NCT02045602

Brief Summary

The purpose of this study is to determine the safety and tolerability of VCN-01 either administered alone or in combination with Abraxane®/Gemcitabine, and to determine the recommended phase II dose of VCN-01 alone or in combination with Abraxane®/Gemcitabine.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
42

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Jan 2014

Longer than P75 for phase_1

Geographic Reach
1 country

5 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2014

Completed
20 days until next milestone

First Submitted

Initial submission to the registry

January 21, 2014

Completed
6 days until next milestone

First Posted

Study publicly available on registry

January 27, 2014

Completed
5.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2019

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2020

Completed
Last Updated

October 8, 2020

Status Verified

October 1, 2020

Enrollment Period

5.3 years

First QC Date

January 21, 2014

Last Update Submit

October 7, 2020

Conditions

Keywords

CancerSolid TumorsGemcitabineOncolytic virusMetastaticPancreatic cancer

Outcome Measures

Primary Outcomes (2)

  • Safety and Tolerability by means of Adverse Events (AEs) and laboratory data

    At least 6 months

  • Recommended Phase 2 Dose (RP2D) by determination of highest feasible dose (MFD) and any Dose Limiting Toxicities

    At least 6 months

Secondary Outcomes (6)

  • Presence of VCN-01 in tumor

    Day 8-10

  • Viral Pharmacokinetics

    Up to 48 h

  • Viral Shedding

    Up to day 28

  • Neutralizing antibodies anti-VCN-01

    30 days after end of treatment phase

  • Preliminary anti-tumor activity by Overall Response Rate (ORR)

    CT or MRI scans every 8 weeks until disease progression

  • +1 more secondary outcomes

Study Arms (3)

Part I: Dose Escalation, Single Agent

EXPERIMENTAL

Single intravenous injection of VCN-01 oncolytic adenovirus

Genetic: VCN-01

Part II: Dose Escalation, Combination

EXPERIMENTAL

Single intravenous injection of VCN-01 oncolytic adenovirus in combination with Abraxane®/Gemcitabine

Genetic: VCN-01Drug: GemcitabineDrug: Abraxane®

Part III: Dose Escalation, Combination, "delayed" schedule

EXPERIMENTAL

Single intravenous injection of VCN-01 oncolytic adenovirus in combination with Abraxane®/Gemcitabine

Genetic: VCN-01Drug: GemcitabineDrug: Abraxane®

Interventions

VCN-01GENETIC

Genetically modified human adenovirus encoding human PH20 hyaluronidase

Part I: Dose Escalation, Single AgentPart II: Dose Escalation, CombinationPart III: Dose Escalation, Combination, "delayed" schedule

1000 mg/m2 intravenous administration

Part II: Dose Escalation, CombinationPart III: Dose Escalation, Combination, "delayed" schedule

125 mg/m2 intravenous administration

Part II: Dose Escalation, CombinationPart III: Dose Escalation, Combination, "delayed" schedule

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male/Female patients aged 18 years or over
  • Patients must provide written informed consent
  • Part I: Patients with histologically confirmed, locally advanced or metastatic solid tumors. Part II and Part III: Patients with histologically confirmed, pancreatic adenocarcinoma for which the established therapy is Abraxane®/Gemcitabine (clinical standard of care)
  • Life expectancy above 3 months
  • Patients willing to comply with treatment follow-up
  • ECOG Performance status 0 or 1
  • Adequate baseline organ function (hematologic, liver, renal and nutritional)
  • Use a reliable method of contraception in fertile men and women

You may not qualify if:

  • Active infection or other serious illness or autoimmune disease
  • Treatment with live attenuated vaccines in the last three weeks
  • Known chronic liver disease (liver cirrhosis, chronic hepatitis)
  • Treatment with another investigational agent within its five half-lives prior to VCN-01 infusion
  • Chronic immunosuppressive therapy
  • Concurrent malignant hematologic or solid disease
  • Pregnancy or lactation. Patients must agree to use effective contraception or be surgically sterile.
  • Patients receiving full-dose anticoagulant / antiplatelet therapy
  • Adequate levels of neutralizing antibodies against adenovirus
  • Patients with Li Fraumeni syndrome or with previous known retinoblastoma protein pathway germinal deficiency

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (5)

Hospital Vall d'Hebron

Barcelona, 08035, Spain

Location

Institut Català d'Oncologia

L'Hospitalet de Llobregat, 08908, Spain

Location

Centro Integral Oncológico Clara Campal

Madrid, 25080, Spain

Location

Hospital Universitario Ramón y Cajal

Madrid, 28034, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Related Publications (1)

  • Garcia-Carbonero R, Bazan-Peregrino M, Gil-Martin M, Alvarez R, Macarulla T, Riesco-Martinez MC, Verdaguer H, Guillen-Ponce C, Farrera-Sal M, Moreno R, Mato-Berciano A, Maliandi MV, Torres-Manjon S, Costa M, Del Pozo N, Martinez de Villarreal J, Real FX, Vidal N, Capella G, Alemany R, Blasi E, Blasco C, Cascallo M, Salazar R. Phase I, multicenter, open-label study of intravenous VCN-01 oncolytic adenovirus with or without nab-paclitaxel plus gemcitabine in patients with advanced solid tumors. J Immunother Cancer. 2022 Mar;10(3):e003255. doi: 10.1136/jitc-2021-003255.

MeSH Terms

Conditions

NeoplasmsNeoplasm MetastasisPancreatic Neoplasms

Interventions

GemcitabineAlbumin-Bound Paclitaxel

Condition Hierarchy (Ancestors)

Neoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and SymptomsDigestive System NeoplasmsNeoplasms by SiteEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

Heterocyclic CompoundsDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingPaclitaxelTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsDiterpenesTerpenesAlbuminsProteinsAmino Acids, Peptides, and Proteins

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 21, 2014

First Posted

January 27, 2014

Study Start

January 1, 2014

Primary Completion

May 1, 2019

Study Completion

January 1, 2020

Last Updated

October 8, 2020

Record last verified: 2020-10

Locations