NCT02071459

Brief Summary

Evaluate the effects of L-Threo DOPS on orthostatic hypotension symptoms and other non-motor symptoms in patients with Multiple System Atrophy (MSA) after 12 weeks following randomization to continued therapy with droxidopa or placebo.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
107

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jan 2014

Longer than P75 for phase_2

Geographic Reach
1 country

13 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 21, 2014

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

February 21, 2014

Completed
4 days until next milestone

First Posted

Study publicly available on registry

February 25, 2014

Completed
5.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 28, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 28, 2019

Completed
Last Updated

April 8, 2026

Status Verified

April 1, 2026

Enrollment Period

5.8 years

First QC Date

February 21, 2014

Last Update Submit

April 2, 2026

Conditions

Keywords

L-threo DOPS (DroxiDopa)Orthostatic HypotensionMultiple system atrophy

Outcome Measures

Primary Outcomes (1)

  • Evaluate the efficacy of long term efficacy of L-threo DOPS

    Evaluate the efficacy of long term efficacy of L-threo DOPS (droxidopa) in MSA patients (probable or possible - cerebellar (C) or parkinsonian (P) type) with symptomatic NOH as measured by the relative change in mean score of Orthostatic Hypotension Symptom Assessment (OHSA) (Part I of the questionnaire on the symptoms OH (OHQ) (Kaufmann et al., 2011)) 12 weeks following randomization to therapy with droxidopa or placebo (including 8 weeks to maximum tolerated dose).

    12 weeks

Secondary Outcomes (4)

  • efficacy of L-ThreoDOPS on symptomatic OH

    12 weeks

  • effects of L-Threo DOPS on motor symptoms

    12 weeks

  • effect of L-Threo DOPS on dysautonomic symptoms

    12 weeks

  • safety of high doses of L-ThreoDOPS

    12 Weeks

Study Arms (2)

L-Threo DOPS

EXPERIMENTAL

patients with Multiple System Atrophy (MSA) after 12 weeks to continued therapy with L-Threo DOPS

Drug: L-Threo DOPS

placebo

PLACEBO COMPARATOR

patients with Multiple System Atrophy (MSA) after 12 weeks to continued therapy with placebo

Drug: placebo

Interventions

initial dose titration period (4 weeks) followed by 8 weeks at the max tolerated dose

Also known as: L DOPS or DroxiDopa
L-Threo DOPS

initial period (4 weeks) followed by 8 weeks

placebo

Eligibility Criteria

Age30 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • MSA patients (possible or probable, MSA-P or C (according to revised criteria, Gilman et al 2008)).
  • Aged 30 to 80 years,
  • Able to walk at least 10 meters
  • With symptomatic OH (score of at least 3 at one of the items of Part I of the OH scale (OHQ))
  • Documented fall in systolic blood pressure of at least 20 mmHg, and/or in diastolic blood pressure of at least 10 mmHg, within 3 minutes after standing.
  • Able to fill in the evaluation questionnaires with or without help
  • With no significant problems with swallowing.
  • Stable anti-parkinsonian, dysautonomia and depression treatments for the 4 weeks before the study and during the entire study
  • Signed written informed consent for the present study.

You may not qualify if:

  • Dementia (DSM-IV, Mini-Mental State Examination (MMSE) \< 24/30)
  • Concomitant use of vaso-constrictive drugs, other than midodrine. Patients taking vasoconstrictor agents such as ephedrine, dihydroergotamine, must stop taking these drugs at least 2 days or 7 half-lives prior to their baseline visit (Visit 1); the association with midodrine may be kept at a stable dose not exceeding 3 tablets (7.5 mg) / day if the patient has no CV history. This will be discussed case by case with the coordinating center and the safety committee of this study.
  • Taking anti-hypertensive medication

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (13)

Centre hospitalier d'Angers

Angers, 49933, France

Location

CHU bordeaux

Bordeaux, France

Location

CHU de Clermont-Ferrand

Clermont-Ferrand, 63000, France

Location

CHU de Dijon

Dijon, 21000, France

Location

CHRU de lille

Lille, 59037, France

Location

CHU de limoges

Limoges, 87042, France

Location

Hôpital La Timone

Marseille, 13000, France

Location

Hôpital G. & R. Laennec

Nantes, 44093, France

Location

Hôpital Pitié-Salpétrière

Paris, 75013, France

Location

CHU de Poitiers

Poitiers, 86021, France

Location

CHU Pontchaillou

Rennes, 35033, France

Location

CHU de Rouen

Rouen, 76031, France

Location

chu de Strasbourg

Strasbourg, 67091, France

Location

Related Publications (1)

  • Dierickx LO, Bettiol C, Huglo D, Marcelli F, Sibert L, Gouel P, Ferretti L, Orlhac F, Huyghe E. Is 18F-fluorodexyglucose testicular uptake using positron emission tomography/computed tomography correlated with the results of a testicular sperm extraction procedure in the case of azoospermia (French prospective multicenter AZOPREDHISTOTEP study)? Eur J Nucl Med Mol Imaging. 2026 Apr;53(5):3283-3290. doi: 10.1007/s00259-025-07583-7. Epub 2025 Nov 21.

MeSH Terms

Conditions

Multiple System AtrophyHypotension, Orthostatic

Interventions

Droxidopa

Condition Hierarchy (Ancestors)

Primary DysautonomiasAutonomic Nervous System DiseasesNervous System DiseasesBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative DiseasesOrthostatic IntoleranceHypotensionVascular DiseasesCardiovascular Diseases

Intervention Hierarchy (Ancestors)

NorepinephrineCatecholaminesAminesOrganic ChemicalsCatecholsPhenolsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsSerineAmino Acids, NeutralAmino AcidsAmino Acids, Peptides, and Proteins

Study Officials

  • Anne PAVY-LE-TRAON, PHD

    University Hospital, Toulouse

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 21, 2014

First Posted

February 25, 2014

Study Start

January 21, 2014

Primary Completion

October 28, 2019

Study Completion

October 28, 2019

Last Updated

April 8, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will not share

Locations