NCT02050828

Brief Summary

The purpose of this study is to evaluate the safety and efficacy of AKB-9778 administered as daily subcutaneous injections with and without monthly intravitreal injections of ranibizumab for 3 months in patients with diabetic macular edema.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
144

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jan 2014

Shorter than P25 for phase_2

Geographic Reach
1 country

39 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2014

Completed
28 days until next milestone

First Submitted

Initial submission to the registry

January 29, 2014

Completed
2 days until next milestone

First Posted

Study publicly available on registry

January 31, 2014

Completed
1.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2015

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2015

Completed
Last Updated

March 16, 2017

Status Verified

March 1, 2017

Enrollment Period

1.2 years

First QC Date

January 29, 2014

Last Update Submit

March 15, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Mean change from baseline in spectral domain optical coherence tomography (sdOCT)-measured central subfield thickness (CST)

    Month 3

Secondary Outcomes (1)

  • Mean change from baseline in Early Treatment Diabetic Retinopathy Study (ETDRS) Best Corrected Visual Acuity (BCVA)

    Month 3

Study Arms (3)

AKB-9778 15 mg BID monotherapy

EXPERIMENTAL

Subcutaneous AKB-9778 15 mg BID (total daily dose of 30 mg/day) plus monthly sham intravitreal injection for 3 months.

Drug: AKB-9778Drug: Sham

AKB-9778 15 mg BID + ranibizumab 0.3 mg

EXPERIMENTAL

Subcutaneous AKB-9778 15 mg BID (total daily dose of 30 mg/day) plus ranibizumab 0.3 mg monthly intravitreal injection for 3 months.

Drug: AKB-9778Drug: ranibizumab

ranibizumab 0.3 mg monotherapy

ACTIVE COMPARATOR

Placebo subcutaneous injection (BID) plus ranibizumab 0.3 mg monthly intravitreal injection for 3 months.

Drug: ranibizumabDrug: Placebo

Interventions

AKB-9778 15 mg BID + ranibizumab 0.3 mgAKB-9778 15 mg BID monotherapy
Also known as: Lucentis
AKB-9778 15 mg BID + ranibizumab 0.3 mgranibizumab 0.3 mg monotherapy
ranibizumab 0.3 mg monotherapy
ShamDRUG
AKB-9778 15 mg BID monotherapy

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Adults between 18 to 80 years of age, inclusive
  • Diagnosis of diabetes mellitus (type 1 or type 2)
  • Decrease in vision in the study eye determined to be primarily the result of DME
  • Definite retinal thickening due to diffuse DME involving the central macula in the study eye
  • Central subfield thickness of at least 325 µm by sdOCT with presence of intraretinal fluid in the study eye
  • ETDRS BCVA letter score ≤ 76 and ≥ 24 in the study eye

You may not qualify if:

  • Hemoglobin A1C (HbA1C) ≥ 12.0% at Screening
  • History of non infectious uveitis
  • Decrease in visual acuity due to causes other than DME in the study eye
  • Prior pars plana vitrectomy
  • Any ocular surgery within 3 months prior to Day 1
  • YAG capsulotomy within 3 months prior to Day 1
  • Panretinal scatter photocoagulation (PRP) or focal laser within 3 months prior to Day 1 or anticipated need for PRP during the course of the study
  • Prior intravitreal, subtenon, or periocular steroid therapy within 3 months prior to Day 1
  • Prior treatment with intravitreal anti-vascular endothelial growth factor (VEGF) treatment within 8 weeks prior to Day 1

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (39)

Unknown Facility

Pheonix, Arizona, 85014, United States

Location

Unknown Facility

Pheonix, Arizona, 85020, United States

Location

Unknown Facility

Tucson, Arizona, 85704, United States

Location

Unknown Facility

Arcadia, California, 91007, United States

Location

Unknown Facility

Bakersfield, California, 93309, United States

Location

Unknown Facility

Beverly Hills, California, 90211, United States

Location

Unknown Facility

Palm Desert, California, 92260, United States

Location

Unknown Facility

Sacramento, California, 95819, United States

Location

Unknown Facility

Santa Ana, California, 92705, United States

Location

Unknown Facility

Santa Barbara, California, 93103, United States

Location

Unknown Facility

Golden, Colorado, 80401, United States

Location

Unknown Facility

Boynton Beach, Florida, 33426, United States

Location

Unknown Facility

Fort Lauderdale, Florida, 33334, United States

Location

Unknown Facility

Fort Myers, Florida, 33912, United States

Location

Unknown Facility

Miami, Florida, 33126, United States

Location

Unknown Facility

Sarasota, Florida, 34239, United States

Location

Unknown Facility

Stuart, Florida, 34994, United States

Location

Unknown Facility

Winter Haven, Florida, 33880, United States

Location

Unknown Facility

Baltimore, Maryland, 21287, United States

Location

Unknown Facility

Jackson, Michigan, 49202, United States

Location

Unknown Facility

Omaha, Nebraska, 68198, United States

Location

Unknown Facility

Reno, Nevada, 89502, United States

Location

Unknown Facility

Rochester, New York, 14620, United States

Location

Unknown Facility

Charlotte, North Carolina, 28210, United States

Location

Unknown Facility

Cincinnati, Ohio, 45242, United States

Location

Unknown Facility

Cleveland, Ohio, 44195, United States

Location

Unknown Facility

Portland, Oregon, 97210, United States

Location

Unknown Facility

Florence, South Carolina, 29501, United States

Location

Unknown Facility

Rapid City, South Dakota, 57701, United States

Location

Unknown Facility

Nashville, Tennessee, 37203, United States

Location

Unknown Facility

Abilene, Texas, 79606, United States

Location

Unknown Facility

Austin, Texas, 78705, United States

Location

Unknown Facility

Fort Worth, Texas, 76102, United States

Location

Unknown Facility

Houston, Texas, 77030, United States

Location

Unknown Facility

McAllen, Texas, 78503, United States

Location

Unknown Facility

San Antonio, Texas, 78240, United States

Location

Unknown Facility

Salt Lake City, Utah, 84107, United States

Location

Unknown Facility

Warrenton, Virginia, 20186, United States

Location

Unknown Facility

Bellevue, Washington, 98004, United States

Location

MeSH Terms

Interventions

AKB-9778Ranibizumabsalicylhydroxamic acid

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 29, 2014

First Posted

January 31, 2014

Study Start

January 1, 2014

Primary Completion

April 1, 2015

Study Completion

May 1, 2015

Last Updated

March 16, 2017

Record last verified: 2017-03

Locations