NCT02076399

Brief Summary

The purpose of this study is to determine whether fostamatinib is safe and effective in the treatment of persistent/chronic Immune Thrombocytopenic Purpura (ITP).

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
76

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Jul 2014

Geographic Reach
8 countries

52 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 26, 2014

Completed
5 days until next milestone

First Posted

Study publicly available on registry

March 3, 2014

Completed
4 months until next milestone

Study Start

First participant enrolled

July 14, 2014

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 21, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 21, 2016

Completed
2.7 years until next milestone

Results Posted

Study results publicly available

January 11, 2019

Completed
Last Updated

February 12, 2019

Status Verified

October 1, 2018

Enrollment Period

1.8 years

First QC Date

February 26, 2014

Results QC Date

October 15, 2018

Last Update Submit

January 24, 2019

Conditions

Keywords

Persistent Immune Thrombocytopenic PurpuraChronic Immune Thrombocytopenic Purpura

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Stable Platelet Response (Count of ≥50,000/µL on at Least 4 of the Last 6 Scheduled Visits Between Weeks 14 and 24)

    A stable platelet response by Week 24 defined as a platelet count of at least 50,000/μL on at least 4 of the last 6 scheduled visits between Weeks 14 and 24

    From Week 14 to Week 24

Secondary Outcomes (6)

  • Number of Participants With Platelet Count ≥ 50,000/µL at Week 12

    Week 12

  • Number of Participants With Platelet Count ≥ 50,000/µL at Week 24

    Week 24

  • Platelet Count ≥ 30,000/μL and ≥ 20,000/μL Above Baseline in Subjects With Baseline Platelet Count of <15,000/μL at Week 12.

    Baseline to Week 12

  • Platelet Count ≥ 30,000/μL and ≥ 20,000/μL Above Baseline in Subjects With Baseline Platelet Count of <15,000/μL at Week 24.

    Baseline to Week 24

  • Mean of the ITP Bleeding Score (IBLS)

    Assessed over the 24-week study period

  • +1 more secondary outcomes

Study Arms (2)

Fostamatinib Disodium

EXPERIMENTAL

Subjects begin with Fostamatinib Disodium tablet 100 mg PO bid and increase to 150 mg big after week 4 based on platelet count and tolerability.

Drug: Fostamatinib disodium

Placebo

OTHER

Placebo tablet PO bid (morning and evening) over the course of 24 weeks

Drug: Placebo

Interventions

Fostamatinib (100 mg PO bid or 150 mg PO bid)

Also known as: R935788, R788, Fostamatinib
Fostamatinib Disodium

Placebo tablet PO bid (morning and evening) over the course of 24 weeks

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Clinical diagnosis of persistent/chronic ITP for at least 3 months.
  • Average platelet count \< 30,000/µL (and none \> 35,000 unless as a result of rescue therapy) from at least 3 qualifying counts

You may not qualify if:

  • Clinical diagnosis of autoimmune hemolytic anemia
  • Uncontrolled or poorly controlled hypertension
  • History of coagulopathy including prothrombotic conditions

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (52)

Arizona Oncology Associates

Tucson, Arizona, 85710, United States

Location

University of Southern California

Los Angeles, California, 90089, United States

Location

Lakeland Regional Cancer Center

Lakeland, Florida, 33805-1965, United States

Location

Bleeding & Clotting Disorders Institute

Peoria, Illinois, 61614, United States

Location

Horizon Oncology Research, Inc

Lafayette, Indiana, 47905, United States

Location

Center for Cancer and Blood Disorders

Bethesda, Maryland, 20817, United States

Location

Weill Cornell Medical College/New York Presbyterian Hospital

New York, New York, 10065, United States

Location

Pitt County Memorial Hospital

Greenville, North Carolina, 27858, United States

Location

Bill Hefner VA Medical Center

Salisbury, North Carolina, 28144, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

Signal Point Clinical Research Center LLC

Middletown, Ohio, 45042, United States

Location

University of Utah Health Sciences Center

Salt Lake City, Utah, 84132, United States

Location

University of Virginia

Charlottesville, Virginia, 22908, United States

Location

Concord Repatriation General Hospital

Concord, New South Wales, 2139, Australia

Location

St George Hospital

Kogarah, New South Wales, 2217, Australia

Location

Liverpool Hospital

Liverpool, New South Wales, 2170, Australia

Location

Prince of Wales Hospital

Randwick, New South Wales, 2031, Australia

Location

Westmead Hospital

Westmead, New South Wales, 2145, Australia

Location

Launceston General Hospital

Launceston, Tasmania, 7250, Australia

Location

Frankston Hospital

Frankston, Victoria, 3199, Australia

Location

Dept of Haematology, The Alfred Hospital and Monash Medical Centre

Melbourne, Victoria, 3004, Australia

Location

Perth Blood Institute

Nedlands, Western Australia, 6009, Australia

Location

Hamilton Health Sciences Corporation

Hamilton, Ontario, L8N 3Z5, Canada

Location

Ottawa Hospital Research Institute

Ottawa, Ontario, K1 H8L6, Canada

Location

St. Michael's Hospital

Toronto, Ontario, M5B1W8, Canada

Location

Herlev Hospital University of Copenhagen, Department of Hematology L124

Herlev, DK, 2730, Denmark

Location

Dept. of Haematology, Odense University Hospital

Odense C, DK, DK-5000, Denmark

Location

Hematological department, Roskilde Hospital

Roskilde, DK, 4000, Denmark

Location

Aarhus University Hospital

Aalborg, 9000, Denmark

Location

Semmelweis University 1st

Budapest, H-1083, Hungary

Location

University of Debrecen

Debrecen, H-1083, Hungary

Location

Pecs University

Pécs, H-7624, Hungary

Location

Ematologia - Padigilione 8, Policinico S. Orsola Malpighi, Azienda Ospedaliero Universitaria di Bologna

Bologna, 40138, Italy

Location

Ospedale San Raffaele S.r.l. Dipartimento di Oncoematologia

Milan, 20132, Italy

Location

Universitã Federico II di Napoli

Napoli, 80131, Italy

Location

OspedaleCivile-ClinicaEmatologica/PUGD

Udine, 33100, Italy

Location

ULSS 6 Vicenza-Ospedale San Bortolo di Vicenza

Vicenza, Italy

Location

HAGA ziekenhuis

Haag, NL, 2545 CH, Netherlands

Location

Kent & Canterbury Hospital

Kent, Canterbury, CT1 3NG, United Kingdom

Location

Colchester General Hospital

Colchester, Essex, CO4 5JL, United Kingdom

Location

Royal Liverpool University Hospital

Liverpool, UK, L78XP, United Kingdom

Location

St. James's Hospital

Leeds, LS9 7TF, United Kingdom

Location

Leicester Royal Infirmary

Leicester, LE1 5WW, United Kingdom

Location

Royal London Hospital

London, E1 2ES, United Kingdom

Location

Hammersmith Hospital, Catherine Lewis Centre

London, W12 0HS, United Kingdom

Location

University College Hospital

London, WC1E 6HX, United Kingdom

Location

Manchester Royal Infirmary

Manchester, M139WL, United Kingdom

Location

Royal Victoria Infirmary

Newcastle upon Tyne, NE1 4LP, United Kingdom

Location

James Paget University Hospital

Norfolk, NR31 6LA, United Kingdom

Location

Oxford University Hospital

Oxford, OX3 9BQ, United Kingdom

Location

University Hospital of North Staffordshire

Stoke-on-Trent, ST4 6QG, United Kingdom

Location

Sandwell General Hospital

West Bromwich, B71 4HJ, United Kingdom

Location

Related Publications (1)

  • Cooper N, Altomare I, Thomas MR, Nicolson PLR, Watson SP, Markovtsov V, Todd LK, Masuda E, Bussel JB. Assessment of thrombotic risk during long-term treatment of immune thrombocytopenia with fostamatinib. Ther Adv Hematol. 2021 Apr 30;12:20406207211010875. doi: 10.1177/20406207211010875. eCollection 2021.

MeSH Terms

Conditions

Purpura, Thrombocytopenic, Idiopathic

Interventions

fostamatinib

Condition Hierarchy (Ancestors)

Purpura, ThrombocytopenicPurpuraBlood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesThrombotic MicroangiopathiesThrombocytopeniaBlood Platelet DisordersCytopeniaHemorrhagic DisordersAutoimmune DiseasesImmune System DiseasesHemorrhagePathologic ProcessesPathological Conditions, Signs and SymptomsSkin ManifestationsSigns and Symptoms

Results Point of Contact

Title
Anne-Marie Duliege, MD
Organization
Rigel

Study Officials

  • Rigel Pharmaceuticals, Inc.

    Rigel Pharmaceuticals,Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 26, 2014

First Posted

March 3, 2014

Study Start

July 14, 2014

Primary Completion

April 21, 2016

Study Completion

April 21, 2016

Last Updated

February 12, 2019

Results First Posted

January 11, 2019

Record last verified: 2018-10

Data Sharing

IPD Sharing
Will not share

Locations