NCT02027779

Brief Summary

This study primarily will address the safety and secondarily will assess efficacy of GreenGene™ F in subjects with severe hemophilia A previously treated ≥50 exposure days with a GreenGene™ F, and without presence inhibitor to FVIII (Factor VIII).

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
150

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Jan 2014

Geographic Reach
1 country

2 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2014

Completed
1 day until next milestone

First Submitted

Initial submission to the registry

January 2, 2014

Completed
4 days until next milestone

First Posted

Study publicly available on registry

January 6, 2014

Completed
1.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2015

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2016

Completed
Last Updated

January 6, 2014

Status Verified

January 1, 2014

Enrollment Period

1.9 years

First QC Date

January 2, 2014

Last Update Submit

January 3, 2014

Conditions

Keywords

GreenGene™ F, Previously Treated Patients

Outcome Measures

Primary Outcomes (1)

  • Number of subjects with development of inhibitors

    Development of neutralizing antibodies (inhibitors) will be followed during the regular visits, average of 3 months.

    every 3 months, up to 18 months

Study Arms (2)

Prophylaxis safety and efficacy substudy

EXPERIMENTAL

Hemostatic efficacy of GreenGene™ F will be assessed by its effectiveness in controlling spontaneous or traumatic bleeding episodes and by the rate of breakthrough bleeding during prophylaxis over ≥ 50 additional exposure days.

Biological: GreenGene™ F

On-demand safety and efficacy substudy

EXPERIMENTAL

Hemostatic efficacy of GreenGene™ F will be assessed by its effectiveness in controlling spontaneous or traumatic bleeding episodes and by the rate of breakthrough bleeding in a minimum of 10 on demand treated subjects during additional 50 exposure days.

Biological: GreenGene™ F

Interventions

GreenGene™ FBIOLOGICAL

Prophylaxis safety and efficacy substudy: intra venous infusion, 30 ± 10 IU/kg infusions 3 times per week with dose escalation to 45 ± 10 IU/kg if appropriate, for 50 exposure days

Also known as: GreenGeneF, GreenGene F
Prophylaxis safety and efficacy substudy

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Subjects must have participated in the "GreenGene™ F\_P3", (with Eudra CT number 2012-001445-40) or a pediatric study with GreenGene™ F
  • Have ≥50 previous exposure days to GreenGene™ F, as documented in the subject's medical records.
  • Normal liver and kidney function
  • Platelet count ≥ 100,000㎕
  • Normal prothrombin time or International Normalized Ratio (INR) \< 1.5
  • Subjects receiving therapy for human immunodeficiency virus (HIV) or hepatitis must be on a stable treatment regimen
  • Subjects must be able to withhold FVIII infusions for approximately 72 h prior to each inhibitor assay
  • Absolute CD4 lymphocyte cell count ≥ 200㎕
  • Signed the written informed consent form or informed consent was obtained from the subject's legal guardian
  • Females must not be lactating or pregnant at screening or Baseline (as documented by a negative beta-human chorionic gonadotropin \[β-hCG\] test with a minimum sensitivity of 25 IU/L or equivalent units of β-hCG). A test was obtained more than 72 hours before the first dose of study drug
  • All females will be considered to be of childbearing potential unless they are appropriate age group and without other known or suspected cause) or have been sterilized surgically (i.e. bilateral tubal ligation, total hysterectomy or bilateral oophorectomy, all with surgery at least one month before dosing)
  • Willing and able to comply with all aspects of the protocol

You may not qualify if:

  • Presence at Screening of FVIII inhibitor ≥ 0.6 BU as tested with the Nijmegen modification of the Bethesda assay.
  • Laboratory or clinical evidence of portal vein hypertension including, but not limited to, an INR \> 1.4, the presence of splenomegaly and/or spider angiomata of physical examination and/or a history of esophageal hemorrhage or documented esophageal varices
  • Uncontrolled hypertension (diastolic blood pressure \>100 mm Hg)
  • Hemoglobin \< 10 g/dL
  • Severe renal dysfunction (creatinine \> 2x upper limit of normal \[ULN\], total bilirubin \> 2x the ULN)
  • Liver disease (alanine aminotransferase \[ALT\], aspartate aminotransferase \[AST\] \> 3x the ULN)
  • History of diabetes or other metabolic disease
  • History of hypersensitivity or serious adverse reaction to recombinant or plasma-derived FVIII concentrates
  • History of pretreatment prior to the administration of FVIII products (e.g., antihistamines)
  • Regular use of antifibrinolytics or medications affecting platelet function
  • Hypersensitivity to hamster- or mouse derived proteins
  • Blood transfusions within 30 days of enrollment into the study
  • Current participation in another investigational drug or device study, or participated in a clinical study involving an investigational drug or device within 30 days of enrollment into the study
  • Unable or unwilling to cooperate with study procedures
  • Females who are pregnant (positive β-hCG test) or breastfeeding

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Arkansas Children's Hospital

Little Rock, Arkansas, 72202, United States

RECRUITING

Long Island Jewish Medical Center - Hemophilia Treatment Center

New Hyde Park, New York, 11040, United States

RECRUITING

MeSH Terms

Conditions

Hemophilia A

Condition Hierarchy (Ancestors)

Blood Coagulation Disorders, InheritedBlood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesCoagulation Protein DisordersHemorrhagic DisordersGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 2, 2014

First Posted

January 6, 2014

Study Start

January 1, 2014

Primary Completion

December 1, 2015

Study Completion

February 1, 2016

Last Updated

January 6, 2014

Record last verified: 2014-01

Locations