, 39401, United States

Location

Nebraska Cancer Specialists

Omaha, Nebraska, 68130, United States

Location

Memorial Sloan Kettering

New York, New York, 10065, United States

Location

Levine Cancer Institute

Charlotte, North Carolina, 28204, United States

Location

Oncology Hematology Care - Blue Ash

Cincinnati, Ohio, 45242, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

Ohio State University

Columbus, Ohio, 43210, United States

Location

Knight Cancer Institute at Oregon Health & Science University

Portland, Oregon, 97239, United States

Location

Prairie Lakes Health Care System

Watertown, South Dakota, 57201, United States

Location

Sarah Cannon Research Institute

Nashville, Tennessee, 37203, United States

Location

Simmons Cancer Center - UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Virginia Cancer Specialists

Fairfax, Virginia, 22031, United States

Location

WVU - Mary Babb Randolph Cancer Center

Morgantown, West Virginia, 26506, United States

Location

Medical College of Wisconsin Cancer Center

Milwaukee, Wisconsin, 53226, United States

Location

MeSH Terms

Interventions

carfilzomibProteasome InhibitorsfilanesibDexamethasoneSteroidsFilgrastimGranulocyte Colony-Stimulating FactorInjections, Subcutaneous

Intervention Hierarchy (Ancestors)

Protease InhibitorsEnzyme InhibitorsMolecular Mechanisms of Pharmacological ActionPharmacologic ActionsChemical Actions and UsesPregnadienetriolsPregnadienesPregnanesFused-Ring CompoundsPolycyclic CompoundsSteroids, FluorinatedColony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological FactorsInjectionsDrug Administration RoutesDrug TherapyTherapeutics

Study Officials

  • Clinical Trial Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 5, 2013

First Posted

November 21, 2013

Study Start

November 1, 2013

Primary Completion

February 1, 2016

Study Completion

May 1, 2016

Last Updated

September 16, 2020

Record last verified: 2020-09

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations